BKM120 for Patients With PI3K-activated Tumors

NCT ID: NCT01833169

Last Updated: 2018-10-19

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

146 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-03-29

Study Completion Date

2016-09-26

Brief Summary

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The purpose of this signal seeking study was is to determine whether treatment with BKM120 demonstrates sufficient efficacy in select pathway-activated solid tumors and/or hematologic malignancies to warrant further study.

Detailed Description

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Conditions

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PI3K Pathway Activated Tumors

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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BKM120

BKM120 100 mg (oral gelatine capsules) was administered orally once daily starting from cycle 1 day 1 and will be dosed continuously every day for each 28- day cycle

Group Type EXPERIMENTAL

BKM120

Intervention Type DRUG

BKM120 100 mg (oral gelatine capsules) was administered orally once daily starting from cycle 1 day 1 and will be dosed continuously every day for each 28-day cycle

Interventions

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BKM120

BKM120 100 mg (oral gelatine capsules) was administered orally once daily starting from cycle 1 day 1 and will be dosed continuously every day for each 28-day cycle

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Patient had a confirmed diagnosis of a solid tumor or hematological malignancy with the exception of endometrial cancer, glioblastoma, nonsmall cell lung cancer, prostate cancer or breast cancer.
* Patient's tumor was evaluated and pre-identified to have activation of the PI3K pathway, at a CLIA certified laboratory
* Patient must have received at least one prior treatment for recurrent metastatic and /or locally advanced disease and for whom no standard therapy options was anticipated to result in a durable remission.
* Patient must have had progressive and measurable disease as per RECIST 1.1. or other appropriate hematological guidelines
* Patient had an Eastern Cooperative Oncology Group (ECOG) performance status ≤ 1

Exclusion Criteria

Patient had received previous treatment with BKM120 Patient had symptomatic CNS metastases Patient had mood disorder as outlined in Section 5 Patient had received chemotherapy or other anticancer therapy ≤ 4 weeks (6 weeks for nitrosourea, antibodies or mitomycin-C) prior to starting study drug.
Minimum Eligible Age

18 Years

Maximum Eligible Age

100 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Arizona Oncology Associates HOPE Division

Phoenix, Arizona, United States

Site Status

Arizona Oncology Associates PC- HAL

Sedona, Arizona, United States

Site Status

Highlands Oncology Group

Fayetteville, Arkansas, United States

Site Status

Sarcoma Oncology Center

Santa Monica, California, United States

Site Status

Rocky Mountain Cancer Centers RMCC - Aurora

Greenwood Village, Colorado, United States

Site Status

Whittingham Cancer Center Norwalk Hospital

Norwalk, Connecticut, United States

Site Status

Eastern Connecticut Hematology & Oncology Associates The Norwich Cancer Center

Norwich, Connecticut, United States

Site Status

Florida Cancer Specialists Dept of Oncology (2)

Fort Myers, Florida, United States

Site Status

Florida Hospital Cancer Institute FL Hosp. Cancer Instit.

Orlando, Florida, United States

Site Status

Florida Cancer Specialists

West Palm Beach, Florida, United States

Site Status

University Cancer & Blood Center, LLC

Athens, Georgia, United States

Site Status

Southeastern Regional Medical Center

Newnan, Georgia, United States

Site Status

Lurie Children's Hospital of Chicago Developmental Therapeutics

Chicago, Illinois, United States

Site Status

Cancer Care Specialists of Central Illinois

Decatur, Illinois, United States

Site Status

Illinois Cancer Care P.C. IL. Cancer Care

Peoria, Illinois, United States

Site Status

Illinois Cancer Care P.C.

Peoria, Illinois, United States

Site Status

Cancer Treatment Centers of America Southwestern Regional Med. Ctr

Schaumburg, Illinois, United States

Site Status

Northern Indiana Cancer Research Consortium No. Indiana Cancer Res.

