A Study to Evaluate Efficacy and Safety of Oral BAY63-2521 in Patients With Pulmonary Arterial Hypertension (PAH)

NCT ID: NCT00810693

Last Updated: 2023-11-22

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

445 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-12-17

Study Completion Date

2012-05-14

Brief Summary

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The aim of the study is to assess the efficacy and safety of different doses of BAY63-2521 given orally for 12 weeks, in patients with symptomatic Pulmonary Arterial Hypertension (PAH).

Detailed Description

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Conditions

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Pulmonary Hypertension

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Riociguat (Adempas, BAY63-2521) up to 2.5 mg_IDT

Participants received Riociguat orally as a film-coated tablet up to 2.5mg three times daily (tid) (titration between 1.0 mg and 2.5 mg tid based on an individual dose titration (IDT) scheme) for 12 weeks

Group Type EXPERIMENTAL

Riociguat (Adempas, BAY63-2521)

Intervention Type DRUG

BAY63-2521: 1mg tid - 2.5mg tid orally for 12 weeks

Riociguat (Adempas, BAY63-2521) up to 1.5 mg_IDT

Participants received Riociguat orally as a film-coated tablet up to 1.5mg three times daily (tid) (titration between 1.0 mg and 1.5 mg tid based on an individual dose titration (IDT) scheme) for 12 weeks

Group Type EXPERIMENTAL

Riociguat (Adempas, BAY63-2521)

Intervention Type DRUG

BAY63-2521: 1.5mg tid orally for 12 weeks

Placebo

Participants received Placebo orally as a film-coated tablet three times daily (tid) for 12 weeks

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching Placebo tid orally for 12 weeks

Interventions

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Riociguat (Adempas, BAY63-2521)

BAY63-2521: 1mg tid - 2.5mg tid orally for 12 weeks

Intervention Type DRUG

Riociguat (Adempas, BAY63-2521)

BAY63-2521: 1.5mg tid orally for 12 weeks

Intervention Type DRUG

Placebo

Matching Placebo tid orally for 12 weeks

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Male and female patients with symptomatic PAH (Idiopathic, Familial, Associated PAH due to connective tissue disease, congenital heart disease, portal hypertension with liver cirrhosis, or due to anorexigen or amphetamine use)
* Treatment naive patients and patients pre-treated with an Endothelin Antagonist or a Prostacyclinanalogue (except I.V.).
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bayer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bayer Study Director

Role: STUDY_DIRECTOR

Bayer

Locations

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Tucson, Arizona, United States

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La Jolla, California, United States

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Los Angeles, California, United States

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Sacramento, California, United States

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Aurora, Colorado, United States

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Louisville, Kentucky, United States

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Boston, Massachusetts, United States

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Boston, Massachusetts, United States

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Omaha, Nebraska, United States

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New York, New York, United States

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Cincinnati, Ohio, United States

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Cleveland, Ohio, United States

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Columbus, Ohio, United States

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Fairfield, Ohio, United States

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Providence, Rhode Island, United States

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Dallas, Texas, United States

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El Paso, Texas, United States

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Houston, Texas, United States

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Capital Federal, , Argentina

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Darlinghurst, New South Wales, Australia

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New Lambton Heights, New South Wales, Australia

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Auchenflower, Queensland, Australia

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Herston, Queensland, Australia

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Royal Hobart Hospital

Hobart, Tasmania, Australia

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Prahran, Victoria, Australia

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Linz, Upper Austria, Austria

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Innsbruck, , Austria

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Vienna, , Austria

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Bruxelles - Brussel, , Belgium

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Leuven, , Belgium

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Porto Alegre, Rio Grande do Sul, Brazil

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São Paulo, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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Rio de Janeiro, , Brazil

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Calgary, Alberta, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Guangzhou, Guangdong, China

