Study of Palifosfamide-tris in Combination With Doxorubicin in Patients With Front-line Metastatic Soft Tissue Sarcoma

NCT ID: NCT01168791

Last Updated: 2013-07-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

447 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-07-31

Study Completion Date

2013-03-31

Brief Summary

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This is an international, randomized, double-blind, placebo-controlled trial to evaluate the clinical efficacy of palifosfamide-tris administered with doxorubicin in combination, compared with doxorubicin administered with placebo in front-line patients diagnosed with metastatic soft tissue sarcoma (STS).

Detailed Description

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Conditions

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Soft Tissue Sarcoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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doxorubicin plus palifosfamide-tris

Group Type EXPERIMENTAL

doxorubicin in combination with palifosfamide-tris

Intervention Type DRUG

palifosfamide-tris: 150 mg/m2 3 days every 21 days for a maximum of 6 cycles.

doxorubicin: 75 mg/m2 1 day every 21 days for a maximum of 6 cycles.

doxorubicin plus placebo

Group Type ACTIVE_COMPARATOR

doxorubicin in combination with placebo

Intervention Type DRUG

doxorubicin: 75 mg/m2 of doxorubicin 1 day every 21 days for a maximum of 6 cycles.

placebo: 250 mL of normal saline 3 days every 21 days for a maximum of 6 cycles.

Interventions

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doxorubicin in combination with palifosfamide-tris

palifosfamide-tris: 150 mg/m2 3 days every 21 days for a maximum of 6 cycles.

doxorubicin: 75 mg/m2 1 day every 21 days for a maximum of 6 cycles.

Intervention Type DRUG

doxorubicin in combination with placebo

doxorubicin: 75 mg/m2 of doxorubicin 1 day every 21 days for a maximum of 6 cycles.

placebo: 250 mL of normal saline 3 days every 21 days for a maximum of 6 cycles.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Age ≥18 years.
* Documented soft tissue sarcoma
* Metastatic disease for which the patient has not received any prior treatment, and for whom treatment with doxorubicin is considered medically acceptable.
* ECOG Performance Status of 0, 1 or 2
* Adequate bone marrow and organ function based on the results of protocol- specified laboratory tests
* Male and female patients must agree to use a highly reliable method of birth control during study participation.
* Able to provide informed consent

To be eligible, each patient must meet NONE of the following criteria:

* Specific sarcoma histological subtypes including GIST and Ewing's sarcoma.
* Systemic therapy for the treatment of metastatic sarcoma, prior to or during the study. However, patients may have received neo-adjuvant/adjuvant Gemzar and Taxotere chemotherapy for their primary sarcoma, prior to the development of metastatic disease
* Any prior anthracycline use.
* Known allergy to any of the study drugs or their excipients.
* Any unstable or clinically significant concurrent medical condition that would, in the opinion of the investigator, jeopardize the safety of a patient and/or their compliance with the protocol, based on screening tests, physical examination and medical history (as specifically defined in the clinical protocol).
* Myocardial dysfunction defined as left ventricular ejection fraction (LVEF) \<50%.
* Documented metastases to brain or meninges.
* Any malignancy other than sarcoma within the last 5 years prior to screening, with the exception of cervical carcinoma in situ, basal cell carcinoma, or superficial bladder tumors (Ta, Tis, or T1) that have been successfully and curatively treated with no evidence of recurrent or residual disease.
* Currently pregnant or nursing.
* Radiotherapy with curative intent within 4 weeks of first dose of study drug.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Alaunos Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Birmingham, Alabama, United States

Site Status

Arizona Oncology Associates

Phoenix, Arizona, United States

Site Status

Scottsdale, Arizona, United States

Site Status

Arizona Cancer Center

Tucson, Arizona, United States

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University of Arkansas for Medical Sciences

Little Rock, Arkansas, United States

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University of California, Los Angeles

Los Angeles, California, United States

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Los Angeles, California, United States

Site Status

University of California, Irvine

Orange, California, United States

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Pomona, California, United States

Site Status

Sarcoma Oncology Center

Santa Monica, California, United States

Site Status

University of Colorado Cancer Center

Aurora, Colorado, United States

Site Status

Rocky Mountain Cancer Centers

Denver, Colorado, United States

Site Status

Medical Oncology Hematology Consultants

Newark, Delaware, United States

Site Status

MedStar Research Institute

Washington D.C., District of Columbia, United States

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Washington D.C., District of Columbia, United States

