Efficacy and Safety of Etelcalcetide (AMG 416) in the Treatment of Secondary Hyperparathyroidism (SHPT) in Patients With Chronic Kidney Disease (CKD) on Hemodialysis

NCT ID: NCT01788046

Last Updated: 2019-08-20

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

515 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-03-12

Study Completion Date

2014-05-09

Brief Summary

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This study is designed to assess the efficacy and safety of etelcalcetide (AMG 416) compared with placebo in the treatment of SHPT in CKD patients receiving hemodialysis.

Detailed Description

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Conditions

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Hyperparathyroidism, Secondary

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Placebo

Participants received placebo administered by intravenous bolus injection at the end of each hemodialysis session, three times per week (TIW) for 26 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered intravenously (IV) three times per week.

Etelcalcetide

Participants received etelcalcetide administered by intravenous bolus injection at the end of each hemodialysis session TIW for 26 weeks.

Group Type EXPERIMENTAL

Etelcalcetide

Intervention Type DRUG

Administered intravenously three times per week. The starting dose was 5 mg. The dose may have been increased at weeks 5, 9, 13, and 17 (4-week intervals) by 2.5 mg or 5 mg on the basis of the predialysis parathyroid hormone and corrected calcium concentrations obtained in the prior week. The minimum dose was 2.5 mg and the maximum dose was 15 mg.

Interventions

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Etelcalcetide

Administered intravenously three times per week. The starting dose was 5 mg. The dose may have been increased at weeks 5, 9, 13, and 17 (4-week intervals) by 2.5 mg or 5 mg on the basis of the predialysis parathyroid hormone and corrected calcium concentrations obtained in the prior week. The minimum dose was 2.5 mg and the maximum dose was 15 mg.

Intervention Type DRUG

Placebo

Administered intravenously (IV) three times per week.

Intervention Type DRUG

Other Intervention Names

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AMG 416

Eligibility Criteria

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Inclusion Criteria

* Subject understands the study procedures and agrees to participate in the study by giving written informed consent.
* Subject is 18 years of age or older.
* Subject agrees to not participate in another study of an investigational agent during the study.
* Subject must be receiving hemodialysis 3 times weekly for at least 3 months

Exclusion Criteria

* Currently receiving treatment in another investigational device or drug study, or ended treatment on another investigational device or drug study(s) within 8 weeks prior to screening.
* Other investigational procedures while participating in this study are excluded.
* Anticipated or scheduled parathyroidectomy during the study period.
* Subject has received a parathyroidectomy within 3 months prior to dosing.
* Anticipated or scheduled kidney transplant during the study period.
* Subject has known sensitivity to any of the products or components to be administered during dosing.
* Subject has participated in a prior clinical trial of AMG 416
* Subject has an unstable medical condition based on medical history, physical examination, and routine laboratory tests, or is otherwise unstable in the judgment of the Investigator.
* Subject has a history of any illness that, in the opinion of the Investigator, might confound the results of the study or pose additional risk to the subject.
Minimum Eligible Age

18 Years

Maximum Eligible Age

100 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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Research Site

Mobile, Alabama, United States

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Azusa, California, United States

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Beverly Hills, California, United States

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Chula Vista, California, United States

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Fairfield, California, United States

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Glendale, California, United States

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Los Angeles, California, United States

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Northridge, California, United States

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Norwalk, California, United States

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Riverside, California, United States

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Simi Valley, California, United States

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Denver, Colorado, United States

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Stamford, Connecticut, United States

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Lauderdale Lakes, Florida, United States

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Miami, Florida, United States

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Ocala, Florida, United States

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Augusta, Georgia, United States

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Macon, Georgia, United States

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Chicago, Illinois, United States

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Gurnee, Illinois, United States

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Merrillville, Indiana, United States

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Wichita, Kansas, United States

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Shreveport, Louisiana, United States

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Bethesda, Maryland, United States

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Ft. Washington, Maryland, United States

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Detroit, Michigan, United States

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Brookhaven, Mississippi, United States

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Lincoln, Nebraska, United States

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Las Vegas, Nevada, United States

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Eatontown, New Jersey, United States

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Brooklyn, New York, United States

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Fresh Meadows, New York, United States

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Great Neck, New York, United States

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Charlotte, North Carolina, United States

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New Bern, North Carolina, United States

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Cincinnati, Ohio, United States

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Columbia, South Carolina, United States

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Chattanooga, Tennessee, United States

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Knoxville, Tennessee, United States

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Arlington, Texas, United States

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Houston, Texas, United States

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Lubbock, Texas, United States

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Rutland, Vermont, United States

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Alexandria, Virginia, United States

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Morgantown, West Virginia, United States

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Westmead, New South Wales, Australia

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Brisbane, Queensland, Australia

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Adelaide, South Australia, Australia

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Clayton, Victoria, Australia

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Bonheiden, , Belgium

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Brussels, , Belgium

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Brussels, , Belgium

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Liège, , Belgium

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Roeselare, , Belgium

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Tournai, , Belgium

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Edmonton, Alberta, Canada

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New Westminster, British Columbia, Canada

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Halifax, Nova Scotia, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Nový Jičín, , Czechia

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Pilsen, , Czechia

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Prague, , Czechia

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Ústí nad Orlicí, , Czechia

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Bordeaux, , France

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Caen, , France

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Grenoble, , France

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Marseille, , France

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Marseille, , France

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Perpignan, , France

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Erfurt, , Germany

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Budapest, , Hungary

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Budapest, , Hungary

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Esztergom, , Hungary

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Kecskemét, , Hungary

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Miskolc, , Hungary

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Zalaegerszeg, , Hungary

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Jerusalem, , Israel

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Kfar Saba, , Israel

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Tel Litwinsky, , Israel

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Ẕerifin, , Israel

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Ancona, , Italy

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Lecco, , Italy

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Milan, , Italy

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Quartu Sant'Elena CA, , Italy

