Clinical Study to Evaluate the Efficacy, Safety, and Tolerability of ACT-128800 in Patients With Relapsing-remitting Multiple Sclerosis

NCT ID: NCT01006265

Last Updated: 2025-03-30

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

464 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-10-01

Study Completion Date

2011-07-01

Brief Summary

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This study will assess the efficacy, safety, and tolerability of ACT-128800 in patients with relapsing-remitting multiple sclerosis.

Detailed Description

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Conditions

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Multiple Sclerosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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ACT-128800 Dose 1

ACT-128800 Dose 1

Group Type EXPERIMENTAL

ACT-128800 Dose 1

Intervention Type DRUG

ACT-128800 (Dose 1) administered orally once daily

ACT-128800 Dose 2

ACT-128800 Dose 2

Group Type EXPERIMENTAL

ACT-128800 Dose 2

Intervention Type DRUG

ACT-128800 (Dose 2) administered orally once daily

ACT-128800 Dose 3

ACT-128800 Dose 3

Group Type EXPERIMENTAL

ACT-128800 Dose 3

Intervention Type DRUG

ACT-128800 (Dose 3) administered orally once daily

Placebo

Matching placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching placebo administered orally once daily

Interventions

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ACT-128800 Dose 1

ACT-128800 (Dose 1) administered orally once daily

Intervention Type DRUG

Placebo

Matching placebo administered orally once daily

Intervention Type DRUG

ACT-128800 Dose 2

ACT-128800 (Dose 2) administered orally once daily

Intervention Type DRUG

ACT-128800 Dose 3

ACT-128800 (Dose 3) administered orally once daily

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Adult males and females
* Diagnosis of RRMS as defined by the revised (2005) McDonald Diagnostic Criteria for Multiple Sclerosis (MS).
* Signed inform consent prior to initiation of any study-mandated procedure.

Exclusion Criteria

* A diagnosis of MS categorized as primary progressive or secondary progressive or progressive relapsing.
* Patients currently treated for an autoimmune disorder other than MS.
* Contraindications for MRI.
* Ongoing bacterial, viral, or fungal infection.
* History or presence of malignancy.
Minimum Eligible Age

18 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Actelion

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Actelion Pharmaceuticals

Role: STUDY_DIRECTOR

Actelion

Locations

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Clinical Investigative Site 3132

Scottsdale, Arizona, United States

Site Status

Clinical Investigative Site 3100

Tucson, Arizona, United States

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Clinical Investigative Site 3115

Sacramento, California, United States

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Clinical Investigative Site 3117

Stanford, California, United States

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Clinical Invesigative Site 3116

Sarasota, Florida, United States

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Clinical Investigative Site 3101

Indianapolis, Indiana, United States

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Clinical Investigative Site 3105

Kansas City, Kansas, United States

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Clinical Investigative Site 3107

Lenexa, Kansas, United States

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Clinical Investigative Site 3118

Baltimore, Maryland, United States

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Clinical Investigative Site 3133

Worcester, Massachusetts, United States

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Clinical Investigator 3136

St Louis, Missouri, United States

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Clinical Investigative Site # 3135

Newark, New Jersey, United States

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Clinical Investigative Site 3129

Latham, New York, United States

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Clinical Investigative Site # 3128

New York, New York, United States

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Clinical Investigative Site 3127

Schenectady, New York, United States

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Clinical Investigative Site 3120

Stony Brook, New York, United States

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Clinical Investigative Site 3119

Raleigh, North Carolina, United States

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Clinical Investigator 3126

Akron, Ohio, United States

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Clinical Investigative Site 3113

Cincinnati, Ohio, United States

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Clinical Investigative Site 3130

Columbus, Ohio, United States

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Clinical Investigator 3104

Portland, Oregon, United States

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Clinical Investigative Site 3125

Philadelphia, Pennsylvania, United States

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Clinical Investigative Site 3112

Burlington, Vermont, United States

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Clinical Investigative Site 3111

Richmond, Virginia, United States

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Clinical Investigative Site 3102

