A Study of Pirtobrutinib (LOXO-305) Versus Bendamustine Plus Rituximab (BR) in Untreated Patients With Chronic Lymphocytic Leukemia (CLL)/Small Lymphocytic Lymphoma (SLL)

NCT ID: NCT05023980

Last Updated: 2026-01-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

309 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-09-23

Study Completion Date

2027-10-31

Brief Summary

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The purpose of this study is to compare the efficacy and safety of pirtobrutinib (LOXO-305; Arm A) compared to BR (Arm B) in patients with CLL/SLL who have not been treated. Participation could last up to five years.

Detailed Description

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Conditions

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Chronic Lymphocytic Leukemia Small Lymphocytic Lymphoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Eligible patients will be randomized 1:1 into Arm A and Arm B. Patients randomized to Arm B who have disease progression (PD) confirmed by independent review committee (IRC) may be eligible to crossover into Arm A.
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm A (Pirtobrutinib)

Pirtobrutinib administered orally

Group Type EXPERIMENTAL

Pirtobrutinib

Intervention Type DRUG

Oral

Arm B (BR)

Bendamustine plus rituximab administered intravenously (IV)

Group Type ACTIVE_COMPARATOR

Bendamustine

Intervention Type DRUG

IV

Rituximab

Intervention Type DRUG

IV

Interventions

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Pirtobrutinib

Oral

Intervention Type DRUG

Bendamustine

IV

Intervention Type DRUG

Rituximab

IV

Intervention Type DRUG

Other Intervention Names

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LOXO-305 LY3527727 Treanda Treakisym Ribomustin Levact Rituxan MabThera Truxima Riabni Ruxience

Eligibility Criteria

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Inclusion Criteria

* Confirmed diagnosis of CLL/SLL requiring therapy, per iwCLL 2018 criteria
* Eastern Cooperative Oncology Group (ECOG) Performance Status 0-2
* Adequate organ function
* Platelets greater than or equal to (≥)75 x 10⁹/liter (L) (≥50 × 10⁹/L for patients with evidence of bone marrow infiltrate), hemoglobin ≥8 grams/deciliter (g/dL), and absolute neutrophil count ≥0.75 x 10⁹/L
* Kidney function: Estimated creatinine clearance ≥40 milliliters per minute (mL/min)

Exclusion Criteria

* Known or suspected Richter's transformation at any time preceding enrollment
* Prior systemic therapy for CLL/SLL
* Presence of 17p deletion
* Central nervous system (CNS) involvement
* Active uncontrolled auto-immune cytopenia (e.g., autoimmune hemolytic anemia \[AIHA\], idiopathic thrombocytopenic purpura \[ITP\])
* Significant cardiovascular disease
* Active hepatitis B or hepatitis C
* Active cytomegalovirus (CMV) infection
* Active uncontrolled systemic bacterial, viral, fungal, or parasitic infection
* Known human immunodeficiency virus (HIV) infection, regardless of cluster of differentiation 4 (CD4) count
* Concurrent use of investigational agent or anticancer therapy except hormonal therapy
* Patients requiring therapeutic anticoagulation with warfarin or another Vitamin K antagonist
* Vaccination with a live vaccine within 28 days prior to randomization
* Patients with the following hypersensitivity:

* Known hypersensitivity, including anaphylaxis, to any component or excipient of pirtobrutinib or bendamustine
* Prior significant hypersensitivity to rituximab
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Eli Lilly and Company

INDUSTRY

Sponsor Role collaborator

Loxo Oncology, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 9 AM - 5 PM Eastern time (UTC/GMT - 5 hours, EST)

Role: STUDY_DIRECTOR

Eli Lilly and Company

Locations

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California Research Institute

Los Angeles, California, United States

Site Status

Innovative Clinical Research Institute

Whittier, California, United States

Site Status

Oncology-Hematology Associates of West Broward

Coral Springs, Florida, United States

Site Status

New Jersey Center for Cancer Research

Brick, New Jersey, United States

Site Status

Clinical Research Alliance, Inc.

