Pharmacokinetic and Pharmacodynamic Study of Emixustat in Subjects With Geographic Atrophy Associated With Dry Age-Related Macular Degeneration

NCT ID: NCT02130531

Last Updated: 2016-01-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

26 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-04-30

Study Completion Date

2015-11-30

Brief Summary

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The purpose of this study is to characterize emixustat hydrochloride pharmacokinetic and pharmacodynamic parameters in subjects with geographic atrophy associated with dry age-related macular degeneration.

Detailed Description

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This is a multi-center, randomized, masked, multiple-dose, crossover study of the pharmacokinetics of emixustat hydrochloride (HCl) in subjects with geographic atrophy (GA) associated with dry age-related macular degeneration (AMD). Subjects will receive study drug during multiple dose periods in a crossover design, and serve as their own controls. There is a 21-28 day washout period between dose periods. The final Study Exit visit is 21 to 28 days after the subject's last dose of study drug at the end of the final dosing period.

Conditions

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Geographic Atrophy Age-Related Macular Degeneration

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Cohort 1

Two dose periods in any sequence (subjects will be assigned to 1 of 2 possible sequences):

* Emixustat HCl Tablet Strength B (mid dose); 1 tablet once daily \& 1 placebo tablet once daily for 7 days
* Emixustat HCl Tablet Strength A (low dose); 1 tablet twice daily for 7 days

Group Type EXPERIMENTAL

Emixustat HCl Tablet

Intervention Type DRUG

Tablet for oral administration

Placebo Tablet

Intervention Type OTHER

Tablet for oral administration

Cohort 2

Three dose periods in any sequence (subjects will be assigned to 1 of 6 possible sequences):

* Emixustat HCl Tablet Strength A (low dose); 1 tablet daily for 7 days
* Emixustat HCl Tablet Strength B (mid dose); 1 tablet daily for 7 days
* Emixustat HCl Tablet Strength C (high dose); 1 tablet daily for 7 days

Group Type EXPERIMENTAL

Emixustat HCl Tablet

Intervention Type DRUG

Tablet for oral administration

Interventions

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Emixustat HCl Tablet

Tablet for oral administration

Intervention Type DRUG

Placebo Tablet

Tablet for oral administration

Intervention Type OTHER

Other Intervention Names

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ACU-4429

Eligibility Criteria

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Inclusion Criteria

* Males or females age ≥65 years
* Clinical diagnosis of GA associated with AMD
* Able and willing to provide written informed consent
* Able to reliably administer oral medication by self or with available assistance

Exclusion Criteria

* Geographic atrophy associated with a condition other than AMD
* History of, active or high risk of developing choroidal neovascularization (CNV) in either eye
* Known serious allergy to the fluorescein sodium for injection in angiography
* Pre-specified laboratory abnormalities at screening
* Treatment with any investigational study drug within 30 days of screening or device within 60 days of screening
* Prior participation in any clinical study of emixustat
* History of other disease, metabolic dysfunction, chronic immunosuppression, physical examination finding
* Male subjects who are not surgically sterile and are not willing to practice a medically accepted method of birth control with their female partner of childbearing potential from screening through 21 days after the last dose of study drug
Minimum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Kubota Vision Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Acucela Medical Monitor

Role: STUDY_DIRECTOR

Kubota Vision Inc.

Locations

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Seattle, Washington, United States

Site Status

Countries

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United States

Other Identifiers

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4429-101

Identifier Type: -

Identifier Source: org_study_id

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