A Phase 2/ 3 Trial to Evaluate the Efficacy and Safety of BAY86-6150

NCT ID: NCT01625390

Last Updated: 2015-07-01

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

10 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-06-30

Study Completion Date

2014-03-31

Brief Summary

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Haemophilia is a disorder, usually genetic, affecting mostly male individuals, in which one of the proteins needed to form blood clots (FVIII) is missing or not present in sufficient levels. In a person with haemophilia, the clotting process is much slower and the person experiences bleeding episodes that can result in serious problems and potential disability.

The current haemophilia standard of care is to maintain FVIII activity level above 1%. Sometimes, patients can develop antibodies (so called "inhibitors") against FVIII and it is no longer effective at controlling bleeds. Bleeds in these patients are currently treated using other proteins involved in the clotting process.

The purpose of this study is to investigate how effectively BAY86-6150 may stop acute bleeds in "inhibitor" patients. This study consists of two parts, A and B. The purpose of part A is to find the most effective yet tolerable out of four doses of BAY86-6150 with regard to efficacy and safety (dose-finding part). Part A is expected to last 9 - 29 months. The purpose of part B is to confirm efficacy and safety of the dose found in part A in all participating patients (confirmatory part). Part B is expected to last 12-32 months.

Approximately 60 male subjects 12 to 62 years-of-age with moderate or severe haemophilia A or B, with inhibitors to FVIII or FIX, who have had 4 or more bleeding episodes in the last 6 months, will participate in this study.

Patient's bleeds will be treated with BAY86-6150 and with a rescue medication if no response is made to BAY86-6150. Patients will attend the treatment centre at regular intervals and be required to keep an electronic diary.

Detailed Description

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Conditions

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Hemophilia A, Hemophilia B

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

CROSSOVER

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm 1

Group Type EXPERIMENTAL

BAY86-6150

Intervention Type DRUG

Four dose levels (6.5 µg/kg, 20 µg/kg, 50 µg/kg and 90 µg/kg) of BAY86-6150 will be studied.

Arm 2

Group Type ACTIVE_COMPARATOR

eptacog alfa [activated]

Intervention Type DRUG

comparative PK/PD (pharmacokinetics/pharmacodynamics) evaluation

Arm 3

Group Type EXPERIMENTAL

BAY86-6150

Intervention Type DRUG

Confirmation of recommended dose of BAY86-6150 to be evaluated further as determined in Part A.

Interventions

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BAY86-6150

Four dose levels (6.5 µg/kg, 20 µg/kg, 50 µg/kg and 90 µg/kg) of BAY86-6150 will be studied.

Intervention Type DRUG

eptacog alfa [activated]

comparative PK/PD (pharmacokinetics/pharmacodynamics) evaluation

Intervention Type DRUG

BAY86-6150

Confirmation of recommended dose of BAY86-6150 to be evaluated further as determined in Part A.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Male subjects
* 12 to 62 years-of-age
* History of moderate or severe congenital hemophilia A or B with inhibitors to FVIII or FIX
* 4 or more bleeding episodes in the last 6 months before enrollment.

Exclusion Criteria

* Clinically relevant coagulation disorder other than congenital hemophilia A or B with inhibitors
* History of coronary and/or peripheral atherosclerotic disease
* Disseminated intravascular coagulopathy, or stage 2 hypertension
* Angina pectoris
* Myocardial infarction
* Transient ischemic attack
* Stroke
* Congestive heart failure
* Thromboembolic event
Minimum Eligible Age

12 Years

Maximum Eligible Age

62 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Bayer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bayer Study Director

Role: STUDY_DIRECTOR

Bayer

Locations

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Sacramento, California, United States

Site Status

Chattanooga, Tennessee, United States

Site Status

Melbourne, Victoria, Australia

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Rio de Janeiro, Rio de Janeiro, Brazil

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São Paulo, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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Sofia, , Bulgaria

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Santiago, , Chile

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Guangzhou, Guangdong, China

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Beijing, , China

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Tianjin, , China

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Barranquilla, Atlántico, Colombia

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Bogotá, , Colombia

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Aarhus N, , Denmark

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Lyon, , France

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Tours, , France

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Villingen-Schwenningen, Baden-Wurttemberg, Germany

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Mainz, Rhineland-Palatinate, Germany

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Budapest, , Hungary

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Debrecen, , Hungary

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Hyderabad, Andhra Pradesh, India

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Ludhiana, Punjab, India

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Bangalore, , India

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Pune, , India

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Tel Litwinsky, , Israel

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Florence, , Italy

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Milan, , Italy

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Kashihara, Nara, Japan

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Shinjuku-ku, Tokyo, Japan

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Suginami, Tokyo, Japan

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Guadalajara, Jalisco, Mexico

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Oaxaca City, Oaxaca, Mexico

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San Luis Potosí City, San Luis Potosí, Mexico

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México D. F., , Mexico

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Utrecht, , Netherlands

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Christchurch, , New Zealand

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Warsaw, , Poland

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Timișoara, Timiș County, Romania

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Bucharest, , Romania

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Bucharest, , Romania

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Khabarovsk, , Russia

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Saint Petersburg, , Russia

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Samara, , Russia

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Yekaterinburg, , Russia

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Singapore, , Singapore

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Singapore, , Singapore

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Bloemfontein, Freestate, South Africa

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Johannesburg, Gauteng, South Africa

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Pretoria, Gauteng, South Africa

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Seoul, , South Korea

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Gothenburg, , Sweden

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Taipei, Taipei, Taiwan

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Changhua, , Taiwan

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Taipei, , Taiwan

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Istanbul, , Turkey (Türkiye)

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Izmir, , Turkey (Türkiye)

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Donetsk, , Ukraine

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Lviv, , Ukraine

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Odesa, , Ukraine

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London, , United Kingdom

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Truro, , United Kingdom

Site Status

Countries

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United States Australia Brazil Bulgaria Chile China Colombia Denmark France Germany Hungary India Israel Italy Japan Mexico Netherlands New Zealand Poland Romania Russia Singapore South Africa South Korea Sweden Taiwan Turkey (Türkiye) Ukraine United Kingdom

Other Identifiers

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15534

Identifier Type: -

Identifier Source: org_study_id

2011-000323-33

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

U1111-1133-2156

Identifier Type: OTHER

Identifier Source: secondary_id

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