Efficacy and Safety of AMR101 (Ethyl Icosapentate) in Patients With Fasting Triglyceride (Tg) Levels ≥ 500 and ≤ 2000 mg/dL

NCT ID: NCT01047683

Last Updated: 2022-04-25

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

229 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-12-31

Study Completion Date

2011-07-31

Brief Summary

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The primary objective is to determine the efficacy of AMR101 (ethyl icosapentate) compared to placebo in lowering fasting triglyceride levels in patients with very high fasting triglyceride levels ≥ 500 and ≤ 2000 mg/dL.

Detailed Description

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Conditions

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Hypertriglyceridemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo 4 capsules/day for 12 weeks (Weeks 1-12)

AMR101 (ethyl icosapentate) - 2 g/day

Group Type EXPERIMENTAL

AMR101 (ethyl icosapentate) - 2 g/day

Intervention Type DRUG

AMR101 (ethyl icosapentate) 2 capsules/day with placebo 2 capsules/day for 12 weeks (Weeks 1-12)

AMR101 (ethyl icosapentate) - 4 g/day

Group Type EXPERIMENTAL

AMR101 (ethyl icosapentate) - 4 g/day

Intervention Type DRUG

AMR101 (ethyl icosapentate) 4 capsules/day for 12 weeks (Weeks 1-12)

Interventions

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AMR101 (ethyl icosapentate) - 4 g/day

AMR101 (ethyl icosapentate) 4 capsules/day for 12 weeks (Weeks 1-12)

Intervention Type DRUG

AMR101 (ethyl icosapentate) - 2 g/day

AMR101 (ethyl icosapentate) 2 capsules/day with placebo 2 capsules/day for 12 weeks (Weeks 1-12)

Intervention Type DRUG

Placebo

Placebo 4 capsules/day for 12 weeks (Weeks 1-12)

Intervention Type DRUG

Other Intervention Names

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VASCEPA® (icosapent ethyl) VASCEPA® (icosapent ethyl)

Eligibility Criteria

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Inclusion Criteria

* Men and women, ages \>18
* Fasting triglyceride ≥500 mg/dL and ≤2000 mg/dL
* Provide written informed consent and authorization for protected health information disclosure

Exclusion Criteria

* Women who are pregnant or lactating, or planning to become pregnant
* Use of non-statin lipid-altering drugs which cannot be stopped including fibrates, niacin, fish oil and other products containing omega-3 fatty acids or other dietary supplements with potential lipid-altering effects
* History of pancreatitis
* History of bariatric surgery or currently on weight loss drugs
* Uncontrolled hypertension (BP \> 160/100)
* HIV infection or on treatment with HIV-protease inhibitors, cyclophosphamide,or isotretinoin
* Consumption of more than 2 alcoholic beverages per day
* History of cancers (except if been disease free for \>5 years OR history was basal or squamous cell skin cancer)
* Participation in another clinical trial involving an investigational agent in the last 30 days
* Other parameters will be assessed at the study center to ensure eligibility for this study.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amarin Pharma Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Amarin Investigational Site