Kirkland, Washington, United States

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Clinical Investigative Site # 1001

Fitzroy, , Australia

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Clinical Investigative Site 1000

Westmead, , Australia

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Clinical Investigative Site 1102

Amstetten, , Austria

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Clinical Investigative Site 1100

Sankt Pölten, , Austria

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Clinical Investigative Site 1101

Vienna, , Austria

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Clinical Investigative Site 1201

La Louvière, , Belgium

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Clinical Investigative Site # 1205

Liège, , Belgium

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Clinical Investigative Site 1204

Ottignies, , Belgium

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Clinical Investigative Site 1203

Sijsele-Damme, , Belgium

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Clinical Investigative Site 1302

Sofia, , Bulgaria

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Clinical Investigative Site 1301

Sofia, , Bulgaria

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Clinical Investigative Site 1303

Varna, , Bulgaria

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Clinical Investigative Site 1304

Varna, , Bulgaria

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Clinical Investigative Site 1401

Burbaby, British Columbia, Canada

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Clinical Investigative Site # 1401

Burnaby, , Canada

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Clinical Investigative Site 1400

Ottawa, , Canada

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Clinical Investigative Site 1502

Brno, , Czechia

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Clinical Investigative Site 1506

Jihlava, , Czechia

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Clinical Investigative Site 1504

Olomouc, , Czechia

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Clinical Investigative Site 1501

Ostrava-Poruba, , Czechia

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Clinical Investigative Site 1500

Prague, , Czechia

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Clinical Investigative Site 1503

Teplice, , Czechia

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Clinical Investigative Site 1600

Helsinki, , Finland

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Clinical Investigative Site 1601

Hyvinkää, , Finland

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Clinical Investigative Site 1603

Tampere, , Finland

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Clinical Investigative Site 1602

Turku, , Finland

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Clinical Investigative Site 1701

Montpellier, , France

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Clinical Investigative Site # 1806

Bayreuth, , Germany

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Clinical Investigative 1807

Berlin, , Germany

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Clinical Investigative Site 1803

Berlin, , Germany

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Clinical Investigative site 1800

Düsseldorf, , Germany

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Clinical Investigative Site 1802

Essen, , Germany

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Clinical Investigative Site 1805

Homburg/Saar, , Germany

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Clinical Investigative Site 1804

Ulm, , Germany

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Clinical Investigative Site 1905

Budapest, , Hungary

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Clinical Investigative Site # 1904

Budapest, , Hungary

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Clinical Investigative Site 1908

Budapest, , Hungary

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Clinical Investigative Site 1902

Győr, , Hungary

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Clinical Investigative Site 1900

Petofi, , Hungary

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Clinical Investigative Site 1901

Szentpeteri-Kapu, , Hungary

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Clinical Investigative Site 2000

Ashkelon, , Israel

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Clinical Investigative Site 2003

Tel Aviv, , Israel

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Clinical Investigative Site 2001

Tel Litwinsky, , Israel

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Clinical Investigative Site 2002

Ẕerifin, , Israel

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Clinical Investigative Site 2101

Gallarte, , Italy

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Clinical Investigative Site 2104

Genova, , Italy

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Clinical Investigative Site # 2106

Milan, , Italy

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Clinical Investigative Site 2102

Padua, , Italy

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Clinical Investigative Site 2103

Roma, , Italy

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Clinical Investigative Site 2105

Siena, , Italy

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Clinical Investigative Site 2203

Breda, , Netherlands

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Clinical Investigative Site 2202

Nijmegen, , Netherlands

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Clinical Investigative Site 2201

Sittard-Geleen, , Netherlands

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Clinical Investigative Site 2305

Katowice, , Poland

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Clinical Investigative Site 2303

Poznan, , Poland

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Clinical Investigative Site 2304

Warsaw, , Poland

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Clinical Investigative Site 2302

Wroclaw, , Poland

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Clinical Investigative Site 2400

Bucharest, , Romania

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Clinical Investigative Site 2401

Cluj-Napoca, , Romania

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Clinical Investigative Site 2402

