A Global Study to Compare the Effects of Fulvestrant and Arimidex in a Subset of Patients With Breast Cancer.

NCT ID: NCT01602380

Last Updated: 2026-01-12

Study Results

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Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

462 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-10-17

Study Completion Date

2027-08-06

Brief Summary

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The purpose of the study is to compare how treatment with Fulvestrant (FASLODEX) or Anastrozole (ARIMIDEX) effects disease progression for women with locally advanced or metastatic breast cancer who have not had prior hormonal treatment.

Detailed Description

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A Randomised, Double-blind, Parallel-group, Multicentre, Phase III Study to Compare the Efficacy and Tolerability of Fulvestrant (FASLODEX) 500 mg with Anastrozole (ARIMIDEX) 1 mg as Hormonal Treatment for Postmenopausal Women with Hormone Receptor-Positive Locally Advanced or Metastatic Breast Cancer Who Have Not Previously Been Treated With Any Hormonal Therapy.

Conditions

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Hormone Receptor Positive Breast Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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faslodex+placebo

Blinded: Fulvestrant 500mg intramuscular injection (2x250mg) plus dummy Anastrozole tablets

Group Type EXPERIMENTAL

faslodex 500mg

Intervention Type DRUG

2 x intramuscular injections at day 1, 14, 28 and every 28 days thereafter

arimidex dummy

Intervention Type DRUG

oral tablet 1 daily

arimidex +placebo

Blinded: Anastrozole 1mg tablets plus dummy Fulvestrant intramuscular injection (2x0mg)

Group Type ACTIVE_COMPARATOR

arimidex 1mg

Intervention Type DRUG

oral tablet 1 daily

faslodex dummy

Intervention Type DRUG

2 x intramuscular injections at day 1, 14, 28 and every 28 days thereafter

Interventions

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faslodex 500mg

2 x intramuscular injections at day 1, 14, 28 and every 28 days thereafter

Intervention Type DRUG

arimidex 1mg

oral tablet 1 daily

Intervention Type DRUG

faslodex dummy

2 x intramuscular injections at day 1, 14, 28 and every 28 days thereafter

Intervention Type DRUG

arimidex dummy

oral tablet 1 daily

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Histological confirmation of breast cancer in post menopausal women (age \>=60). Positive hormone receptor status (ER +ve and/or PgR +ve) of primary or metastatic tumour tissue based on local laboratory assessment.
* EITHER locally advanced disease (1 line of chemotherapy allowed only if remain unsuitable for therapy of curative intent) OR Metastatic disease. (1 line of chemotherapy for breast cancer allowed only if subsequent evidence of further progressive disease)
* At least 1 lesion (measurable and/or non-measurable) that can be accurately assessed at baseline and is suitable for repeated assessment.
* Postmenopausal women, fulfilling 1 of:

* Prior bilateral oophorectomy
* Age \>60 years
* Age \< 60 years and amenorrheic for 12+months in the absence of chemotherapy, tamoxifen, toremifene, or ovarian suppression and FSH and oestradiol in the postmenopausal range

Exclusion Criteria

* Presence of life-threatening metastatic disease
* Any of:

* Extensive hepatic involvement
* involving brain or meninges
* symptomatic pulmonary lymph spread
* Discrete lung metastases are acceptable if respiratory function is not significantly compromised
* Prior systemic therapy for breast cancer other than one line of cytotoxic chemotherapy (the last dose of chemotherapy must have been received more than 28 days prior to randomisation)
* Radiation therapy if not completed within 28 days prior to randomisation (with the exception of radiotherapy given for control of bone pain, started prior to randomisation). Prior hormonal treatment for breast cancer.
* Current or prior malignancy within previous 3 years (other than breast cancer or adequately treated basal cell or squamous cell carcinoma of the skin or in situ carcinoma of the cervix).
Minimum Eligible Age

18 Years

Maximum Eligible Age

130 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Shankar S, MD

Role: STUDY_DIRECTOR

AstraZeneca

John Robertson, MD

Role: PRINCIPAL_INVESTIGATOR

Graduate Medicine and Health School, University of Nottingham, UK

Matthew Ellis, DM

Role: PRINCIPAL_INVESTIGATOR

Washington University School of Medicine, USA

Locations

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Modesto, California, United States

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Savannah, Georgia, United States

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Auburn, Maine, United States

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Worcester, Massachusetts, United States

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Detroit, Michigan, United States

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St Louis, Missouri, United States

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Lincoln, Nebraska, United States

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Somerset, New Jersey, United States

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Columbus, Ohio, United States

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Montgomery, Ohio, United States

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Memphis, Tennessee, United States

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Salt Lake City, Utah, United States

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La Rioja, , Argentina

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Mar del Plata, , Argentina

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Pergamino, , Argentina

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Rosario, , Argentina

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Porto Alegre, , Brazil

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Santo André, , Brazil

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Abbotsford, British Columbia, Canada

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Vancouver, British Columbia, Canada

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Kitchener, Ontario, Canada

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Thunder Bay, Ontario, Canada

