Efficacy and Safety of Idelalisib in Combination With Bendamustine and Rituximab in Adults With Previously Untreated Chronic Lymphocytic Leukemia

NCT ID: NCT01980888

Last Updated: 2018-11-19

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

311 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-02-05

Study Completion Date

2016-06-16

Brief Summary

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The primary objective of this study is to evaluate the progression-free survival in participants with previously untreated chronic lymphocytic leukemia (CLL) who would otherwise be suitable for bendamustine and rituximab treatment as standard of care.

An increased rate of deaths and serious adverse events (SAEs) among participants with front-line CLL and early-line indolent non-Hodgkin lymphoma (iNHL) treated with idelalisib in combination with standard therapies was observed by the independent data monitoring committee (DMC) during regular review of 3 Gilead Phase 3 studies. Gilead reviewed the unblinded data and terminated this study in agreement with the DMC recommendation and in consultation with the US Food and Drug Administration (FDA).

Detailed Description

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Conditions

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Chronic Lymphocytic Leukemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Idelalisib+bendamustine+rituximab

Participants will receive idelalisib for 96 weeks plus bendamustine+rituximab for 21 weeks.

Group Type EXPERIMENTAL

Idelalisib

Intervention Type DRUG

150 mg tablet administered orally twice daily

Bendamustine

Intervention Type DRUG

Administered intravenously at a starting dose of 90 mg/m\^2 for up to 6 cycles. Dosing will be based on mg/m\^2 of body surface area.

Rituximab

Intervention Type DRUG

Single-use vials administered intravenously weekly starting at 375 mg/m\^2 on Day 1 (Week 0) and 500 mg/m\^2 thereafter for a total of 6 infusions

Placebo+bendamustine+rituximab

Participants will receive placebo to match idelalisib for 96 weeks plus bendamustine+rituximab for 21 weeks.

Group Type PLACEBO_COMPARATOR

Bendamustine

Intervention Type DRUG

Administered intravenously at a starting dose of 90 mg/m\^2 for up to 6 cycles. Dosing will be based on mg/m\^2 of body surface area.

Rituximab

Intervention Type DRUG

Single-use vials administered intravenously weekly starting at 375 mg/m\^2 on Day 1 (Week 0) and 500 mg/m\^2 thereafter for a total of 6 infusions

Placebo

Intervention Type DRUG

Placebo to match idelalisib administered orally twice daily

Interventions

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Idelalisib

150 mg tablet administered orally twice daily

Intervention Type DRUG

Bendamustine

Administered intravenously at a starting dose of 90 mg/m\^2 for up to 6 cycles. Dosing will be based on mg/m\^2 of body surface area.

Intervention Type DRUG

Rituximab

Single-use vials administered intravenously weekly starting at 375 mg/m\^2 on Day 1 (Week 0) and 500 mg/m\^2 thereafter for a total of 6 infusions

Intervention Type DRUG

Placebo

Placebo to match idelalisib administered orally twice daily

Intervention Type DRUG

Other Intervention Names

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Zydelig® GS-1101 CAL-101

Eligibility Criteria

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Inclusion Criteria

* Documented diagnosis of B-cell CLL, with diagnosis established according to International Workshop on Chronic Lymphocytic Leukemia (IWCLL)
* No prior therapy for CLL other than corticosteroids for disease complications
* CLL that warrants treatment
* Presence of measurable lymphadenopathy
* Eastern Cooperative Oncology Group (ECOG) performance status of ≤ 2

Exclusion Criteria

* Known histological transformation from CLL to an aggressive lymphoma (ie, Richter transformation)
* Known presence of myelodysplastic syndrome
* Evidence of ongoing systemic bacterial, fungal, or viral infection at the time of randomization
* Ongoing liver injury
* History of non-infectious pneumonitis
* Ongoing inflammatory bowel disease
* History of prior allogeneic bone marrow progenitor cell or solid organ transplantation
* Ongoing immunosuppressive therapy other than corticosteroids
* Received last dose of study drug on another therapeutic clinical trial within 30 days prior to randomization
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gilead Study Director

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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St. Jude Heritage Healthcare Virginia K. Crosson Cancer Center