South Bend, Indiana, United States

Site Status

University of Iowa Hospitals & Clinics Regulatory Contact 2

Iowa City, Iowa, United States

Site Status

Eastern Maine Medical Center Research Center SC

Bangor, Maine, United States

Site Status

Mount Auburn Hospital

Cambridge, Massachusetts, United States

Site Status

Michigan Medicine University of Michigan Int. Medicine Oncology

Ann Arbor, Michigan, United States

Site Status

Cancer and Hematology Centers of West Michigan Dept. of Oncology

Grand Rapids, Michigan, United States

Site Status

Minnesota Oncology Hematology, P.A. Minnesota Oncology Hematology

Minneapolis, Minnesota, United States

Site Status

Nebraska Cancer Specialists Oncology Hematology West

Omaha, Nebraska, United States

Site Status

Comprehensive Cancer Centers

Las Vegas, Nevada, United States

Site Status

Hematology Oncology Associates of Northern New Jersey PA Regional Cancer Care Assoc.

Morristown, New Jersey, United States

Site Status

Cancer Center at Presbyterian

Albuquerque, New Mexico, United States

Site Status

New York Oncology Hematology NY Onc Hem

Albany, New York, United States

Site Status

Waverly Hematology Oncology

Cary, North Carolina, United States

Site Status

University of N C at Chapel Hill Physician Office Building

Chapel Hill, North Carolina, United States

Site Status

Duke University Medical Center Seeley G. Mudd Bldg.

Durham, North Carolina, United States

Site Status

Cleveland Clinic Foundation Cleveland Clinic (19)

Cleveland, Ohio, United States

Site Status

Mid Ohio Oncology/Hematology Mark H. Zangmeister Center

Columbus, Ohio, United States

Site Status

Bend Memorial Clinic Bend Mem. Clinic

Bend, Oregon, United States

Site Status

Northwest Cancer Specialists Compass Oncology (36)

Portland, Oregon, United States

Site Status

Oregon Health and Science University Oregon Health & Science U (56)

Portland, Oregon, United States

Site Status

Salem Health

Salem, Oregon, United States

Site Status

Gettysburg Cancer Center

Gettysburg, Pennsylvania, United States

Site Status

West Penn Allegheny Oncology Network

Natrona Heights, Pennsylvania, United States

Site Status

University of Pittsburgh Medical Center UPMC

Pittsburgh, Pennsylvania, United States

Site Status

Abington Hematology Oncology Associates, Inc Abington Hem Onc Assoc (5)

Willow Grove, Pennsylvania, United States

Site Status

Sanford University of South Dakota Medical Center Sanford Health

Sioux Falls, South Dakota, United States

Site Status

Chattanooga Oncology and Hematology Assoicates, PC Chattanooga Oncology

Chattanooga, Tennessee, United States

Site Status

West Cancer Clinic

Memphis, Tennessee, United States

Site Status

Sarah Cannon Research Institute

Nashville, Tennessee, United States

Site Status

Texas Oncology P A Round Rock

Dallas, Texas, United States

Site Status

Texas Oncology Sammons Cancer Center Sammons Cancer Center (10)

Dallas, Texas, United States

Site Status

Texas Oncology, P.A. Texas Oncololgy, P.A. (8)

Fort Worth, Texas, United States

Site Status

Oncology Consultants Oncology Group

Houston, Texas, United States

Site Status

MD Anderson Cancer Center/University of Texas MD Anderson Cancer Center (3)

Houston, Texas, United States

Site Status

Cancer Care Centers of South Texas HOAST CCC of So. TX-San Antonio (3)

San Antonio, Texas, United States

Site Status

Tyler Cancer Center

Tyler, Texas, United States

Site Status

Intermountain Medical Center Intermountain Healthcare

Murray, Utah, United States

Site Status

Virginia Cancer Specialists Virginia Cancer Specialists

Fairfax, Virginia, United States

Site Status

Blue Ridge Research Center at Roanoke Neurological Center McKesson Specialty Care

Roanoke, Virginia, United States

Site Status

Kadlec Clinic Hematology and Oncology Kadlec Clinic Hematology & Onc

Kennewick, Washington, United States

Site Status

Northwest Medical Specialties Hematology/Oncology

Tacoma, Washington, United States

Site Status

Medical College of Wisconsin Cancer Center

Milwaukee, Wisconsin, United States

Site Status

Countries

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United States

Other Identifiers

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CBKM120ZUS40

Identifier Type: -

Identifier Source: org_study_id

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