Westbury, New York, United States

Site Status

Liverpool Hospital

Liverpool, New South Wales, Australia

Site Status

Westmead Hospital

Wentworthville, New South Wales, Australia

Site Status

Peninsula Private Hospital

Frankston, Victoria, Australia

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Uniklinikum Salzburg

Salzburg, , Austria

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Klinik Ottakring

Vienna, , Austria

Site Status

Hospital de Clinicas de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

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Irmandade da Santa Casa de Misericórdia de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Centro Gaucho Integrado - Mae de Deus Center

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hemocentro Unicamp

Campinas, São Paulo, Brazil

Site Status

Fundação Doutor Amaral Carvalho

Jaú, São Paulo, Brazil

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UMHAT "Sveti Georgi" EAD

Plovdiv, , Bulgaria

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UMHAT 'Sv. Ivan Rilski', EAD

Sofia, , Bulgaria

Site Status

"SHATHD" EAD, Sofia

Sofia, , Bulgaria

Site Status

UMHAT - Prof. Dr. Stoyan Kirkovich" AD

Stara Zagora, , Bulgaria

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Anhui Provincial Cancer Hospital

Hefei, Anhui, China

Site Status

Peking University First Hospital

Beijing, Beijing Municipality, China

Site Status

Peking University Third Hospital

Beijing, Beijing Municipality, China

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The First Affiliated Hospital of Guangzhou Medical University

Guangzhou, Guangdong, China

Site Status

Union Hospital Tongji Medical College Huazhong University of Science and Technology

Wuhan, Hubei, China

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Xiangya Hospital Central South University

Changsha, Hunan, China

Site Status

Hunan Cancer Hospital

Changsha, Hunan, China

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The Affiliated Hospital of Inner Mongolia Medical University

Hohhot, Inner Mongolia, China

Site Status

The First Affiliated Hospital of Nanchang University

Nanchang, Jiangxi, China

Site Status

Shengjing Hospital of China Medical University

Shenyany, Liaoning, China

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Jiangsu Province Hospital

Nanjing, Nanjing, China

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Shanghai Tongren Hospital

Changning District, Shanghai Municipality, China

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West China Hospital of Sichuan University

Chengdu, Sichuan, China

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Institute of hematology&blood disease hospital

Tianjin, Tianjin Municipality, China

Site Status

Tianjin Medical University Cancer Institute and Hospital

Tianjin, Tianjin Municipality, China

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The First People's Hospital of Hangzhou Linping District

Hangzhou, Zhejiang, China

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Beijing Hospital

Beijing, , China

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Chongqing Cancer Hospital

Chongqing, , China

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Henan Cancer Hospital

Zhengzhou, , China

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Fakultni nemocnice Brno

Brno, , Czechia

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Fakultni nemocnice Hradec Kralove

Hradec Králové, , Czechia

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Hospitalier Le Mans

Le Mans, , France

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Debreceni Egyetem Orvos-es Egészsegtudomanyi Centrum

Debrecen, , Hungary

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SzSzB Megyei Korhazak es Egyetemi Oktatokorhaz

Nyíregyháza, , Hungary

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Fejer Megyei Szent Gyorgy Egyetemi Oktato Korhaz

Székesfehérvár, , Hungary

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Irccs Crob

Rionero in Vulture, Potenza, Italy

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Azienda Socio Sanitaria Territoriale Papa Giovanni XXIII

Bergamo, , Italy

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Azienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia

Brescia, , Italy

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Istituto Scientifico Romagnolo per lo Studio e la Cura dei Tumori

Meldola, , Italy

Site Status

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico

Milan, , Italy

Site Status

ASST Grande Ospedale Metropolitano Niguarda Comitato Etico Milano Area C

Milan, , Italy

Site Status

Azienda Socio Sanitaria Territoriale di Monza (Presidio San Gerardo)

Monza, , Italy

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Azienda Ospedale Maggiore Della Carita

Novara, , Italy

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Istituto di Ematologia-C.R.E.O. (Centro di Ricerche Emato-Oncologich)

Perugia, , Italy

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Ospedale Santa Maria delle Croci

Ravenna, , Italy

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Azienda Ospedaliera Santa Maria Terni

Terni, , Italy

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Azienda sanitaria integrata università di Trieste

Trieste, , Italy

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Nagoya City University Hospital

Nagoya, Aichi-ken, Japan

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Chiba Cancer Center

Chiba, Chiba, Japan

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Fukui Medical University Hospital

Yoshida-Gun, Fukui, Japan

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Hokuyukai Sapporo Hokuyu Hospital

Sapporo, Hokkaido, Japan

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Kochi Medical School Hospital

Nankoku, Kochi, Japan

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Tohoku University Hospital

Sendai, Miyagi, Japan

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NHO Sendai Medical Center

Sendai, Miyagi, Japan

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Dokkyo Medical University - Koshigaya Hospital

Koshigaya, Saitama, Japan

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University of Yamanashi Hospital

Chūō, Yamanshi, Japan

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Aomori Prefectural Centeral Hospital