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Amsterdam, , Netherlands

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Enschede, , Netherlands

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Rotterdam, , Netherlands

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Venlo, , Netherlands

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Gdansk, , Poland

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Golub-Dobrzyń, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Rybnik, , Poland

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Warsaw, , Poland

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Moscow, , Russia

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Saint Petersburg, , Russia

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Yaroslavl, , Russia

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Córdoba, Andalusia, Spain

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Granada, Andalusia, Spain

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Barcelona, Catalonia, Spain

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Barcelona, Catalonia, Spain

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Majadahonda, Madrid, Spain

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Karlstad, , Sweden

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Stockholm, , Sweden

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Uppsala, , Sweden

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Countries

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United States Australia Belgium Canada Czechia France Germany Hungary Israel Italy Netherlands Poland Russia Spain Sweden

References

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Block GA, Bushinsky DA, Cunningham J, Drueke TB, Ketteler M, Kewalramani R, Martin KJ, Mix TC, Moe SM, Patel UD, Silver J, Spiegel DM, Sterling L, Walsh L, Chertow GM. Effect of Etelcalcetide vs Placebo on Serum Parathyroid Hormone in Patients Receiving Hemodialysis With Secondary Hyperparathyroidism: Two Randomized Clinical Trials. JAMA. 2017 Jan 10;317(2):146-155. doi: 10.1001/jama.2016.19456.

Reference Type BACKGROUND
PMID: 28097355 (View on PubMed)

Kroenke MA, Weeraratne DK, Deng H, Sloey B, Subramanian R, Wu B, Serenko M, Hock MB. Clinical immunogenicity of the d-amino acid peptide therapeutic etelcalcetide: Method development challenges and anti-drug antibody clinical impact assessments. J Immunol Methods. 2017 Jun;445:37-44. doi: 10.1016/j.jim.2017.03.005. Epub 2017 Mar 6.

Reference Type BACKGROUND
PMID: 28274835 (View on PubMed)

Stollenwerk B, Iannazzo S, Akehurst R, Adena M, Briggs A, Dehmel B, Parfrey P, Belozeroff V. A Decision-Analytic Model to Assess the Cost-Effectiveness of Etelcalcetide vs. Cinacalcet. Pharmacoeconomics. 2018 May;36(5):603-612. doi: 10.1007/s40273-017-0605-2.

Reference Type BACKGROUND
PMID: 29392552 (View on PubMed)

Stollenwerk B, Iannazzo S, Cooper K, Belozeroff V. Exploring the potential value of improved care for secondary hyperparathyroidism with a novel calcimimetic therapy. J Med Econ. 2017 Oct;20(10):1110-1115. doi: 10.1080/13696998.2017.1360309. Epub 2017 Aug 14.

Reference Type BACKGROUND
PMID: 28803497 (View on PubMed)

Chen P, Narayanan A, Wu B, Gisleskog PO, Gibbs JP, Chow AT, Melhem M. Population Pharmacokinetic and Pharmacodynamic Modeling of Etelcalcetide in Patients with Chronic Kidney Disease and Secondary Hyperparathyroidism Receiving Hemodialysis. Clin Pharmacokinet. 2018 Jan;57(1):71-85. doi: 10.1007/s40262-017-0550-4.

Reference Type BACKGROUND
PMID: 28508378 (View on PubMed)

Block GA, Chertow GM, Sullivan JT, Deng H, Mather O, Tomlin H, Serenko M. An integrated analysis of safety and tolerability of etelcalcetide in patients receiving hemodialysis with secondary hyperparathyroidism. PLoS One. 2019 Mar 15;14(3):e0213774. doi: 10.1371/journal.pone.0213774. eCollection 2019.

Reference Type BACKGROUND
PMID: 30875390 (View on PubMed)

Cunningham J, Block GA, Chertow GM, Cooper K, Evenepoel P, Iles J, Sun Y, Urena-Torres P, Bushinsky DA. Etelcalcetide Is Effective at All Levels of Severity of Secondary Hyperparathyroidism in Hemodialysis Patients. Kidney Int Rep. 2019 Apr 16;4(7):987-994. doi: 10.1016/j.ekir.2019.04.010. eCollection 2019 Jul.

Reference Type BACKGROUND
PMID: 31317120 (View on PubMed)

Wolf M, Block GA, Chertow GM, Cooper K, Fouqueray B, Moe SM, Sun Y, Tomlin H, Vervloet M, Oberbauer R. Effects of etelcalcetide on fibroblast growth factor 23 in patients with secondary hyperparathyroidism receiving hemodialysis. Clin Kidney J. 2019 Apr 26;13(1):75-84. doi: 10.1093/ckj/sfz034. eCollection 2020 Feb.

Reference Type BACKGROUND
PMID: 32082556 (View on PubMed)

Hain D, Tomlin H, Gibson C. Administration of Etelcalcetide for the Treatment of Secondary Hyperparathyroidism in Patients with CKD-MBD on Hemodialysis: A Nephrology Nursing Perspective. Nephrol Nurs J. 2019 May-Jun;46(3):315-290.

Reference Type BACKGROUND
PMID: 31199098 (View on PubMed)

Related Links

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http://www.amgentrials.com

AmgenTrials clinical trials website

Other Identifiers

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KAI-4169-007

Identifier Type: OTHER

Identifier Source: secondary_id

2012-002806-31

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

20120230

Identifier Type: -

Identifier Source: org_study_id

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