Sacramento, California, United States

Site Status

Amarin Investigational Site

Golden, Colorado, United States

Site Status

Amarin Investigational Site

Miami, Florida, United States

Site Status

Amarin Investigational Site

Miami, Florida, United States

Site Status

Amarin Investigational Site

Ocala, Florida, United States

Site Status

Amarin Investigational Site

Addison, Illinois, United States

Site Status

Amarin Investigational Site

Chicago, Illinois, United States

Site Status

Amarin Investigational Site

Louisville, Kentucky, United States

Site Status

Amarin Investigational Site

Butte, Montana, United States

Site Status

Amarin Investigational Site

Raleigh, North Carolina, United States

Site Status

Amarin Investigational Site

Winston-Salem, North Carolina, United States

Site Status

Amarin Investigational Site

Cincinnati, Ohio, United States

Site Status

Amarin Investigational Site

Cincinnati, Ohio, United States

Site Status

Amarin Investigational Site

Lyndhurst, Ohio, United States

Site Status

Amarin Investigational Site

Tulsa, Oklahoma, United States

Site Status

Amarin Investigational Site

Corpus Christi, Texas, United States

Site Status

Amarin Investigational Site

Houston, Texas, United States

Site Status

Amarin Investigational Site

Richmond, Virginia, United States

Site Status

Amarin Investigational Site

Aalborg, , Denmark

Site Status

Amarin Investigational Site

Herlev, , Denmark

Site Status

Amarin Investigational Site

Oulu, , Finland

Site Status

Amarin Investigational Site

Dresden, , Germany

Site Status

Amarin Investigational Site

Giessen, , Germany

Site Status

Amarin Investigational Site

Magdeburg, , Germany

Site Status

Amarin Investigational Site

München, , Germany

Site Status

Amarin Investigational Site

München, , Germany

Site Status

Amarin Investigational Site

Nuremberg, , Germany

Site Status

Amarin Investigational Site

Ahmedabad, , India

Site Status

Amarin Investigational Site

Bangalore, , India

Site Status

Amarin Investigational Site

Bangalore, , India

Site Status

Amarin Investigational Site

Bangalore, , India

Site Status

Amarin Investigational Site

Gopālapuram, , India

Site Status

Amarin Investigational Site

Indore, , India

Site Status

Amarin Investigational Site

Mysore, , India

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Amarin Investigational Site

Genova, , Italy

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Amarin Investigational Site

Palermo, , Italy

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Amarin Investigational Site

Guadalajara, Jalisco, , Mexico

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Amarin Investigational Site

Mexico City, , Mexico

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Amarin Investigational Site

Mexico City, , Mexico

Site Status

Amarin Investigational Site

Monterrey Nuevo Leon, , Mexico

Site Status

Amarin Investigational Site

Amsterdam, , Netherlands

Site Status

Amarin Investigational Site

Groningen, , Netherlands

Site Status

Amarin Investigational Site

Rotterdam, , Netherlands

Site Status

Amarin Investigational Site

Rotterdam, , Netherlands

Site Status

Amarin Investigational Site

Utrecht, , Netherlands

Site Status

Amarin Investigational Site

Moscow, , Russia

Site Status

Amarin Investigational Site

Moscow, , Russia

Site Status

Amarin Investigational Site

Saint Petersburg, , Russia

Site Status

Amarin Investigational Site

Saint Petersburg, , Russia

Site Status

Amarin Investigational Site

Saint Petersburg, , Russia

Site Status

Amarin Investigational Site

Bloemfontein, , South Africa

Site Status

Amarin Investigational Site

Cape Town, , South Africa

Site Status

Amarin Investigational Site

Johannesburg, , South Africa

Site Status

Amarin Investigational Site

Parktown, , South Africa

Site Status

Amarin Investigational Site

Pretoria, , South Africa

Site Status

Amarin Investigational Site

Somerset West, , South Africa

Site Status

Amarin Investigational Site

Ivano-Frankivsk, , Ukraine

Site Status

Amarin Investigational Site

Kiev, , Ukraine

Site Status

Amarin Investigational Site

Kyiv, , Ukraine

Site Status

Amarin Investigational Site

Odesa, , Ukraine

Site Status

Countries

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United States Denmark Finland Germany India Italy Mexico Netherlands Russia South Africa Ukraine

References

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Bays HE, Ballantyne CM, Kastelein JJ, Isaacsohn JL, Braeckman RA, Soni PN. Eicosapentaenoic acid ethyl ester (AMR101) therapy in patients with very high triglyceride levels (from the Multi-center, plAcebo-controlled, Randomized, double-blINd, 12-week study with an open-label Extension [MARINE] trial). Am J Cardiol. 2011 Sep 1;108(5):682-90. doi: 10.1016/j.amjcard.2011.04.015. Epub 2011 Jun 16.

Reference Type RESULT
PMID: 21683321 (View on PubMed)

Bays HE, Braeckman RA, Ballantyne CM, Kastelein JJ, Otvos JD, Stirtan WG, Soni PN. Icosapent ethyl, a pure EPA omega-3 fatty acid: effects on lipoprotein particle concentration and size in patients with very high triglyceride levels (the MARINE study). J Clin Lipidol. 2012 Nov-Dec;6(6):565-72. doi: 10.1016/j.jacl.2012.07.001. Epub 2012 Jul 24.

