A Study of Pirtobrutinib (LOXO-305) Versus Ibrutinib in Participants With Chronic Lymphocytic Leukemia (CLL)/Small Lymphocytic Lymphoma (SLL)

NCT ID: NCT05254743

Last Updated: 2025-11-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

662 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-07-22

Study Completion Date

2028-01-31

Brief Summary

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The purpose of Part 1 of this study is to compare the efficacy and safety of pirtobruitinib (LOXO-305) to ibrutinib in participants with CLL/SLL; participants may or may not have already had treatment for their cancer. The purpose of Part 2 of this study evaluates pirtobrutinib monotherapy in treatment-naïve participants with CLL/SLL with 17p deletions. Participation could last up to six years for Part 1. Participation could last up to 2 years for Part 2.

Detailed Description

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Conditions

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Chronic Lymphocytic Leukemia Leukemia, Lymphocytic Leukemia, B-cell Small Lymphocytic Lymphoma

Keywords

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BTKi Hematologic Disease Lymphoma, non-Hodgkin's Lymphoma, B-cell

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Pirtobrutinib Part 1

Participants will receive pirtobrutinib orally.

Group Type EXPERIMENTAL

Pirtobrutinib

Intervention Type DRUG

Administered orally.

Ibrutinib

Participants will receive ibrutinib orally.

Group Type ACTIVE_COMPARATOR

Ibrutinib

Intervention Type DRUG

Administered orally.

Pirtobrutinib Part 2

Participants will receive pirtobrutinib orally.

Group Type EXPERIMENTAL

Pirtobrutinib

Intervention Type DRUG

Administered orally.

Interventions

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Pirtobrutinib

Administered orally.

Intervention Type DRUG

Ibrutinib

Administered orally.

Intervention Type DRUG

Other Intervention Names

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LOXO-305 LY3527727

Eligibility Criteria

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Inclusion Criteria

* Confirmed diagnosis of CLL/SLL requiring therapy per iwCLL 2018 criteria
* Part 1 - Known 17p deletion status (wildtype or deleted). Part 2 - Must have deletion of 17p as determined by FISH testing
* Eastern Cooperative Oncology Group (ECOG) Performance Status 0-2
* Adequate organ function

* Platelets greater than or equal to ≥ 50 x 10⁹/liter (L) or ≥30 x 10⁹/L in participants with documented bone marrow involvement considered to impair hematopoiesis,
* Hemoglobin ≥8 grams/deciliter (g/dL) or ≥6 g/dL in participants with documented bone marrow involvement considered to impair hematopoiesis
* Absolute neutrophil count ≥0.75 x 10⁹/L or ≥0.50 × 10⁹/L in participants with documented bone marrow involvement considered to impair hematopoiesis
* Kidney function: Estimated creatinine clearance ≥30 milliliters per minute (mL/min)

Exclusion Criteria

* Known or suspected Richter's transformation to diffuse large B-cell lymphoma (DLBCL), prolymphocytic leukemia, or Hodgkin's lymphoma at any time preceding enrollment
* Known or suspected central nervous system (CNS) involvement
* A significant history of renal, neurologic, psychiatric, endocrine, metabolic or immunologic disease
* Active uncontrolled auto-immune cytopenia (e.g., autoimmune hemolytic anemia \[AIHA\], idiopathic thrombocytopenic purpura \[ITP\])
* Significant cardiovascular disease including ejection fraction \< 40% and any grade ongoing atrial fibrillation or atrial flutter
* Hepatitis B or hepatitis C testing indicating active/ongoing infection, based on Screening laboratory tests
* Active cytomegalovirus (CMV) infection
* Active uncontrolled systemic bacterial, viral, or fungal infection
* Known human immunodeficiency virus (HIV) infection, regardless of cluster of differentiation 4 (CD4) count
* Clinically significant active malabsorption syndrome or other condition likely to affect GI absorption of the oral-administered study treatments
* Ongoing inflammatory bowel disease
* Previous treatment for CLL/SLL - Part 1: Treatment-naïve and previously treated, except prior exposure to BTK inhibitor (covalent or noncovalent).

