Ribavirin Pre-treatment Followed by Combined Standard Therapy in Hepatitis C Virus (HCV) Recipients

NCT ID: NCT00993122

Last Updated: 2015-06-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE4

Total Enrollment

100 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-10-31

Study Completion Date

2012-02-29

Brief Summary

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The results of antiviral therapy in patients with recurrent hepatitis C after liver transplantation are lower than standard. Ribavirin has immune-modulating effects and seems to be crucial to optimize viral treatment. The aim of this multicenter controlled study is to examine the effect of Ribavirin pre-treatment preceding the combination therapy with peginterferon plus ribavirin on the sustained virological response.

Detailed Description

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Ribavirin Pre-Treatment Study Protocol

1. Introduction:

* Recurrence of hepatitis C infection and liver transplant:

Recurrence of hepatitis C after liver transplant is almost universal. After liver transplantation, the progression of chronic hepatitis C is more aggressive and an high percentage of recipients develop cirrhosis and rapid liver decompensation (1). Recent studies have shown that the long-term-survival-rate is significantly lower compared with non-HCV infected recipients (2). Other studies founded that antiviral treatment improves survival in these patients. Thus, the treatment of hepatitis C patients after LT is a priority for transplant units.

To date, the rate of sustained virologic response (SVR) in patients with recurrent hepatitis C after liver transplantation is about 20% with standard IFN and increases to 30% with pegylated IFN and Ribavirin (3). Lack in tolerability and low compliance to the antiviral therapy may represent an important limiting factor in order to improve the SVR. Severe myelosuppression is frequent in these patients, due to the additional effect of immunosuppressive therapy, being an additional reason to reduce antiviral drug dosage (3).
* Ribavirin:

Recent studies have evaluated the effects of a ribavirin priming before the standard combined antiviral therapy in immuno-competent patients with chronic hepatitis C (4-7). The conclusion of these studies may suggest that ribavirin pre-treatment may be a way to improve the SVR.
2. Aim of the study:

The study is a randomized un-blind multicenter project to compare the efficacy of antiviral treatment with a RBV priming vs standard antiviral treatment in patients with recurrent hepatitis C after liver transplantation.

Ribavirin pre-treatment may:
* Ameliorate therapy-compliance
* Avoid a concomitant drugs-related hematological side effects
* Modify the intra-hepatic cytokine pattern toward a better antiviral action
* Improve the SVR.

This controlled trial is not sponsored by a drug company.
3. Patients:

The protocol of the study needs to be approved by the local ethic committee. Patients are enrolled in the study after been informed of the purpose and protocol of treatment and need to sign a written informed consent.
4. Statistical analysis, sample size and randomization:

Sample size calculations were performed using EVR as the primary outcome measure. We assumed that 48 weeks intended treatment with pegylated interferon and ribavirin in transplant patients with recurrent hepatitis C induced EVR in about 60% of patients (10). In our pilot study ribavirin priming followed by 48 weeks of pegylated interferon and ribavirin obtained EVR in 92% of patients. To show an improvement of EVR from 60 to 92% , assuming an alpha level of 0.05, and 90% power ( beta =0.20) fifty patients per group are needed.

Patients will be randomized after inclusion in the study, using an opaque envelope technique to be assigned to their treatment by a predetermined sequence at the Coordinator Center. Randomization will be stratified for genotype 1 and non1 to decrease the likelihood that uneven distribution of underlying disease severity would bias the results. Randomization will occur in blocks of four.
5. Definitions:

The following definitions are going to be used; during the study:
* Rapid Virological Response: complete viral clearance at week 4
* Early Virologic Response: viral reduction \> 2 log after 12 weeks of combined therapy.
* Complete Early Virological Response: complete viral clearance after 12 weeks of combined therapy.
* End of treatment Virologic Response: complete viral clearance at the end of the treatment period
* Sustained Virologic Response: complete viral clearance 24 weeks after the end of treatment
* Non Responder: Absence of virological response after 12 weeks
* Relapse: recurrence of viral replication after a complete clearance during treatment time or after the conclusion of it.
6. Protocol of the study:

Basal Evaluation:

* Liver biopsy within the last 6 months
* Complete biochemical assessment (liver function tests, renal function, blood tests, levels of immunosuppressive therapy)
* HCV-RNA quantitative determination

Randomization: Patient are randomized to treatment A or Treatment B):

* Treatment A:

Pre-treatment:

Ribavirin is started at 600 mg/day (or 400mg/ day if \< 60 kg) and increased to 10,4 mg/kg within week 2, the therapy is continued for 8 complete weeks.

