A Study of NGM621 in Participants With Geographic Atrophy

NCT ID: NCT04465955

Last Updated: 2025-07-01

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

320 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-07-22

Study Completion Date

2022-08-16

Brief Summary

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This is a multi-center evaluation of NGM621 in a randomized, double-masked, sham-controlled study in participants with Geographic Atrophy secondary to Age-related Macular Degeneration.

Detailed Description

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Conditions

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Geographic Atrophy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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NGM621 Treatment Group A (every 4 weeks)

NGM621 single intravitreal (IVT) injection

Group Type EXPERIMENTAL

NGM621

Intervention Type BIOLOGICAL

NGM621 Dose 1

NGM621 Treatment Group C (every 8 weeks)

NGM621 single IVT injection

Group Type EXPERIMENTAL

NGM621

Intervention Type BIOLOGICAL

NGM621 Dose 2

Sham Group B (every 4 weeks)

Sham single IVT injection

Group Type SHAM_COMPARATOR

Sham Comparator

Intervention Type OTHER

Sham Comparator

Sham Group D (every 8 weeks)

Sham single IVT injection

Group Type SHAM_COMPARATOR

Sham Comparator

Intervention Type OTHER

Sham Comparator

Interventions

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NGM621

NGM621 Dose 1

Intervention Type BIOLOGICAL

NGM621

NGM621 Dose 2

Intervention Type BIOLOGICAL

Sham Comparator

Sham Comparator

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Male or female (non-pregnant, non-lactating) subjects ≥ 55 years
* Standard luminance BCVA score of 34 letters or better using ETDRS charts at the starting distance of 4 meters (approximately 20/200 Snellen equivalent or better) in study eye
* Clinical diagnosis of GA secondary to AMD:

1. Total GA area must be ≥ 2.5 and ≤ 17.5 mm²
2. If GA is multifocal, at least one focal lesion must be ≥ 1.25 mm² (0.5 DA), with the overall area of GA ≥ 2.5 and ≤ 17.5 mm²
3. Well demarcated GA with no anatomical evidence of current or prior CNV in the study eye

Exclusion Criteria

Study Eye

* GA secondary to a condition other than AMD in either eye (e.g., monogenetic macular dystrophies like Stargardt disease, cone rod dystrophy, or toxic maculopathies)
* Any history of or active choroidal neovascularization (CNV)

Both Eyes

* Any history of or active bacterial, viral, fungal, or parasitic infection in either eye in the 3 months prior to randomization
Minimum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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NGM Biopharmaceuticals, Inc

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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NGM Study Director

Role: STUDY_DIRECTOR

NGM Biopharmaceuticals

Locations

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Associated Retina Consultants

Phoenix, Arizona, United States

Site Status

California Retina Consultants

Bakersfield, California, United States

Site Status

Retina Vitreous Associates

Beverly Hills, California, United States

Site Status

Retinal Diagnostic Center

Campbell, California, United States

Site Status

The Retina Partners

Encino, California, United States

Site Status

Retina Consultants of Orange County

Fullerton, California, United States

Site Status

Loma Linda University Health

Loma Linda, California, United States

Site Status

University of California Los Angeles

Los Angeles, California, United States

Site Status

Northern California Retina Vitreous Associates

Mountain View, California, United States

Site Status

Retina Institute of California

Palm Desert, California, United States

Site Status

California Eye Specialists

Pasadena, California, United States

Site Status

Retina Consultants San Diego

Poway, California, United States

Site Status

Retinal Consultants Medical Group Inc

Sacramento, California, United States

Site Status

University of California San Francisco

San Francisco, California, United States

Site Status

Orange County Retina Medical Group

Santa Ana, California, United States

Site Status

California Retina Consultants

Santa Barbara, California, United States

Site Status

Retina Consultants of Southern Colorado PC

Colorado Springs, Colorado, United States

Site Status

Colorado Retina Associates PC

Golden, Colorado, United States

Site Status

New England Retina Associates PC

Waterford, Connecticut, United States

Site Status

Florida Eye Microsurgical Institute

Boynton Beach, Florida, United States

Site Status

University of Miami

Coral Gables, Florida, United States

Site Status

Specialty Retina Center (Coral Springs)

