Study of Palifosfamide-tris in Combination With Carboplatin and Etoposide in Chemotherapy Naïve Patients With Extensive-Stage Small Cell Lung Cancer (The MATISSE Study)

NCT ID: NCT01555710

Last Updated: 2013-05-21

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE3

Total Enrollment

548 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-05-31

Study Completion Date

2015-06-30

Brief Summary

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This is a multinational, multicenter, randomized controlled, open-label, adaptive study to evaluate the efficacy of PaCE chemotherapy in chemotherapy naive subjects with extensive-stage SCLC. Eligible subjects will be stratified according to age, gender, and Eastern Cooperative Oncology Group (ECOG) performance status, and randomized in a 1:1 ratio to receive either PaCE or CE chemotherapy.

The study design uses an adaptive group sequential approach with sample size re-estimation at the interim analysis.

Secondary efficacy endpoints include ORR, PFS, duration of response and changes in QOL and disease-related symptoms. Tumor-related endpoints will be assessed according to the Response Evaluation Criteria in Solid Tumors (RECIST) v1.1 guidelines.

The safety of study treatments will be assessed by the frequency and severity of adverse events as determined by National Cancer Institute (NCI) Common Terminology Criteria for Adverse Events (CTCAE) v4.03. To provide an initial confirmation of safety, an early interim analysis of safety data only will be performed.

An independent Data Monitoring Committee (DMC) will be convened to assess the safety and efficacy of the study interventions and to monitor the overall conduct of the clinical trial.

Detailed Description

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Conditions

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Extensive-Stage Small Cell Lung Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Palifosfamide-tris plus Carboplatin and Etoposide

Drug: palifosfamide-tris in combination with carboplatin and etoposide palifosfamide-tris: 130 mg/m2/day 3 days every 21 days for a max of 6 cycles. carboplatin: AUC 4 mg/mL/min 1 day every 21 days for a max of 6 cycles. etoposide: 100 mg/m2/day 3 days every 21 days for a max of 6 cycles.

Group Type EXPERIMENTAL

Carboplatin

Intervention Type DRUG

AUC 4 mg/mL/min 1 day every 21 days for a max of 6 cycles.

Palifosfamide-tris

Intervention Type DRUG

130 mg/m2/day 3 days every 21 days for a max of 6 cycles.

Etoposide

Intervention Type DRUG

100 mg/m2/day 3 days every 21 days for a maximum of 6 cycles.

Carboplatin plus Etoposide

Drug: carboplatin in combination with etoposide carboplatin: AUC 5mg/mL/min 1 day every 21 days for a maximum of 6 cycles. etoposide: 100 mg/m2/day 3 days every 21 days for a maximum of 6 cycles.

Group Type ACTIVE_COMPARATOR

Etoposide

Intervention Type DRUG

100 mg/m2/day 3 days every 21 days for a maximum of 6 cycles.

Carboplatin

Intervention Type DRUG

AUC 5 mg/mL/min 1 day every 21 days for a max of 6 cycles.

Interventions

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Carboplatin

AUC 4 mg/mL/min 1 day every 21 days for a max of 6 cycles.

Intervention Type DRUG

Palifosfamide-tris

130 mg/m2/day 3 days every 21 days for a max of 6 cycles.

Intervention Type DRUG

Etoposide

100 mg/m2/day 3 days every 21 days for a maximum of 6 cycles.

Intervention Type DRUG

Carboplatin

AUC 5 mg/mL/min 1 day every 21 days for a max of 6 cycles.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Documented extensive-stage small cell lung cancer.
* Patient has received no prior chemotherapy, adjuvant therapy, or radiotherapy for lung cancer.
* ECOG Performance Status of 0, 1 or 2.
* Adequate bone marrow and organ function based on the results of protocol- specified laboratory tests.
* Male and female patients must agree to use a highly reliable method of birth control during study participation.
* Able to provide informed consent

