Olaparib as Adjuvant Treatment in Patients With Germline BRCA Mutated High Risk HER2 Negative Primary Breast Cancer

NCT ID: NCT02032823

Last Updated: 2026-01-16

Study Results

Results available

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Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

1836 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-04-22

Study Completion Date

2029-05-28

Brief Summary

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Olaparib treatment in patients with germline BRCA1/2 mutations and high risk HER2 negative primary breast cancer who have completed definitive local treatment and neoadjuvant or adjuvant chemotherapy

Detailed Description

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Patients will be randomised in 1:1 ratio to either olaparib or placebo. Randomisation will be stratified by Hormone receptor status (ER and/or PgR positive/HER2 negative versus TNBC), prior neoadjuvant versus adjuvant chemotherapy and prior platinum use for breast cancer.

Randomised patients will receive study treatment for up to a maximum of 12 months. All patients will have safety assessments every 2 weeks during the first month, every 4 weeks for the following 5 months and 3 monthly for the remaining 6 months of study treatment plus 30 days after its discontinuation. Following randomisation, all patients will be assessed regularly for signs, symptoms and evidence of disease recurrence by taking medical history, physical examination and mammogram/breast MRI. Efficacy assessments will be performed on a 3 monthly basis during the first 2 years, followed by 6 monthly assessments for years 3, 4 and 5 and annually thereafter. All patients (except those with bilateral mastectomy) will have mammogram / breast MRI annually for 10 years beginning 6 months after randomisation.

All randomised patients will have clinical assessment visits for 10 years following their randomisation into the study. Once a patient completes 10 years of clinical assessment they will enter the survival follow up phase of the trial which will continue until approximately 10 years after the last patient is randomised.

Conditions

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Breast Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Olaparib

Olaparib tablets 300mg b.i.d. p.o.

Group Type EXPERIMENTAL

Olaparib

Intervention Type DRUG

Patients will be administred olaparib orally twice daily (b.i.d.) at 300 mg. Two (2) x 150 mg olaparib tablets should be taken at the same times each morning and evening of each day, approximately 12 hours apart with approximately 240 ml of water

Placebo

Placebo tablets b.i.d. p.o.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Patients will be administred matching placebo. Two (2) tablets should be taken at the same times each morning and evening of each day, approximately 12 hours apart with approximately 240 ml of water

Interventions

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Olaparib

Patients will be administred olaparib orally twice daily (b.i.d.) at 300 mg. Two (2) x 150 mg olaparib tablets should be taken at the same times each morning and evening of each day, approximately 12 hours apart with approximately 240 ml of water

Intervention Type DRUG

Placebo

Patients will be administred matching placebo. Two (2) tablets should be taken at the same times each morning and evening of each day, approximately 12 hours apart with approximately 240 ml of water

Intervention Type DRUG

Other Intervention Names

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Lynparza

Eligibility Criteria

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Inclusion Criteria

* Histologically confirmed non-metastatic primary invasive adenocarcinoma of the breast that is one of the following phenotypes:

1. Triple negative breast cancer defined as: ER and PgR negative AND HER2 negative (not eligible for anti-HER2 therapy)
2. ER and/or PgR positive, HER2 negative
* Documented germline mutation in BRCA1 or BRCA2 that is predicted to be deleterious or suspected deleterious (known or predicted to be detrimental/lead to loss of function).
* Completed adequate breast and axilla surgery.
* Completed at least 6 cycles neoadjuvant or adjuvant chemotherapy containing anthracyclines, taxanes or the combination of both. Prior platinum as potentially curative treatment for prior cancer (e.g. ovarian) or as adjuvant or neoadjuvant treatment for breast cancer is allowed.
* ECOG 0-1.

Exclusion Criteria

* Any previous treatment with a PARP inhibitor, including olaparib and/or known hypersensitivity to any of the excipients of study treatment.
* Patients with second primary malignancy. EXCEPTIONS are:

1. adequately treated non-melanoma skin cancer, curatively treated in situ cancer of the cervix, Ductal Carcinoma in situ (DCIS) of the breast, stage 1 grade 1 endometrial carcinoma
2. other solid tumours and lymphomas (without bone marrow involvement) diagnosed ≥ 5 years prior to randomisation and treated with no evidence of disease recurrence and for whom no more than one line of chemotherapy was applied.
* Concomitant use of known strong CYP3A inhibitors (e.g., itraconazole, telithromycin, clarithromycin, protease inhibitors boosted with ritonavir or cobicistat, indinavir, saquinavir, nelfinavir, boceprevir, telaprevir) or moderate CYP3A inhibitors (e.g., ciprofloxacin, erythromycin, diltiazem, fluconazole, verapamil). The required washout period prior to starting study treatment is 2 weeks. Concomitant use of known strong (e.g., phenobarbital, enzalutamide, phenytoin, rifampicin, rifabutin, rifapentine, carbamazepine, nevirapine and St John's Wort) or moderate CYP3A inducers (e.g., bosentan, efavirenz, modafinil). The required washout period prior to starting study treatment is 5 weeks for enzalutamide or phenobarbital and 3 weeks for other agents.
* Evidence of metastatic breast cancer
Minimum Eligible Age

18 Years

Maximum Eligible Age

130 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role lead

Breast International Group

OTHER

Sponsor Role collaborator

Frontier Science & Technology Research Foundation, Inc.

