Safety and Effectiveness of AZLI (an Inhaled Antibiotic) in Adults With Non-Cystic Fibrosis Bronchiectasis

NCT ID: NCT01314716

Last Updated: 2014-04-16

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

274 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-04-30

Study Completion Date

2013-07-31

Brief Summary

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The AIR-BX2 study enrolled people with non-cystic fibrosis (non-CF) bronchiectasis and gram-negative airway infection. Participants received two 28-day courses of either Aztreonam for Inhalation Solution (AZLI) or placebo taken 3 times a day. Each course was followed by a 28-day off-drug period. Following the two blinded courses, all participants received a 28-day course of open-label AZLI then were followed for an additional 56 days.

Detailed Description

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Conditions

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Bronchiectasis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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AZLI-AZLI

Participants were randomized to receive blinded AZLI for 2 cycles of 28 days on treatment with each cycle followed by 28 days off treatment, followed by open-label AZLI for 28 days plus 56 days of treatment-free follow-up.

Group Type EXPERIMENTAL

AZLI

Intervention Type DRUG

AZLI 75 mg reconstituted with diluent and administered via nebulizer three times daily

Placebo-AZLI

Participants were randomized to receive blinded placebo to match AZLI for 2 cycles of 28 days on treatment with each cycle followed by 28 days off treatment, followed by open-label AZLI for 28 days plus 56 days of treatment-free follow-up.

Group Type PLACEBO_COMPARATOR

AZLI

Intervention Type DRUG

AZLI 75 mg reconstituted with diluent and administered via nebulizer three times daily

Placebo

Intervention Type DRUG

Placebo to match AZLI administered via nebulizer three times daily

Interventions

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AZLI

AZLI 75 mg reconstituted with diluent and administered via nebulizer three times daily

Intervention Type DRUG

Placebo

Placebo to match AZLI administered via nebulizer three times daily

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Male/Female 18 years or older with non-CF bronchiectasis
* Chronic sputum production on most days
* Positive sputum culture for gram-negative organisms
* Must have met lung function requirements

Exclusion Criteria

* History of CF
* Hospitalized within 14 days prior to joining the study
* Previous exposure to AZLI
* Pregnant, breastfeeding, or unwilling to follow contraceptive measures for the study
* Must have met liver and kidney function requirements
* Continuous oxygen use of greater than 2 liters per minute (supplemental oxygen with activity and at night was allowed)
* Treatment for nontuberculous mycobacteria infection or active mycobacterium tuberculosis infection within 1 year of enrollment
* Other serious medical conditions.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Anne O'Donnell, MD

Role: PRINCIPAL_INVESTIGATOR

Georgetown University Hospital

Locations

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Florence Research Associates

Florence, Alabama, United States

Site Status

Clinical Trials Connection

Flagstaff, Arizona, United States

Site Status

Phoenix Medical Group

Peoria, Arizona, United States

Site Status

Pulmonary Associates

Phoenix, Arizona, United States

Site Status

AZ Pulmonary Specialists, LTD

Scottsdale, Arizona, United States

Site Status

Pulmonary Consultants & Primary Care Physicians Medical Group, Inc.

Orange, California, United States

Site Status

UC San Diego Medical Center

San Diego, California, United States

Site Status

California Pacific Medical Center

San Francisco, California, United States

Site Status

Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status

University of Florida

Jacksonville, Florida, United States

Site Status

University of Miami Miller School of Medicine

Miami, Florida, United States

Site Status

Central Florida Pulmonary Group

Orlando, Florida, United States

Site Status

Sarasota Memorial Hospital - Clinical Research Center

Sarasota, Florida, United States

Site Status

Pasadena Center for Medical Research

St. Petersburg, Florida, United States

Site Status

Tampa General Hospital - New Lung Associates

Tampa, Florida, United States

Site Status

Florida Premier Research Institute

Winter Park, Florida, United States

Site Status

Southeastern Lung Care PC

Decatur, Georgia, United States

Site Status

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status

Loess Hills Clinical Research

Council Bluffs, Iowa, United States

Site Status

Kentuckiana Pulmonary Associates

Louisville, Kentucky, United States

Site Status

Pulmonary & Critical Care Associates of Baltimore

Rosedale, Maryland, United States

Site Status

Robert Wood Johnson Medical School

New Brunswick, New Jersey, United States

Site Status

Pulmonary & Allergy Associates, P.A.

