Intrathecal Stem Cells for Cerebral Palsy Phase II

NCT ID: NCT02231242

Last Updated: 2014-09-04

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE2

Total Enrollment

60 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-09-30

Study Completion Date

2016-06-30

Brief Summary

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The purpose of this study is to determine whether the infusion of intrathecal autologous bone marrow total nucleated cells would improve the neurologic evolution of pediatric patients with quadriparetic cerebral palsy.

Detailed Description

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There is accumulated evidence that shows that the administration of bone marrow total nucleated cells (TNC) into the brain may produce some benefits by different mechanisms like cytokine production, in several neurological areas such as motor, social, adaptative and cognitive.

It has been found that after introducing TNC in the subarachnoid space of the spinal cord, these cells may be transported through the cerebrospinal fluid and can be delivered more efficiently to the injured area, compared with intravenous route in patients with neurologic injury.

Patients will be stimulated for 3 consecutive days with subcutaneous granulocyte colony stimulating factor (G-CSF) and then their bone marrow will be harvested according to their weight. Bone marrow will be processed in order to obtain the buffy coat and minimize the amount of red blood cells. An inoculum of 10mL of this TNC will be infused intrathecally. Patients will be evaluated with the "Gross Motor Functional Classification System" before the procedure and one, three and six months after that.

Conditions

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Cerebral Palsy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

Primary Study Purpose

SUPPORTIVE_CARE

Blinding Strategy

SINGLE

Outcome Assessors

Study Groups

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Intrathecal Autologous Bone Marrow TNC

Procedure/Surgery: Intrathecal Autologous Bone Marrow TNC. Other Names: Autologous Stem Cell Transplantation Patients will be stimulated with Granulocyte Colony Stimulating Factor (G-CSF) (10mcgr/kg of body weight) for 3 consecutive days. Bone marrow will be harvested under sedation and, after being processed in the laboratory, the autologous TNC concentrate of 10 mL will be infused intrathecally.

Group Type EXPERIMENTAL

Autologous Stem Cell Transplantation

Intervention Type BIOLOGICAL

Patients will be stimulated with Granulocyte Colony Stimulating Factor (G-CSF) 3 consecutive days. Bone marrow will be harvested under sedation and, after being processed in the laboratory, the buffy coat (TNC) of 10 mL will be infused intrathecally.

Intrathecal Autologous Bone Marrow TNC

Control group

Patients will be evaluated with the "Gross Motor Functional Classification System" initially, at one, three and six months, and then cross to the intervention arm.

Group Type NO_INTERVENTION

No interventions assigned to this group

Interventions

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Autologous Stem Cell Transplantation

Patients will be stimulated with Granulocyte Colony Stimulating Factor (G-CSF) 3 consecutive days. Bone marrow will be harvested under sedation and, after being processed in the laboratory, the buffy coat (TNC) of 10 mL will be infused intrathecally.

Intrathecal Autologous Bone Marrow TNC

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

* Patients with quadriplegic cerebral palsy, with an age from 7 to 9 years of age, regardless the age at the time of injury, time post-injury, or previously received therapies, different from ours

Exclusion Criteria

* Patients with neurodegenerative or autoimmune diseases
* Patients with active infection in any organ or tissue at the time of entering the study, the onset of stimulation with G-CSF or at the procedure
* Patients who do not sign the informed consent form
Minimum Eligible Age

7 Years

Maximum Eligible Age

9 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hospital Universitario Dr. Jose E. Gonzalez

OTHER

Sponsor Role lead

Responsible Party

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Consuelo Mancias Guerra

Dra. Consuelo Mancias Guerra

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Consuelo Mancias-Guerra, MD

Role: PRINCIPAL_INVESTIGATOR

Hospital Universitario Dr. Jose E. Gonzalez

Locations

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Hematology Service, Hospital Universitario Dr. Jose E. Gonzalez

Monterrey, Nuevo León, Mexico

Site Status RECRUITING

Countries

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Mexico

Central Contacts

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Consuelo Mancias-Guerra, MD

Role: CONTACT

+52 81 83 48 61 36 ext. 413

Oscar Gonzalez-Llano, MD

Role: CONTACT

+52 86 75 67 18

Facility Contacts

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Consuelo Mancias-Guerra, MD

Role: primary

+52 81 83 48 61 36 ext. 413

David Gomez-Almaguer, MD

Role: backup

+52 81 83 48 61 36

References

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Related Links

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Other Identifiers

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HE13-004

Identifier Type: -

Identifier Source: org_study_id

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