A Study of the Experimental Drug BKM120 With Paclitaxel in Patients With HER2 Negative, Locally Advanced or Metastatic Breast Cancer, With or Without PI3K Activation

NCT ID: NCT01572727

Last Updated: 2017-03-09

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

416 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-08-31

Study Completion Date

2015-06-30

Brief Summary

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This study evaluated whether the addition of daily BKM120 to weekly paclitaxel was effective and safe in treating patients with HER2- locally advanced or metastatic breast cancer.

Detailed Description

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Based on the efficacy results at the time of the interim analyses, the DMC recommended stopping the study at Phase II during the interim as it met the protocol pre-specified futility criteria. Consequently, the Phase III portion of the study was not conducted.

Conditions

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Breast Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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BKM120 and paclitaxel

Adult females with histologically confirmed, inoperable, locally advanced or metastatic HER2- BC who received study drug plus paclitaxel.

Group Type EXPERIMENTAL

Paclitaxel

Intervention Type DRUG

intravenous paclitaxel 80 mg/m2 per week given until progression

BKM120

Intervention Type DRUG

Buparlisib (BKM120) were supplied as 100 mg and 50 mg hard gelatin capsules. Buparlisib was dosed on a flat scale of mg/day and was not adjusted to body weight or body surface area.

Placebo and paclitaxel

Adult females with histologically confirmed, inoperable, locally advanced or metastatic HER2- BC who received placebo plus paclitaxel.

Group Type ACTIVE_COMPARATOR

Paclitaxel

Intervention Type DRUG

intravenous paclitaxel 80 mg/m2 per week given until progression

BKM120 matching placebo

Intervention Type DRUG

Buparlisib maching plaxcebo were supplied as 100 mg and 50 mg hard gelatin capsules.

Buparlisib placebo was dosed on a flat scale of mg/day and was not adjusted to body weight or body surface area.

Interventions

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Paclitaxel

intravenous paclitaxel 80 mg/m2 per week given until progression

Intervention Type DRUG

BKM120 matching placebo

Buparlisib maching plaxcebo were supplied as 100 mg and 50 mg hard gelatin capsules.

Buparlisib placebo was dosed on a flat scale of mg/day and was not adjusted to body weight or body surface area.

Intervention Type DRUG

BKM120

Buparlisib (BKM120) were supplied as 100 mg and 50 mg hard gelatin capsules. Buparlisib was dosed on a flat scale of mg/day and was not adjusted to body weight or body surface area.

Intervention Type DRUG

Other Intervention Names

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Taxol Buparlisib

Eligibility Criteria

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Inclusion Criteria

* Breast cancer that is locally advanced or metastatic
* HER2 negative disease, and a known hormone receptor status - ER/PgR (common breast cancer classification tests)
* A tumor sample must be shipped to a central lab for identification of biomarkers (PI3K activation status) before randomization
* Adequate bone marrow and organ function
* Measurable or non-measurable disease

Exclusion Criteria

* Prior chemotherapy for locally advanced or metastatic disease
* Previous treatment with PI3K or AKT inhibitors
* Patient has symptomatic CNS metastases
* Concurrent malignancy or malignancy within 3 years of study enrollment
* Hematopoietic colony-stimulating growth factors or radiation within 2-4 weeks prior to starting study drug
* Increasing or chronic treatment (\> 5 days) with corticosteroids or another immunosuppressive agent
* Active heart (cardiac) disease as defined in the protocol
* Known hypersensitivity or contraindications to use paclitaxel
* Pregnant or nursing (lactating) woman
* Certain scores on an anxiety and depression mood questionaire given at screening
* Other protocol defined criteria may apply
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Ironwood Cancer and Research Centers SC

Chandler, Arizona, United States

Site Status

Arizona Oncology Associates Dept of Oncology

Phoenix, Arizona, United States

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Highlands Oncology Group Dept of Highlands Oncology Grp

Fayetteville, Arkansas, United States

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California Cancer Care Marian Speciality

Greenbrae, California, United States

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Rocky Mountain Cancer Centers RMCC Hale Pkwy

Greenwood Village, Colorado, United States

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H. Lee Moffitt Cancer Center & Research Institute SC

Tampa, Florida, United States

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Emory University School of Medicine/Winship Cancer Institute Dept.of WinshipCancerInst. (2)

Atlanta, Georgia, United States

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Northwest Georgia Oncology Center NW Georgia Onc

Marietta, Georgia, United States

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University of Kansas Cancer Center Univ Kansas 2

Kansas City, Kansas, United States

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Norton Healthcare, Inc.