Part 2: participants must be treatment naïve

* Concurrent use of investigational agent or anticancer therapy except hormonal therapy
* Participants requiring therapeutic anticoagulation with warfarin or another Vitamin K antagonist
* Use of \> 20 mg prednisone daily or equivalent dose of steroid at the time of first dose of study drug
* Vaccination with a live vaccine within 28 days prior to randomization
* Participants receiving chronic therapy with a strong cytochrome P450 (CYP)3A inhibitor (except posaconazole and voriconazole) which cannot be stopped within 3-5 half lives of the CYP3A inhibitor therapy prior to start of study drug treatment
* Participants with known hypersensitivity, including anaphylaxis, to any component or excipient of pirtobrutinib or ibrutinib
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Loxo Oncology, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 8 AM - 8 PM Eastern time (UTC/GMT - 5 hours, EST)

Role: STUDY_DIRECTOR

Eli Lilly and Company

Locations

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Pacific Cancer Medical Center, Inc

Anaheim, California, United States

Site Status RECRUITING

TOI Clinical Research

Cerritos, California, United States

Site Status ACTIVE_NOT_RECRUITING

Stanford School of Medicine-Cancer Clinical Trials Office

Palo Alto, California, United States

Site Status RECRUITING

California Cancer Associates for Research and Excellence

San Marcos, California, United States

Site Status ACTIVE_NOT_RECRUITING

Florida Cancer Specialists

Fort Myers, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Cancer Specialists of North Florida -St Augustine

Saint Augustine, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Florida Cancer Specialists East

