A 52 Week Study To Assess The Use Of Bococizumab (PF-04950615; RN316) In Subjects With Heterozygous Familial Hypercholesterolemia

NCT ID: NCT01968980

Last Updated: 2017-06-26

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

370 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-10-23

Study Completion Date

2016-04-15

Brief Summary

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This is a multicenter, randomized study in subjects with heterozygous familial hypercholesterolemia receiving highly effective statins to assess the safety, efficacy and tolerability of Bococizumab (PF-04950615; RN316) to lower LDL-C.

Detailed Description

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Conditions

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Heterozygous Familial Hypercholesterolemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Bococizumab (PF-04950615;RN316)

Bococizumab (PF-04950615;RN316)

Group Type EXPERIMENTAL

Bococizumab (PF-04950615;RN316)

Intervention Type DRUG

150 mg every 2 weeks, subcutaneous injection, 12 months

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

subcutaneous injection every 2 weeks for 12 months

Interventions

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Bococizumab (PF-04950615;RN316)

150 mg every 2 weeks, subcutaneous injection, 12 months

Intervention Type DRUG

Placebo

subcutaneous injection every 2 weeks for 12 months

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Treated with a statin.
* Fasting LDL-C \> 70 mg/dL and triglyceride \<=400 mg/dL.
* High or very high risk of incurring a cardiovascular event.
* Heterozygous familial hypercholesterolemia.

Exclusion Criteria

* Pregnant or breastfeeding females.
* Cardiovascular or cerebrovascular event of procedures during the past 30 days.
* Congestive heart failure NYHA class IV.
* Poorly controlled hypertension.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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IMD Medical Group

Los Angeles, California, United States

Site Status

Hartford Hospital, JB704

Hartford, Connecticut, United States

Site Status

Best Quality Research, Inc.

Hialeah, Florida, United States

Site Status

Medical Research Center

Miami, Florida, United States

Site Status

Premier Research Associate, Inc

Miami, Florida, United States

Site Status

Columbus Clinical Services, LLC

Miami, Florida, United States

Site Status

NewPhase Clinical Trials, Corp.

Miami Beach, Florida, United States

Site Status

Om Medical

Las Vegas, Nevada, United States

Site Status

The University of North Carolina at Chapel Hill Center for Heart & Vascular Care

Chapel Hill, North Carolina, United States

Site Status

The University of North Carolina Hospitals - Clinical and Translational Research Center Clinic

Chapel Hill, North Carolina, United States

Site Status

Metabolic and Atherosclerosis Research Center

Cincinnati, Ohio, United States

Site Status

Oklahoma Heart Hospital Physicians

Oklahoma City, Oklahoma, United States

Site Status

Oklahoma Heart Hospital Research Foundation

Oklahoma City, Oklahoma, United States

Site Status

Oklahoma Heart Hospital

Oklahoma City, Oklahoma, United States

Site Status

Thomas Jefferson University

Philadelphia, Pennsylvania, United States

Site Status

OnSite Clinical Solutions, LLC

Gaffney, South Carolina, United States

Site Status

Galenos Research

Dallas, Texas, United States

Site Status

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status

Pioneer Research Solutions, Inc.

Houston, Texas, United States

Site Status

Pioneer Research Solutions, Inc.

Sugar Land, Texas, United States

Site Status

Focus Clinical Research, LLC

Draper, Utah, United States

Site Status

Burke Internal Medicine & Research

Burke, Virginia, United States

Site Status

SHAT in Cardiology EAD

Pleven, , Bulgaria

Site Status

UMHAT "Sveti Georgi" EAD, Clinic of Cardiology

Plovdiv, , Bulgaria

Site Status

Second MHAT - Sofia EAD

Sofia, , Bulgaria

Site Status

MHAT "Sveta Anna", Clinic of Internal Diseases

Sofia, , Bulgaria

Site Status

St. Paul's Hospital, Healthy Heart

Vancouver, British Columbia, Canada

Site Status

Discovery Clinical Services Ltd.

