A Study to Evaluate the Efficacy of Lenalidomide as Maintenance Therapy After Completion of First-line Combination Chemotherapy in Patients With Mantle Cell Lymphoma (MCL).

NCT ID: NCT01021423

Last Updated: 2019-11-19

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

9 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-04-01

Study Completion Date

2011-03-01

Brief Summary

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A study to evaluate the efficacy of lenalidomide as maintenance therapy after completion of first-line combination chemotherapy in patients with mantle cell lymphoma (MCL) who are not candidates for transplantation and have achieved partial response (PR) or complete response (CR).

This study was prematurely terminated by the sponsor in light of new unpublished data that rendered the current design of the study no longer clinically relevant. A study design with the control arm of no active treatment was no longer appropriate. The termination of the trial was not based on any safety concerns in the study.

Detailed Description

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Conditions

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Mantle Cell Lymphoma Non-Hodgkin's Lymphoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Lenalidomide

Lenalidomide - 15 mg orally once daily on Days 1-21 of every 28-day cycle for a maximum of 2 years or until disease progression, unacceptable toxicity develops or voluntary withdrawal.

Group Type EXPERIMENTAL

Lenalidomide

Intervention Type DRUG

15 mg orally once daily on Days 1-21 of every 28-day cycle for a maximum of 2 years or until disease progression, unacceptable toxicity develops or voluntary withdrawal.

Placebo

Placebo (identical matched capsule) orally once daily on Days 1-21 of every 28-day cycle for a maximum of 2 years or until disease progression, unacceptable toxicity develops or voluntary withdrawal.

Group Type EXPERIMENTAL

Placebo

Intervention Type OTHER

Placebo (identical matched capsule) orally once daily on Days 1-21 of every 28-day cycle for a maximum of 2 years or until disease progression, unacceptable toxicity develops or voluntary withdrawal.

Interventions

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Lenalidomide

15 mg orally once daily on Days 1-21 of every 28-day cycle for a maximum of 2 years or until disease progression, unacceptable toxicity develops or voluntary withdrawal.

Intervention Type DRUG

Placebo

Placebo (identical matched capsule) orally once daily on Days 1-21 of every 28-day cycle for a maximum of 2 years or until disease progression, unacceptable toxicity develops or voluntary withdrawal.

Intervention Type OTHER

Other Intervention Names

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Revlimid

Eligibility Criteria

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Inclusion Criteria

* Histologically-proven mantle cell non-Hodgkin's lymphoma,
* One of the following first-line induction chemotherapy regimens with rituximab: (1) combination regimen containing all of the following components: cyclophosphamide, vincristine, adriamycin and a glucocorticoid; (2) Fludarabine containing regimen such as FC (fludarabine, cyclophosphamide)
* Achieved a PR or better response after the first-line induction chemotherapy regimen (assessed by 2007 Revised Response Criteria for Malignant Lymphoma)
* ECOG performance status score of ≤ 2
* Willing to follow pregnancy precaution

Exclusion Criteria

* Patients who have received more than 1 line of induction chemotherapy;
* Patients who have received less than 4 cycles of R-CHOP, R-CHOP-like, or R-FC are ineligible;
* Patients who achieved stable disease or progressive disease as best response with first line-induction chemotherapy;
* Any of the following laboratory abnormalities:
* Absolute neutrophil count (ANC) \< 1,500 cells/mm3 (1.5\*10\^9/L)
* Platelet count \< 60,000/mm\^3 (60\*10\^9/L)
* Serum aspartate transaminase (AST/SGOT) or alanine transaminase (ALT/SGPT)) \> 3.0 times upper limit of normal (ULN), except in patients with documented liver involvement by lymphoma
* Serum bilirubin \> 1.5 times ULN, except in case of Gilbert's Syndrome and documented liver involvement by lymphoma
* Calculated creatinine clearance (i.e. Cockcroft-Gault formula) of \< 30 mL /min
* Active or any history of central nervous system (CNS) lymphoma or leptomeningeal involvement by lymphoma
* Subjects at high risk for deep vein thrombosis (DVT) not willing to take DVT prophylaxis
* Known seropositive for or active viral infection with human immunodeficiency virus (HIV), hepatitis B virus (HBV) or hepatitis C virus (HCV)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Celgene

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Martin Dreyling, Prof. Dr

Role: PRINCIPAL_INVESTIGATOR

Medizinische Klinik III der Universität München

Locations

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Sharp Healthcare Oncology Associates of San Diego

San Diego, California, United States

Site Status

Rocky Mountain Cancer Center

Denver, Colorado, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Indiana University Melvin and Bren Simon Cancer Center