Reference Type RESULT
PMID: 23312052 (View on PubMed)

Bays HE, Ballantyne CM, Braeckman RA, Stirtan WG, Soni PN. Icosapent ethyl, a pure ethyl ester of eicosapentaenoic acid: effects on circulating markers of inflammation from the MARINE and ANCHOR studies. Am J Cardiovasc Drugs. 2013 Feb;13(1):37-46. doi: 10.1007/s40256-012-0002-3.

Reference Type RESULT
PMID: 23325450 (View on PubMed)

Braeckman RA, Manku MS, Bays HE, Stirtan WG, Soni PN. Icosapent ethyl, a pure EPA omega-3 fatty acid: effects on plasma and red blood cell fatty acids in patients with very high triglyceride levels (results from the MARINE study). Prostaglandins Leukot Essent Fatty Acids. 2013 Sep;89(4):195-201. doi: 10.1016/j.plefa.2013.07.005. Epub 2013 Aug 1.

Reference Type RESULT
PMID: 23992935 (View on PubMed)

Bays HE, Ballantyne CM, Braeckman RA, Stirtan WG, Doyle RT Jr, Philip S, Soni PN, Juliano RA. Icosapent Ethyl (Eicosapentaenoic Acid Ethyl Ester): Effects Upon High-Sensitivity C-Reactive Protein and Lipid Parameters in Patients With Metabolic Syndrome. Metab Syndr Relat Disord. 2015 Aug;13(6):239-47. doi: 10.1089/met.2014.0137. Epub 2015 Apr 20.

Reference Type RESULT
PMID: 25893544 (View on PubMed)

Ballantyne CM, Bays HE, Braeckman RA, Philip S, Stirtan WG, Doyle RT Jr, Soni PN, Juliano RA. Icosapent ethyl (eicosapentaenoic acid ethyl ester): Effects on plasma apolipoprotein C-III levels in patients from the MARINE and ANCHOR studies. J Clin Lipidol. 2016 May-Jun;10(3):635-645.e1. doi: 10.1016/j.jacl.2016.02.008. Epub 2016 Feb 23.

Reference Type RESULT
PMID: 27206952 (View on PubMed)

Ballantyne CM, Bays HE, Philip S, Doyle RT Jr, Braeckman RA, Stirtan WG, Soni PN, Juliano RA. Icosapent ethyl (eicosapentaenoic acid ethyl ester): Effects on remnant-like particle cholesterol from the MARINE and ANCHOR studies. Atherosclerosis. 2016 Oct;253:81-87. doi: 10.1016/j.atherosclerosis.2016.08.005. Epub 2016 Aug 20.

Reference Type RESULT
PMID: 27596132 (View on PubMed)

Bays HE, Ballantyne CM, Doyle RT Jr, Juliano RA, Philip S. Icosapent ethyl: Eicosapentaenoic acid concentration and triglyceride-lowering effects across clinical studies. Prostaglandins Other Lipid Mediat. 2016 Sep;125:57-64. doi: 10.1016/j.prostaglandins.2016.07.007. Epub 2016 Jul 11.

Reference Type RESULT
PMID: 27418543 (View on PubMed)

Mosca L, Ballantyne CM, Bays HE, Guyton JR, Philip S, Doyle RT Jr, Juliano RA. Usefulness of Icosapent Ethyl (Eicosapentaenoic Acid Ethyl Ester) in Women to Lower Triglyceride Levels (Results from the MARINE and ANCHOR Trials). Am J Cardiol. 2017 Feb 1;119(3):397-403. doi: 10.1016/j.amjcard.2016.10.027. Epub 2016 Nov 1.

Reference Type RESULT
PMID: 27939227 (View on PubMed)

Other Identifiers

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The MARINE Study

Identifier Type: OTHER

Identifier Source: secondary_id

AMR-01-01-0016

Identifier Type: -

Identifier Source: org_study_id

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