Safety and Efficacy of BKM120 in Patients With Metastatic Non-small Cell Lung Cancer

NCT ID: NCT01297491

Last Updated: 2016-03-11

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

63 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-05-31

Study Completion Date

2014-10-31

Brief Summary

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The purpose of this two-stage phase II study is to assess the efficacy of BKM120, as measured by determining the progression free survival (PFS), in patients with pretreated metastatic Non-small Cell Lung Cancer (NSCLC) that exhibits PI3K pathway activation. BKM120 will be investigated in two groups of NSCLC patients according to the histology of the cancer: squamous and non-squamous.

Detailed Description

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Conditions

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Non-small Cell Lung Cancer

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Squamous BKM120 100mg qd

Diagnosed patients with non-small cell lung cancer (NSCLC) that progressed after one prior, platinum-based chemotherapy line for metastatic disease.

Group Type EXPERIMENTAL

BKM120

Intervention Type DRUG

Buparlisib was supplied as 10mg or 50mg capsules. It was administered on a continuous once daily dosing schedule at a dose of 100 mg. The patient was dosed on a flat scale of mg/day and not adjusted to body weight or body surface area.

Non-Squamous BKM120 100mg qd

Diagnosed patients with non-squamous NSCLC that progressed after one or two prior antineoplastic therapy lines for metastatic disease.

Group Type EXPERIMENTAL

BKM120

Intervention Type DRUG

Buparlisib was supplied as 10mg or 50mg capsules. It was administered on a continuous once daily dosing schedule at a dose of 100 mg. The patient was dosed on a flat scale of mg/day and not adjusted to body weight or body surface area.

Interventions

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BKM120

Buparlisib was supplied as 10mg or 50mg capsules. It was administered on a continuous once daily dosing schedule at a dose of 100 mg. The patient was dosed on a flat scale of mg/day and not adjusted to body weight or body surface area.

Intervention Type DRUG

Other Intervention Names

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Buparlisib

Eligibility Criteria

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Inclusion Criteria

* Histologically confirmed NSCLC with activated PI3K pathway
* Progressive disease after prior systemic antineoplastic treatment(s) for advanced NSCLC
* Archival or fresh tumor biopsy must be available for profiling
* Measurable and/or non-measurable disease as per RECIST 1.1 criteria
* Eastern Cooperative Oncology Group (ECOG) performance status ≤ 2
* Adequate organ function as assessed by laboratory tests

Exclusion Criteria

* Patient has received previous treatment with PI3K inhibitors
* Patient with squamous NSCLC has received more than one line of chemotherapy treatment for metastatic disease; patient with non-squamous NSCLC has received more than two lines of systemic antineoplastic treatment for metastatic disease
* Uncontrolled or symptomatic CNS metastases
* Concurrent use of any other approved or investigational antineoplastic agent
* Radiotherapy ≤ 28 days prior to starting study drug
* Major surgery within 28 days prior to starting study drug
* History of clinically significant cardiac dysfunction, mood disorders, or poorly controlled diabetes mellitus
* Current treatment with medication that has a known risk to prolong the QT interval or inducing Torsades de Pointes
* Impairment of gastrointestinal (GI) function
* Chronic treatment with steroids or another immunosuppressive agent.
* Concurrent severe and/or uncontrolled medical condition
* Currently receiving Warfarin or another coumarin derivative
* Known history of HIV infection
* Sensory neuropathy with functional impairment (CTC grade 2 neuropathy, regardless of causality)
* Pregnancy, lactation, or breastfeeding
* Woman of child-bearing potential
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Ironwood Cancer and Research Centers SC

Chandler, Arizona, United States

Site Status

Arizona Oncology Associates Tucson (Rudasill & La Cholla)

Phoenix, Arizona, United States

Site Status

Mayo Clinic - Arizona Mayo Scottsdale AZ

Scottsdale, Arizona, United States

Site Status

Highlands Oncology Group Dept of Highlands Oncology Grp

Fayetteville, Arkansas, United States

Site Status

Cedars Sinai Medical Center Dept.of Cedars-Sinai Med. Ctr.

Los Angeles, California, United States

Site Status

University of California at San Diego, Moores Cancer Ctr SC

San Diego, California, United States

Site Status

University of Colorado Univ CO

Aurora, Colorado, United States

Site Status

Rocky Mountain Cancer Centers Dept. of Rocky Mountain Cancer

Greenwood Village, Colorado, United States

Site Status

H. Lee Moffitt Cancer Center & Research Institute H Lee Moffitt

Tampa, Florida, United States

Site Status

Emory University School of Medicine/Winship Cancer Institute Emory 2

Atlanta, Georgia, United States

Site Status

Rush University Medical Center SC

Chicago, Illinois, United States

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University of Chicago Medical Center Unvi Chi

Chicago, Illinois, United States

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University of Kansas Cancer Center Univ of KS

Kansas City, Kansas, United States

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Massachusetts General Hospital Mass General