INDUSTRY

Sponsor Role collaborator

NRG Oncology

OTHER

Sponsor Role collaborator

Myriad Genetic Laboratories, Inc.

INDUSTRY

Sponsor Role collaborator

The Breast Adjuvant Study Team

OTHER

Sponsor Role collaborator

Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role collaborator

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Andrew Tutt, Doctor of Medicine

Role: PRINCIPAL_INVESTIGATOR

Integrated Cancer Centre Guy's Hospital, King's College, London School of Medicine, London, UK

Judy Garber, Doctor of Medicine

Role: PRINCIPAL_INVESTIGATOR

Harvard Medical School, Center for Cancer Genetics and Prevention, Dana-Farber Cancer Institute, Susan F. Smither Center for Women's Cancers, 450 Brookline Avenue, Boston; MA 02215, US

Charles Geyer, Doctor of Medicine

Role: PRINCIPAL_INVESTIGATOR

Virginia Commonwealth University Massey Cancer Center, McGlothlin Medical Education Center, Room 12-217, 1201 East Marshall St., PO Box 980070, Richmond, VA 23298-0070, USA

Locations

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Anchorage, Alabama, United States

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Anchorage, Alaska, United States

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Gilbert, Arizona, United States

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Fort Smith, Arkansas, United States

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Baldwin Park, California, United States

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Berkeley, California, United States

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Duarte, California, United States

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Fontana, California, United States

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Fresno, California, United States

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Greenbrae, California, United States

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Los Angeles, California, United States

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Los Angeles, California, United States

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Martinez, California, United States

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Newport Beach, California, United States

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Oakland, California, United States

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Palo Alto, California, United States

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Paradise, California, United States

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Roseville, California, United States

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San Marcos, California, United States

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Santa Cruz, California, United States

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Santa Rosa, California, United States

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Stockton, California, United States

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Vacaville, California, United States

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Vallejo, California, United States

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Aurora, Colorado, United States

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Derby, Connecticut, United States

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Guilford, Connecticut, United States

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New Haven, Connecticut, United States

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Orange, Connecticut, United States

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Torrington, Connecticut, United States

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Trumbull, Connecticut, United States

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Waterbury, Connecticut, United States

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Newark, Delaware, United States

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Newark, Delaware, United States

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Washington D.C., District of Columbia, United States

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Daytona Beach, Florida, United States

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Deerfield Beach, Florida, United States

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Gainesville, Florida, United States

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Miami, Florida, United States

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Orlando, Florida, United States

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Plantation, Florida, United States

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Honolulu, Hawaii, United States

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Boise, Idaho, United States

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Centralia, Illinois, United States

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Jackson, Michigan, United States

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Kalamazoo, Michigan, United States

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Troy, Michigan, United States

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Bemidji, Minnesota, United States

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Burnsville, Minnesota, United States

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Duluth, Minnesota, United States

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Edina, Minnesota, United States

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Fridley, Minnesota, United States

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Mankato, Minnesota, United States

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Maple Grove, Minnesota, United States

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Maplewood, Minnesota, United States

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Minneapolis, Minnesota, United States

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Rochester, Minnesota, United States

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Saint Cloud, Minnesota, United States

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Saint Paul, Minnesota, United States

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Shakopee, Minnesota, United States

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Waconia, Minnesota, United States

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Woodbury, Minnesota, United States

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Jackson, Mississippi, United States

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Cape Girardeau, Missouri, United States

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Joplin, Missouri, United States

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Kansas City, Missouri, United States

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Lee's Summit, Missouri, United States

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Springfield, Missouri, United States

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St Louis, Missouri, United States

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St Louis, Missouri, United States

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St Louis, Missouri, United States

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Bozeman, Montana, United States

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Grand Island, Nebraska, United States

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Lincoln, Nebraska, United States

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Lincoln, Nebraska, United States

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Norfolk, Nebraska, United States

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Omaha, Nebraska, United States

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Omaha, Nebraska, United States

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Omaha, Nebraska, United States

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Lebanon, New Hampshire, United States

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Manchester, New Hampshire, United States

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Nashua, New Hampshire, United States