Summit, New Jersey, United States

Site Status

Jamaica Hospital Medical Center

Jamaica, New York, United States

Site Status

Columbia University, NY Presbyterian Hospital

New York, New York, United States

Site Status

UNC Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

The Oregon Clinic P.C./ Pulmonary Division

Portland, Oregon, United States

Site Status

University of Pennsylvania Medical Center

Philadelphia, Pennsylvania, United States

Site Status

University of Texas Health Science Center at Tyler

Tyler, Texas, United States

Site Status

University of Utah

Salt Lake City, Utah, United States

Site Status

Pulmonary Consultants, PLLC

Tacoma, Washington, United States

Site Status

University of Wisconsin Hospital and Clinics

Madison, Wisconsin, United States

Site Status

Medical College of Wisconsin Froedtert Hospital

Milwaukee, Wisconsin, United States

Site Status

Concord Hospital

Concord, New South Wales, Australia

Site Status

St Vincent's Hospital

Darlinghurst, New South Wales, Australia

Site Status

St George Hospital

Kogarah, New South Wales, Australia

Site Status

Royal Perth Hospital

Perth, New South Wales, Australia

Site Status

Westmead Hospital

Westmead, New South Wales, Australia

Site Status

Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status

Repatriation General Hospital

Daw Park, South Australia, Australia

Site Status

Burnside War Memorial Hospital Pharmacy

Toorak Gardens, South Australia, Australia

Site Status

Sir Charles Gairdner Hospital

Nedlands, Western Australia, Australia

Site Status

CUB Hôpital Erasme

Brussels, , Belgium

Site Status

Universitair Ziekenhuis Antwerpen

Edegem, , Belgium

Site Status

KUL UZ Gasthuisberg

Leuven, , Belgium

Site Status

Kelowna Respiratory Research and Allergy Clinic

Kelowna, British Columbia, Canada

Site Status

The Lung Centre at Vancouver General Hospital

Vancouver, British Columbia, Canada

Site Status

St. Michael's Hospital

Toronto, Ontario, Canada

Site Status

CHICAS - Centre Hospitalier Intercommunal des Alpes du sud, site de GAP

Gap, PACA, , France

Site Status

Service Activite Ambulatoire Pole Cardiovasculaire Hopital Nord

Marseille, , France

Site Status

CHU de Montpellier-Hopital Arnaud de Villeneuve

Montpellier, , France

Site Status

Hôpital Pasteur, CHU de Nice

Nice, , France

Site Status

Hopital Haut-Leveque

Pessac, , France

Site Status

CHU Toulouse - Hôpital Larrey

Toulouse, , France

Site Status

Charite Campus Virchow-Klinikum

Berlin, , Germany

Site Status

Research Center for Medical Studies (RCMS)

Berlin-Charlottenburg (Westend), , Germany

Site Status

Universitätsklinikum Freiburg

Freiburg im Breisgau, , Germany

Site Status

University Hospital Giessen

Giessen, , Germany

Site Status

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status

Universitätsklinikum des Saarlandes

Homburg, , Germany

Site Status

Universitätsklinikum Jena Clinic for Internal Medicine II

Jena, , Germany

Site Status

Univ.-Klinikum Leipzig, Innere Med.

Leipzig, , Germany

Site Status

POIS Leipzig GbR

Leipzig, , Germany

Site Status

Klinikum Innenstadt der LMU Munchen

Munich, , Germany

Site Status

S.Anna Hospital, University of Ferrara

Ferrara, , Italy

Site Status

UO Broncopneumologia IRCCS Fondazione Cà Granda Milano

Milan, , Italy

Site Status

University of Modena and Reggio Emilia

Modena, , Italy

Site Status

Azienda Universitaria Federico II

Naples, , Italy

Site Status

Università di Pisa - Ospedale Cisanello

Pisa, , Italy

Site Status

Ospendale Civile Maggiore Centro Regionale Fibrosi Cistica

Verona, , Italy

Site Status

Medisch Centrum Alkmaar

Alkmaar, , Netherlands

Site Status

Erasmus MC

Rotterdam, , Netherlands

Site Status

Hospital Vall d´Hebrón

Barcelona, , Spain

Site Status

Hospital Clinic i Provincial

Barcelona, , Spain

Site Status

Hospital Universitario de Bellvitge

Barcelona, , Spain

Site Status

Hospital Josep Trueta

Girona, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital La Fe

Valencia, , Spain

Site Status

Papworth Hospital NHS Trust

Cambridgeshire, , United Kingdom

Site Status

Royal Infirmary of Edinburgh

Edinburgh, , United Kingdom

Site Status

Royal Devon and Exeter Hospital, NHS Foundation Trust

Exeter, , United Kingdom

Site Status

Sir William Leech Centre for Lung Research, Freeman Hospital

Newcastle upon Tyne, , United Kingdom

Site Status

GBS RE Sheffield Teaching Hospitals NHS Foundation Trust

Sheffield, , United Kingdom

Site Status

Torbay District General Hospital

Torquay, Devon, , United Kingdom

Site Status

Royal Wolverhampton Hospitals NHS Trust

Wolverhampton, , United Kingdom

Site Status

Countries

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United States Australia Belgium Canada France Germany Italy Netherlands Spain United Kingdom

References

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Barker AF, O'Donnell AE, Flume P, Thompson PJ, Ruzi JD, de Gracia J, Boersma WG, De Soyza A, Shao L, Zhang J, Haas L, Lewis SA, Leitzinger S, Montgomery AB, McKevitt MT, Gossage D, Quittner AL, O'Riordan TG. Aztreonam for inhalation solution in patients with non-cystic fibrosis bronchiectasis (AIR-BX1 and AIR-BX2): two randomised double-blind, placebo-controlled phase 3 trials. Lancet Respir Med. 2014 Sep;2(9):738-49. doi: 10.1016/S2213-2600(14)70165-1. Epub 2014 Aug 18.

Reference Type DERIVED
PMID: 25154045 (View on PubMed)

Other Identifiers

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GS-US-219-0104

Identifier Type: -

Identifier Source: org_study_id

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