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Beijing, , China

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Beijing, , China

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Shanghai, , China

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Shanghai, , China

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Prague, , Czechia

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Aarhus N, , Denmark

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Besançon, , France

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Brest, , France

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Grenoble, , France

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Lille, , France

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Montpellier, , France

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Nice, , France

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Pessac, , France

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Rouen, , France

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Heidelberg, Baden-Wurttemberg, Germany

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München, Bavaria, Germany

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Giessen, Hesse, Germany

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Hanover, Lower Saxony, Germany

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Greifswald, Mecklenburg-Vorpommern, Germany

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Cologne, North Rhine-Westphalia, Germany

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Homburg, Saarland, Germany

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Dresden, Saxony, Germany

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Leipzig, Saxony, Germany

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Chaïdári, , Greece

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Petah Tikva, , Israel

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Trieste, Friuli Venezia Giulia, Italy

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Rome, Lazio, Italy

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Milan, Lombardy, Italy

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Pavia, Lombardy, Italy

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Turin, Piedmont, Italy

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Nagoya, Aichi-ken, Japan

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Yoshida, Fukui, Japan

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Kobe, Hyōgo, Japan

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Toride, Ibaraki, Japan

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Tsukuba, Ibaraki, Japan

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Kanazawa, Ishikawa-ken, Japan

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Sagamihara, Kanagawa, Japan

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Sendai, Miyagi, Japan

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Tomigusuku, Okinawa, Japan

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Bunkyo-ku, Tokyo, Japan

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Mitaka, Tokyo, Japan

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Ōta-ku, Tokyo, Japan

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Shinjuku-ku, Tokyo, Japan

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Hiroshima, , Japan

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Okayama, , Japan

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Guadalajara, Jalisco, Mexico

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Guadalajara, Jalisco, Mexico

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Monterrey, Nuevo León, Mexico

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Culiacán, Sinaloa, Mexico

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Mexico City, , Mexico

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Querétaro, , Mexico

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Christchurch, , New Zealand

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Otwock, , Poland

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Coimbra, , Portugal

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Lisbon, , Portugal

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Lisbon, , Portugal

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Porto, , Portugal

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Moscow, , Russia

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Saint Petersburg, , Russia

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Singapore, , Singapore

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Singapore, , Singapore

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Seoul, Seoul Teugbyeolsi, South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Barcelona, , Spain

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Barcelona, , Spain

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Seville, , Spain

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Linköping, , Sweden

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Lund, , Sweden

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Umeå, , Sweden

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Zurich, , Switzerland

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Kaohsiung City, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Bangkok, , Thailand

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Chiang Mai, , Thailand

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Ankara, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Izmir, , Turkey (Türkiye)

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Cambridge, Cambridgeshire, United Kingdom

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Clydebank, West Dunbartonshire, United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Countries

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United States Argentina Australia Austria Belgium Brazil Canada China Czechia Denmark France Germany Greece Israel Italy Japan Mexico New Zealand Poland Portugal Russia Singapore South Korea Spain Sweden Switzerland Taiwan Thailand Turkey (Türkiye) United Kingdom

References

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Archer SL. Riociguat for pulmonary hypertension--a glass half full. N Engl J Med. 2013 Jul 25;369(4):386-8. doi: 10.1056/NEJMe1306684. No abstract available.

Reference Type RESULT
PMID: 23883383 (View on PubMed)

Ghofrani HA, Galie N, Grimminger F, Grunig E, Humbert M, Jing ZC, Keogh AM, Langleben D, Kilama MO, Fritsch A, Neuser D, Rubin LJ; PATENT-1 Study Group. Riociguat for the treatment of pulmonary arterial hypertension. N Engl J Med. 2013 Jul 25;369(4):330-40. doi: 10.1056/NEJMoa1209655.

