Safety and Effectiveness of AZLI (an Inhaled Antibiotic) in Adults With Non-Cystic Fibrosis Bronchiectasis

NCT ID: NCT01313624

Last Updated: 2014-04-16

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

266 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-04-30

Study Completion Date

2013-06-30

Brief Summary

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The AIR-BX1 study enrolled people with non-cystic fibrosis (non-CF) bronchiectasis and gram-negative airway infection. Participants received two 28-day courses of either Aztreonam for Inhalation Solution (AZLI) or placebo taken 3 times a day. Each course was followed by a 28-day off-drug period. Following the two blinded courses, all participants received a 28-day course of open-label AZLI then were followed for an additional 56 days.

Detailed Description

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Conditions

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Bronchiectasis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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AZLI-AZLI

Participants were randomized to receive blinded AZLI for 2 cycles of 28 days on treatment with each cycle followed by 28 days off treatment, followed by open-label AZLI for 28 days plus 56 days of treatment-free follow-up.

Group Type EXPERIMENTAL

AZLI

Intervention Type DRUG

AZLI 75 mg reconstituted with diluent and administered via nebulizer three times daily

Placebo-AZLI

Participants were randomized to receive blinded placebo to match AZLI for 2 cycles of 28 days on treatment with each cycle followed by 28 days off treatment, followed by open-label AZLI for 28 days plus 56 days of treatment-free follow-up.

Group Type PLACEBO_COMPARATOR

AZLI

Intervention Type DRUG

AZLI 75 mg reconstituted with diluent and administered via nebulizer three times daily

Placebo

Intervention Type DRUG

Placebo to match AZLI administered via nebulizer three times daily

Interventions

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AZLI

AZLI 75 mg reconstituted with diluent and administered via nebulizer three times daily

Intervention Type DRUG

Placebo

Placebo to match AZLI administered via nebulizer three times daily

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Male/Female 18 years or older with non-CF bronchiectasis
* Chronic sputum production on most days
* Positive sputum culture for gram-negative organisms
* Must have met lung function requirements

Exclusion Criteria

* History of CF
* Hospitalized within 14 days prior to joining the study
* Previous exposure to AZLI
* Pregnant, breastfeeding, or unwilling to follow contraceptive measures for the study
* Must have met liver and kidney function requirements
* Continuous oxygen use of greater than 2 liters per minute (supplemental oxygen with activity and at night was allowed)
* Treatment for nontuberculous mycobacteria infection or active mycobacterium tuberculosis infection within 1 year of enrollment
* Other serious medical conditions.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Alan Barker, MD

Role: PRINCIPAL_INVESTIGATOR

Oregon Health and Science University

Locations

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Pulmonary Associates

Phoenix, Arizona, United States

Site Status

Arizona Pulmonary Specialists, LTD

Phoenix, Arizona, United States

Site Status

St. Joseph's Hospital and Medical Center Heart and Lung Institute

Phoenix, Arizona, United States

Site Status

Arizona Pulmonary Specialists

Scottsdale, Arizona, United States

Site Status

David Geffen School of Medicine at UCLA

Los Angeles, California, United States

Site Status

UC Davis Medical Center Division of Pulmonary, Critical Care and Sleep Medicine

Sacramento, California, United States

Site Status

Landon Pediatric Foundation

Ventura, California, United States

Site Status

National Jewish Health

Denver, Colorado, United States

Site Status

University of Connecticut Health Center

Farmington, Connecticut, United States

Site Status

Bay Area Chest Physicians

Clearwater, Florida, United States

Site Status

University of Florida

Gainesville, Florida, United States

Site Status

Pulmonary Disease Specialists (PDS) Research

Kissimmee, Florida, United States

Site Status

University of Miami - Miller School of Medicine

Miami, Florida, United States

Site Status

Central Florida Pulmonary Group

Orlando, Florida, United States

Site Status

Cleveland Clinic Florida

Weston, Florida, United States

Site Status

Atlanta Pulmonary Group

Atlanta, Georgia, United States

Site Status

Pulmonary and Critical Care Associates of Baltimore

Baltimore, Maryland, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Cardio Pulmonary Research at St. Luke's Hospital

