Head-to-Head Study of Etelcalcetide (AMG 416) and Cinacalcet

NCT ID: NCT01896232

Last Updated: 2019-07-18

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

683 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-08-13

Study Completion Date

2015-01-08

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to demonstrate that treatment with etelcalcetide (AMG 416) is not inferior to treatment with cinacalcet for lowering serum parathyroid hormone (PTH) levels by \> 30% from baseline among patients with chronic kidney disease (CKD) and secondary hyperparathyroidism (SHPT) who require management with hemodialysis.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Secondary Hyperparathyroidism Chronic Kidney Disease

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Cinacalcet

Participants were randomized to receive oral cinacalcet once daily and placebo intravenous bolus injection at the end of each hemodialysis session, three times per week (TIW) for 26 weeks. The starting dose of cinacalcet was 30 mg daily and could have been titrated at weeks 5, 9, 13, and 17 to target predialysis serum PTH ≤ 300 pg/mL but no lower than 100 pg/mL while maintaining corrected calcium (cCa) ≥ 8.3 mg/dL.

Group Type ACTIVE_COMPARATOR

Cinacalcet

Intervention Type DRUG

Cinacalcet was administered orally once a day. The starting dose was 30 mg daily, titrated up to 180 mg daily based on serum PTH and corrected calcium levels.

Intravenous Placebo

Intervention Type DRUG

Administered intravenously (IV) three times per week.

Etelcalcetide

Participants were randomized to receive etelcalcetide administered by intravenous bolus injection at the end of each hemodialysis session TIW, and daily oral doses of placebo tablets for 26 weeks. The starting dose of etelcalcetide was 5 mg, and could have been titrated at weeks 5, 9, 13, and 17 to target predialysis serum PTH ≤ 300 pg/mL but no lower than 100 pg/mL while maintaining cCa ≥ 8.3 mg/dL.

Group Type EXPERIMENTAL

Etelcalcetide

Intervention Type DRUG

Administered intravenously three times per week. The starting dose was 5 mg, titrated up to 15 mg based on serum PTH and corrected calcium levels.

Oral Placebo

Intervention Type DRUG

Administered orally once a day.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Etelcalcetide

Administered intravenously three times per week. The starting dose was 5 mg, titrated up to 15 mg based on serum PTH and corrected calcium levels.

Intervention Type DRUG

Cinacalcet

Cinacalcet was administered orally once a day. The starting dose was 30 mg daily, titrated up to 180 mg daily based on serum PTH and corrected calcium levels.

Intervention Type DRUG

Oral Placebo

Administered orally once a day.

Intervention Type DRUG

Intravenous Placebo

Administered intravenously (IV) three times per week.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

AMG 416 Sensipar®, Mimpara®

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Eligible subjects must be receiving adequate thrice weekly maintenance hemodialysis with a dialysate calcium concentration ≥ 2.5 mEq/L for at least 3 months prior to screening laboratory assessments
* Subjects must have SHPT as defined by one central laboratory screening predialysis serum PTH value \> 500 pg/mL, measured on separate days within 2 weeks prior to randomization
* Subjects must have one serum cCa value ≥ 8.3 mg/dL obtained before dialysis within 2 weeks of the date of randomization
* Subjects receiving calcium supplements must have no more than a maximum dose change of 50% within 2 weeks before screening laboratory assessments are obtained, and the dose must remain unchanged through randomization

Exclusion Criteria

* Eligible subjects cannot have received cinacalcet during the 3 months preceding the first screening laboratory assessment
* Other criteria may apply
Minimum Eligible Age

