Allogeneic UCB Therapy With EPO in Children With CP

NCT ID: NCT01991145

Last Updated: 2020-01-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

NA

Total Enrollment

92 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-11-26

Study Completion Date

2017-06-24

Brief Summary

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This randomized controlled study aims to evaluate the efficacy and safety of allogeneic umbilical cord blood therapy combined with erythropoietin for children with cerebral palsy.

Detailed Description

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Cerebral palsy (CP) is a group of neurodevelopmental conditions with abnormal movement and posture resulted from a non-progressive cerebral disturbance. It is the most common cause of motor disability in childhood. Most therapies are palliative rather than restorative. Umbilical cord blood (UCB) and erythropoetin (EPO) may be used as restorative approach for children with CP.

Many experimental animal studies have revealed that UCB is beneficial to improve and repair neurological injuries. EPO is also known to have neuroprotective effects.

Based on animal studies and some clinical trials, UCB is suggested as a potential therapy for children with CP. EPO is combined to add synergistic effects to UCB therapy.

Conditions

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Cerebral Palsy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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UCB and EPO

UCB + EPO + Rehabilitation

Group Type EXPERIMENTAL

Umbilical Cord Blood therapy

Intervention Type PROCEDURE

HLA (Human Leukocyte Antigen) typing

Erythropoietin alfa

Intervention Type BIOLOGICAL

Rehabilitation

Intervention Type OTHER

Active rehabilitation

UCB and placebo EPO

UCB + placebo EPO + Rehabilitation

Group Type ACTIVE_COMPARATOR

Umbilical Cord Blood therapy

Intervention Type PROCEDURE

HLA (Human Leukocyte Antigen) typing

Rehabilitation

Intervention Type OTHER

Active rehabilitation

Placebo EPO

Intervention Type BIOLOGICAL

placebo UCB and EPO

placebo UCB + EPO + Rehabilitation

Group Type ACTIVE_COMPARATOR

Erythropoietin alfa

Intervention Type BIOLOGICAL

Rehabilitation

Intervention Type OTHER

Active rehabilitation

Placebo UCB

Intervention Type PROCEDURE

placebo UCB and placebo EPO

placebo UCB + placebo EPO + Rehabilitation

Group Type PLACEBO_COMPARATOR

Rehabilitation

Intervention Type OTHER

Active rehabilitation

Placebo UCB

Intervention Type PROCEDURE

Placebo EPO

Intervention Type BIOLOGICAL

Interventions

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Umbilical Cord Blood therapy

HLA (Human Leukocyte Antigen) typing

Intervention Type PROCEDURE

Erythropoietin alfa

Intervention Type BIOLOGICAL

Rehabilitation

Active rehabilitation

Intervention Type OTHER

Placebo UCB

Intervention Type PROCEDURE

Placebo EPO

Intervention Type BIOLOGICAL

Other Intervention Names

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Espogen (LG Life Science Ltd.)

Eligibility Criteria

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Inclusion Criteria

* Diagnosed with cerebral palsy
* Age of ≥10 months and ≤6 years
* Mismatch in HLA-A, B, and DR ≤2, and total nucleated cell count ≥3x107/kg. If the cell count is less than given values, more than 1 unit could be used.
* Hemoglobin ≤13.6 g/dL
* Decision of participation in the study by and acquisition of informed consent from the subject's representative
* Willingness and ability to be hospitalized according to the schedule specified in the protocol and continue the study for 12 months after study entry

Exclusion Criteria

* Current aspiration pneumonia
* Known genetic disease
* History of hypersensitivity reaction to any study drugs pertinent to the study
* History of participation in any other study with stem cell
* Prior treatment with EPO within 3 months prior to study entry
* Known coagulopathy with family history of thrombosis or medical history of recurrent thrombosis
* Patient with severe seizure disease who has clinical convulsion despite combination therapy with 3 or more agents
* Uncontrolled hypertension defined as systolic blood pressure \>115 mmHg and/or diastolic blood pressure \>70 mmHg
* Hepatic impairment defined as asparate aminotransferase (AST) \>55 IU/L and/or alanine aminotransferase (ALT) \>45 IU/L
* Renal impairment defined as creatinine (Cr) ≥1.2 mg/dL
* Absolute neutrophil count ≤500/dL
* Presence of diagnosed or suspected malignant tumor and/or hematologic malignancy
* Non-compliance with study visits specified in the protocol or unwillingness of care-giver due to lack of understanding of the patient
Minimum Eligible Age

10 Months

Maximum Eligible Age

6 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ministry of Health & Welfare, Korea

OTHER_GOV

Sponsor Role collaborator

LG Life Sciences

INDUSTRY

Sponsor Role collaborator

Chong Kun Dang Pharmaceutical

INDUSTRY

Sponsor Role collaborator

CHA University

OTHER

Sponsor Role collaborator

MinYoung Kim, MD, PhD

OTHER

Sponsor Role lead

Responsible Party

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MinYoung Kim, MD, PhD

Professor of CHA University, M.D., Ph.D.

Responsibility Role SPONSOR_INVESTIGATOR

Principal Investigators

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MinYoung Kim, M.D., Ph.D.

Role: PRINCIPAL_INVESTIGATOR

CHA University

Locations

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CHA Bundang Medical Center, CHA University

Seongnam-si, Gyeonggi-do, South Korea

Site Status

Countries

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South Korea

References

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Min K, Suh MR, Cho KH, Park W, Kang MS, Jang SJ, Kim SH, Rhie S, Choi JI, Kim HJ, Cha KY, Kim M. Potentiation of cord blood cell therapy with erythropoietin for children with CP: a 2 x 2 factorial randomized placebo-controlled trial. Stem Cell Res Ther. 2020 Nov 27;11(1):509. doi: 10.1186/s13287-020-02020-y.

Reference Type DERIVED
PMID: 33246489 (View on PubMed)

Other Identifiers

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UCBnEPOinCP

Identifier Type: -

Identifier Source: org_study_id

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