A Phase 3 Safety and Efficacy Study of Fovista® (E10030) Intravitreous Administration in Combination With Lucentis® Compared to Lucentis® Monotherapy

NCT ID: NCT01944839

Last Updated: 2024-10-30

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

619 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-08-31

Study Completion Date

2016-12-31

Brief Summary

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The objectives of this study are to evaluate the safety and efficacy of intravitreal administration of Fovista® administered in combination with Lucentis® compared to Lucentis® monotherapy in subjects with subfoveal choroidal neovascularization secondary to age-related macular degeneration (AMD).

Detailed Description

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Subjects will be randomized in a 1:1 ratio to the following dose groups:

* Fovista® 1.5 mg/eye + Lucentis® 0.5 mg/eye
* Fovista® sham + Lucentis® 0.5 mg/eye

Subjects will be treated for a total of 24 months with active Fovista® or sham in combination with Lucentis® with the primary endpoint at 12 months.

Primary Efficacy Endpoint:

The primary efficacy endpoint is the mean change in visual acuity (ETDRS letters) from baseline at the month 12 visit.

Safety Endpoints:

Safety endpoints include adverse events, vital signs, ophthalmic variables \[ophthalmic examination, intraocular pressure (IOP), fluorescein angiogram (FA), optical coherence tomography (OCT)\], ECG, and laboratory variables.

Approximately 622 subjects will be randomized into one of the two treatment cohorts (311 patients per dose group).

Conditions

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Age-Related Macular Degeneration

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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E10030 + ranibizumab

E10030 1.5 mg intravitreal injection + ranibizumab 0.5 mg intravitreal injection

Group Type EXPERIMENTAL

E10030

Intervention Type DRUG

ranibizumab

Intervention Type DRUG

Sham + ranibizumab

E10030 sham intravitreal injection + ranibizumab 0.5 mg intravitreal injection

Group Type ACTIVE_COMPARATOR

ranibizumab

Intervention Type DRUG

E10030 sham intravitreal injection

Intervention Type DRUG

Pressure on the eye with a syringe with no needle

Interventions

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E10030

Intervention Type DRUG

ranibizumab

Intervention Type DRUG

E10030 sham intravitreal injection

Pressure on the eye with a syringe with no needle

Intervention Type DRUG

Other Intervention Names

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Fovista® Lucentis® Sham

Eligibility Criteria

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Inclusion Criteria

* Subjects of either gender aged ≥ 50 years
* Active subfoveal choroidal neovascularization (CNV) secondary to AMD
* Presence of sub-retinal hyper-reflective material (SD-OCT)

Exclusion Criteria

* Any prior treatment for AMD in the study eye prior to the Day 1 visit, except oral supplements of vitamins and minerals
* Any prior intravitreal treatment in the study eye prior to the Day 1 visit, regardless of indication (including intravitreal corticosteroids)
* Any intraocular surgery or thermal laser within three (3) months of trial entry. Any prior thermal laser in the macular region, regardless of indication
* Subjects with subfoveal scar or subfoveal atrophy are excluded
* Diabetes mellitus
Minimum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ophthotech Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Phoenix, Arizona, United States

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Bakersfield, California, United States

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Beverly Hills, California, United States

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Los Angeles, California, United States

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San Francisco, California, United States

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Santa Barbara, California, United States

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Colorado Springs, Colorado, United States

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Bridgeport, Connecticut, United States

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New London, Connecticut, United States

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Altamonte Springs, Florida, United States

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Fort Myers, Florida, United States

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Sarasota, Florida, United States

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Tampa, Florida, United States

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Tampa, Florida, United States

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Winter Haven, Florida, United States

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Marietta, Georgia, United States

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Springfield, Illinois, United States

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Indianapolis, Indiana, United States

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Leawood, Kansas, United States

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Lexington, Kentucky, United States

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Lexington, Kentucky, United States

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Louisville, Kentucky, United States

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New Orleans, Louisiana, United States

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Chevy Chase, Maryland, United States

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Boston, Massachusetts, United States

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Boston, Massachusetts, United States

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Jackson, Michigan, United States

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Southfield, Michigan, United States

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Rochester, Minnesota, United States

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St Louis, Missouri, United States

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Las Vegas, Nevada, United States

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Portsmouth, New Hampshire, United States

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Northfield, New Jersey, United States

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Albuquerque, New Mexico, United States

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Great Neck, New York, United States

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Shirley, New York, United States

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Cincinnati, Ohio, United States

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Cleveland, Ohio, United States

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Ashland, Oregon, United States

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Camp Hill, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Ladson, South Carolina, United States

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Nashville, Tennessee, United States

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Abilene, Texas, United States

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Austin, Texas, United States

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Tyler, Texas, United States

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Salt Lake City, Utah, United States

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Fairfax, Virginia, United States

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Madison, Wisconsin, United States

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Graz, , Austria

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Innsbruck, , Austria

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Linz, , Austria

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Vienna, , Austria

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Deurne, Antwerpen, Belgium

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Leuven, Vlaams-Brabant, Belgium

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Goiânia, Goiás, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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Minas Gerais, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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Calgary, Alberta, Canada

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Vancouver, British Columbia, Canada

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Winnipeg, Manitoba, Canada

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Halifax, Nova Scotia, Canada

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London, Ontario, Canada

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Mississauga, Ontario, Canada

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Ottawa, Ontario, Canada

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Toronto, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Saskatoon, Saskatchewan, Canada

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Brno, , Czechia

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Kralovice, , Czechia

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Libeň, , Czechia

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Olomouc, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Harju, , Estonia

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Tallinn, , Estonia

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Tartu, , Estonia

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Ancona, , Italy

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Bologna, , Italy

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Ferrara, , Italy

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Florence, , Italy

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Milan, , Italy

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Milan, , Italy

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Milan, , Italy

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Padua, , Italy

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Roma, , Italy

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Roma, , Italy

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Torino, , Italy

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Udine, , Italy

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Riga, , Latvia

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Riga, , Latvia

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Bydgoszcz, , Poland

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Katowice, , Poland

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Lodz, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Banská Bystrica, , Slovakia

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Bratislava, , Slovakia

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Trenčín, , Slovakia

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Basel, , Switzerland

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Bern, , Switzerland

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Lausanne, , Switzerland

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Zurich, , Switzerland

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Belfast, , United Kingdom

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Liverpool, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Plymouth, , United Kingdom

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Southampton, , United Kingdom

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Surrey Quays, , United Kingdom

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Countries

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United States Austria Belgium Brazil Canada Czechia Estonia Italy Latvia Poland Slovakia Switzerland United Kingdom

References

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Park EJ, Choi J, Lee KC, Na DH. Emerging PEGylated non-biologic drugs. Expert Opin Emerg Drugs. 2019 Jun;24(2):107-119. doi: 10.1080/14728214.2019.1604684. Epub 2019 Apr 19.

Reference Type DERIVED
PMID: 30957581 (View on PubMed)

Other Identifiers

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OPH1002

Identifier Type: -

Identifier Source: org_study_id

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