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Jacksonville, Florida, United States

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Orlando, Florida, United States

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Moffitt Cancer Center

Tampa, Florida, United States

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Palm Beach Cancer Institute

West Palm Beach, Florida, United States

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Emory

Atlanta, Georgia, United States

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Medical College of Georgia

Augusta, Georgia, United States

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Kootenai Cancer Center

Post Falls, Idaho, United States

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Chicago, Illinois, United States

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Park Ridge, Illinois, United States

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Indiana University Simon Cancer Center

Indiannapolis, Indiana, United States

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University of Iowa Hospital and Clinics

Iowa City, Iowa, United States

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Kansas City Cancer Center

Overland Park, Kansas, United States

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New Orleans, Louisiana, United States

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LSU Health Sciences Center, Feist-Weiller Cancer Center

Shreveport, Louisiana, United States

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Baltimore, Maryland, United States

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Dana-Farber Cancer Institute

Boston, Massachusetts, United States

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Ann Arbor, Michigan, United States

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Mayo Clinic

Rochester, Minnesota, United States

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St.Louis University

St Louis, Missouri, United States

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Washington University School of Medicine

St Louis, Missouri, United States

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Las Vegas, Nevada, United States

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Hackensack, New Jersey, United States

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Morristown, New Jersey, United States

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Saint Barnabas

West Orange, New Jersey, United States

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Albuquerque, New Mexico, United States

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Mount Sinai School of Medicine

New York, New York, United States

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Columbia University Medical Center

New York, New York, United States

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University of Rochester

Rochester, New York, United States

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The Bronx, New York, United States

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University of North Carolina

Chapel Hill, North Carolina, United States

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Durham, North Carolina, United States

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Raleigh, North Carolina, United States

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Wake Forest University Health Sciences

Winston-Salem, North Carolina, United States

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Summa Health System

Akron, Ohio, United States

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UC Cancer Institute

Cinncinnati, Ohio, United States

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Cleveland Clinic

Cleveland, Ohio, United States

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The Ohio State University Medical Center

Columbus, Ohio, United States

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Cancer Care Associates

Tulsa, Oklahoma, United States

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Oregon Health and Science University

Portland, Oregon, United States

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Bethelehem, Pennsylvania, United States

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Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

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Pennsylvania Oncology/Hematology Associates

Philadelphia, Pennsylvania, United States

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University of Pittsburgh

Pittsburgh, Pennsylvania, United States

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Providence, Rhode Island, United States

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Charleston, South Carolina, United States

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Cancer Centers of the Carolinas

Greenville, South Carolina, United States

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Memphis, Tennessee, United States

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Nashville, Tennessee, United States

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Texas Oncology

Bedford, Texas, United States

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Texas Oncology - Medical City Dallas

Dallas, Texas, United States

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Cancer Therapy and Research Center

San Antonio, Texas, United States

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Utah Cancer Specialists

Salt Lake City, Utah, United States

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Burlington, Vermont, United States

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Virginia Cancer Specialists

Fairfax, Virginia, United States

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University of Washington/Seattle Cancer Care Alliance

Seattle, Washington, United States

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Bellin Cancer Center

Green Bay, Wisconsin, United States

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University of Wisconsin

Madison, Wisconsin, United States

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Milwaukee, Wisconsin, United States

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Ciudad de Buenos Aires, , Argentina

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Córdoba, , Argentina

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Ramos Mejía, , Argentina

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Instituto CAICI

Rosario, , Argentina

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Sante Fe, , Argentina

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North Adelaide Oncology

Adelaide, , Australia

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Royal Adelaide Hospital

Adelaide, , Australia

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Camperdown, , Australia

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East Melbourne, , Australia

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The Canberra Hospital

Garran, , Australia

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Garran, , Australia

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Kurralta Park, , Australia

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Nedlands, , Australia

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Prince of Wales Hospital

Randwick, , Australia

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Princess Alexandra Hospital

Woolloongabba, , Australia

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Antwerp, , Belgium

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Brussels, , Belgium

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Leuven, , Belgium

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Liège, , Belgium

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Institution name: Hospital de Câncer de Barretos - Fundação PIOXII

