Multiple Escalating Dose Study of BAY1093884 in Adults With Hemophilia A or B With or Without Inhibitors

NCT ID: NCT03597022

Last Updated: 2020-11-30

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

24 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-07-24

Study Completion Date

2019-10-15

Brief Summary

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The purpose of this study was to assess the safety and tolerability of multiple doses of a human monoclonal antibody (BAY1093884) given under the skin in subjects with hemophilia A or B. This antibody was intended to protect from bleeds by inhibiting a substance (Tissue Factor Pathway Inhibitor, TFPI) that reduces the ability of the body to form blood clots.

Detailed Description

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The primary objective of the study was to assess the safety and tolerability of multiple subcutaneous injections of BAY1093884 (anti-TFPI monoclonal antibody, immunoglobulin G2, IgG2) in patients with hemophilia A or B with or without inhibitors.

Conditions

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Hemophilia A and B

Keywords

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Subcutaneous Prophylaxis Non-Inhibitors Inhibitors

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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BAY1093884 100mg

Subjects received BAY1093884 100 mg once a week until premature termination of the study

Group Type EXPERIMENTAL

Befovacimab (BAY1093884)

Intervention Type DRUG

Once weekly doses until premature termination of the study, subcutaneous injection

BAY1093884 225mg

Subjects received BAY1093884 225 mg once a week until premature termination of the study

Group Type EXPERIMENTAL

Befovacimab (BAY1093884)

Intervention Type DRUG

Once weekly doses until premature termination of the study, subcutaneous injection

BAY1093884 400mg

Subjects received BAY1093884 400mg once a week until premature termination of the study

Group Type EXPERIMENTAL

Befovacimab (BAY1093884)

Intervention Type DRUG

Once weekly doses until premature termination of the study, subcutaneous injection

Interventions

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Befovacimab (BAY1093884)

Once weekly doses until premature termination of the study, subcutaneous injection

Intervention Type DRUG

Other Intervention Names

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Anti-TFPI (Tissue Factor Pathway Inhibitor) monoclonal antibody (immunoglobulin G2; IgG2)

Eligibility Criteria

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Inclusion Criteria

* Male severe hemophilic patients with undetectable FVIII activity \<1% or FIX activity \<2%, with or without inhibitors (any titer) are eligible.
* Subjects with a past history of inhibitors (any inhibitor titer) are eligible.
* Age ≥18 years.
* Documentation of ≥4 bleeding episodes (any type or location of bleeds, treated or not) within the 6 months prior to screening.
* For subjects on prophylaxis: Willingness to interrupt ongoing prophylaxis.
* For subjects on immune tolerance induction (ITI): Willingness to interrupt ongoing ITI.

Exclusion Criteria

* History of any other coagulation disorder (particularly disseminated intravascular coagulopathy or combined FVIII/FV deficiency) or platelet disorder.
* History of diseases related to venous thromboembolic events (e.g., pulmonary embolism, deep vein thrombosis, thrombophlebitis) or thrombotic microangiopathy.
* Risk factors for venous or arterial diseases (e.g., uncontrolled hypertension, uncontrolled diabetes).
* History of cardiac, coronary and/or arterial peripheral atherosclerotic disease
* Platelet count \<100,000/μL.
* Human immunodeficiency virus (HIV) infection with a cluster of differentiation 4 (CD4+) lymphocyte count of \<200/mm\^3
Minimum Eligible Age

18 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Bayer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Fiona Stanley Hospital

Murdoch, Western Australia, Australia

Site Status

Universitätsklinikum AKH Wien

Vienna, , Austria

Site Status

Medical centre Hipokrat - N EOOD

Plovdiv, , Bulgaria

Site Status

SHATHD Spec. Hospi. for Active Treatm. of Haematol. Dis. EAD

Sofia, , Bulgaria

Site Status

MHAT Sveta Marina EAD

Varna, , Bulgaria

Site Status

Hôpital Louis Pradel - Bron

Bron, , France

Site Status

Hôpital Robert Debré - Reims Cedex

Reims, , France

Site Status

Pecsi Tudomanyegyetem Klinikai Kozpont

Pécs, , Hungary

Site Status

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, Lombardy, Italy

Site Status

Ogikubo Hospital

Suginami, Tokyo, Japan

Site Status

Hiroshima University Hospital

Hiroshima, , Japan

Site Status

Haematology Service, Canterbury Health Laboratories

Christchurch, , New Zealand

Site Status

Eulji University Hospital

Daejeon, , South Korea

Site Status

Changhua Christian Hospital

Changhua, , Taiwan

Site Status

University Hospital of Wales

Cardiff, , United Kingdom

Site Status

Royal Free Hospital

London, , United Kingdom

Site Status

Manchester Royal Infirmary

Manchester, , United Kingdom

Site Status

Countries

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South Africa Australia Austria Bulgaria France Hungary Italy Japan New Zealand South Korea Taiwan United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://clinicaltrials.bayer.com/

Click here to find results for studies related to Bayer products

http://www.clinicaltrialsregister.eu/

Click here to find information about studies related to Bayer Healthcare products conducted in Europe

Other Identifiers

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2017-003324-67

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

19580

Identifier Type: -

Identifier Source: org_study_id