Louisville, Kentucky, United States

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Washington University School of Medicine Regulatory

St Louis, Missouri, United States

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University of Nebraska Medical Center Unv Nebraska Med Ctr (2)

Omaha, Nebraska, United States

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University of New Mexico Cancer Research Center Dept of Univ New Mexico

Albuquerque, New Mexico, United States

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New York Oncology Hematology, P.C. Dept. of New York Oncology. PC

Troy, New York, United States

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Ohio State Comprehensive Cancer Center/James Cancer Hospital SC-1

Columbus, Ohio, United States

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University of Oklahoma Health Sciences Center OUHSC 2

Oklahoma City, Oklahoma, United States

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Northwest Cancer Specialists Vancouver Loc

Portland, Oregon, United States

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Baylor Health Care System/Sammons Cancer Center Baylor Texas Oncology

Dallas, Texas, United States

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University of Texas Southwestern Medical Center Harry Hines

Dallas, Texas, United States

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Cancer Care Centers of South Texas / HOAST CCC of So. TX- San Antonio

San Antonio, Texas, United States

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Medical Oncology & Hematology Associates of Northern VA Med Onc Hem Northern VA

Reston, Virginia, United States

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Novartis Investigative Site

Sydney, New South Wales, Australia

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Geelong, Victoria, Australia

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Parkville, Victoria, Australia

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Nedlands, Western Australia, Australia

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Salzburg, , Austria

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Vienna, , Austria

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Charleroi, , Belgium

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Liège, , Belgium

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Ottignies, , Belgium

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Sint-Niklaas, , Belgium

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Wilrijk, , Belgium

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Fortaleza, Ceará, Brazil

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São Paulo, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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Montreal, Quebec, Canada

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Brno, Czech Republic, Czechia

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Olomouc, , Czechia

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Prague, , Czechia

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Angers, , France

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Bordeaux, , France

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Créteil, , France

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La Roche-sur-Yon, , France

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Le Mans, , France

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Marseille, , France

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Nice, , France

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Saint-Herblain, , France

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Toulouse, , France

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Villejuif, , France

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Bonn, , Germany

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Dresden, , Germany

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Erlangen, , Germany

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Frankfurt, , Germany

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Fulda, , Germany

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Mainz, , Germany

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München, , Germany

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Ravensburg, , Germany

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Ulm, , Germany

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Hong Kong SAR, , Hong Kong

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Budapest, , Hungary

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Debrecen, , Hungary

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Szolnok, , Hungary

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Ramat Gan, , Israel

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Tel Aviv, , Israel

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Cona, FE, Italy

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Genova, GE, Italy

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Monza, MB, Italy

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Messina, ME, Italy

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Milan, MI, Italy

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Nagoya, Aichi-ken, Japan

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Nagoya, Aichi-ken, Japan

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Sapporo, Hokkaido, Japan

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Isehara, Kanagawa, Japan

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Kawasaki, Kanagawa, Japan

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Yokohama, Kanagawa, Japan

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Kumamoto, Kumamoto, Japan

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Osaka, Osaka, Japan

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Osaka, Osaka, Japan

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Suita, Osaka, Japan

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Koto, Tokyo, Japan

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Breda, Netherlands, Netherlands

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Rotterdam, , Netherlands

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Saint Petersburg, Russia, Russia

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Saint Petersburg, , Russia

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Singapore, Singapore, Singapore

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Johannesburg, , South Africa

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Seoul, Korea, South Korea

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Seoul, Korea, South Korea

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Seoul, Korea, South Korea

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Córdoba, Andalusia, Spain

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Málaga, Andalusia, Spain

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Seville, Andalusia, Spain

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Barcelona, Catalonia, Spain

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Barcelona, Catalonia, Spain

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L'Hospitalet de Llobregat, Catalonia, Spain

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A Coruña, Galicia, Spain

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Madrid, Madrid, Spain

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Madrid, Madrid, Spain

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Madrid, Madrid, Spain

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Madrid, Madrid, Spain

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San Cristóbal de La Laguna, Santa Cruz de Tenerife, Spain

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Valencia, Valencia, Spain

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Valencia, Valencia, Spain

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Zaragoza, Zaragoza, Spain

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Taipei, Taiwan, Taiwan

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Kuei-Shan Chiang, Taoyuan/ Taiwan ROC, Taiwan

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New Taipei City, , Taiwan

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Maidstone, Kent, United Kingdom

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Glasgow - Scotland, , United Kingdom

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London, , United Kingdom

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Metropolitan Borough of Wirral, , United Kingdom

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Countries

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United States Australia Austria Belgium Brazil Canada Czechia France Germany Hong Kong Hungary Israel Italy Japan Netherlands Russia Singapore South Africa South Korea Spain Taiwan United Kingdom

Other Identifiers

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2011-005932-24

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CBKM120F2202

Identifier Type: -

Identifier Source: org_study_id

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