West Palm Beach, Florida, United States

Site Status ACTIVE_NOT_RECRUITING

Hematology Oncology Clinic

Baton Rouge, Louisiana, United States

Site Status ACTIVE_NOT_RECRUITING

Tulane Cancer Center Office of Clinical Research

New Orleans, Louisiana, United States

Site Status ACTIVE_NOT_RECRUITING

American Oncology Partners of Maryland, PA

Bethesda, Maryland, United States

Site Status RECRUITING

St. Vincent Frontier Cancer Center

Billings, Montana, United States

Site Status ACTIVE_NOT_RECRUITING

Cancer Care Associates of York

York, Pennsylvania, United States

Site Status ACTIVE_NOT_RECRUITING

Prisma Health Cancer Institute

Greenville, South Carolina, United States

Site Status ACTIVE_NOT_RECRUITING

Sarah Cannon Research Institute SCRI

Nashville, Tennessee, United States

Site Status ACTIVE_NOT_RECRUITING

Kelsey Research Foundation

Houston, Texas, United States

Site Status ACTIVE_NOT_RECRUITING

Lumi Research

Kingwood, Texas, United States

Site Status RECRUITING

Virginia Cancer Institute

Richmond, Virginia, United States

Site Status RECRUITING

Medical Oncology Associates, PS

Spokane, Washington, United States

Site Status ACTIVE_NOT_RECRUITING

MultiCare Health System Institute for Research and Innovation

Spokane, Washington, United States

Site Status ACTIVE_NOT_RECRUITING

Alexander Fleming

Ciudad Autónoma de Buenos Aire, , Argentina

Site Status RECRUITING

Hospital Privado De Comunidad

Mar del Plata, , Argentina

Site Status ACTIVE_NOT_RECRUITING

Clínica de Nefrología, Urología y Enfermedades Cardiovasculares

Santa Fe, , Argentina

Site Status ACTIVE_NOT_RECRUITING

One Clinical Research

Nedlands, , Australia

Site Status ACTIVE_NOT_RECRUITING

Western Health, Sunshine Hospital

St Albans, , Australia

Site Status ACTIVE_NOT_RECRUITING

The Perth Blood Institute

West Perth, , Australia

Site Status ACTIVE_NOT_RECRUITING

Hanusch Krankenhaus

Vienna, , Austria

Site Status ACTIVE_NOT_RECRUITING

Universitaire Ziekenhuizen Leuven - Campus Gasthuisberg

Leuven, , Belgium

Site Status RECRUITING

VITAZ

Sint-Niklaas, , Belgium

Site Status ACTIVE_NOT_RECRUITING

Fundação Pio XII - Hospital de Câncer de Barretos

Barretos, , Brazil

Site Status RECRUITING

Upeclin - Unidade de Pesquisa Clínica da Faculdade de Medicina de Botucatu - UNESP

Botucatu, , Brazil

Site Status RECRUITING

Hemocentro Unicamp

Campinas, , Brazil

Site Status ACTIVE_NOT_RECRUITING

Hospital Uopeccan - Centro de Pesquisa Clinica

Cascavel, , Brazil

Site Status ACTIVE_NOT_RECRUITING

Centro Integrado de Oncologia de Curitiba

Curitiba, , Brazil

Site Status ACTIVE_NOT_RECRUITING

Hospital Erasto Gaertner - Liga Paranaense de Combate ao Câncer

Curitiba, , Brazil

Site Status ACTIVE_NOT_RECRUITING

Instituto do Câncer - Hospital São Vicente de Paulo

Passo Fundo, , Brazil

Site Status ACTIVE_NOT_RECRUITING

Centro Gaucho Integrado - Mae de Deus Center

Porto Alegre, , Brazil

Site Status RECRUITING

Hospital de Clínicas de Ribeirão Preto

Ribeirão Preto, , Brazil

Site Status ACTIVE_NOT_RECRUITING

CEPHO - Centro de Estudos e Pesquisas de Hematologia e Oncologia

Santo André, , Brazil

Site Status RECRUITING

Centro Integrado de Pesquisa Clinica

São José do Rio Preto, , Brazil

Site Status RECRUITING

Hospital BP

São Paulo, , Brazil

Site Status ACTIVE_NOT_RECRUITING

Hospital da Clinicas da Faculdade de Medicina da USP

São Paulo, , Brazil

Site Status RECRUITING

Hospital Santa Marcelina

São Paulo, , Brazil

Site Status RECRUITING

Royal Victoria Hospital-Montreal

Montreal, , Canada

Site Status TERMINATED

Hopital de L'Enfant Jesus

Québec, , Canada

Site Status RECRUITING

Cancer Care Manitoba

Winnipeg, , Canada

Site Status ACTIVE_NOT_RECRUITING

Inmunocel

Santiago, , Chile

Site Status ACTIVE_NOT_RECRUITING

CeCim Biocinetic

Santiago, , Chile

Site Status ACTIVE_NOT_RECRUITING

Sociedad de Investigaciones Médicas Limitada

Temuco, , Chile

Site Status ACTIVE_NOT_RECRUITING

Centro de Investigaciones Clínicas Viña del Mar (CIC)