Victoria, British Columbia, Canada

Site Status

Asper Clinical Research Institute

Winnipeg, Manitoba, Canada

Site Status

Health Sciences Centre

St. John's, Newfoundland and Labrador, Canada

Site Status

University of Ottawa Heart Institute

Ottawa, Ontario, Canada

Site Status

Ecogene-21

Chicoutimi, Quebec, Canada

Site Status

Montreal Heart Institute

Montreal, Quebec, Canada

Site Status

Institut de Recherches Cliniques de Montreal

Montreal, Quebec, Canada

Site Status

Clinique des maladies lipidiques de Quebec Inc

Québec, Quebec, Canada

Site Status

Helsinki Central University Hospital

Helsinki, , Finland

Site Status

Pohjois-Karjala Projekti Saatio/Ita-Suomen

Joensuu, , Finland

Site Status

Pohjois-Karjala Projekti Saatio

Joensuu, , Finland

Site Status

Laakarikeskus Aava Kerava/Aava Kerava Medical Center

Kerava, , Finland

Site Status

Oulu University Hospital

Oulu, , Finland

Site Status

Division of Medicine Turku University Hospital

Turku, , Finland

Site Status

Policlinico "Paolo Giaccone"

Palermo, PA, Italy

Site Status

Ospedale "Santa Maria della Misericordia"

Perugia, PG, Italy

Site Status

Ospedale di Circolo e Fondazione Macchi

Varese, VA, Italy

Site Status

Azienda Ospedaliero Universitaria "Federico II" di Napoli

Napoli, , Italy

Site Status

St. Franciscus Gasthuis

Rotterdam, South Holland, Netherlands

Site Status

Admiraal de Ruyter ziekenhuis

Goes, Zeeland, Netherlands

Site Status

Academic Medical Center

Amsterdam, , Netherlands

Site Status

Amphia Hospital

Breda, , Netherlands

Site Status

Deventer Ziekenhuis

Deventer, , Netherlands

Site Status

Rotterdam Research Institute

Rotterdam, , Netherlands

Site Status

Albert Schweitzer Hospital

Sliedrecht, , Netherlands

Site Status

Hagaziekenhuis

The Hague, , Netherlands

Site Status

UMC Utrecht

Utrecht, , Netherlands

Site Status

Oslo Universitetssykehus HF

Oslo, , Norway

Site Status

Oslo Universitetssykehus HF, Ulleval

Oslo, , Norway

Site Status

NZOZ Vitamed

Bydgoszcz, , Poland

Site Status

NZOZ Centrum Zdrowia i Profilaktyki Dabie Sp zo.o.

Krakow, , Poland

Site Status

NZOZ Przychodnia Specjalistyczna Andrzej Wittek Henryk Rudzki S.C

Ruda Śląska, , Poland

Site Status

IATROS International

Bloemfontein, Free State, South Africa

Site Status

Unitas hospital

Centurion, Gauteng, South Africa

Site Status

Midrand Medical Centre

Halfway House, Gauteng, South Africa

Site Status

Medipark Centre for Clinical Research

Pretoria, Gauteng, South Africa

Site Status

Jongaie Research

Pretoria, Gauteng, South Africa

Site Status

Synexus Watermeyer Clinical Research Centre

Pretoria, Gauteng, South Africa

Site Status

Roodepoort Medicross Clinical Research Centre

Roodepoort, Gauteng, South Africa

Site Status

Chelmsford Medical Centre 3

Durban, KwaZulu-Natal, South Africa

Site Status

Tiervlei Trial Centre, Karl Bremer Hospital

Bellville, Cape Town, Western Cape, South Africa

Site Status

TREAD Research cc.

