BAX 326 (rFIX) Continuation Study

NCT ID: NCT01286779

Last Updated: 2021-05-20

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

117 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-04-12

Study Completion Date

2017-06-29

Brief Summary

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The purpose of this BAX 326 Continuation Study is to further investigate incremental recovery over time, the hemostatic efficacy, the safety, immunogenicity, and health-related quality of life (HR QoL) of BAX 326 in previously treated patients (PTPs) with severe and moderately severe hemophilia B who participated in BAX 326 pivotal study 250901 or BAX 326 pediatric study 251101.

Detailed Description

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Conditions

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Hemophilia B

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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BAX 326

Group Type EXPERIMENTAL

BAX 326 (Recombinant factor IX)

Intervention Type BIOLOGICAL

The treatment with BAX 326 will be at the discretion of the investigator and will consist of either twice weekly prophylactic treatment with 50 IU/kg, modified prophylaxis, or on-demand treatment.

Interventions

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BAX 326 (Recombinant factor IX)

The treatment with BAX 326 will be at the discretion of the investigator and will consist of either twice weekly prophylactic treatment with 50 IU/kg, modified prophylaxis, or on-demand treatment.

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

* Subject and/or legal representative has/have voluntarily provided signed informed consent
* Subject has completed Baxter clinical study 250901 (pivotal study) or Baxter clinical study 251101 (pediatric study)
* Subject was 12 to 65 years old at the time of screening for Study 250901 or \< 12 years old at the time of screening for Study 251101
* Subject has severe (FIX level \< 1%) or moderately severe (FIX level 1-2%) hemophilia B (based on the one stage activated partial thromboplastin time (aPTT) assay), as tested at screening at the central laboratory
* Subject has not developed an inhibitory FIX antibody during Baxter Pivotal Study 250901 or Pediatric Study 251101

Exclusion Criteria

* Subject received factor IX product(s) other than BAX 326 upon completion of Baxter Pivotal Study 250901 or Pediatric Study 251101
* Subject has been diagnosed with an acquired hemostatic defect other than hemophilia B
* For subjects transferring from Pivotal Study 250901: Subject's weight is \< 35 kg or \> 120 kg
* Subject is planned to take part in any other clinical study, with the exception of BAX 326 Surgery study as described in this protocol, during the course of the Continuation Study
Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Baxalta now part of Shire

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

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Instituto de Hematología y Medicina Clíncia Rubén Dávoli

Rosario, , Argentina

Site Status

UNIFESP - Universidade Estadual de Sao Paulo

São Paulo, , Brazil

Site Status

Specialized Haematological Hospital "Joan Pavel"

Sofia, , Bulgaria

Site Status

Hospital Dr. Sotero del Rio

Santiago, , Chile

Site Status

Hospital de San Jose

Bogotá, , Colombia

Site Status

Centro Medico Imbanaco

Cali, , Colombia

Site Status

Hospital Pablo Tobon Uribe

Medellín, , Colombia

Site Status

Klinika detské hematologie a onkologie

Prague, , Czechia

Site Status

Maulana Azad Medical College and Associated Hospital

New Delhi, , India

Site Status

St. James's Hospital, National Center for Hereditary Coagulation Disorders

Dublin, , Ireland

Site Status

University Hospital Policlinico Vittorio Emanuele, Hospital Ferrarotto Alessi

Catania, , Italy

Site Status

University Hospital Careggi, Agency of Hemophilia - Regional Reference Center for Inherited Bleeding

Florence, , Italy

Site Status

University of Foggia Riuniti Hospital, Department of Clinical and Experimental Medicine

Foggia, , Italy

Site Status

Hospital San Giovanni Bosco, Center for Hemophilia and Thrombosis, Department of Hematology

Naples, , Italy

Site Status

Padova University Hospital, Medical Clinic II, Center for Hemophilia

Padua, , Italy

Site Status

Nara Medical University, Department of Pediatrics

Nara, , Japan

Site Status

Tokyo Medical University

Tokyo, , Japan

Site Status

Ogikubo Hospital

Tokyo, , Japan

Site Status

Hematology and Transplantology Clinic, University Clinic Centre - Medical University Hospital

Gdansk, , Poland

Site Status

University Pediatric Hospital in Cracow

Krakow, , Poland

Site Status

Medical College of the Jagiellonian University, Department of Hematology

Krakow, , Poland

Site Status

Copernicus Hospital, Medical University in Lodz, Department of Hematology

Lodz, , Poland

Site Status

Professor Tadeusz Sokolowski Independent Public Teaching Hospital No. 1 of the Pomeranian Medical University in Szczecin

Szczecin, , Poland

Site Status

Klinika Hematologii

Warsaw, , Poland

Site Status

Institute of Haematology and Transfusion Medicine

Warsaw, , Poland

Site Status

Prof. Dr. C.T. Nicolau National Institute for Transfusional Hematology

Bucharest, , Romania

Site Status

Louis Turcanu Emergency Clinical Children´s Hospital

Timișoara, , Romania

Site Status

Federal State Institution Kirov Hematology and Blood Transfusion Research Institute under the Federal Agency for High-Tech Medical Care

Kirov, , Russia

Site Status

Pediatric Regional Clinical Hospital, Hematology Department

Krasnodar, , Russia

Site Status

Hematology Research Center RAMS, Department of Reconstructive Orthopedics for Haemophilia Patients

Moscow, , Russia

Site Status

Republican Center for Hemophilia Treatment Outpatient Clinic No. 37

Saint Petersburg, , Russia

Site Status

Regional clinical hospital

Yekaterinburg, , Russia

Site Status

Malmö University Hospital, Department of Coagulation Disorders

Malmo, , Sweden

Site Status

Taipei Medical University Hospital

Taipei City, Taipei, Taiwan

Site Status

Chung-Ho Memorial Hospital

Kaohsiung City, , Taiwan

Site Status

China Medical University Hospital

Taichung, , Taiwan

Site Status

Taichung Veterans General Hospital

Taichung, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Tri-Service General Hospital

Taipei, , Taiwan

Site Status

State Institution "Institute of Blood Pathology and Transfusion Medicine of the Academy of Medical Sciences of Ukraine"

Lviv, , Ukraine

Site Status

Katharine Dormandy Haemophilia Centre and Haemostasis Unit, Royal Free Hospital

London, , United Kingdom

Site Status

Manchester Children's Hospital

Manchester, , United Kingdom

Site Status

Countries

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Argentina Brazil Bulgaria Chile Colombia Czechia India Ireland Italy Japan Poland Romania Russia Sweden Taiwan Ukraine United Kingdom

References

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Windyga J, Stasyshyn O, Lissitchkov T, Mamonov V, Serban M, Rusen L, Ploder B, Tangada S. Safety, Immunogenicity, and Hemostatic Efficacy of Nonacog Gamma in Patients With Severe or Moderately Severe Hemophilia B: A Continuation Study. Clin Appl Thromb Hemost. 2020 Jan-Dec;26:1076029620950836. doi: 10.1177/1076029620950836.

Reference Type DERIVED
PMID: 32866032 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2010-022726-33

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

251001

Identifier Type: -

Identifier Source: org_study_id

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