Efficacy and Safety of Cinacalcet in Pediatric Patients With Secondary Hyperparathyroidism (SHPT) and Chronic Kidney Disease (CKD) on Dialysis

NCT ID: NCT02138838

Last Updated: 2020-06-29

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

55 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-11-07

Study Completion Date

2016-06-23

Brief Summary

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The primary objective was to evaluate the efficacy of cinacalcet for reducing the plasma intact parathyroid hormone (iPTH) level by ≥ 30%.

Detailed Description

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This was a 24-week, randomized, multicenter, open-label, controlled study. Participants were randomized into one of two treatment arms; oral administration of cinacalcet daily in addition to standard of care treatment, or standard of care alone. Randomization was stratified by age group (6 to \< 12 and 12 to \< 18 years of age). All participants received standard of care which could include therapy with Vitamin D sterols, calcium supplementation, and phosphate binders.

Participants in both treatment groups who completed the 20-week treatment period and those who ended the study due to study closure were eligible to enroll in an open-label extension study (20140159; NCT02341417) for further safety follow-up.

Conditions

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Chronic Kidney Disease, Secondary Hyperparathyroidism

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Standard of Care

Standard of care therapy included the use of vitamin D sterols, calcium supplementation, and phosphate binders.

Group Type ACTIVE_COMPARATOR

Standard of Care

Intervention Type DIETARY_SUPPLEMENT

Standard of care therapy included the use of vitamin D sterols, calcium supplementation, and phosphate binders.

Cinacalcet

In addition to standard of care participants received cinacalcet at a starting dose (based on dry body weight) of 0.20 mg/kg administered once a day by mouth. Dose adjustments and withholding were based on ionized calcium levels, plasma iPTH, and corrected calcium levels.

Group Type EXPERIMENTAL

Cinacalcet HCl

Intervention Type DRUG

Capsules were opened and either sprinkled onto soft food (≥ 5 mg dose) or suspended into a sucrose syrup (≥ 2.5 mg dose) to create a liquid suspension for administration. Tablets were used for doses of 30 mg and higher in participants who could swallow tablets.

Standard of Care

Intervention Type DIETARY_SUPPLEMENT

Standard of care therapy included the use of vitamin D sterols, calcium supplementation, and phosphate binders.

Interventions

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Cinacalcet HCl

Capsules were opened and either sprinkled onto soft food (≥ 5 mg dose) or suspended into a sucrose syrup (≥ 2.5 mg dose) to create a liquid suspension for administration. Tablets were used for doses of 30 mg and higher in participants who could swallow tablets.

Intervention Type DRUG

Standard of Care

Standard of care therapy included the use of vitamin D sterols, calcium supplementation, and phosphate binders.

Intervention Type DIETARY_SUPPLEMENT

Other Intervention Names

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Sensipar® Mimpara®

Eligibility Criteria

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Inclusion Criteria

* Age 6 - \< 18 years
* Diagnosis of SHPT with the mean of the two consecutive central laboratory iPTH values ≥ 300 pg/mL during screening
* Corrected calcium value of ≥ 8.8 mg/dL during screening
* Diagnosis of CKD, receiving either hemodialysis or peritoneal dialysis, for ≥ 30 days prior to screening
* Parent or legally acceptable representative has provided written informed consent and subject has provided written assent when required by institutional guidelines

Exclusion Criteria

* History of congenital long QT syndrome, second or third degree heart block, ventricular tachyarrhythmias or other conditions associated with prolonged QT interval
* Corrected QT interval (QTc) \> 500 ms, using Bazett's formula
* QTc ≥ 450 to ≤ 500 ms, using Bazett's formula, unless written permission to enroll is provided by the investigator after consultation with a pediatric cardiologist
* Use of grapefruit juice, herbal medications, or potent cytochrome P450 3A4 (CYP3A4) inhibitors (eg, erythromycin, clarithromycin, ketoconazole, itraconazole)
* Use of concomitant medications that may prolong the QTc interval (eg, ondansetron, albuterol)
Minimum Eligible Age

6 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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Research Site

Los Angeles, California, United States

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Wilmington, Delaware, United States

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Atlanta, Georgia, United States

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Chicago, Illinois, United States

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Iowa City, Iowa, United States

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Louisville, Kentucky, United States

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Baltimore, Maryland, United States

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Boston, Massachusetts, United States

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Detroit, Michigan, United States

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Minneapolis, Minnesota, United States

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Jackson, Mississippi, United States

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Kansas City, Missouri, United States

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St Louis, Missouri, United States

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St Louis, Missouri, United States

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West Orange, New Jersey, United States

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New York, New York, United States

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The Bronx, New York, United States

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Greenville, North Carolina, United States

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Cincinnati, Ohio, United States

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Cleveland, Ohio, United States

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Columbus, Ohio, United States

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Philadelphia, Pennsylvania, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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Salt Lake City, Utah, United States

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Brussels, , Belgium

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Ghent, , Belgium

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Leuven, , Belgium

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Prague, , Czechia

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Bron, , France

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Lille, , France

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Marseille, , France

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Nice, , France

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Paris, , France

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Paris, , France

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Paris, , France

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Hanover, , Germany

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Heidelberg, , Germany

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Marburg, , Germany

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Athens, , Greece

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Thessaloniki, , Greece

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Budapest, , Hungary

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Szeged, , Hungary

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Genova, , Italy

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Napoli, , Italy

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Torino, , Italy

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Vilinus, , Lithuania

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Grafton, Auckland, , New Zealand

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Krakow, , Poland

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Lodz, , Poland

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Warsaw, , Poland

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Porto, , Portugal

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Moscow, , Russia

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Saint Petersburg, , Russia

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Samara, , Russia

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Košice, , Slovakia

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Barcelona, Catalonia, Spain

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Espluques de LLobregat, Catalonia, Spain

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Kyiv, , Ukraine

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Countries

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United States Belgium Czechia France Germany Greece Hungary Italy Lithuania New Zealand Poland Portugal Russia Slovakia Spain Ukraine

References

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Chen P, Sohn W, Narayanan A, Gisleskog PO, Melhem M. Bridging adults and paediatrics with secondary hyperparathyroidism receiving haemodialysis: a pharmacokinetic-pharmacodynamic analysis of cinacalcet. Br J Clin Pharmacol. 2019 Jun;85(6):1312-1325. doi: 10.1111/bcp.13900. Epub 2019 Apr 25.

Reference Type BACKGROUND
PMID: 30756425 (View on PubMed)

Warady BA, Ng E, Bloss L, Mo M, Schaefer F, Bacchetta J. Cinacalcet studies in pediatric subjects with secondary hyperparathyroidism receiving dialysis. Pediatr Nephrol. 2020 Sep;35(9):1679-1697. doi: 10.1007/s00467-020-04516-4. Epub 2020 May 4.

Reference Type BACKGROUND
PMID: 32367309 (View on PubMed)

Related Links

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http://www.amgentrials.com

AmgenTrials clinical trials website

Other Identifiers

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2013-004958-18

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

20130356

Identifier Type: -

Identifier Source: org_study_id

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