An Open Label Study to Examine the Effects of DAS181 Administered by Dry Powder Inhaler (DPI) or Nebulized Formulation in Immunocompromised Subjects With Parainfluenza (PIV) Infection

NCT ID: NCT01924793

Last Updated: 2017-07-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

23 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-08-31

Study Completion Date

2017-05-31

Brief Summary

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This protocol will seek to enroll up to 60 immunocompromised subjects diagnosed with parainfluenza infection.

All subjects will have additional PK and Immunogenicity blood samples collected.

Detailed Description

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The study will investigate the safety, tolerability, clinical and virologic effect of DAS1814 for the treatment of PIV infections in up to 60 immunocompromised patients with no other treatment options.

Eligible immunocompromised patients positively diagnosed with PIV infection will receive DAS181 by DPI or Nebulized formulation.

DPI: 10 mg DAS181 will be administered for seven (7) consecutive days for up to a total cumulative dose of 70mg.

Nebulized: DAS181 F02 formulation in solution will be administered for seven (7) consecutive days for up to a total cumulative dose of 28.9 mg.

Assessment of viral shedding and viral resistance testing will be performed on collected viral load samples. Blood samples will be obtained to evaluate safety at each scheduled visit.

Routine safety monitoring (including Adverse Event (AE) reporting, clinical laboratory tests, vital signs, electrocardiogram (ECG) and )2 levels) will be conducted in all subjects. A final safety assessment will occur at Day 28 (+/- 2 days) after enrollment/first dose of study drug. Survival, diary cards, and quality of life will be collected at Day 60 and 90. PK will be collected at each visit on all subjects from baseline/visit 2 to visit 11/Day 28. Immunogenicity samples will be collected at selected time points in all subjects.

Conditions

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Parainfluenza

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Formulation of DAS181-F02 Dry Powder in Bulk

The DAS181-F02 nebulized formulation includes 10mL of normal saline to prepare a liquid solution referred to as DAS181-F02 nebulized.

Dry Powder Inhaled Dose:

Non-ventilated subjects, capable of using a cyclohaler, will be treated by Dry Powder Inhalation. Each subject will receive a targeted daily dose of 10mg for 7 days for a total of 70mg of DAS181-F02. If a subject requires ventilation, the subject will be allowed to continue dosing following the Nebulized formulation instruction.

Group Type EXPERIMENTAL

DAS181-F02 Dry Powder in Bulk

Intervention Type DRUG

Administered via DPI

Nebulized Formulation Inhaled Dose

Subjects unable to use the Dry Powder Inhaler (as determined by site Investigator) on continuous positive airway pressure (CPAP), Bi-level positive airway pressure (BIPAP) or requiring mechanical ventilation will be treated by Nebulized formulation. The subject will remain on the nebulized formulation for the duration of the study regardless of ventilation status. DAS-F02 10 mg will be utilized to prepare the nebulized solution per the Study Reference Manual.

Multiple methods (T piece, face mask, direct to ET tube) will be allowed for the nebulized dose administration. Detailed specification for nebulized dose administration will be defined in the Study Reference Manual.

Group Type EXPERIMENTAL

DAS181-F02 Nebulized Formulation Inhaled Dose

Intervention Type DRUG

Administered via Nebulizer

Interventions

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DAS181-F02 Dry Powder in Bulk

Administered via DPI

Intervention Type DRUG

DAS181-F02 Nebulized Formulation Inhaled Dose

Administered via Nebulizer

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Age ≥12 years
2. Able to provide informed consent or child assent with parental consent
3. Immunocompromised, as defined by one of the following:

* Allogeneic hematopoietic cell transplantation (HCT)
* Lung or lung-heart transplantation
* Patients treated with chemotherapy for hematologic malignancies or autologous HCT
4. Confirmed Parainfluenza virus by nasopharyngeal swab or tracheal aspirate for one of the following:

* Respiratory virus panel
* DFA
* Qualitative/quantitative RT-PCR test for parainfluenza virus performed at the local laboratory (a confirmatory PCR test will be done at the central lab but is not required to start the patient on study).
5. Female subjects of child-bearing potential who are capable of conception must be:

post-menopausal (one year or greater without menses), surgically incapable of childbearing, or practicing two effective methods of birth control. Acceptable methods include intrauterine device, spermicide, barrier, male partner surgical sterilization and hormonal contraception. A female subject must agree to practice two acceptable methods of birth control during the 28 day study period. Abstinence is not an acceptable method of contraception. All reproductive female subjects must have a negative serum pregnancy test during the screening visit.
6. Male subjects must agree to use medically accepted form of contraception during the 28 day study period.

Exclusion Criteria

1. Psychiatric or cognitive illness or recreational drug/alcohol use that, in the opinion of the principal investigator, would affect patient safety and/or compliance.
2. Any significant finding in the patient's medical history or physical examination that, in the opinion of the investigator, would affect patient safety, ability to use the dry powder inhaler or compliance with the dosing schedule.
3. Subjects currently treated with oral, aerosolized or IV ribavirin
4. Subjects taking any investigational drug used to research or treat PIV
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ansun Biopharma, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Ron Moss, MD, CEO

Role: STUDY_CHAIR

Ansun Biopharma, Inc.

Locations

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City of Hope

Duarte, California, United States

Site Status

Children's Hospital of Orange County

Orange, California, United States

Site Status

Stanford University Medical Center

Palo Alto, California, United States

Site Status

University of Chicago

Chicago, Illinois, United States

Site Status

Indiana Blood and Marrow Transplantation

Indianapolis, Indiana, United States

Site Status

University of Kansas Cancer Center

Kansas City, Kansas, United States

Site Status

John Hopkins University School of Medicine

Baltimore, Maryland, United States

Site Status

Brigham & Women's Hospital

Boston, Massachusetts, United States

Site Status

University of Minnesota, School of Medicine

Minneapolis, Minnesota, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status

Weill Cornell Medical College/New York Presbyterian Hospital

New York, New York, United States

Site Status

Weill Cornell Medical College-Peds

New York, New York, United States

Site Status

Duke University

Durham, North Carolina, United States

Site Status

The Ohio State University Wexner Medical Center

Columbus, Ohio, United States

Site Status

University of Oklahoma

Oklahoma City, Oklahoma, United States

Site Status

Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

St. Jude Children's Research Hospital

Memphis, Tennessee, United States

Site Status

The University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Seattle Children's Hospital

Seattle, Washington, United States

Site Status

Fred Hutchinson Cencer Research Center

Seattle, Washington, United States

Site Status

Countries

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United States

Other Identifiers

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DAS181-2-06

Identifier Type: -

Identifier Source: org_study_id

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