Reference Type RESULT
PMID: 23883378 (View on PubMed)

Rosenkranz S, Ghofrani HA, Beghetti M, Ivy D, Frey R, Fritsch A, Weimann G, Saleh S, Apitz C. Riociguat for pulmonary arterial hypertension associated with congenital heart disease. Heart. 2015 Nov;101(22):1792-9. doi: 10.1136/heartjnl-2015-307832. Epub 2015 Jul 1.

Reference Type RESULT
PMID: 26135803 (View on PubMed)

Wang C, Jing ZC, Huang YG, Zhou DX, Liu ZH, Meier C, Nikkho S, Curram J, Zhang P, He JG. Riociguat for the treatment of pulmonary hypertension: Chinese subgroup analyses and comparison. Heart Asia. 2016 May 17;8(1):74-82. doi: 10.1136/heartasia-2015-010712. eCollection 2016.

Reference Type RESULT
PMID: 27326239 (View on PubMed)

Ghofrani HA, Humbert M, Langleben D, Schermuly R, Stasch JP, Wilkins MR, Klinger JR. Riociguat: Mode of Action and Clinical Development in Pulmonary Hypertension. Chest. 2017 Feb;151(2):468-480. doi: 10.1016/j.chest.2016.05.024. Epub 2016 Jun 2.

Reference Type RESULT
PMID: 27263466 (View on PubMed)

Benza RL, Boucly A, Farber HW, Frost AE, Ghofrani HA, Hoeper MM, Lambelet M, Rahner C, Bansilal S, Nikkho S, Meier C, Sitbon O. Change in REVEAL Lite 2 risk score predicts outcomes in patients with pulmonary arterial hypertension in the PATENT study. J Heart Lung Transplant. 2022 Mar;41(3):411-420. doi: 10.1016/j.healun.2021.10.013. Epub 2021 Oct 28.

Reference Type RESULT
PMID: 34848133 (View on PubMed)

Benza RL, Farber HW, Frost AE, Ghofrani HA, Corris PA, Lambelet M, Nikkho S, Meier C, Hoeper MM. Application of the REVEAL risk score calculator 2.0 in the CHEST study. Respir Med. 2022 Apr-May;195:106783. doi: 10.1016/j.rmed.2022.106783. Epub 2022 Mar 1.

Reference Type RESULT
PMID: 35256218 (View on PubMed)

Benza RL, Ghofrani HA, Grunig E, Hoeper MM, Jansa P, Jing ZC, Kim NH, Langleben D, Simonneau G, Wang C, Busse D, Meier C, Ghio S. Effect of riociguat on right ventricular function in patients with pulmonary arterial hypertension and chronic thromboembolic pulmonary hypertension. J Heart Lung Transplant. 2021 Oct;40(10):1172-1180. doi: 10.1016/j.healun.2021.06.020. Epub 2021 Jul 10.

Reference Type DERIVED
PMID: 34353714 (View on PubMed)

Humbert M, Coghlan JG, Ghofrani HA, Grimminger F, He JG, Riemekasten G, Vizza CD, Boeckenhoff A, Meier C, de Oliveira Pena J, Denton CP. Riociguat for the treatment of pulmonary arterial hypertension associated with connective tissue disease: results from PATENT-1 and PATENT-2. Ann Rheum Dis. 2017 Feb;76(2):422-426. doi: 10.1136/annrheumdis-2015-209087. Epub 2016 Jul 25.

Reference Type DERIVED
PMID: 27457511 (View on PubMed)

Saleh S, Becker C, Frey R, Muck W. Population pharmacokinetics and the pharmacokinetic/pharmacodynamic relationship of riociguat in patients with pulmonary arterial hypertension or chronic thromboembolic pulmonary hypertension. Pulm Circ. 2016 Mar;6(Suppl 1):S86-96. doi: 10.1086/685404.

Reference Type DERIVED
PMID: 27162632 (View on PubMed)

Related Links

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https://clinicaltrials.bayer.com/study/12934

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Other Identifiers

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2008-003482-68

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

12934

Identifier Type: -

Identifier Source: org_study_id