Chesterfield, Missouri, United States

Site Status

Albany Medical Center

Albany, New York, United States

Site Status

Jamaica Hospital Medical Center

Jamaica, New York, United States

Site Status

Winthrop University Hospital - Clinical Trials Center

Mineola, New York, United States

Site Status

St. Luke's Roosevelt Hospital

New York, New York, United States

Site Status

University of Cincinnati / UC Health

Cincinnati, Ohio, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

Drexel University College of Medicine

Philadelphia, Pennsylvania, United States

Site Status

University of Pennsylvania Medical Center - Pulmonary, Allergy & Critical Care Division

Philadelphia, Pennsylvania, United States

Site Status

Asthma Allergy & Pulmonary Associates

Philadelphia, Pennsylvania, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Metroplex Pulmonary and Sleep Center

McKinney, Texas, United States

Site Status

Alamo Clinical Research Associates

San Antonio, Texas, United States

Site Status

University of Texas Health Science Center at Tyler

Tyler, Texas, United States

Site Status

University of Virginia Pulmonary and Critical Care

Charlottesville, Virginia, United States

Site Status

Inova Fairfax Hospital/ Heart and Vascular Institute Advanced Lung Disease and Transplant Center

Falls Church, Virginia, United States

Site Status

Swedish Medical Center/Minor James Clinic

Seattle, Washington, United States

Site Status

Multicare Pulmonary Specialist

Tacoma, Washington, United States

Site Status

Concord Hospital

Concord, New South Wales, Australia

Site Status

St. Vincent's Hospital

Darlinghurst, New South Wales, Australia

Site Status

Woolcock Institute of Medical Research

Glebe, New South Wales, Australia

Site Status

St. George Hospital

Kogarah, New South Wales, Australia

Site Status

Royal Perth Hospital

Perth, New South Wales, Australia

Site Status

Westmead Hospital

Westmead, New South Wales, Australia

Site Status

Mater Adult Hospital

Brisbane, Queensland, Australia

Site Status

The Prince Charles Hospital

Chermside, Queensland, Australia

Site Status

Royla Adelaide Hospital

Adelaide, South Australia, Australia

Site Status

Repatriation General Hospital

Daws Park, South Australia, Australia

Site Status

Respiratory Clinical Trials

Toorak Gardens, South Australia, Australia

Site Status

Monash Medical Centre

Clayton, Victoria, Australia

Site Status

Peninsula Health

Frankston, Victoria, Australia

Site Status

Alfred Hospital

Westmead, Victoria, Australia

Site Status

Sir Charles Gairdner Hospital

Nedlands, Western Australia, Australia

Site Status

University of Calgary

Calgary, Alberta, Canada

Site Status

University of Alberta

Edmonton, Alberta, Canada

Site Status

Kelowna Respiratory and Allergy Clinic

Kelowna, British Columbia, Canada

Site Status

The Lung Centre at Vancouver General Hospital

Vancouver, British Columbia, Canada

Site Status

St. Paul's Hospital Pacific Lung Research

Vancouver, British Columbia, Canada

Site Status

Kingston General Hospital / Queen's University

Kingston, Ontario, Canada

Site Status

St. Michael's Hospital

Toronto, Ontario, Canada

Site Status

Dr. Anil Dhar Private Practice

Windsor, Ontario, Canada

Site Status

Centre Hospitalier de L'Université de Montréal Hotel Dieu

Montreal, Quebec, Canada

Site Status

Countries

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United States Australia Canada

References

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Barker AF, O'Donnell AE, Flume P, Thompson PJ, Ruzi JD, de Gracia J, Boersma WG, De Soyza A, Shao L, Zhang J, Haas L, Lewis SA, Leitzinger S, Montgomery AB, McKevitt MT, Gossage D, Quittner AL, O'Riordan TG. Aztreonam for inhalation solution in patients with non-cystic fibrosis bronchiectasis (AIR-BX1 and AIR-BX2): two randomised double-blind, placebo-controlled phase 3 trials. Lancet Respir Med. 2014 Sep;2(9):738-49. doi: 10.1016/S2213-2600(14)70165-1. Epub 2014 Aug 18.

Reference Type DERIVED
PMID: 25154045 (View on PubMed)

Other Identifiers

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GS-US-219-0101

Identifier Type: -

Identifier Source: org_study_id

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