Exclusion Criteria

* Previously untreated (non-irradiated), symptomatic brain metastases.
* Known allergy to any of the study drugs or their excipients.
* Any unstable or clinically significant concurrent medical condition that would, in the opinion of the investigator, jeopardize the safety of a patient and/or their compliance with the protocol, based on screening tests, physical examination and medical history (as specifically defined in the clinical protocol).
* Any malignancy other than small cell lung cancer within the last 5 years prior to randomization, with the exception of cervical carcinoma in situ, nonmelanoma skin cancer, or superficial bladder tumors (Ta, Tis, or T1) that have been successfully and curatively treated with no evidence of recurrent or residual disease. (Exception: Subjects with a history of malignancy other than small cell lung cancer may be enrolled after consultation with the medical monitor provided the patient's prognosis is best defined by the extensive-stage small cell lung cancer).
* Currently pregnant or nursing.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Alaunos Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Birmingham Hematology and Oncology Associates, LLC

Birmingham, Alabama, United States

Site Status

University of Southern California

Los Angeles, California, United States

Site Status

Redwood Regional Oncology Group

Santa Rosa, California, United States

Site Status

Christiana Care Health Services

Newark, Delaware, United States

Site Status

Baptist Cancer Institute

Jacksonville, Florida, United States

Site Status

Hematology Oncology Associates of the Treasure Coast

Port Sant Lucie, Florida, United States

Site Status

Peachtree Hematology Oncology Consultants

Atlanta, Georgia, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Medical and Surgical Specialists, LLC

Galesburg, Illinois, United States

Site Status

Illinois Cancer Specialists

Niles, Illinois, United States

Site Status

Central Indiana Cancer Centers

Fishers, Indiana, United States

Site Status

Goshen Center for Cancer Care

Goshen, Indiana, United States

Site Status

Indiana University

Indianapolis, Indiana, United States

Site Status

Horizon Oncology Center

Lafayette, Indiana, United States

Site Status

Indiana University Health Ball Memorial Hospital

Muncie, Indiana, United States

Site Status

University of Kansas Hospital

Overland Park, Kansas, United States

Site Status

Central Baptist Hospital

Lexington, Kentucky, United States

Site Status

Medical Oncology, LLC

Baton Rouge, Louisiana, United States

Site Status

Frederick Memorial Hospital Regional Cancer Therapy Center

Frederick, Maryland, United States

Site Status

Metro Health Cancer Center

Wyoming, Michigan, United States

Site Status

Saint Mary's Medical Center

Duluth, Minnesota, United States

Site Status

Virginia Piper Cancer Institute

Minneapolis, Minnesota, United States

Site Status

John Theurer Cancer Center at Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status

Hematology Oncology Associates of Northern New Jersey, PA, Carol G. Simon Cancer Center