18 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

MD

Role: STUDY_DIRECTOR

Amgen

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Research Site

Azusa, California, United States

Site Status

Research Site

Bakersfield, California, United States

Site Status

Research Site

Bakersfield, California, United States

Site Status

Research Site

Chula Vista, California, United States

Site Status

Research Site

Covina, California, United States

Site Status

Research Site

Granada Hills, California, United States

Site Status

Research Site

La Mesa, California, United States

Site Status

Research Site

La Puente, California, United States

Site Status

Research Site

Los Angeles, California, United States

Site Status

Research Site

San Diego, California, United States

Site Status

Research Site

San Gabriel, California, United States

Site Status

Research Site

Whittier, California, United States

Site Status

Research Site

Arvada, Colorado, United States

Site Status

Research Site

Aurora, Colorado, United States

Site Status

Research Site

Longmont, Colorado, United States

Site Status

Research Site

Westminster, Colorado, United States

Site Status

Research Site

Orange, Connecticut, United States

Site Status

Research Site

Pembroke Pines, Florida, United States

Site Status

Research Site

Pinecrest, Florida, United States

Site Status

Research Site

Tampa, Florida, United States

Site Status

Research Site

Baton Rouge, Louisiana, United States

Site Status

Research Site

Lafayette, Louisiana, United States

Site Status

Research Site

Southgate, Michigan, United States

Site Status

Research Site

Columbus, Mississippi, United States

Site Status

Research Site

Gulfport, Mississippi, United States

Site Status

Research Site

Sewell, New Jersey, United States

Site Status

Research Site

Great Neck, New York, United States

Site Status

Research Site

Mineola, New York, United States

Site Status

Research Site

Ridgewood, New York, United States

Site Status

Research Site

Rosedale, New York, United States

Site Status

Research Site

The Bronx, New York, United States

Site Status

Research Site

Wilmington, North Carolina, United States

Site Status

Research Site

Cincinnati, Ohio, United States

Site Status

Research Site

Columbus, Ohio, United States

Site Status

Research Site

Philadelphia, Pennsylvania, United States

Site Status

Research Site

Houston, Texas, United States

Site Status

Research Site

San Antonio, Texas, United States

Site Status

Research Site

Burlington, Vermont, United States

Site Status

Research Site

Fairfax, Virginia, United States

Site Status

Research Site

Portsmouth, Virginia, United States

Site Status

Research Site

Madison, Wisconsin, United States

Site Status

Research Site

Feldkirch, , Austria

Site Status

Research Site

Linz, , Austria

Site Status

Research Site

Vienna, , Austria

Site Status

Research Site

Genk, , Belgium

Site Status

Research Site

Hasselt, , Belgium

Site Status

Research Site

Kortrijk, , Belgium

Site Status

Research Site

Roeselare, , Belgium

Site Status

Research Site

Edmonton, Alberta, Canada

Site Status

Research Site

Saint John, New Brunswick, Canada

Site Status

Research Site

St. John's, Newfoundland and Labrador, Canada

Site Status

Research Site

Brampton, Ontario, Canada

Site Status

Research Site

Greenfield Park, Quebec, Canada

Site Status

Research Site

Nový Jičín, , Czechia

Site Status

Research Site

Prague, , Czechia

Site Status

Research Site

Praha 4 - Nusle, , Czechia

Site Status

Research Site

Slavkov u Brna, , Czechia

Site Status

Research Site

Třinec, , Czechia

Site Status

Research Site

Ústí nad Orlicí, , Czechia

Site Status

Research Site

Aalborg, , Denmark

Site Status

Research Site

Copenhagen, , Denmark

Site Status

Research Site

Fredericia, , Denmark

Site Status

Research Site

Odense, , Denmark

Site Status

Research Site

Roskilde, , Denmark

Site Status

Research Site

Tallinn, , Estonia

Site Status

Research Site

Tallinn, , Estonia

Site Status

Research Site

Tartu, , Estonia

Site Status

Research Site

Boulogne-sur-Mer, , France

Site Status

Research Site

Lille, , France

Site Status

Research Site

Nouilly, , France

Site Status

Research Site

Paris, , France

Site Status

Research Site

Paris, , France

Site Status

Research Site

Saint-Ouen, , France

Site Status

Research Site

Saint-Priest-en-Jarez, , France

Site Status

Research Site

Sainte-Foy-lès-Lyon, , France

Site Status

Research Site

Aachen, , Germany

Site Status

Research Site

Coburg, , Germany

Site Status

Research Site

Hamburg, , Germany

Site Status

Research Site

Hanover, , Germany

Site Status

Research Site

Magdeburg, , Germany