Indianapolis, Indiana, United States

Site Status

Providence Cancer Center

Indianapolis, Indiana, United States

Site Status

Nebraska Hematology-Oncology, PC

Lincoln, Nebraska, United States

Site Status

Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status

Arena Oncology Associates

Lake Success, New York, United States

Site Status

Weill Cornell Medical College/New York Presbyterian Hospital

New York, New York, United States

Site Status

SUNY Upstate Medical University

Syracuse, New York, United States

Site Status

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

Avera Cancer Institute

Sioux Falls, South Dakota, United States

Site Status

University of Virginia Health Systems

Charlottesville, Virginia, United States

Site Status

Fakultni nemocnice Hradec Králové II. Interni klinika-Oddeleni klinicke hematologie

Hradec Králové, , Czechia

Site Status

Fakultni Nemocnice Olomouc, Hemato-Onkologicka Klinika

Olomouc, , Czechia

Site Status

Fakultni Nemocnice Kralovske Vinohrady

Prague, , Czechia

Site Status

Vseobecna Fakultni Nemocnice

Prague, , Czechia

Site Status

Clinic of Oncology Faculty Hospital Motol

Prague, , Czechia

Site Status

CHU Amiens Sud, Centre de Recherche Clinique - Pharmacologie Clinique

Amiens, , France

Site Status

CHU Hôpital Hotel Dieu

Angers, , France

Site Status

CHU ESTAING, Service d'Hématologie

Clermont-Ferrand, , France

Site Status

Hôpital Henri Mondor Unité Hémopathies Lymphoides

Créteil, , France

Site Status

CHD Les Oudairies, Service d'Oncologie Hématologie

La Roche-sur-Yon, , France

Site Status

Centre Hospitalier Lyon Sud, Pavillon Marcel Bérard 1F Hématologie

La Tronche, , France

Site Status

CHRU - Hôpital Claude Huriez

Lille, , France

Site Status

CHU Montpellier - Hôpital Saint Eloi Hématologie et Oncologie Médicale

Montpellier, , France

Site Status

CHRU - Hotel Dieu

Nantes, , France

Site Status

Hôpital Saint-Louis

Paris, , France

Site Status

CHRU - Hôpital du Haut Lévêque, maladies du sang, Centre François Magendie

Pessac, , France

Site Status

Centre Hospitalier Lyon Sud, Pavillon Marcel Bérard 1F Hématologie

Pierre-Bénite, , France

Site Status

CHU de Poitiers, Pôle Régional de Cancérologie, Service d'Oncologie Hématologie et Thérapie Cellulaire

Poitiers, , France

Site Status

CHU de Reims, Hôpital Robert Debré, Hématologie Clinique

Reims, , France

Site Status

Hôpital Pontchaillou Hématologie Clinique

Rennes, , France

Site Status

Centre Henri Becquerel

Rouen, , France

Site Status

Hôpital Purpan CHU de Toulouse

Toulouse, , France

Site Status

Hôpital Bretonneau - CHU Tours

Tours, , France

Site Status

CHU de Nancy Hôpital de Brabois, Service d'Hématologie et Médecine Interne

Vandœuvre-lès-Nancy, , France

Site Status

Universitätsklinikum Essen Zentrum für Innere Medizin

Essen, , Germany

Site Status

Universitätsklinikum Freiburg - Medizinische Klinik - Abteilung Innere Medizin I: Hämatologie und Onkologie

Freiburg im Breisgau, , Germany

Site Status

UKG Universitätsklinikum Göttingen Zentrum Innere Medizin Hämatologie / Onkologie

Göttingen, , Germany

Site Status

Asklepios Klinik St. Georg - Abteilung für Hämatologie und Stammzelltransplantation

Hamburg, , Germany

Site Status

Städtisches Klinikum Karlsruhe - Hämatologie / Onkologie Karlsruhe

Karlsruhe, , Germany

Site Status

Klinikum der Universität München - Großhadern, Medizinische Klinik III

München, , Germany

Site Status

Universitaetsklinikum Tuebingen

Tübingen, , Germany

Site Status

Soroka Medical Center The Institute of Hematology

Beersheba, , Israel

Site Status

Davidoff Cancer Center The Institute of Hematology

Petah Tikva, , Israel

Site Status

Az. Osp. SS.Antonio e Biagio SC Ematologia

Alessandria, , Italy

Site Status

Ospedale Regionale di Bolzano - Divisione di Ematologia

Bolzano, , Italy

Site Status

Hematology Dept, Azienda Ospedaliero Universitaria Careggi

Florence, , Italy

Site Status

Azienda Ospedaliera Universitaria "San Martino"

Genova, , Italy

Site Status

Az. Osp. Ospedali Riuniti Papardo - Piemonte - S.C. Ematologia

Messina, , Italy

Site Status

A,O Ospedale Niguarda Ca Granda Dept Hematology

Milan, , Italy

Site Status

Fondazione San Raffaele del Monte Tabor I.R.C.C.S.