Viña del Mar, , Chile

Site Status ACTIVE_NOT_RECRUITING

The Second Xiangya Hospital of Central South University

Changsha, , China

Site Status ACTIVE_NOT_RECRUITING

Hunan Cancer Hospital

Changsha, , China

Site Status ACTIVE_NOT_RECRUITING

Sun Yat-sen University Cancer Center

Guangzhou, , China

Site Status ACTIVE_NOT_RECRUITING

Southern Medical University Nanfang Hospital

Guangzhou, , China

Site Status ACTIVE_NOT_RECRUITING

Hainan General Hospital

Haikou, , China

Site Status ACTIVE_NOT_RECRUITING

First Affiliated Hosp of College of Med, Zhejiang University

Hangzhou, , China

Site Status ACTIVE_NOT_RECRUITING

The Second Affiliated Hospital of Zhejiang University School of Medicine

Hangzhou, , China

Site Status ACTIVE_NOT_RECRUITING

Anhui Provincial Hospital

Hefei, , China

Site Status ACTIVE_NOT_RECRUITING

The Second Hospital of Anhui Medical University

Hefei, , China

Site Status ACTIVE_NOT_RECRUITING

Jiangxi Provincial Cancer Hospital

Nanchang, , China

Site Status ACTIVE_NOT_RECRUITING

Guangxi Medical University Affiliated Tumor Hospital

Nanning, , China

Site Status ACTIVE_NOT_RECRUITING

Fudan University Shanghai Cancer Center

Shanghai, , China

Site Status ACTIVE_NOT_RECRUITING

Blood Institute of the Chinese Academy of Medical science

Tianjin, , China

Site Status ACTIVE_NOT_RECRUITING

Tianjin Medical University General Hospital

Tianjin, , China

Site Status ACTIVE_NOT_RECRUITING

Affiliated Cancer Hospital of Xinjiang Medical University

Ürümqi, , China

Site Status ACTIVE_NOT_RECRUITING

Union Hospital Tongji Medical College Huazhong University of Science and Technology

Wuhan, , China

Site Status ACTIVE_NOT_RECRUITING

Wu Han Tongji Hospital

Wuhan, , China

Site Status ACTIVE_NOT_RECRUITING

The Fourth Affiliated Hospital Zhejiang University School of Medicine

Yiwu, , China

Site Status ACTIVE_NOT_RECRUITING

Fakultni nemocnice Brno

Brno, , Czechia

Site Status ACTIVE_NOT_RECRUITING

Fakultni nemocnice Hradec Kralove

Hradec Králové, , Czechia

Site Status ACTIVE_NOT_RECRUITING

Fakultni Nemocnice Ostrava

Ostrava, , Czechia

Site Status ACTIVE_NOT_RECRUITING

Fakultni Nemocnice Plzen

Pilsen, , Czechia

Site Status ACTIVE_NOT_RECRUITING

Fakultni nemocnice Kralovske Vinohrady

Prague, , Czechia

Site Status RECRUITING

Vseobecna fakultni nemocnice v Praze

Prague, , Czechia

Site Status ACTIVE_NOT_RECRUITING

CHD Vendee

La Roche-sur-Yon, , France

Site Status RECRUITING

Centre Hospitalier du Mans

Le Mans, , France

Site Status ACTIVE_NOT_RECRUITING

Centre Hospitalier Universitaire (Limoges) (CHU DUPUYTREN 1)

Limoges, , France

Site Status ACTIVE_NOT_RECRUITING

CHU de Nantes - Hotel Dieu

Nantes, , France

Site Status ACTIVE_NOT_RECRUITING

Centre Antoine Lacassagne

Nice, , France

Site Status ACTIVE_NOT_RECRUITING

Hopital de la Pitie Salpetriere

Paris, , France

Site Status RECRUITING

Centre Hospitalier Lyon Sud

Pierre-Bénite, , France

Site Status ACTIVE_NOT_RECRUITING

Hôpital de Pontchaillou

Rennes, , France

Site Status ACTIVE_NOT_RECRUITING

Centre de Lutte Contre le Cancer - Centre Henri Becquerel Normandie Rouen

Rouen, , France

Site Status ACTIVE_NOT_RECRUITING

CHRU De Tours

Tours, , France

Site Status ACTIVE_NOT_RECRUITING

Gemeinschaftspraxis für Hämatologie und Onkologie (Gefos)

Dortmund, , Germany

Site Status ACTIVE_NOT_RECRUITING

Onkologische Gemeinschaftspraxis / BAG

Dresden, , Germany

Site Status ACTIVE_NOT_RECRUITING

Universitaetsklinikum Carl Gustav Carus an der TU Dresden, Medizinische Klinik und Poliklinik 1