Timișoara, , Romania

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Clinical Investigative Site # 3202

Moscow, , Russia

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Clinical Investigative Site # 3203

Nizhny Novgorod, , Russia

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Clinical Investigative Site # 3206

Pyatigorsk, , Russia

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Clinical Investigative Site # 3204

Saint Petersburg, , Russia

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Clinical Investigative Site 3201

Saint Petersburg, , Russia

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Clinical Investigative Site 3200

Saint Petersburg, , Russia

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Clinical Investigative Site # 3201

Samara, , Russia

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Clinical Investigative Site 3209

Saratov, , Russia

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Clinical Investigative Site 3208

Ufa, , Russia

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Clinical Investigative Site 2501

Belgrade, , Serbia

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Clinical Investigative Site 2503

Kragujevac, , Serbia

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Clinical Investigative Site 2502

Niš, , Serbia

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Clinical Investigative Site 2706

Barcelona, , Spain

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Clinical Investigative Site 2702

Madrid, , Spain

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Clinical Investigative Site 2705

Madrid, , Spain

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Clinical Investigative Site 2701

Málaga, , Spain

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Clinical Investigative Site 2700

Seville, , Spain

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Clinical Investigative Site 2704

Valencia, , Spain

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Clinical Investigative Site 2802

Gothenburg, , Sweden

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Clinical Investigative Site 2800

Stockholm, , Sweden

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Clinical Investigative Site 2801

Umed, , Sweden

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Clinical Investigative Site 2901

Lugano, , Switzerland

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Clinical Investigative Site 2900

Sankt Gallen, , Switzerland

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Clinical Investigative Site 3302

Chernihiv, , Ukraine

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Clinical Investigative Site 3303

Dnipropetrovsk, , Ukraine

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Clinical Investigative Site 3300

Kyiv, , Ukraine

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Clinical Investigative Site 3304

Odesa, , Ukraine

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Clinical Investigative Site 3003

Bristol, , United Kingdom

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Clinical Investigative Site 3004

Devon, , United Kingdom

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Clinical Investigative Site 3002

London, , United Kingdom

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Countries

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United States Australia Austria Belgium Bulgaria Canada Czechia Finland France Germany Hungary Israel Italy Netherlands Poland Romania Russia Serbia Spain Sweden Switzerland Ukraine United Kingdom

References

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Olsson T, Boster A, Fernandez O, Freedman MS, Pozzilli C, Bach D, Berkani O, Mueller MS, Sidorenko T, Radue EW, Melanson M. Oral ponesimod in relapsing-remitting multiple sclerosis: a randomised phase II trial. J Neurol Neurosurg Psychiatry. 2014 Nov;85(11):1198-208. doi: 10.1136/jnnp-2013-307282. Epub 2014 Mar 21.

Reference Type RESULT
PMID: 24659797 (View on PubMed)

Gisleskog PO, Valenzuela B, Scherz T, Burcklen M, Perez-Ruixo JJ, Poggesi I. An Exposure-Response Analysis of the Clinical Efficacy of Ponesimod in a Randomized Phase II Study in Patients with Multiple Sclerosis. Clin Pharmacokinet. 2021 Sep;60(9):1227-1237. doi: 10.1007/s40262-021-01020-2. Epub 2021 Apr 29.

Reference Type DERIVED
PMID: 33914286 (View on PubMed)

Related Links

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https://filehosting-v2.pharmacm.com/api/Attachment/Download?tenantId=80217051&parentIdentifier=AC-058B201&attachmentIdentifier=e1d8c0a4-1949-4873-b703-5a8f2bbc4094&fileName=AC-058B201_Additional_result_data_CH.pdf&versionIdentifier=

A dose-finding study to evaluate the efficacy, safety, and tolerability of three doses of ACT-128800, an oral S1P1 receptor agonist, administered for twenty-four weeks in patients with relapsing-remitting multiple sclerosis

Other Identifiers

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AC-058B201

Identifier Type: -

Identifier Source: org_study_id

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