Aomori, , Japan

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JCHO Kyushu Hospital

Fukoka-ken, , Japan

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North Shore Hospital, Haematology Research

Takapuna, Auckland, New Zealand

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Tauranga Hospital

Tauranga, Bay of Plenty, New Zealand

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Christchurch Hospital

Christchurch, , New Zealand

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Middlemore Clinical Trials

Papatoetoe, , New Zealand

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Wojewodzki Szpital Specjalistyczny

Iwaszkiewicza 5, Legnica, Poland

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Klinika Hematoonkologii i Transplantacji Szpiku SPSK1 Lublin

Lublin, Lubelskie V, Poland

Site Status

Uniwersyteckie Centrum Kliniczne

Gdansk, Pomeranian Voivodeship, Poland

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Centrum Medyczne Pratia Poznan

Skorzewo, Poznan, Poland

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KO-MED Centra Kliniczne

Biała Podlaska, , Poland

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Szpital Uniwersytecki nr 1 im. Antoniego Jurasza

Bydgoszcz, , Poland

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Pratia Onkologia Katowice

Katowice, , Poland

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Pratia MCM Krakow

Krakow, , Poland

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Centrum Onkologii Ziemi Lubelskiej

Lublin, , Poland

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Nasz Lekarz Osrodek Badan Klinicznych

Torun, , Poland

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Narodowy Instytut Onkologii im. Marii Skłodowskiej-Cuire - Państwowy Instytut Badawczy

Warsaw, , Poland

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Uniwersytecki Szpital Kliniczny Klinika

Wroclaw, , Poland

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Centro Clínico Académico - Braga (2CA-Braga) (Hospital de Braga)

Braga, , Portugal

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Centro Hospitalar de Lisboa Norte, E.P.E. - Hospital de Santa Maria

Lisbon, , Portugal

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Instituto Português de Oncologia do Porto Francisco Gentil, EPE

Porto, , Portugal

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Spitalul Clinic Municipal Filantropia Craiova

Craiova, Dolj, Romania

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Institutul Clinic Fundeni - Centrul de Hematologie si Transplant Medular

Bucharest, , Romania

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Institutul Oncologic "Prof. Dr. Ion Chiricuta" Cluj-Napoca

Cluj-Napoca, , Romania

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Institutului Regional de Oncologie IASI

Iași, , Romania

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Academician I.P. Pavlov First St-Petersburg State Medical University

Saint Petersburg, , Russia

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Gachon University Gil Medical Center

Namdong-gu, Incheon-gwangyeoksi [Incheon], South Korea

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The Catholic University of Korea-Seoul St. Mary's Hospital

Seocho-Gu, Seoul, South Korea

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Seoul National University Hospital

Seoul, Seoul, Korea, South Korea

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Severance Hospital, Yonsei University Health System

Seoul, Seoul-teukbyeolsi [Seoul], South Korea

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Samsung Medical Center

Seoul, Seoul-teukbyeolsi [Seoul], South Korea

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Inje Univ Busan Paik Hospital

Busan, , South Korea

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Hospital Universitario HM Sanchinarro

Madrid, Madrid, Comunidad de, Spain

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Hospital Universitario Central de Asturias

Oviedo, Principality of Asturias, Spain

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Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

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Hospital Universitario Fundación Jiménez Díaz

Madrid, , Spain

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Hospital Universitario Virgen del Rocío

Seville, , Spain

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Hospital Universitario Virgen de Valme

Seville, , Spain

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Chang Bing Show Chwan Memorial Hospital

Changhua, , Taiwan

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China Medical University Hospital

Taichung, , Taiwan

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National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Chang Gung Memorial Hospital - Linkou

Taoyuan, , Taiwan

Site Status

Birmingham Heartlands Hospital

Birmingham, England, United Kingdom

Site Status

Countries

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United States Australia Austria Brazil Bulgaria China Czechia France Hungary Italy Japan New Zealand Poland Portugal Romania Russia South Korea Spain Taiwan United Kingdom

Related Links

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https://trials.lilly.com/en-US/trial/302156

A Study of Pirtobrutinib (LOXO-305) Versus Bendamustine Plus Rituximab (BR) in Untreated Patients With Chronic Lymphocytic Leukemia (CLL)/Small Lymphocytic Lymphoma (SLL) (BRUIN CLL-313)

Other Identifiers

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J2N-OX-JZNP

Identifier Type: OTHER

Identifier Source: secondary_id

LOXO-BTK-20023

Identifier Type: OTHER

Identifier Source: secondary_id

18088

Identifier Type: -

Identifier Source: org_study_id

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