Beraprost-314d Added-on to Tyvaso® (BEAT)

NCT ID: NCT01908699

Last Updated: 2020-08-03

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

273 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-05-31

Study Completion Date

2019-02-19

Brief Summary

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This is a multicenter, double-blind, randomized, placebo-controlled Phase 3 study, to assess the efficacy and safety of BPS-314d-MR when added-on to inhaled treprostinil (Tyvaso®)in patients with pulmonary arterial hypertension.

Patients new to Tyvaso, will enter a run-in period on inhaled treprostinil until 90 days of experience is achieved to ensure drug tolerability before enrolling in the study.

Treatment groups consist of one active and one placebo group. Subjects will be randomly allocated in a 1:1 ratio to one of the two treatment groups.

Detailed Description

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Conditions

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Pulmonary Arterial Hypertension

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Beraprost Sodium 314d Modified Release Tablets

Available as 15 μg tablets for oral, 1 or 2 tablets four times daily (QID) administration.

Group Type EXPERIMENTAL

Beraprost Sodium 314d Modified Release Tablets

Intervention Type DRUG

Available as 15 μg tablets for oral, 1 or 2 tablets four times daily (QID) administration

Placebo

Placebo tablets, which are identical in size and appearance to those containing BPS-314d-MR.

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

Placebo tablets, which are identical in size and appearance to those containing BPS-314d-MR

Interventions

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Beraprost Sodium 314d Modified Release Tablets

Available as 15 μg tablets for oral, 1 or 2 tablets four times daily (QID) administration

Intervention Type DRUG

Placebo

Placebo tablets, which are identical in size and appearance to those containing BPS-314d-MR

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Male or female, age 18 to 80 years (inclusive).
2. Established diagnosis of pulmonary arterial hypertension that is either idiopathic or familial PAH, collagen vascular disease associated PAH, PAH associated with HIV infection, PAH induced by anorexigens/toxins, or PAH associated with repaired congenital systemic-to-pulmonary shunts (repaired ≥1 years).
3. If HIV positive, has a CD4 lymphocyte count ≥200 cells/mm3 within 30 days of Baseline Visit and is receiving current standard of care antiretroviral or other effective medication.
4. At the Screening Visit, WHO functional class III or IV and who have declining or unsatisfactory clinical response to current PAH therapy.
5. At the Baseline Visit, WHO functional class III or IV and who have declining or unsatisfactory clinical response to inhaled treprostinil therapy.
6. Able to walk unassisted (oxygen use allowed).
7. A 6-Minute Walk distance (6MWD) of ≥ 100 meters at the Screening Visit.
8. Previous (within five years prior to the Baseline Visit) right heart cardiac catheterization (RHC) with findings consistent with PAH, specifically mean Pulmonary Arterial Pressure (PAPm) ≥25 mmHg (at rest), Pulmonary Capillary Wedge Pressure (PCWP) (or left ventricular end diastolic pressure) ≤15 mmHg, and Pulmonary Vascular Resistance (PVR) \>3 mmHg/L/min.
9. Echocardiography excluding any clinically significant left heart disease (e.g. left sided valve disease, wall motion abnormality suggesting of myocardial infarction, left ventricular hypertrophy, etc).
10. Pulmonary function tests conducted within 12 months before or during the Screening period to confirm the following:

1. Total lung capacity (TLC) is at least 60% (predicted value) and
2. Forced expiratory volume at one second (FEV1) of at least 50% (predicted value).
11. Subjects receiving additional FDA approved PAH therapies must be stable on their current dose for at least 30 days prior to the Baseline Visit, apart from modification of anticoagulant or diuretic dosages.
12. Must have completed 90 days of uninterrupted inhaled treprostinil treatment and received a stable dose of inhaled treprostinil for at least 30 days prior to Baseline to be eligible for randomization into the study.
13. Women of child-bearing potential (defined as less than 1 year post-menopausal and not surgically sterile) must be practicing abstinence or using two highly effective methods of contraception (defined as a method of birth control that result in a low failure rate, i.e., less than 1% per year, such as approved hormonal contraceptives, barrier methods \[such as a condom or diaphragm\] used with a spermicide, or an intrauterine device). Subject must have a negative pregnancy test at the Screening and Baseline Visits.
14. Willing and able to comply with study requirements and restrictions.