Coral Springs, Florida, United States

Site Status

Retina Group of Florida

Fort Lauderdale, Florida, United States

Site Status

National Ophthalmic Research Institute

Fort Myers, Florida, United States

Site Status

Florida Eye Associates

Melbourne, Florida, United States

Site Status

Retina Specialty Institute

Pensacola, Florida, United States

Site Status

Southern Vitreoretinal Associates

Tallahassee, Florida, United States

Site Status

Retina Vitreous Associates of Florida

Tampa, Florida, United States

Site Status

Georgia Retina PC

Marietta, Georgia, United States

Site Status

Gailey Eye Clinic - Bloomington

Bloomington, Illinois, United States

Site Status

University of Illinois

Chicago, Illinois, United States

Site Status

University Retina and Macula Associates, PC

Lemont, Illinois, United States

Site Status

Raj K. Maturi, MD, PC

Indianapolis, Indiana, United States

Site Status

Retina Associates, PA

Shawnee Mission, Kansas, United States

Site Status

Thompson Sjaarda, PA

Baltimore, Maryland, United States

Site Status

Elman Retina Group PA

Baltimore, Maryland, United States

Site Status

Ophthalmic Consultants of Boston

Boston, Massachusetts, United States

Site Status

Associated Retina Consultants PC

Royal Oak, Michigan, United States

Site Status

Associated Retina Consultants PC

Traverse City, Michigan, United States

Site Status

Vitreoretinal Surgery PA

Minneapolis, Minnesota, United States

Site Status

Deep Blue Retina Clinical Research

Southaven, Mississippi, United States

Site Status

Sierra Eye Associates

Reno, Nevada, United States

Site Status

Long Island Vitreoretinal Consultants

Great Neck, New York, United States

Site Status

Vitreous Retina Macula Consultants of NY

New York, New York, United States

Site Status

Albany Troy Cataract & Laser Associates

Troy, New York, United States

Site Status

Western Carolina Retinal Associates

Asheville, North Carolina, United States

Site Status

Southeast Clinical Research

Charlotte, North Carolina, United States

Site Status

Duke University

Durham, North Carolina, United States

Site Status

Sterling Research Group, Ltd.

Cincinnati, Ohio, United States

Site Status

Retina Associates of Cleveland

Cleveland, Ohio, United States

Site Status

The Cleveland Clinic

Cleveland, Ohio, United States

Site Status

Cascade Medical Research Institute

Springfield, Oregon, United States

Site Status

Eye Care Specialists

Kingston, Pennsylvania, United States

Site Status

Retinovitreous Associates

Philadelphia, Pennsylvania, United States

Site Status

Black Hills Regional Eye Institute

Rapid City, South Dakota, United States

Site Status

Southeastern Retina Associates

Knoxville, Tennessee, United States

Site Status

Tennessee Retina

Nashville, Tennessee, United States

Site Status

Texas Retina Associates

Arlington, Texas, United States

Site Status

Retina Foundation of the Southwest

Dallas, Texas, United States

Site Status

Texas Retina Associates-Plano

Dallas, Texas, United States

Site Status

Retina Consultants of Houston

Houston, Texas, United States

Site Status

Retina Consultants of Houston

The Woodlands, Texas, United States

Site Status

Strategic Clinical Research Group, LLC

Willow Park, Texas, United States

Site Status

University of Virginia

Charlottesville, Virginia, United States

Site Status

Spokane Eye Clinical Research

Spokane, Washington, United States

Site Status

Countries

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United States

References

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Tzoumas N, Riding G, Williams MA, Steel DH. Complement inhibitors for age-related macular degeneration. Cochrane Database Syst Rev. 2023 Jun 14;6(6):CD009300. doi: 10.1002/14651858.CD009300.pub3.

Reference Type DERIVED
PMID: 37314061 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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621-GA-201

Identifier Type: -

Identifier Source: org_study_id

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