BAX 802 in CHA With Inhibitors

NCT ID: NCT02895945

Last Updated: 2021-10-20

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

8 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-12-22

Study Completion Date

2021-01-22

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of BAX 802 in males with congenital hemophilia A (CHA) with inhibitors who are undergoing major or minor elective surgical, dental, or other invasive procedures.

Detailed Description

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Conditions

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Hemophilia A

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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BAX 802 in Surgery

Participants who are undergoing major or minor elective surgical, dental, or other invasive procedures.

Group Type EXPERIMENTAL

Antihemophilic Factor (Recombinant), Porcine Sequence (BAX 802)

Intervention Type BIOLOGICAL

In case of major surgery, FVIII target level is ≥80% for major surgeries/ procedures and ≥50% for minor surgeries/ procedures.

Interventions

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Antihemophilic Factor (Recombinant), Porcine Sequence (BAX 802)

In case of major surgery, FVIII target level is ≥80% for major surgeries/ procedures and ≥50% for minor surgeries/ procedures.

Intervention Type BIOLOGICAL

Other Intervention Names

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BAX 802 recombinant porcine factor VIII Obizur rpFVIII

Eligibility Criteria

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Inclusion Criteria

1. Participant requires a major or minor elective surgical, dental or other invasive procedure
2. Participant is male and ≥ 12 to ≤ 75 years old at the time of screening
3. Participant has provided signed informed consent (and assent for adolescent participants, as applicable) in accordance with local regulatory requirements
4. Participant has severe (factor VIII (FVIII) level \< 1%) or moderately severe (FVIII level ≤ 2%) congenital hemophilia A (CHA) with inhibitors to human factor VIII (hFVIII) of ≥ 0.6 Bethesda units (BU), as tested at screening at the central laboratory
5. Participant is not currently receiving or has recently received (\< 30 days) immune tolerance induction (ITI) therapy
6. Participant has a Karnofsky performance score of ≥ 60 at screening
7. Participant is human immunodeficiency virus negative (HIV-); or HIV+ with stable disease and CD4+ count ≥ 200 cells/mm\^3 at screening
8. Participant is hepatitis C virus negative (HCV-) by antibody or polymerase chain reaction (PCR) testing; or HCV+ with chronic stable hepatitis disease. Positive serologies will be confirmed by PCR testing.
9. Participant is willing and able to comply with the requirements of the protocol.

Exclusion Criteria

1. The participant requires emergency surgery
2. Severe chronic liver dysfunction or disease (e.g., ≥ 5 × upper limit of normal \[ULN\] alanine aminotransferase \[ALT\], as confirmed by central laboratory at screening or a documented prothrombin time/international normalized ratio \[PT/INR\] \> 1.5)
3. Clinically symptomatic renal disease (serum creatinine \> 2.0 mg/dL), as confirmed by central laboratory at screening
4. Anti-porcine factor VIII (pFVIII) inhibitor \> 10 BU prior to surgery
5. Platelet count \< 100,000/μL at screening
6. Participant has another active coagulation disorder, other than hemophilia A, as per the medical history
7. Planned use of α-interferon with or without ribavirin for HCV infected patients or planned use of a protease inhibitor for HIV infected patients. Patients currently taking any of these medications for ≥ 30 days are eligible
8. Known hypersensitivity to recombinant porcine factor VIII (rpFVIII), or hamster or murine proteins
9. Participant has an ongoing or recent (within 3 months of screening) thrombo-embolic disease, fibrinolysis or disseminated intravascular coagulation (DIC)
10. Participant has been exposed to an IP within 30 days prior to enrollment or is scheduled to participate in another clinical study involving an investigational product (IP) or investigational device during the course of this study
11. Participant is unable to tolerate quantity of blood to be drawn for protocol procedures
12. Participant is a family member or employee of the Investigator.
Minimum Eligible Age

12 Years

Maximum Eligible Age

75 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Baxalta Innovations GmbH, now part of Shire

INDUSTRY

Sponsor Role collaborator

Baxalta now part of Shire

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Shire

Locations

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Bleeding and Clotting Disorders Institute

Peoria, Illinois, United States

Site Status

Wake Forest University Baptist Medical Center

Winston-Salem, North Carolina, United States

Site Status

Case Western Reserve University

Cleveland, Ohio, United States

Site Status

UMHAT 'Tsaritsa Yoanna - ISUL', EAD

Sofia, , Bulgaria

Site Status

UMHATEM 'N.I. Pirogov', EAD

Sofia, , Bulgaria

Site Status

Hopital Maisonneuve-Rosemont d/b/a CIUSSS de l'Est-de-l'Île-de-Montréal

Montreal, Quebec, Canada

Site Status

Universitaetsklinikum Bonn AoeR

Bonn, , Germany

Site Status

Zentrum für Hämostaseologie, Universitätsklinikum Leipzig AöR

Leipzig, , Germany

Site Status

Presidio Ospedaliero di Castelfranco Veneto

Castelfranco Veneto, Treviso, Italy

Site Status

Azienda Ospedaliera Universitaria Careggi

Florence, , Italy

Site Status

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, , Italy

Site Status

Azienda Ospedaliera di Padova

Padua, , Italy

Site Status

UMC Utrecht

Utrecht, , Netherlands

Site Status

Oslo Universitetssykehus - Rikshospitalet

Oslo, , Norway

Site Status

Instytut Hematologii i Transfuzjologii-1-1Y7-1347

Warsaw, , Poland

Site Status

FSBI of Science "Kirov Scientific and Research Institute of Hematology and Blood Transfusion of FMBA.

Kirov, , Russia

Site Status

Bleeding Disorders Unit and Clinical Haematology Service at Charlotte Maxeke JHB Academic Hospital

Johannesburg, , South Africa

Site Status

Hospital Universitari i Politecnic La Fe

Valencia, Valencia, Spain

Site Status

Complejo Hospitalario Universitario A Coruña

A Coruña, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Ankara University Medical Faculty

Ankara, , Turkey (Türkiye)

Site Status

Ege University Medical Faculty

Izmir, , Turkey (Türkiye)

Site Status

Ege University Medical Faculty

Izmir, , Turkey (Türkiye)

Site Status

Kocaeli University Medical Faculty

Kocaeli, , Turkey (Türkiye)

Site Status

Countries

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United States Bulgaria Canada Germany Italy Netherlands Norway Poland Russia South Africa Spain Turkey (Türkiye)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://clinicaltrials.takeda.com/study-detail/5f6b5fc64db2bf003ab45d54

To obtain more information on the study, click here/on this link

Other Identifiers

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2015-005521-39

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

241502

Identifier Type: -

Identifier Source: org_study_id