Site Status

Research Site

Mettmann, , Germany

Site Status

Research Site

Minden, , Germany

Site Status

Research Site

München, , Germany

Site Status

Research Site

Wiesbaden, , Germany

Site Status

Research Site

Zwickau, , Germany

Site Status

Research Site

Alexandroupoli, , Greece

Site Status

Research Site

Athens, , Greece

Site Status

Research Site

Ioannina, , Greece

Site Status

Research Site

Larissa, , Greece

Site Status

Research Site

Nikaia, Piraeus, , Greece

Site Status

Research Site

Pátrai, , Greece

Site Status

Research Site

Thessaloniki, , Greece

Site Status

Research Site

Budapest, , Hungary

Site Status

Research Site

Győr, , Hungary

Site Status

Research Site

Kaposvár, , Hungary

Site Status

Research Site

Kistarcsa, , Hungary

Site Status

Research Site

Pécs, , Hungary

Site Status

Research Site

Pécs, , Hungary

Site Status

Research Site

Székesfehérvár, , Hungary

Site Status

Research Site

Szigetvár, , Hungary

Site Status

Research Site

Zalaegerszeg, , Hungary

Site Status

Research Site

Cagliari, , Italy

Site Status

Research Site

Florence, , Italy

Site Status

Research Site

Genova, , Italy

Site Status

Research Site

Lecco, , Italy

Site Status

Research Site

Lucca, , Italy

Site Status

Research Site

Milan, , Italy

Site Status

Research Site

Pavia, , Italy

Site Status

Research Site

Pisa, , Italy

Site Status

Research Site

Pordenone, , Italy

Site Status

Research Site

San Giovanni Rotondo FG, , Italy

Site Status

Research Site

Riga, , Latvia

Site Status

Research Site

Riga, , Latvia

Site Status

Research Site

Valmiera, , Latvia

Site Status

Research Site

Alytus, , Lithuania

Site Status

Research Site

Kaunas, , Lithuania

Site Status

Research Site

Kaunas, , Lithuania

Site Status

Research Site

Kėdainiai, , Lithuania

Site Status

Research Site

Klaipėda, , Lithuania

Site Status

Research Site

Šiauliai, , Lithuania

Site Status

Research Site

Ukmerge, , Lithuania

Site Status

Research Site

Hamilton, , New Zealand

Site Status

Research Site

Papatoetoe, Auckland, , New Zealand

Site Status

Research Site

Takapuna, Auckland City, , New Zealand

Site Status

Research Site

Gdansk, , Poland

Site Status

Research Site

Katowice, , Poland

Site Status

Research Site

Poznan, , Poland

Site Status

Research Site

Poznan, , Poland

Site Status

Research Site

Sieradz, , Poland

Site Status

Research Site

Wadowice, , Poland

Site Status

Research Site

Warsaw, , Poland

Site Status

Research Site

Warsaw, , Poland

Site Status

Research Site

Zabrze, , Poland

Site Status

Research Site

Żyrardów, , Poland

Site Status

Research Site

Almada, , Portugal

Site Status

Research Site

Aveiro, , Portugal

Site Status

Research Site

Estoril, , Portugal

Site Status

Research Site

Forte Da Casa, , Portugal

Site Status

Research Site

Guimarães, , Portugal

Site Status

Research Site

Lisbon, , Portugal

Site Status

Research Site

Santo Tirso, , Portugal

Site Status

Research Site

Setúbal, , Portugal

Site Status

Research Site

Vila Franca de Xira, , Portugal

Site Status

Research Site

Mitishi, , Russia

Site Status

Research Site

Moscow, , Russia

Site Status

Research Site

Moscow, , Russia

Site Status

Research Site

Petrozavodsk, , Russia

Site Status

Research Site

Saint Petersburg, , Russia

Site Status

Research Site

Saint Petersburg, , Russia

Site Status

Research Site

Saint Petersburg, , Russia

Site Status

Research Site

Saint Petersburg, , Russia

Site Status

Research Site

Saint Petersburg, , Russia

Site Status

Research Site

Yaroslavl, , Russia

Site Status

Research Site

Córdoba, Andalusia, Spain

Site Status

Research Site

Puerto Real, Andalusia, Spain

Site Status

Research Site

Galdakao, Basque Country, Spain

Site Status

Research Site

Badalona, Catalonia, Spain

Site Status

Research Site

Lleida, Catalonia, Spain

Site Status

Research Site

Badajoz, Extremadura, Spain

Site Status

Research Site

Pamplona, Navarre, Spain

Site Status

Research Site

Torrevieja, Valencia, Spain

Site Status

Research Site

Valencia, Valencia, Spain

Site Status

Research Site

Madrid, , Spain

Site Status

Research Site

Madrid, , Spain

Site Status

Research Site

Malmo, , Sweden

Site Status

Research Site

Stockholm, , Sweden

Site Status

Research Site

Trollhättan, , Sweden

Site Status

Research Site

Aarau, , Switzerland

Site Status

Research Site

Bern, , Switzerland

Site Status

Research Site

Geneva, , Switzerland

Site Status

Research Site

Lausanne, , Switzerland

Site Status

Research Site

Lausanne, , Switzerland

Site Status

Research Site

Locarno, , Switzerland

Site Status

Research Site

Zurich, , Switzerland

Site Status

Research Site

Ankara, , Turkey (Türkiye)