4. History of interstitial lung disease, unless subject has collagen vascular disease and has had pulmonary function testing conducted within 12 months of the Baseline Visit demonstrating a total lung capacity ≥60% of predicted.
5. Has active hemorrhagic condition (e.g., upper digestive tract hemorrhage, hemoptysis, etc), or has a pre-existing condition that, in the Investigator's judgment, may increase the risk for developing hemorrhage during the study (e.g., hemophilia). Transient hemorrhage (e.g., epistaxis, normal menstrual bleeding, gingival bleeding, hemorrhoidal bleeding, etc) will not preclude enrollment.
6. Has received any investigational drug, device or therapy within 30 days prior to the Baseline Visit or is scheduled to receive another investigational drug, device or therapy during the course of the study.
7. Has any musculoskeletal disease or any other disease that would significantly limit ambulation.
8. Has any form of unrepaired or recently repaired (\< 1 year) congenital systemic-to-pulmonary shunt other than patent foramen ovale.
9. Evidence of significant coronary arterial disease with symptoms, such as angina.
10. Left sided myocardial disease as evidenced by left ventricular ejection fraction \< 40%, or shortening fraction \<22%.
11. Has creatinine clearance \<30 (using the Cockroft-Gault formula) or requires hemodialysis.
12. Has Childs-Pugh class C liver cirrhosis.
13. Has had previous atrial septostomy.
14. Any other clinically significant illness or abnormal laboratory values (measured during the Screening period) that, in the opinion of the Investigator, might put the subject at risk of harm during the study or might adversely affect the interpretation of the study data.
15. Anticipated survival less than 1 year due to concomitant disease.

The Sponsor recognizes that the pulmonary hypertension population is complex and diverse. In order to facilitate enrollment of appropriate subjects to this pivotal trial, Investigators are strongly encouraged to contact the medical director or study team to discuss potential study subjects who have comorbid conditions before enrollment into this study. See Appendix 9 for additional details.

No waivers to entry criteria are allowable in this study. Subjects who are initially ineligible for this study may be reassessed for eligibility after consultation with the Sponsor.

Exclusion Criteria

Patients who meet any of the following criteria will be excluded from the study:

1. Pregnant or lactating.
2. Has previous experience with beraprost or BPS-314d (i.e., BPS-IR, BPS-MR or BPS-314d- MR).
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Lung Biotechnology PBC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Cedars-Sinai Medical Center Heart Institute

Beverly Hills, California, United States

Site Status

Allianz Research Institute Inc.

Fountain Valley, California, United States

Site Status

University of California San Francisco - Fresno

Fresno, California, United States

Site Status

University of California - San Diego

La Jolla, California, United States

Site Status

University of California Los Angeles

Los Angeles, California, United States

Site Status

Keck Medical Center of USC

Los Angeles, California, United States

Site Status

Veterans Affairs Greater Los Angeles Healthcare System

Los Angeles, California, United States

Site Status

Center for Advanced Pulmonary Medicine

Rancho Mirage, California, United States

Site Status

University of California - San Francisco

San Francisco, California, United States

Site Status

Cottage Pulmonary Hypertension Center

Santa Barbara, California, United States

Site Status

Stanford University

Stanford, California, United States

Site Status

Harbor-UCLA Medical Center

Torrance, California, United States

Site Status

University of Colorado Denver

Aurora, Colorado, United States

Site Status

Aurora Denver Cardiology Associates

Denver, Colorado, United States

Site Status

South Denver Cardiology Associates P.C.

Littleton, Colorado, United States

Site Status

Yale School of Medicine

New Haven, Connecticut, United States

Site Status

Bay Area Cardiology Associates, P.A.