Parow, Cape Town, Western Cape, South Africa

Site Status

Synexus Helderberg Clinical Research Centre

Somerset West, Western Cape, South Africa

Site Status

Hospital Universitario de Bellvitge

L'Hospitalet de Llobregat, Barcelona, Spain

Site Status

Hospital Clinico Universitario, Santiago de Compostela

Santiago de Compostela, Galicia, Spain

Site Status

Hospital Universitario Sant Joan de Reus

Reus, Tarragona, Spain

Site Status

Hospital Clinic

Barcelona, , Spain

Site Status

Hospital Universitario Reina Sofia

Córdoba, , Spain

Site Status

Hospital General Universitario Gregorio Maranon

Madrid, , Spain

Site Status

Fundacion Jimenez Diaz; Servicio de Medicina Interna

Madrid, , Spain

Site Status

Hospital Clinico San Carlos; U. de Lipidos; Medicina Interna III

Madrid, , Spain

Site Status

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status

Hospital Clinico Universitario Miguel Servet; Medicina Interna

Zaragoza, , Spain

Site Status

Clinical Trials Pharmacy, 4th Floor Inpatient Pharmacy

Manchester, Greater Manchester, United Kingdom

Site Status

Pennine Acute Hospitals NHS Trust

Oldham, Greater Manchester, United Kingdom

Site Status

East and North Hertfordshire NHS Trust

Stevenage, Hertfordshire, United Kingdom

Site Status

Burton Hospitals NHS Foundation Trust

Burton-on-Trent, Staffordshire, United Kingdom

Site Status

Heart of England NHS Foundation Trust

Birmingham, West Midlands, United Kingdom

Site Status

Royal Free London NHS Foundation Trust

London, , United Kingdom

Site Status

Central Manchester University Hospitals NHS Foundation Trust

Manchester, , United Kingdom

Site Status

Peterborough and Stamford Hospitals NHS Foundation Trust

Peterborough, , United Kingdom

Site Status

Countries

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United States Bulgaria Canada Finland Italy Netherlands Norway Poland South Africa Spain United Kingdom

References

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Wang EQ, Kaila N, Plowchalk D, Gibiansky L, Yunis C, Sweeney K. Population PK/PD modeling of low-density lipoprotein cholesterol response in hypercholesterolemic participants following administration of bococizumab, a potent anti-PCSK9 monoclonal antibody. CPT Pharmacometrics Syst Pharmacol. 2023 Dec;12(12):2013-2026. doi: 10.1002/psp4.13050. Epub 2023 Nov 22.

Reference Type DERIVED
PMID: 37994400 (View on PubMed)

McCush F, Wang E, Yunis C, Schwartz P, Baltrukonis D. Anti-drug Antibody Magnitude and Clinical Relevance Using Signal to Noise (S/N): Bococizumab Case Study. AAPS J. 2023 Sep 2;25(5):85. doi: 10.1208/s12248-023-00846-x.

Reference Type DERIVED
PMID: 37658997 (View on PubMed)

Chasman DI, Hyde CL, Giulianini F, Danning RD, Wang EQ, Hickling T, Ridker PM, Loomis AK. Genome-wide pharmacogenetics of anti-drug antibody response to bococizumab highlights key residues in HLA DRB1 and DQB1. Sci Rep. 2022 Mar 11;12(1):4266. doi: 10.1038/s41598-022-07997-5.

Reference Type DERIVED
PMID: 35277540 (View on PubMed)

Ridker PM, Rose LM, Kastelein JJP, Santos RD, Wei C, Revkin J, Yunis C, Tardif JC, Shear CL; Studies of PCSK9 Inhibition and the Reduction of vascular Events (SPIRE) Investigators. Cardiovascular event reduction with PCSK9 inhibition among 1578 patients with familial hypercholesterolemia: Results from the SPIRE randomized trials of bococizumab. J Clin Lipidol. 2018 Jul-Aug;12(4):958-965. doi: 10.1016/j.jacl.2018.03.088. Epub 2018 Apr 3.

Reference Type DERIVED
PMID: 29685591 (View on PubMed)

Ridker PM, Tardif JC, Amarenco P, Duggan W, Glynn RJ, Jukema JW, Kastelein JJP, Kim AM, Koenig W, Nissen S, Revkin J, Rose LM, Santos RD, Schwartz PF, Shear CL, Yunis C; SPIRE Investigators. Lipid-Reduction Variability and Antidrug-Antibody Formation with Bococizumab. N Engl J Med. 2017 Apr 20;376(16):1517-1526. doi: 10.1056/NEJMoa1614062. Epub 2017 Mar 17.

Reference Type DERIVED
PMID: 28304227 (View on PubMed)

Related Links

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Other Identifiers

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2013-002644-87

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

SPIRE-HF

Identifier Type: OTHER

Identifier Source: secondary_id

B1481021

Identifier Type: -

Identifier Source: org_study_id

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