Site Status

Research Site

Ankara, , Turkey (Türkiye)

Site Status

Research Site

Ankara, , Turkey (Türkiye)

Site Status

Research Site

Istanbul, , Turkey (Türkiye)

Site Status

Research Site

Istanbul, , Turkey (Türkiye)

Site Status

Research Site

Izmir, , Turkey (Türkiye)

Site Status

Research Site

Izmir, , Turkey (Türkiye)

Site Status

Research Site

Izmir, , Turkey (Türkiye)

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Austria Belgium Canada Czechia Denmark Estonia France Germany Greece Hungary Italy Latvia Lithuania New Zealand Poland Portugal Russia Spain Sweden Switzerland Turkey (Türkiye)

References

Explore related publications, articles, or registry entries linked to this study.

Block GA, Bushinsky DA, Cheng S, Cunningham J, Dehmel B, Drueke TB, Ketteler M, Kewalramani R, Martin KJ, Moe SM, Patel UD, Silver J, Sun Y, Wang H, Chertow GM. Effect of Etelcalcetide vs Cinacalcet on Serum Parathyroid Hormone in Patients Receiving Hemodialysis With Secondary Hyperparathyroidism: A Randomized Clinical Trial. JAMA. 2017 Jan 10;317(2):156-164. doi: 10.1001/jama.2016.19468.

Reference Type BACKGROUND
PMID: 28097356 (View on PubMed)

Stollenwerk B, Iannazzo S, Akehurst R, Adena M, Briggs A, Dehmel B, Parfrey P, Belozeroff V. A Decision-Analytic Model to Assess the Cost-Effectiveness of Etelcalcetide vs. Cinacalcet. Pharmacoeconomics. 2018 May;36(5):603-612. doi: 10.1007/s40273-017-0605-2.

Reference Type BACKGROUND
PMID: 29392552 (View on PubMed)

Stollenwerk B, Iannazzo S, Cooper K, Belozeroff V. Exploring the potential value of improved care for secondary hyperparathyroidism with a novel calcimimetic therapy. J Med Econ. 2017 Oct;20(10):1110-1115. doi: 10.1080/13696998.2017.1360309. Epub 2017 Aug 14.

Reference Type BACKGROUND
PMID: 28803497 (View on PubMed)

Wu B, Melhem M, Subramanian R, Chen P, Jaramilla Sloey B, Fouqueray B, Hock MB, Skiles GL, Chow AT, Lee E. Clinical Pharmacokinetics and Pharmacodynamics of Etelcalcetide, a Novel Calcimimetic for Treatment of Secondary Hyperparathyroidism in Patients With Chronic Kidney Disease on Hemodialysis. J Clin Pharmacol. 2018 Jun;58(6):717-726. doi: 10.1002/jcph.1090. Epub 2018 Mar 13.

Reference Type BACKGROUND
PMID: 29534286 (View on PubMed)

Block GA, Chertow GM, Sullivan JT, Deng H, Mather O, Tomlin H, Serenko M. An integrated analysis of safety and tolerability of etelcalcetide in patients receiving hemodialysis with secondary hyperparathyroidism. PLoS One. 2019 Mar 15;14(3):e0213774. doi: 10.1371/journal.pone.0213774. eCollection 2019.

Reference Type BACKGROUND
PMID: 30875390 (View on PubMed)

Wolf M, Block GA, Chertow GM, Cooper K, Fouqueray B, Moe SM, Sun Y, Tomlin H, Vervloet M, Oberbauer R. Effects of etelcalcetide on fibroblast growth factor 23 in patients with secondary hyperparathyroidism receiving hemodialysis. Clin Kidney J. 2019 Apr 26;13(1):75-84. doi: 10.1093/ckj/sfz034. eCollection 2020 Feb.

Reference Type BACKGROUND
PMID: 32082556 (View on PubMed)

Related Links

Access external resources that provide additional context or updates about the study.

http://www.amgentrials.com

AmgenTrials clinical trials website

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2013-000192-33

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

20120360

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.