Brandon, Florida, United States

Site Status

Florida Lung, Asthma, and Sleep Institute

Celebration, Florida, United States

Site Status

University of Florida

Gainesville, Florida, United States

Site Status

University of Florida College of Medicine

Jacksonville, Florida, United States

Site Status

Mayo Clinic

Jacksonville, Florida, United States

Site Status

Florida Hospital

Orlando, Florida, United States

Site Status

Orlando Health Heart Institute

Orlando, Florida, United States

Site Status

South Miami Heart Specialists

South Miami, Florida, United States

Site Status

Cleveland Clinic Florida

Weston, Florida, United States

Site Status

Emory University

Atlanta, Georgia, United States

Site Status

Pulmonary & Critical Care of Atlanta

Atlanta, Georgia, United States

Site Status

Georgia Clinical Research

Austell, Georgia, United States

Site Status

Gwinnett Biomedical Research

Lawrenceville, Georgia, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

University of Chicago Medicine

Chicago, Illinois, United States

Site Status

Advocate Health and Hospitals Corporation

Oakbrook Terrace, Illinois, United States

Site Status

Indiana University - Health Physicians

Carmel, Indiana, United States

Site Status

University of Iowa

Iowa City, Iowa, United States

Site Status

Kentuckiana Pulmonary Associates

Louisville, Kentucky, United States

Site Status

University of Louisville Department of Medicine

Louisville, Kentucky, United States

Site Status

John Ochsner Heart & Vascular Institute

New Orleans, Louisiana, United States

Site Status

Maine Medical Center

Portland, Maine, United States

Site Status

University of Maryland

Baltimore, Maryland, United States

Site Status

Johns Hopkins University School of Medicine

Baltimore, Maryland, United States

Site Status

Brigham and Women's Hospital

Boston, Massachusetts, United States

Site Status

Beaumont Health Systems

Troy, Michigan, United States

Site Status

Rutgers University Hospital

Newark, New Jersey, United States

Site Status

Albany Medical College

Albany, New York, United States

Site Status

Winthrop University Hospital

Mineola, New York, United States

Site Status

Beth Israel Medical Center

New York, New York, United States

Site Status

Mount Sinai Medical Center

New York, New York, United States

Site Status

Columbia University Medical Center

New York, New York, United States

Site Status

Pulmonary Health Physicians, PC

Syracuse, New York, United States

Site Status

University of North Carolina, Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

University of Cincinnati

Cincinnati, Ohio, United States

Site Status

University Hospitals Case Medical Center

Cleveland, Ohio, United States

Site Status

Ohio State University

Columbus, Ohio, United States

Site Status

University of Toledo Medical Center

Toledo, Ohio, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

Thomas Jefferson University

Philadelphia, Pennsylvania, United States

Site Status

Allegheny General Hospital

Pittsburgh, Pennsylvania, United States

Site Status

UPMC Presbyterian Hospital

Pittsburgh, Pennsylvania, United States

Site Status

Rhode Island Hospital

Providence, Rhode Island, United States

Site Status

Anderson Pharmaceutical Research

Anderson, South Carolina, United States

Site Status

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status

Houston Methodist Hospital

Houston, Texas, United States

Site Status

Methodist Healthcare Clinical Trials Office

San Antonio, Texas, United States

Site Status

Scott & White Memorial Hospital

Temple, Texas, United States

Site Status

Sentara Norfolk General Hospital

Norfolk, Virginia, United States

Site Status

University of Washington Medical Center

Seattle, Washington, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Soroka Medical Center

Beersheba, , Israel

Site Status

The Lady Davis Carmel Medical Center

Haifa, , Israel

Site Status

Hadassah University Hospital - Ein Kerem

Jerusalem, , Israel

Site Status

Rabin Medical Center-Beilinson Campus

Petah Tikva, , Israel

Site Status

Chaim Sheba Medical Center

Ramat Gan, , Israel

Site Status

Kaplan Medical Center

Rehovot, , Israel

Site Status

Countries

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United States Israel

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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BPS-314d-MR-PAH-302

Identifier Type: -

Identifier Source: org_study_id

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