Biochemical assessment is repeated at week 2, 4, 8. Samples are stored at the same times.

HCV-RNA quantitative determination is repeated at week 8. Drug reduction is allowed when hemoglobin level is below 10 g/dL though EPO administration or whenever it is considered necessary.

Combined antiviral therapy:

For 48 weeks patients are treated with Ribavirin (same dosage) and IFN alfa2b (1,5 mcg/kg/week).

Patients are followed monthly or more frequently if required. Biochemical and virological assessment is recorded at week 4, 12, 24, 48. Surveillance is performed for any collateral effects and dose adjustment or growth factor need.

Ribavirin reduction is required when hemoglobin level is below 10 g/dL though EPO use.

IFN weekly administration should be reduced when neutrophiles count is \< 750 in spite of G-CSF administration.

IFN interruption is required when neutrophiles are \< 500 or platelets are \< 35000.

* Treatment B:

For 48 weeks patients are treated with Ribavirin (10 mg/kg ) and pegylated IFN alfa2b weekly.

Ribavirin is started at 600 mg/day and increased to 10 mg/kg within week 2. Pegylated IFN alfa2b is administered weekly at a dose of 1,5/kg/week. Patients are followed twice monthly in the first month and at least monthly thereafter (more frequently whenever is required).

Biochemical and virological assessment is recorded at week 4, 12, 24, 48. Surveillance is performed for any collateral effects and dose adjustment or growth factor need.

Ribavirin reduction is required when hemoglobin level is below 10 g/dL though EPO use.

IFN weekly administration should be reduced when neutrophiles count is \< 750 in spite of G-CSF administration.

IFN interruption is required when neutrophiles are \< 500 or platelets are \< 35000.

End-points of the study:

* Rapid Virological Response ( week 4)
* Early Virological Response (week 12)
* Complete Early Virological Response (week 12)
* End of treatment Virological Response (week 48)
* End of treatment Biochemical Response (week 48)
* Sustained Virological Response (Six months after the end of therapy)

Collateral effects, dose adjustment and use of growth factors are recorded.

Conditions

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Hepatitis C

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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ribavirin pre-treatment

patient will receive ribavirin in monotherapy for 8 weeks before the combined 48 weeks antiviral therapy

Group Type ACTIVE_COMPARATOR

ribavirin pre-treatment

Intervention Type DRUG

patients receive ribavirin (10,4 mg/kg/day) and pegylated interferon alfa-2b (1,5 mcg/kg/week).Pre-treatment arm will receive a 8-week monotherapy treatment with only ribavirin (same dosage) and the controlled arm will receive 48 week of standard combined therapy (ribavirin plus pegylated interferon)

combined stardard therapy

patients will receive the standard combined therapy with ribavirin and pegylated interferon for 48 weeks

Group Type ACTIVE_COMPARATOR

ribavirin pre-treatment

Intervention Type DRUG

patients receive ribavirin (10,4 mg/kg/day) and pegylated interferon alfa-2b (1,5 mcg/kg/week).Pre-treatment arm will receive a 8-week monotherapy treatment with only ribavirin (same dosage) and the controlled arm will receive 48 week of standard combined therapy (ribavirin plus pegylated interferon)

Interventions

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ribavirin pre-treatment

patients receive ribavirin (10,4 mg/kg/day) and pegylated interferon alfa-2b (1,5 mcg/kg/week).Pre-treatment arm will receive a 8-week monotherapy treatment with only ribavirin (same dosage) and the controlled arm will receive 48 week of standard combined therapy (ribavirin plus pegylated interferon)

Intervention Type DRUG

Other Intervention Names

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ribavirin pre treatment ribavirin priming Recurrence of hepatitis c hepatitis c transplanted patients ribavirin HCV

Eligibility Criteria

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Inclusion Criteria

1. Liver transplantation from \> 6 months
2. Positive HCV-RNA viremia
3. Elevated transaminase levels (greater than 1,2 normal values) in at least two consecutive determinations during the last month
4. Histology pattern showing hepatitis C recurrence

Exclusion Criteria

1. Multiple organ transplantation
2. Histology showing evidence of hepatic allograft rejection \> 3/9 RAI score
3. Concomitant active biliary disease
4. Concomitant HBV infection
5. Normal transaminases levels
6. Less than 1500 neutrophiles in more than one blood test
7. Less than 50000 platelets in more than one blood test
8. Hemoglobin \< 9 g/ dL
9. Creatinine clearance \< 35 ml/min
10. Positive antibodies \> 1:80
11. Auto-immune thyroid pathology
12. Severe psychiatric disease
13. Diagnosis of ischemic cardiopathy in the last 12 months
14. Active alcohol abuse
15. Low compliance to other medical treatments
Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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University of Roma La Sapienza

