Phase 2 Study to Evaluate LUM001 in Combination With Ursodeoxycholic Acid in Patients With Primary Biliary Cirrhosis

NCT ID: NCT01904058

Last Updated: 2019-03-27

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

66 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-08-31

Study Completion Date

2015-04-30

Brief Summary

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The study is a randomized, double-blind, placebo-controlled, multicenter study. It is a 13-week Phase 2 study in adults with primary biliary cirrhosis designed to compare the effect of daily dosing with UDCA in combination with LUM001 or placebo.

Detailed Description

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Conditions

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PBC Primary Biliary Cirrhosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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LUM001 and Ursodeoxycholic Acid (UDCA)

Administered orally once daily

Group Type EXPERIMENTAL

LUM001

Intervention Type DRUG

Ursodeoxycholic Acid

Intervention Type DRUG

Placebo and Ursodeoxycholic Acid (UDCA)

Administered orally once daily

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Ursodeoxycholic Acid

Intervention Type DRUG

Interventions

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LUM001

Intervention Type DRUG

Placebo

Intervention Type DRUG

Ursodeoxycholic Acid

Intervention Type DRUG

Other Intervention Names

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UDCA

Eligibility Criteria

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Inclusion Criteria

1. Diagnosis of Primary Biliary Cirrhosis
2. Moderate to severe pruritus
3. Taking ursodeoxycholic acid (UDCA) for at least 6 months, or unable to tolerate UDCA
4. Ability to understand and willingness to sign informed consent prior to initiation of any study procedures

Exclusion Criteria

1. History or presence of other concomitant significant liver disease
2. Liver transplant
3. Known HIV infection
4. Women who are pregnant or lactating
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Mirum Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Mirum

Locations

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Scripps Clinic

La Jolla, California, United States

Site Status

University of California at Davis

Sacramento, California, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status

Indiana University

Indianapolis, Indiana, United States

Site Status

University of Louisville

Louisville, Kentucky, United States

Site Status

Henry Ford Health System

Detroit, Michigan, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Minnesota Gastroenterology

Saint Paul, Minnesota, United States

Site Status

St. Louis University

St Louis, Missouri, United States

Site Status

Weill Cornell Medical College

New York, New York, United States

Site Status

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status

Advanced Liver Therapies at St. Lukes Episcopal Hospital

Houston, Texas, United States

Site Status

University of Utah Health Science Center

Salt Lake City, Utah, United States

Site Status

Liver Institute of Virginia

Newport News, Virginia, United States

Site Status

Hunter Holmes McGuire VA Medical Center

Richmond, Virginia, United States

Site Status

University of Washington Harborview Medical Center

Seattle, Washington, United States

Site Status

University Health Network, Toronto Western Hospital

Toronto, Ontario, Canada

Site Status

University of Birmingham

Birmingham, England, United Kingdom

Site Status

Royal Liverpool & Broadgreen University Hospital

Liverpool, England, United Kingdom

Site Status

Newcastle University

Newcastle upon Tyne, England, United Kingdom

Site Status

Oxford University Hospitals (John Radcliffe)

Oxford, England, United Kingdom

Site Status

Royal Free Hospital

London, , United Kingdom

Site Status

Imperial College London St Mary's Hospital

London, , United Kingdom

Site Status

Countries

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United States Canada United Kingdom

Related Links

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Other Identifiers

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2013-000482-36

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

LUM001-201

Identifier Type: -

Identifier Source: org_study_id

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