Milan, , Italy

Site Status

Istituto Nazionale Tumori Fondazione "G. Pascale" - Oncoematologia

Napoli, , Italy

Site Status

Università del Piemonte Orientale "Amedeo Avogadro"

Novara, , Italy

Site Status

Policlinico San Matteo - Dip. Di Ematologia

Pavia, , Italy

Site Status

Az. Osp. Bianchi Melacrino Morelli, Div. Di Ematologia

Reggio Calabria, , Italy

Site Status

Università Cattolica del Sacro Cuore Policlinico A. Gemelli

Roma, , Italy

Site Status

IRCCS Casa Sollievo della Sofferenza Div. Di Oncoematologia

S.Giovanni Rotondo (FG), , Italy

Site Status

Azienda Sanitaria Ospedaliera San Giovanni Battista (Molinette)

Torino, , Italy

Site Status

Ospedale Cardinale G. Panico - Ematologia e Immunoematologia

Tricase, , Italy

Site Status

Clinica Ematologica - DIRM Azienda Ospedaliera Universitaria

Udine, , Italy

Site Status

Małopolskie Centrum Medyczne

Krakow, , Poland

Site Status

Wojewodzki Szpital Specjalistczny im. Mikolaja Kopernika

Lodz, , Poland

Site Status

Dolnoslaskie Centrum Transplantacji Komórkowych

Wroclaw, , Poland

Site Status

Serviço de Hematologia

Coimbra, , Portugal

Site Status

Instituto Português de Oncologia (IPO) de Lisboa

Lisbon, , Portugal

Site Status

Instituto Português de Oncologia (IPO) do Porto

Porto, , Portugal

Site Status

Centro de Cancer, Hospital Espanol Auxilio de Puerto Rico

San Juan, , Puerto Rico

Site Status

Republican Clinical Oncological Dispensary

Kazan', , Russia

Site Status

Russian Oncological Research Centre

Moscow, , Russia

Site Status

Perm Regional Clinical Hospital

Perm, , Russia

Site Status

Russian Scientific-research Institute of Hematology and Transfusiology of Federal Medical-biological agency

Saint Petersburg, , Russia

Site Status

State Educational Institution of High Professional Education

Saint Petersburg, , Russia

Site Status

Federal Center of Heart, Blood and Endocrinology n.a. V.A. Almazov Rosmedtechnologies

Saint Petersburg, , Russia

Site Status

State Healthcare Institution "Volgograd Regional Clinical OncologyDispensary #1

Volgograd, , Russia

Site Status

Sverdlovsk Regional Clinical Hospital - Volgogradskaya

Yekaterinburg, , Russia

Site Status

Hospital Universitario Vall d´Hebrón Hematology Department

Barcelona, , Spain

Site Status

Hospital de Madrid Norte- Sanchinarro

Madrid, , Spain

Site Status

Hospital Costa del Sol, Oncology

Marbella (Málaga), , Spain

Site Status

C. H. de Orense

Ourense, , Spain

Site Status

Clinica Universitaria de Navarra, Hematology

Pamplona, , Spain

Site Status

Hospital Clínico Universitario de Salamanca

Salamanca, , Spain

Site Status

Hospital Marques de Valdecilla

Santander, , Spain

Site Status

Kent and Canterbury Hospital

Canterbury, Kent, , United Kingdom

Site Status

Torbay Hospital

County of Devon, , United Kingdom

Site Status

Royal Devon & Exeter Hospital

Exeter, , United Kingdom

Site Status

Beatson West of Scotland Cancer Centre

Glasgow, , United Kingdom

Site Status

Barts & The London NHS Trust Medical Oncology

London, , United Kingdom

Site Status

Derriford Hospital

Plymouth, , United Kingdom

Site Status

Salisbury NHS Foundation Trust, Haematology

Salisbury, , United Kingdom

Site Status

St Helens Hospital, Lilac Lower Ground

St Helens, , United Kingdom

Site Status

Countries

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United States Czechia France Germany Israel Italy Poland Portugal Puerto Rico Russia Spain United Kingdom

References

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Vose JM, Habermann TM, Czuczman MS, Zinzani PL, Reeder CB, Tuscano JM, Lossos IS, Li J, Pietronigro D, Witzig TE. Single-agent lenalidomide is active in patients with relapsed or refractory aggressive non-Hodgkin lymphoma who received prior stem cell transplantation. Br J Haematol. 2013 Sep;162(5):639-47. doi: 10.1111/bjh.12449. Epub 2013 Jul 9.

Reference Type DERIVED
PMID: 23834234 (View on PubMed)

Other Identifiers

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CC-5013-MCL-003

Identifier Type: -

Identifier Source: org_study_id

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