A Phase 3 Safety and Efficacy Study of Fovista® (E10030) Intravitreous Administration in Combination With Lucentis® Compared to Lucentis® Monotherapy

NCT ID: NCT01940900

Last Updated: 2024-10-30

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

627 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-08-31

Study Completion Date

2016-12-31

Brief Summary

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The objectives of this study are to evaluate the safety and efficacy of intravitreal administration of Fovista® administered in combination with Lucentis® compared to Lucentis® monotherapy in subjects with subfoveal choroidal neovascularization secondary to age-related macular degeneration (AMD).

Detailed Description

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Subjects will be randomized in a 1:1 ratio to the following dose groups:

* Fovista® 1.5 mg/eye + Lucentis® 0.5 mg/eye
* Fovista® sham + Lucentis® 0.5 mg/eye

Subjects will be treated for a total of 24 months with active Fovista® or sham in combination with Lucentis® with the primary endpoint at 12 months.

Primary Efficacy Endpoint:

The primary efficacy endpoint is the mean change in visual acuity (ETDRS letters) from baseline at the month 12 visit.

Safety Endpoints:

Safety endpoints include adverse events, vital signs, ophthalmic variables \[ophthalmic examination, intraocular pressure (IOP), fluorescein angiogram (FA), optical coherence tomography (OCT)\], ECG, and laboratory variables.

Approximately 622 subjects will be randomized into one of the two treatment cohorts (311 patients per dose group).

Conditions

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Age-Related Macular Degeneration

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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E10030 + ranibizumab

E10030 1.5 mg intravitreal injection + ranibizumab 0.5 mg intravitreal injection

Group Type EXPERIMENTAL

E10030

Intervention Type DRUG

ranibizumab

Intervention Type DRUG

Sham + ranibizumab

E10030 sham intravitreal injection + ranibizumab 0.5 mg intravitreal injection

Group Type ACTIVE_COMPARATOR

ranibizumab

Intervention Type DRUG

E10030 sham intravitreal injection

Intervention Type DRUG

Pressure on the eye with a syringe with no needle

Interventions

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E10030

Intervention Type DRUG

ranibizumab

Intervention Type DRUG

E10030 sham intravitreal injection

Pressure on the eye with a syringe with no needle

Intervention Type DRUG

Other Intervention Names

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Fovista® Lucentis® Sham

Eligibility Criteria

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Inclusion Criteria

* Subjects of either gender aged ≥ 50 years
* Active subfoveal choroidal neovascularization (CNV) secondary to AMD
* Presence of sub-retinal hyper-reflective material (SD-OCT)

Exclusion Criteria

* Any prior treatment for AMD in the study eye prior to the Day 1 visit, except oral supplements of vitamins and minerals
* Any prior intravitreal treatment in the study eye prior to the Day 1 visit, regardless of indication (including intravitreal corticosteroids)
* Any intraocular surgery or thermal laser within three (3) months of trial entry. Any prior thermal laser in the macular region, regardless of indication
* Subjects with subfoveal scar or subfoveal atrophy are excluded
* Diabetes mellitus
Minimum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ophthotech Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Tucson, Arizona, United States

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Tucson, Arizona, United States

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Fresno, California, United States

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La Jolla, California, United States

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Loma Linda, California, United States

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Mountain View, California, United States

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Sacramento, California, United States

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Santa Ana, California, United States

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Aurora, Colorado, United States

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Golden, Colorado, United States

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Boynton Beach, Florida, United States

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Fort Lauderdale, Florida, United States

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Fort Myers, Florida, United States

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Largo, Florida, United States

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Orlando, Florida, United States

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Atlanta, Georgia, United States

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Augusta, Georgia, United States

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Harvey, Illinois, United States

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West Des Moines, Iowa, United States

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Shawnee Mission, Kansas, United States

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Wichita, Kansas, United States

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Baltimore, Maryland, United States

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Hagerstown, Maryland, United States

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Peabody, Massachusetts, United States

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Worcester, Massachusetts, United States

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Minneapolis, Minnesota, United States

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Lawrenceville, New Jersey, United States

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New York, New York, United States

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Syracuse, New York, United States

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Asheville, North Carolina, United States

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Charlotte, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Cleveland, Ohio, United States

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Cleveland, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Greenville, South Carolina, United States

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West Columbia, South Carolina, United States

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Rapid City, South Dakota, United States

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Nashville, Tennessee, United States

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Austin, Texas, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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McAllen, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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Salt Lake City, Utah, United States

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Richmond, Virginia, United States

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Virginia Beach, Virginia, United States

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Bellevue, Washington, United States

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Córdoba, , Argentina

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Santa Fe, , Argentina

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East Melbourne, , Australia

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Malvern, , Australia

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Nedlands, , Australia

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Parramatta, , Australia

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Sydney, , Australia

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Westmead, , Australia

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Bogotá, , Colombia

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Cali, , Colombia

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Medellín, , Colombia

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Aalborg, , Denmark

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Aarhus C, , Denmark

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Glostrup Municipality, , Denmark

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Odense, , Denmark

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Roskilde, , Denmark

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Créteil, , France

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Lyon, , France

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Lyon, , France

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Marseille, , France

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Paris, , France

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Paris, , France

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Paris, , France

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Paris, , France

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Rouen, , France

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Strasbourg, , France

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Tours, , France

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Aachen, , Germany

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Bonn, , Germany

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Cologne, , Germany

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Freiburg im Breisgau, , Germany

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Göttingen, , Germany

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Hamburg, , Germany

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Heidelberg, , Germany

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Karlsruhe, , Germany

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Kiel, , Germany

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Leipzig, , Germany

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Lübeck, , Germany

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Mainz, , Germany

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München, , Germany

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München, , Germany

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Münster, , Germany

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Münster, , Germany

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Tübingen, , Germany

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Budapest, , Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Debrecen, , Hungary

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Magyarszék, , Hungary

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Pécs, , Hungary

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Szeged, , Hungary

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Haifa, , Israel

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Jerusalem, , Israel

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Kfar Saba, , Israel

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Petah Tikva, , Israel

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Rehovot, , Israel

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Tel Aviv, , Israel

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Barcelona, , Spain

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Bilbao, , Spain

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Las Palmas, , Spain

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Navarro, , Spain

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Sant Cugat del Vallès, , Spain

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Valencia, , Spain

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Ankara, , Turkey (Türkiye)

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Izmir, , Turkey (Türkiye)

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Izmir, , Turkey (Türkiye)

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Countries

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United States Argentina Australia Colombia Denmark France Germany Hungary Israel Spain Turkey (Türkiye)

References

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Park EJ, Choi J, Lee KC, Na DH. Emerging PEGylated non-biologic drugs. Expert Opin Emerg Drugs. 2019 Jun;24(2):107-119. doi: 10.1080/14728214.2019.1604684. Epub 2019 Apr 19.

Reference Type DERIVED
PMID: 30957581 (View on PubMed)

Other Identifiers

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OPH1003

Identifier Type: -

Identifier Source: org_study_id

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