ADVATE 2 mL Post-Authorization Safety Surveillance (PASS)

NCT ID: NCT02093741

Last Updated: 2021-03-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

65 participants

Study Classification

OBSERVATIONAL

Study Start Date

2013-09-20

Study Completion Date

2016-01-20

Brief Summary

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This is a Post-Authorization Safety Surveillance (PASS) study designed to collect data on the safety and effectiveness of ADVATE reconstituted in 2 mL Sterile water for injection (SWFI) during routine clinical practice in children until 12 years of age. This surveillance study is a post-licensure commitment for ADVATE reconstituted in 2 mL SWFI.

Detailed Description

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Conditions

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Hemophilia A Congenital Factor VIII (FVIII) Deficiency

Study Design

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Observational Model Type

CASE_ONLY

Study Time Perspective

PROSPECTIVE

Study Groups

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ADVATE - 2mL

Octocog alfa (recombinant human coagulation factor VIII) [ADVATE]

Intervention Type BIOLOGICAL

The investigators shall determine all treatment regimens according to product labeling information and standard practice.

Interventions

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Octocog alfa (recombinant human coagulation factor VIII) [ADVATE]

The investigators shall determine all treatment regimens according to product labeling information and standard practice.

Intervention Type BIOLOGICAL

Other Intervention Names

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Antihemophilic Factor (Recombinant)- Plasma/albumin free method (rAHF-PFM) ADVATE

Eligibility Criteria

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Inclusion Criteria

* Severe or moderately severe hemophilia A (baseline Factor VIII (FVIII) ≤ 2%)
* ≤12 years of age
* Participant's legally authorized representative(s) has provided written informed consent
* Participant is prescribed ADVATE and will only receive ADVATE reconstituted in 2 mL sterile water for injection (SWFI)
* Documented history of prior exposure to ADVATE
* Documented evidence of negative inhibitor test result during ≤10 EDs prior to study entry

Exclusion Criteria

* Known hypersensitivity to the active substance or to any of the excipients
* Known allergic reaction to mouse or hamster proteins
* Participant has a requirement for a major surgical procedure at the time of enrollment
* Participant has no prior exposure to a FVIII concentrate
* Participant currently being treated with an immune tolerance induction (ITI) regimen
* Participant has been diagnosed with an inherited or acquired hemostatic defect other than hemophilia A (eg, qualitative platelet defect or von Willebrand disease)
* Participant has participated in another clinical study involving an investigational product (IP) or investigational device within 30 days prior to enrollment or is scheduled to participate in another clinical study involving an IP or investigational device or PASS registry during the course of this study
Maximum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Baxalta now part of Shire

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

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CHRU Pellegrin, Hématologie - CRTH

Bordeaux, , France

Site Status

Centre Hospitalier Générale, CTH

Chambéry, , France

Site Status

CRTH Laboratoire d'Hématologie CHRU - Hôpital du Bocage

Dijon, , France

Site Status

American Memorial Hospital, Service de Pédiatrie

Reims, , France

Site Status

CHU de Rennes Hôpital Pontchaillou

Rennes, , France

Site Status

Hôpital Nord, Pédiatrie

Saint-Priest-en-Jarez, , France

Site Status

CHRU Purpan, CRTH - Pavillon Sénac

Toulouse, , France

Site Status

CHU de Nancy - Hôpital de Brabois- CRTH - Laboratoire Hémato-Hémostase

Vandœuvre-lès-Nancy, , France

Site Status

Universitätskliniken des Saarlandes, Klinik für pädiatrische Onkologie und Hämatologie

Homburg, Saarland, Germany

Site Status

Klinikum Stuttgart, Olgahospital, Pädiatrie 5

Stuttgart, , Germany

Site Status

Heim Pál Children's Hospital, Department of Oncology

Budapest, , Hungary

Site Status

Borsod-Abaúj-Zemplén County Hospital, Pediatric Dep

Miskolc, , Hungary

Site Status

Mohacsi Korhaz, Department of Pediatrics

Mohács, , Hungary

Site Status

Josa Andras Egyetemi Oktatokorhaz, Department of Pediatrics

Nyíregyháza, , Hungary

Site Status

Leeds General Infirmary

Leeds, West Yorkshire, United Kingdom

Site Status

Birmingham Children's Hospital NHS Trust

Birmingham, , United Kingdom

Site Status

Great Ormond Street Hospital for Children NHS Trust

London, , United Kingdom

Site Status

Countries

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France Germany Hungary United Kingdom

Related Links

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https://clinicaltrials.takeda.com/study-detail/5f6b5fc24db2bf003ab457db

To obtain more information on the study, click here/on this link.

Other Identifiers

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061101

Identifier Type: -

Identifier Source: org_study_id

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