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Montreal, Quebec, Canada

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Montreal, Quebec, Canada

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Chengdu, , China

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Dalian, , China

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Fuzhou, , China

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Guangzhou, , China

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Shanghai, , China

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Shenyang, , China

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Suzhou, , China

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Tianjin, , China

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Prague, , Czechia

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Příbram, , Czechia

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Avellino, , Italy

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Bari, , Italy

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Benevento, , Italy

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Catania, , Italy

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Genova, , Italy

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Pisa, , Italy

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Roma, , Italy

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Roma, , Italy

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Roma, , Italy

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Treviglio, , Italy

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Fukuoka, , Japan

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Hamamatsu, , Japan

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Kagoshima, , Japan

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Kumamoto, , Japan

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Matsuyama, , Japan

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Mitaka-shi, , Japan

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Nishinomiya-shi, , Japan

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Osaka, , Japan

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Sakaishi, , Japan

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Suita-shi, , Japan

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Mexico City, , Mexico

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Mérida, , Mexico

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Monterrey, , Mexico

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Monterrey, , Mexico

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Monterrey, , Mexico

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Katowice, , Poland

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Lodz, , Poland

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Lublin, , Poland

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Brăila, , Romania

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Craiova, , Romania

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Onești, , Romania

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Timișoara, , Romania

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Barnaul, , Russia

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Moscow, , Russia

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Omsk, , Russia

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Ryazan, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Tomsk, , Russia

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Bardejov, , Slovakia

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Bratislava, , Slovakia

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Bratislava, , Slovakia

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Trenčín, , Slovakia

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Cape Town, , South Africa

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Cape Town, , South Africa

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Cape Town, , South Africa

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Pietermaritzburg, , South Africa

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Pretoria, , South Africa

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Pretoria, , South Africa

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Madrid, , Spain

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Madrid, , Spain

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Pamplona, , Spain

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Pozuelo de Alarcón, , Spain

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Sabadell, , Spain

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Seville, , Spain

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Seville, , Spain

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Seville, , Spain

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Valencia, , Spain

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Valencia, , Spain

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Taichung, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Ankara, , Turkey (Türkiye)

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Gaziantep, , Turkey (Türkiye)

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Cherkasy, , Ukraine

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Dnipro, , Ukraine

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Donetsk, , Ukraine

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Ivano-Frankivsk, , Ukraine

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Kharkiv Region, , Ukraine

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Kyiv, , Ukraine

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Lviv, , Ukraine

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Mariupol, , Ukraine

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Uzhhorod, , Ukraine

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Vinnytsia, , Ukraine

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Airdrie, , United Kingdom

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Derby, , United Kingdom

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Stoke-on-Trent, , United Kingdom

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Countries

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United States Argentina Brazil Canada China Czechia Italy Japan Mexico Peru Poland Romania Russia Slovakia South Africa Spain Taiwan Turkey (Türkiye) Ukraine United Kingdom

References

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Robertson JFR, Shao Z, Noguchi S, Bondarenko I, Panasci L, Singh S, Subramaniam S, Ellis MJ. Fulvestrant Versus Anastrozole in Endocrine Therapy-Naive Women With Hormone Receptor-Positive Advanced Breast Cancer: Final Overall Survival in the Phase III FALCON Trial. J Clin Oncol. 2025 May;43(13):1539-1545. doi: 10.1200/JCO.24.00994. Epub 2025 Jan 7.

Reference Type DERIVED
PMID: 39772884 (View on PubMed)

Robertson JFR, Cheung KL, Noguchi S, Shao Z, Degboe A, Lichfield J, Thirlwell J, Fazal M, Ellis MJ. Health-related quality of life from the FALCON phase III randomised trial of fulvestrant 500 mg versus anastrozole for hormone receptor-positive advanced breast cancer. Eur J Cancer. 2018 May;94:206-215. doi: 10.1016/j.ejca.2018.02.026. Epub 2018 Mar 22.

Reference Type DERIVED
PMID: 29574365 (View on PubMed)

Robertson JFR, Bondarenko IM, Trishkina E, Dvorkin M, Panasci L, Manikhas A, Shparyk Y, Cardona-Huerta S, Cheung KL, Philco-Salas MJ, Ruiz-Borrego M, Shao Z, Noguchi S, Rowbottom J, Stuart M, Grinsted LM, Fazal M, Ellis MJ. Fulvestrant 500 mg versus anastrozole 1 mg for hormone receptor-positive advanced breast cancer (FALCON): an international, randomised, double-blind, phase 3 trial. Lancet. 2016 Dec 17;388(10063):2997-3005. doi: 10.1016/S0140-6736(16)32389-3. Epub 2016 Nov 29.

Reference Type DERIVED
PMID: 27908454 (View on PubMed)

Ellis MJ, Llombart-Cussac A, Feltl D, Dewar JA, Jasiowka M, Hewson N, Rukazenkov Y, Robertson JF. Fulvestrant 500 mg Versus Anastrozole 1 mg for the First-Line Treatment of Advanced Breast Cancer: Overall Survival Analysis From the Phase II FIRST Study. J Clin Oncol. 2015 Nov 10;33(32):3781-7. doi: 10.1200/JCO.2015.61.5831. Epub 2015 Sep 14.

Reference Type DERIVED
PMID: 26371134 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2011-006326-24

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

D699BC00001

Identifier Type: -

Identifier Source: org_study_id

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