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Flemington, New Jersey, United States

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Hamilton, New Jersey, United States

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Morristown, New Jersey, United States

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Mount Holly, New Jersey, United States

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New Brunswick, New Jersey, United States

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Voorhees Township, New Jersey, United States

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Albuquerque, New Mexico, United States

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Albuquerque, New Mexico, United States

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Brooklyn, New York, United States

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Charlotte, New York, United States

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East Syracuse, New York, United States

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New Hyde Park, New York, United States

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New York, New York, United States

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Rochester, New York, United States

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The Bronx, New York, United States

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Albemarle, North Carolina, United States

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Asheville, North Carolina, United States

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Charlotte, North Carolina, United States

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Clinton, North Carolina, United States

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Concord, North Carolina, United States

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Durham, North Carolina, United States

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Gastonia, North Carolina, United States

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Kinston, North Carolina, United States

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Pinehurst, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Fargo, North Dakota, United States

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Minot, North Dakota, United States

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Akron, Ohio, United States

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Beachwood, Ohio, United States

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Canton, Ohio, United States

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Cleveland, Ohio, United States

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Abington, Pennsylvania, United States

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Reading, Pennsylvania, United States

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State College, Pennsylvania, United States

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Wilkes-Barre, Pennsylvania, United States

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Wynnewood, Pennsylvania, United States

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Round Rock, Texas, United States

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Temple, Texas, United States

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Ogden, Utah, United States

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Provo, Utah, United States

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Fairfax, Virginia, United States

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Centralia, Washington, United States

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Poulsbo, Washington, United States

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Charleston, West Virginia, United States

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Huntington, West Virginia, United States

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Burlington, Wisconsin, United States

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References

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Ganz PA, Bandos H, Spanic T, Friedman S, Muller V, Kuemmel S, Delaloge S, Brain E, Toi M, Yamauchi H, de Duenas EM, Armstrong A, Im SA, Song CG, Zheng H, Sarosiek T, Sharma P, Geng C, Fu P, Rhiem K, Frauchiger-Heuer H, Wimberger P, t'Kint de Roodenbeke D, Liao N, Goodwin A, Chakiba-Brugere C, Friedlander M, Lee KS, Giacchetti S, Takano T, Henao-Carrasco F, Virani S, Valdes-Albini F, Domchek SM, Bane C, McCarron EC, Mita M, Rossi G, Rastogi P, Fielding A, Gelber RD, Scheepers ED, Cameron D, Garber J, Geyer CE, Tutt ANJ. Patient-Reported Outcomes in OlympiA: A Phase III, Randomized, Placebo-Controlled Trial of Adjuvant Olaparib in gBRCA1/2 Mutations and High-Risk Human Epidermal Growth Factor Receptor 2-Negative Early Breast Cancer. J Clin Oncol. 2024 Apr 10;42(11):1288-1300. doi: 10.1200/JCO.23.01214. Epub 2024 Feb 1.

Reference Type DERIVED
PMID: 38301187 (View on PubMed)

Perachino M, Poggio F, Arecco L, Blondeaux E, Spinaci S, Marrocco C, Levaggi A, Lambertini M. Update on Pregnancy Following Breast Cancer Diagnosis and Treatment. Cancer J. 2022 May-Jun 01;28(3):176-182. doi: 10.1097/PPO.0000000000000599.

Reference Type DERIVED
PMID: 35594464 (View on PubMed)

Tutt ANJ, Garber JE, Kaufman B, Viale G, Fumagalli D, Rastogi P, Gelber RD, de Azambuja E, Fielding A, Balmana J, Domchek SM, Gelmon KA, Hollingsworth SJ, Korde LA, Linderholm B, Bandos H, Senkus E, Suga JM, Shao Z, Pippas AW, Nowecki Z, Huzarski T, Ganz PA, Lucas PC, Baker N, Loibl S, McConnell R, Piccart M, Schmutzler R, Steger GG, Costantino JP, Arahmani A, Wolmark N, McFadden E, Karantza V, Lakhani SR, Yothers G, Campbell C, Geyer CE Jr; OlympiA Clinical Trial Steering Committee and Investigators. Adjuvant Olaparib for Patients with BRCA1- or BRCA2-Mutated Breast Cancer. N Engl J Med. 2021 Jun 24;384(25):2394-2405. doi: 10.1056/NEJMoa2105215. Epub 2021 Jun 3.

Reference Type DERIVED
PMID: 34081848 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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NSABP B-55

Identifier Type: OTHER

Identifier Source: secondary_id

BIG 6-13

Identifier Type: OTHER

Identifier Source: secondary_id

2024-511096-15-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

2013-003839-30

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

D081CC00006

Identifier Type: -

Identifier Source: org_study_id

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