Boston, Massachusetts, United States

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Fallon Clinic at Worcester Medical Center Fallon Clinic Worcester Med

Worcester, Massachusetts, United States

Site Status

Karmanos Cancer Institute Wayne St Karmanos

Detroit, Michigan, United States

Site Status

Washington University School of Medicine Washington University (16)

St Louis, Missouri, United States

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Hematology Oncology Associates of Northern New Jersey PA DeptofHem-OncofNorthern NJ (2)

Morristown, New Jersey, United States

Site Status

Overlook Hospital - Carol G Simon Cancer Center Carol G Simon

Summit, New Jersey, United States

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Roswell Park Cancer Institute Rosewell

Buffalo, New York, United States

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Memorial Sloan Kettering Cancer Center Sloan Kettering

New York, New York, United States

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Duke University Medical Center Duke 2

Durham, North Carolina, United States

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MetroHealth Medical Center Dept.ofMetroHealthMedCtr.(2)

Cleveland, Ohio, United States

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University of Oklahoma Health Sciences Center Dept. of Oklahoma Univ. HSC

Oklahoma City, Oklahoma, United States

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Northwest Cancer Specialists Compass Oncology -BKM

Portland, Oregon, United States

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University of Pittsburgh Medical Center SC-2

Pittsburgh, Pennsylvania, United States

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Medical University of South Carolina MUSC

Charleston, South Carolina, United States

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Baylor Health Care System/Sammons Cancer Center Baylor Texas Oncology

Dallas, Texas, United States

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Texas Oncology South Texas Oncology

Dallas, Texas, United States

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U of TX Southwestern Medical Center - SimmonsCompCancerCtr Clinical Research Office

Dallas, Texas, United States

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Virginia Oncology Associates VOA - Lake Wright (2)

*see Various Departments*, Virginia, United States

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University of Wisconsin Univ WIsc 2

Madison, Wisconsin, United States

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Novartis Investigative Site

Buenos Aires, Buenos Aires, Argentina

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Córdoba, Córdoba Province, Argentina

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Rio Negro, Viedma, Argentina

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Brussels, , Belgium

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Charleroi, , Belgium

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Genk, , Belgium

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Leuven, , Belgium

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Libramont, , Belgium

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Salvador, Estado de Bahia, Brazil

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Rio de Janeiro, Rio de Janeiro, Brazil

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Florianópolis, Santa Catarina, Brazil

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Barretos, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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Vancouver, British Columbia, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Caen, , France

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Créteil, , France

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Marseille, , France

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Rennes, , France

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Villejuif, , France

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Berlin, , Germany

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Cologne, , Germany

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Essen, , Germany

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Gauting, , Germany

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Großhansdorf, , Germany

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Heidelberg, , Germany

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Nuremberg, , Germany

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Oldenburg, , Germany

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Recklinghausen, , Germany

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Hong Kong, , Hong Kong

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Budapest, , Hungary

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Budapest, , Hungary

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Deszk, , Hungary

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Mátraháza, , Hungary

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Szolnok, , Hungary

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Avellino, AV, Italy

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Genova, GE, Italy

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Milan, MI, Italy

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Milan, MI, Italy

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Parma, PR, Italy

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Udine, UD, Italy

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Kurashiki, Okayama-ken, Japan

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Koto, Tokyo, Japan

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Maastricht, , Netherlands

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Singapore, Singapore, Singapore

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Sabadell, Barcelona, Spain

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Barcelona, Catalonia, Spain

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Mataró, Catalonia, Spain

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Alicante, Valencia, Spain

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Tainan City, Taiwan ROC, Taiwan

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Taipei, Taiwan ROC, Taiwan

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Bangkok, , Thailand

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Chiang Mai, , Thailand

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Izmir, Turkey, Turkey (Türkiye)

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Altunizade, , Turkey (Türkiye)

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Northwood, Middlesex, United Kingdom

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Leicester, , United Kingdom

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Novartis Investigative Site

London, , United Kingdom

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Novartis Investigative Site

Manchester, , United Kingdom

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Countries

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United States Argentina Belgium Brazil Canada France Germany Hong Kong Hungary Italy Japan Netherlands Singapore Spain Taiwan Thailand Turkey (Türkiye) United Kingdom

References

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Vansteenkiste JF, Canon JL, De Braud F, Grossi F, De Pas T, Gray JE, Su WC, Felip E, Yoshioka H, Gridelli C, Dy GK, Thongprasert S, Reck M, Aimone P, Vidam GA, Roussou P, Wang YA, Di Tomaso E, Soria JC. Safety and Efficacy of Buparlisib (BKM120) in Patients with PI3K Pathway-Activated Non-Small Cell Lung Cancer: Results from the Phase II BASALT-1 Study. J Thorac Oncol. 2015 Sep;10(9):1319-1327. doi: 10.1097/JTO.0000000000000607.

Reference Type RESULT
PMID: 26098748 (View on PubMed)

Other Identifiers

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2010-024011-14

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CBKM120D2201

Identifier Type: -

Identifier Source: org_study_id

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