Fullerton, California, United States

Site Status

UCSD Moores Cancer Center

La Jolla, California, United States

Site Status

Central Coast Medical Oncology

Santa Maria, California, United States

Site Status

Georgetown University

Washington D.C., District of Columbia, United States

Site Status

Memorial Healthcare System

Hollywood, Florida, United States

Site Status

Cancer Specialists of North Florida

Jacksonville, Florida, United States

Site Status

Florida Cancer Specialists-South

Sarasota, Florida, United States

Site Status

Franciscan Physician Network Oncology & Hematology

Indianapolis, Indiana, United States

Site Status

Siouxland Hematology-Oncology Associates, LLP

Sioux City, Iowa, United States

Site Status

Center for Cancer and Blood Disorders

Bethesda, Maryland, United States

Site Status

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, United States

Site Status

Hematology /Oncology Associates of Northern New Jersey

Morristown, New Jersey, United States

Site Status

Columbia University Medical Center

New York, New York, United States

Site Status

University of Rochester

Rochester, New York, United States

Site Status

Gabrail Cancer Center Research

Canton, Ohio, United States

Site Status

Sarah Cannon Research Institute

Cincinnati, Ohio, United States

Site Status

Signal Point Clinical Research Center

Middletown, Ohio, United States

Site Status

Saint Francis Hospital

Greenville, South Carolina, United States

Site Status

Sarah Cannon Research Institute

Nashville, Tennessee, United States

Site Status

Texas Oncology-Austin Midtown

Austin, Texas, United States

Site Status

Texas Oncology-Baylor Charles A. Sammons Cancer Center

Dallas, Texas, United States

Site Status

Utah Cancer Specialists

Salt Lake City, Utah, United States

Site Status

Fred Hutchinson Cancer Research Center

Seattle, Washington, United States

Site Status

St Vincent's Hospital, Sydney

Darlinghurst, New South Wales, Australia

Site Status

Jarrett Street Specialist Centre

North Gosford, New South Wales, Australia

Site Status

Calvary Mater Newcastle

Waratah, New South Wales, Australia

Site Status

Haematology and Bone Marrow Transplant Unit, Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status

Flinders Medical Centre, Department of Haematology, Level 6

Bedford Park, South Australia, Australia

Site Status

Ashford Cancer Centre Research

Kurralta Park, South Australia, Australia

Site Status

Queen Elizabeth Hospital

Woodville South, South Australia, Australia

Site Status

Frankston Hospital

Frankston, Victoria, Australia

Site Status

Barwon Health, University Hospital Geelong

Geelong, Victoria, Australia

Site Status

Z N A Stuivenberg

Antwerp, , Belgium

Site Status

AZ Sint-Jan AV Brugge-Oostende

Bruges, , Belgium

Site Status

University Hospital Leuven

Leuven, , Belgium

Site Status

Cancercare Manitoba - Maccharles Unit

Winnipeg, Manitoba, Canada

Site Status

Sunnybrook Health Sciences Centre

Toronto, Ontario, Canada

Site Status

Princess Margaret Cancer Centre

Toronto, Ontario, Canada

Site Status

Hôpital du Sacré-Coeur de Montréal

Montreal, Quebec, Canada

Site Status

CHU de Québec - Hôpital de l'Enfant-Jésus

Québec, Quebec, Canada

Site Status

Klinicka bolnica Dubrava

Zagreb, , Croatia

Site Status

Klinicka bolnica Merkur

Zagreb, , Croatia

Site Status

UHC Zagreb

Zagreb, , Croatia

Site Status

Faculty hospital Ostrava

Ostrava-Poruba, Moravian-Silesian, Czechia

Site Status

University Hospital

Brno, , Czechia

Site Status

Faculty Hospital Hradec Kralove

Hradec Králové, , Czechia

Site Status

Faculty Hospital Plzen

Pilsen, , Czechia

Site Status

Faculty Hospital Kralovske Vinohrady

Prague, , Czechia

Site Status

CHRU de Lille, Hopital Claude Huriez

Lille, , France

Site Status

Hospital Saint-Louis

Paris, , France

Site Status

CHU Bretonneau

Tours, , France

Site Status

Szent Borbála Hospital

Tatabánya, Komárom-Esztergom, Hungary

Site Status

Kaposi Mor Oktato Korhaz, Intezeti Gyogyszertar,

Kaposvár, Somogy County, Hungary

Site Status

Semmelweis University

Budapest, , Hungary

Site Status

National Institute of Oncology

Budapest, , Hungary

Site Status

University of Debrecen HSC Institute of internal Medicine, Department of Hematology