Morristown, New Jersey, United States

Site Status

University of New Mexico Cancer Center

Albuquerque, New Mexico, United States

Site Status

New York Oncology Hematology, PC

Albany, New York, United States

Site Status

Montefiore Medical Center

The Bronx, New York, United States

Site Status

The Christ Hospital

Cincinnati, Ohio, United States

Site Status

Dayton Cancer Center, Medical Oncology Hematology Associates

Dayton, Ohio, United States

Site Status

Medical Oncology Associates Of Wyoming Valley, PC

Kingston, Pennsylvania, United States

Site Status

Charleston Hematology Oncology Associates, PA

Charleston, South Carolina, United States

Site Status

Texas Oncology-Medical City Dallas

Dallas, Texas, United States

Site Status

Texas Oncology- Baylor, Charles A. Sammons Cancer Center

Dallas, Texas, United States

Site Status

University of Texas Medical Branch at Galveston

Galveston, Texas, United States

Site Status

Oncology Consultants, PA

Houston, Texas, United States

Site Status

Texas Oncology, PA

Wichita Falls, Texas, United States

Site Status

Fletcher Allen Health Care

Burlington, Vermont, United States

Site Status

Fairfax Northern Virginia Hematology-Oncology, PC

Fairfax, Virginia, United States

Site Status

Swedish Medical Center

Seattle, Washington, United States

Site Status

Wisconsin Institutes for Medical Research

Madison, Wisconsin, United States

Site Status

Southern Medical Day Oncology Care Centre

Wollongong, New South Wales, Australia

Site Status

CancerCare Manitoba

Winnipeg, Manitoba, Canada

Site Status

R. S. McLaughlin Durham Regional Cancer Center at Lakeridge Health Oshawa

Oshawa, Ontario, Canada

Site Status

Hôpital Laval

Sainte-Foy, Quebec, Canada

Site Status

Centre Hospitalier Lyon Sud

Pierre Bénité, Auvergne-Rhône-Alpes, France

Site Status

Centre François Baclesse

Caen, Basse-normandie, France

Site Status

Centre Hospitalier Universitaire -Hôpital Morvan

Brest, Brittany Region, France

Site Status

Centre Hospitalier Universitaire, Hopital Bretonneau

Tours, Centre-Val de Loire, France

Site Status

Hôpital du Cluzeau

Limoges, Limousin, Lorraine, France

Site Status

Institut de Cancérologie de l'Ouest - René Gauducheau

Saint-Herblain, Pays de la Loire Region, France

Site Status

Hôpital Saint Joseph

Marseille, Provence-Alpes-Côte d'Azur Region, France

Site Status

Centre Paul Strauss

Strasbourg, , France

Site Status

Debreceni Egyetem Orvos és Egészségtudományi Centrum

Debrecen, Hajdú-Bihar, Hungary

Site Status

Mátrai Gyógyintézet

Mátraháza, Heves County, Hungary

Site Status

Rambam Medical Center

Haifa, , Israel

Site Status

Hadassah Medical Organization, Ein Kerem

Jerusalem, , Israel

Site Status

Meir Hospital Sapir Medical Center

Kfar Saba, , Israel

Site Status

Western Gallilee Medical Center

Nahariya, , Israel

Site Status

Rabin Medical Center Beilinson Campus

Petah Tikva, , Israel

Site Status

Istituto Nazionale per la Ricerca sul Cancro

Genova, Genova, Italy

Site Status

Presidio Ospedaliero S. Chiara

Trento, Trento, Italy

Site Status

Azienda Ospedaliera Ospedale Niguarda Ca' Granda

Milan, , Italy

Site Status

Centrum Onkologii - Instytut im. M. Sklodowskiej-Curie w Warszawie

Warsaw, Masovian Voivodeship, Poland

Site Status

Uniwersyteckie Centrum Kliniczne

Gdansk, Pomeranian Voivodeship, Poland

Site Status

Wojewódzkie Centrum Onkologii

Gdansk, Pomeranian Voivodeship, Poland

Site Status

Specjalistyczny Szpital im. Alfreda Sokolowskiego

Szczecin, West Pomeranian Voivodeship, Poland

Site Status

Republic Clinical Oncology Dispensary of the Ministry of Healthcare of Republic of Bashkortostan

Ufa, Bashkortostan Republic, Russia

Site Status

Ivanovo Regional Oncology Centre

Ivanovo, Ivanovo Oblast, Russia

Site Status

City Oncology Hospital # 62

Moscow Region, Moscow, Russia

Site Status

State Institution of Healthcare "Arkhangelsk Regional Clinical Oncology Dispensary"

Arkhangelsk, Primorskiy (Maritime) Kray, Russia

Site Status

Republican Clinical Oncologic Dispensary of Ministry of health of Republic Tatarstan

Kazan', Tatarstan Republic, Russia

Site Status

State Budget Institution of Healthcare "Chelyabinsk Regional Clinical Oncology Dispensary"

Chelaybinsk, , Russia

Site Status

Cancer Research Center n.a. N.N. Blokhin

Moscow, , Russia

Site Status

GUZ of Nizhegorodskiy region, Nizhnij Novgorod City Oncology Dispensary

Nizhny Novgorod, , Russia

Site Status

State Educational Institution "S.M. Kirov Military Medical Academy of Ministry of Defense of Russia"

Saint Petersburg, , Russia

Site Status

Saint-Petersburg State Medical University n. a. I. P. Pavlov

Saint Petersburg, , Russia

Site Status

State healthcare institution of Yaroslavl region "Regional Clinical Oncologic Hospital"

Yaroslavl, , Russia

Site Status

China Medical University Hospital

Taichung, , Taiwan

Site Status

Wythenshawe Hospital

Manchester, England, United Kingdom

Site Status

Countries

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United States Australia Canada France Hungary Israel Italy Poland Russia Taiwan United Kingdom

Other Identifiers

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IPM3002

Identifier Type: -

Identifier Source: org_study_id

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