Dresden, , Germany

Site Status ACTIVE_NOT_RECRUITING

Universitätsklinikum Ulm

Ulm, , Germany

Site Status ACTIVE_NOT_RECRUITING

Debreceni Egyetem Orvos-es Egészsegtudomanyi Centrum

Debrecen, , Hungary

Site Status ACTIVE_NOT_RECRUITING

Markusovszky Egyetemi Oktatokorhaz

Szombathely, , Hungary

Site Status ACTIVE_NOT_RECRUITING

Hadassah Medical Center

Jerusalem, , Israel

Site Status ACTIVE_NOT_RECRUITING

Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status ACTIVE_NOT_RECRUITING

Azienda Ospedaliera Nazionale Santi Antonio e Biagio e Cesare Arrigo

Alessandria, , Italy

Site Status RECRUITING

Policlinico Sant'Orsola Malpighi

Bologna, , Italy

Site Status ACTIVE_NOT_RECRUITING

Istituto Scientifico Romagnolo per lo Studio e la Cura dei Tumori

Meldola, , Italy

Site Status RECRUITING

IRCCS Ospedale San Raffaele

Milan, , Italy

Site Status ACTIVE_NOT_RECRUITING

Istituto Europeo di Oncologia

Milan, , Italy

Site Status ACTIVE_NOT_RECRUITING

Azienda Unita Sanitaria Locale di Reggio Emilia

Reggio Emilia, , Italy

Site Status ACTIVE_NOT_RECRUITING

A.O.U. Citta' della Salute e della Scienza di Torino

Torino, , Italy

Site Status RECRUITING

Kumamoto University Hospital

Kumamoto, , Japan

Site Status ACTIVE_NOT_RECRUITING

Yamagata University Hospital

Yamagata, , Japan

Site Status RECRUITING

Dunedin Hospital

Dunedin, , New Zealand

Site Status ACTIVE_NOT_RECRUITING

Waikato Hospital

Hamilton, , New Zealand

Site Status ACTIVE_NOT_RECRUITING

Momentum Clinical Research

Newtown, , New Zealand

Site Status ACTIVE_NOT_RECRUITING

Middlemore Clinical Trials

Papatoetoe, , New Zealand

Site Status ACTIVE_NOT_RECRUITING

KO-MED Centra Kliniczne

Biała Podlaska, , Poland

Site Status ACTIVE_NOT_RECRUITING

Szpital Uniwersytecki nr 1 im. Antoniego Jurasza

Bydgoszcz, , Poland

Site Status ACTIVE_NOT_RECRUITING

Uniwersyteckie Centrum Kliniczne

Gdansk, , Poland

Site Status ACTIVE_NOT_RECRUITING

Pratia Onkologia Katowice

Katowice, , Poland

Site Status ACTIVE_NOT_RECRUITING

Pratia MCM Krakow

Krakow, , Poland

Site Status ACTIVE_NOT_RECRUITING

Klinika Hematoonkologii i Transplantacji Szpiku,Samodzielny Publiczny Szpital Kliniczny Nr 1

Lublin, , Poland

Site Status ACTIVE_NOT_RECRUITING

AIDPORT Sp. z o.o.

Skórzewo, , Poland

Site Status RECRUITING

Uniwersytecki Szpital Kliniczny Klinika

Wroclaw, , Poland

Site Status ACTIVE_NOT_RECRUITING

Inje Univ Busan Paik Hospital

Busan, , South Korea

Site Status RECRUITING

The Catholic University of Korea-Seoul St. Mary's Hospital

Seocho-Gu, , South Korea

Site Status ACTIVE_NOT_RECRUITING

Seoul National University Hospital

Seoul, , South Korea

Site Status ACTIVE_NOT_RECRUITING

Samsung Medical Center

Seoul, , South Korea

Site Status ACTIVE_NOT_RECRUITING

Hospital Germans Trias i Pujol

Badalona, , Spain

Site Status RECRUITING

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status ACTIVE_NOT_RECRUITING

Institut Català d'Oncologia de Girona (ICO Girona)