OTHER

Sponsor Role lead

Responsible Party

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Manuela Merli

professor

Responsibility Role PRINCIPAL_INVESTIGATOR

Locations

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Sapienza University of Rome

Rome, Rome, Italy

Site Status

Countries

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Italy

References

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Gordon FD, Kwo P, Vargas HE. Treatment of hepatitis C in liver transplant recipients. Liver Transpl. 2009 Feb;15(2):126-35. doi: 10.1002/lt.21694.

Reference Type BACKGROUND
PMID: 19177439 (View on PubMed)

Furusyo N, Kubo N, Toyoda K, Takeoka H, Nabeshima S, Murata M, Nakamuta M, Hayashi J. Helper T cell cytokine response to ribavirin priming before combined treatment with interferon alpha and ribavirin for patients with chronic hepatitis C. Antiviral Res. 2005 Jul;67(1):46-54. doi: 10.1016/j.antiviral.2005.04.001.

Reference Type BACKGROUND
PMID: 15913800 (View on PubMed)

Feld JJ, Nanda S, Huang Y, Chen W, Cam M, Pusek SN, Schweigler LM, Theodore D, Zacks SL, Liang TJ, Fried MW. Hepatic gene expression during treatment with peginterferon and ribavirin: Identifying molecular pathways for treatment response. Hepatology. 2007 Nov;46(5):1548-63. doi: 10.1002/hep.21853.

Reference Type BACKGROUND
PMID: 17929300 (View on PubMed)

Ogawa K, Hige S, Nakanishi M, Yamamoto Y, Chuma M, Nagasaka A, Asaka M. Immunological and mutagenic actions of ribavirin monotherapy preceding combination therapy with interferon for patients with chronic hepatitis C. Antivir Ther. 2009;14(4):513-22.

Reference Type BACKGROUND
PMID: 19578236 (View on PubMed)

Tox U, Schulte S, Heindl B, Goeser T, Drebber U, Stelzer A, Steffen HM. Ribavirin priming in patients with chronic hepatitis C and normal ALT: a pilot study. Hepatogastroenterology. 2008 Sep-Oct;55(86-87):1666-70.

Reference Type BACKGROUND
PMID: 19102366 (View on PubMed)

Cuevas JM, Gonzalez-Candelas F, Moya A, Sanjuan R. Effect of ribavirin on the mutation rate and spectrum of hepatitis C virus in vivo. J Virol. 2009 Jun;83(11):5760-4. doi: 10.1128/JVI.00201-09. Epub 2009 Mar 25.

Reference Type BACKGROUND
PMID: 19321623 (View on PubMed)

Dixit NM, Perelson AS. The metabolism, pharmacokinetics and mechanisms of antiviral activity of ribavirin against hepatitis C virus. Cell Mol Life Sci. 2006 Apr;63(7-8):832-42. doi: 10.1007/s00018-005-5455-y.

Reference Type BACKGROUND
PMID: 16501888 (View on PubMed)

Berenguer M. Systematic review of the treatment of established recurrent hepatitis C with pegylated interferon in combination with ribavirin. J Hepatol. 2008 Aug;49(2):274-87. doi: 10.1016/j.jhep.2008.05.002. Epub 2008 May 22.

Reference Type BACKGROUND
PMID: 18571272 (View on PubMed)

Berenguer M, Prieto M, Rayon JM, Mora J, Pastor M, Ortiz V, Carrasco D, San Juan F, Burgueno MD, Mir J, Berenguer J. Natural history of clinically compensated hepatitis C virus-related graft cirrhosis after liver transplantation. Hepatology. 2000 Oct;32(4 Pt 1):852-8. doi: 10.1053/jhep.2000.17924.

Reference Type BACKGROUND
PMID: 11003634 (View on PubMed)

Berenguer M, Lopez-Labrador FX, Wright TL. Hepatitis C and liver transplantation. J Hepatol. 2001 Nov;35(5):666-78. doi: 10.1016/s0168-8278(01)00179-9. No abstract available.

Reference Type BACKGROUND
PMID: 11690716 (View on PubMed)

Other Identifiers

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Ribavirin Pre-treatment

Identifier Type: -

Identifier Source: org_study_id

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