Barretos, , Brazil

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Belo Horizonte, , Brazil

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Santa Casa da Misericórdia de Curitiba

Curitiba, , Brazil

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Florianópolis, , Brazil

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Jaú, , Brazil

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Hospital da Cidade de Passo Fundo

Passo Fundo, , Brazil

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Hospital das Clínicas de Porto Alegre

Porto Alegre, , Brazil

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Irmandade da Santa Casa de Misericórdia de Porto Alegre

Porto Alegre, , Brazil

Site Status

Centro de Oncologia da Bahia

Salvador, , Brazil

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São Paulo, , Brazil

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Calgary, Alberta, Canada

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Cross Cancer Institute

Edmonton, Alberta, Canada

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Mount Sinai Hospital

Toronto, Ontario, Canada

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Jewish General Hospital

Montreal, Quebec, Canada

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McGill University

Montreal, Quebec, Canada

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Santiago, , Chile

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Instituto Clínico Oncológico del Sur

Temuco, , Chile

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Viña del Mar, , Chile

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Bogotá, , Colombia

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Medellín, , Colombia

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Montería, , Colombia

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Angers, , France

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Bordeaux, , France

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Institut Paoli Calmettes

Marseille, , France

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Marseille, , France

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Montpellier, , France

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Nice, , France

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Paris, , France

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Toulouse, , France

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Villejuif, , France

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HELIOS Klinikum Berlin Buch

Bad Sarrow, , Germany

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Universitätsklinikum Köln

Cologne, , Germany

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Hanover, , Germany

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Mannheim, , Germany

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Tuebingen University Hospital

Tübingen, , Germany

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Guatemala City, , Guatemala

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Jaipur, , India

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Mumbai, , India

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Nashik, , India

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Pune, , India

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Secunderabad, , India

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Haifa, , Israel

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Shaare Zedek Medical Center

Jerusalem, , Israel

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Jerusalem, , Israel

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Petah Tikva, , Israel

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Ramat Gan, , Israel

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Tel Aviv, , Israel

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Candiolo, , Italy

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Humanitas Cancer Center

Rozzana, , Italy

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Ospedale Gradenigo Oncology

Torino, , Italy

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Centro Hemato Oncologico Paitilla

Panama City, , Panama

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Medical and Research Center

Panama City, , Panama

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Wojewodzkie Centrum Onkologii

Gdansk, , Poland

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Gilwice, , Poland

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Centrum Onkologii Instytut

Warsaw, , Poland

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Bucharest, , Romania

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Cluj-Napoca, , Romania

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Craiova, , Romania

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Moscow, , Russia

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Obninsk, , Russia

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Saint Petersburg, , Russia

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Yaroslavl, , Russia

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Singapore, , Singapore

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Badalona, , Spain

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Madrid, , Spain

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Hospital Universitario Puerta de Hierro

Majadahonda, , Spain

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Valencia, , Spain

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The Royal Marsden NHS Foundation Trust Sarcoma

London, , United Kingdom

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Christie Hospital NHS Foundation Trust

Manchester, , United Kingdom

Site Status

Countries

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United States Argentina Australia Belgium Brazil Canada Chile Colombia France Germany Guatemala India Israel Italy Panama Poland Romania Russia Singapore Spain United Kingdom

References

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Ryan CW, Merimsky O, Agulnik M, Blay JY, Schuetze SM, Van Tine BA, Jones RL, Elias AD, Choy E, Alcindor T, Keedy VL, Reed DR, Taub RN, Italiano A, Garcia Del Muro X, Judson IR, Buck JY, Lebel F, Lewis JJ, Maki RG, Schoffski P. PICASSO III: A Phase III, Placebo-Controlled Study of Doxorubicin With or Without Palifosfamide in Patients With Metastatic Soft Tissue Sarcoma. J Clin Oncol. 2016 Nov 10;34(32):3898-3905. doi: 10.1200/JCO.2016.67.6684. Epub 2016 Sep 30.

Reference Type DERIVED
PMID: 27621408 (View on PubMed)

Other Identifiers

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IPM3001

Identifier Type: -

Identifier Source: org_study_id

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