Girona, , Spain

Site Status RECRUITING

Hospital Duran i Reynals

L'Hospitalet de Llobregat, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital De Gran Canaria Dr. Negrin

Las Palmas de Gran Canaria, , Spain

Site Status RECRUITING

Hospital Universitario Infanta Leonor-INTERNAL MED

Madrid, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario Ramón y Cajal

Madrid, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario Puerta de Hierro Majadahonda

Majadahonda, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Costa Del Sol

Marbella, , Spain

Site Status ACTIVE_NOT_RECRUITING

Clinica Universitaria De Navarra

Pamplona, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital De Navarra

Pamplona, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario Marqués de Valdecilla

Santander, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario Virgen Macarena

Seville, , Spain

Site Status RECRUITING

Hospital Universitario Virgen Del Rocio

Seville, , Spain

Site Status ACTIVE_NOT_RECRUITING

Chang Bing Show Chwan Memorial Hospital

Changhua, , Taiwan

Site Status ACTIVE_NOT_RECRUITING

Chang Gung Memorial Hospital - Chiayi

Chiayi County, , Taiwan

Site Status ACTIVE_NOT_RECRUITING

National Cheng-Kung Uni. Hosp.

Tainan, , Taiwan

Site Status ACTIVE_NOT_RECRUITING

Koo Foundation Sun Yan-Sen Cancer Center

Taipei, , Taiwan

Site Status ACTIVE_NOT_RECRUITING

Gazi University Faculty of Medicine

Ankara, , Turkey (Türkiye)

Site Status ACTIVE_NOT_RECRUITING

9 Eylul University Hospital

Balçova, , Turkey (Türkiye)

Site Status ACTIVE_NOT_RECRUITING

Ege Üniversitesi

Bornova, , Turkey (Türkiye)

Site Status ACTIVE_NOT_RECRUITING

Istanbul University Istanbul Medicine Faculty

Faith, , Turkey (Türkiye)

Site Status ACTIVE_NOT_RECRUITING

American Hospital

Istanbul, , Turkey (Türkiye)

Site Status ACTIVE_NOT_RECRUITING

Acıbadem Maslak Hastanesi

Istanbul, , Turkey (Türkiye)

Site Status COMPLETED

Ankara University Medicine Hospital

Mamak, , Turkey (Türkiye)

Site Status ACTIVE_NOT_RECRUITING

Bristol Haematology and Oncology Centre

Bristol, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Castle Hill Hospital

Cottingham, , United Kingdom

Site Status RECRUITING

HOPE Centre

Leicester, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

St Bartholomew's Hospital

London, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Singleton Hospital

Swansea, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Countries

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United States Argentina Australia Austria Belgium Brazil Canada Chile China Czechia France Germany Hungary Israel Italy Japan New Zealand Poland South Korea Spain Taiwan Turkey (Türkiye) United Kingdom

Central Contacts

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Trial questions or participation questions: 1-877-CTLILLY (1-877-285-4559) or

Role: CONTACT

Phone: 1-317-615-4559

Email: [email protected]

Physicians interested in becoming principal investigators please contact

Role: CONTACT

Email: [email protected]

Facility Contacts

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Role: primary

Role: primary

Role: primary

Role: primary

Role: primary

Role: primary

Role: primary

Role: primary

Role: primary

Role: primary

Role: primary

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Related Links

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https://trials.lilly.com/en-US/trial/334656

A Study of Pirtobrutinib (LOXO-305) Versus Ibrutinib in Participants With Chronic Lymphocytic Leukemia (CLL)/Small Lymphocytic Lymphoma (SLL) (BRUIN-CLL-314)

Other Identifiers

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J2N-OX-JZNU

Identifier Type: OTHER

Identifier Source: secondary_id

LOXO-BTK-20030

Identifier Type: OTHER

Identifier Source: secondary_id

2023-507699-38-00

Identifier Type: CTIS

Identifier Source: secondary_id

18281

Identifier Type: -

Identifier Source: org_study_id