Debrecen, , Hungary

Site Status

Pandy Kalman Hospital

Gyula, , Hungary

Site Status

University Of Pecs, Medical School

Pécs, , Hungary

Site Status

Szegedi Tudomanyegyetem AOK - Szent-Gyorgyi Albert Klinikai Kozpont, II. Belgyógyászati Klinika

Szeged, , Hungary

Site Status

IRCCS Istituto Tumori

Bari, Apulia, Italy

Site Status

Ospedale Oncologico Armando Businco

Cagliari, , Italy

Site Status

Ospedale San Raffaele

Milan, , Italy

Site Status

Azienda Ospedaliero Universitaria Policlinico di Modena

Modena, , Italy

Site Status

AOU Maggiore della Carità

Novara, , Italy

Site Status

Uniwersyteckie Centrum Kliniczne

Gdansk, Pomeranian Voivodeship, Poland

Site Status

Malopolskie Centrum Medyczne s.c.

Krakow, , Poland

Site Status

Wojewodzki Szpital Specjalistyczny im. M. Kopernika Klinika Hematologii

Lodz, , Poland

Site Status

Centralny Szpital Kliniczny MSW w Warszawie Klinika Onkologii i Hematologii

Warsaw, , Poland

Site Status

Centrum Onkologii-Instytut Marii Sklodowskiej -Curie klinika Nowotworow Ukladu Chlonnego

Warsaw, , Poland

Site Status

Samodzielny Publiczny Szpital Kliniczny nr 1 we Wroclawiu Klinika i Katedra Hematologii,Nowotworow Krwi i Transplantacji Szpiku

Wroclaw, , Poland

Site Status

Dolnoslakie Centrum Transplantacji Komorkowych z Krajowym Bankiem Dawcow Szpiku

Wroclaw, , Poland

Site Status

Emergency County Clinical Hospital Brasov

Brasov, , Romania

Site Status

Spitalul Clinic Colentina

Bucharest, , Romania

Site Status

Hospital Vall de Hebron

Barcelona, Catalonia, Spain

Site Status

Hospital Clinic

Barcelona, Catalonia, Spain

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

ICO, Hospitalet de Llobregat

Barcelona, , Spain

Site Status

Hospital Universitario La Princesa

Madrid, , Spain

Site Status

Hospital Gregorio Marañon

Madrid, , Spain

Site Status

Hospital Universitario Ramón Y Cajal

Madrid, , Spain

Site Status

Hospital 12 de Octubre

Madrid, , Spain

Site Status

Hospital Universitario Puerta De Hierro

Madrid, , Spain

Site Status

University College London

London, England, United Kingdom

Site Status

East Kent Hospitals University NHS Foundation Trust

Canterbury, Kent, United Kingdom

Site Status

Royal Marsden NHS Trust

Sutton, Surrey, United Kingdom

Site Status

University Hospital of Wales

Cardiff, , United Kingdom

Site Status

Royal Liverpool & Broadgreen Univ. Hospitals NHS Trust

Liverpool, , United Kingdom

Site Status

Hammersmith Hospitals NHS Trust

London, , United Kingdom

Site Status

Oxford University Hospitals

Oxford, , United Kingdom

Site Status

University Hospital Southampton NHS Trust

Southampton, , United Kingdom

Site Status

Royal Wolverhampton Hospital NHS Trust, New Cross Hospital

Wolverhampton, , United Kingdom

Site Status

Countries

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United States Australia Belgium Canada Croatia Czechia France Hungary Italy Poland Romania Spain United Kingdom

Other Identifiers

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2013-003313-17

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GS-US-312-0123

Identifier Type: -

Identifier Source: org_study_id

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