Efficacy and Safety Study of Peginterferon Beta-1a in Participants With Relapsing Multiple Sclerosis

NCT ID: NCT00906399

Last Updated: 2014-09-19

Study Results

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1516 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-06-30

Study Completion Date

2013-10-31

Brief Summary

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The primary objective of this study is to determine the efficacy of peginterferon beta-1a in reducing the annualized relapse rate (ARR) in participants with relapsing multiple sclerosis (RMS) at 1 year. The secondary objectives of this study are to determine whether peginterferon beta-1a, at 1 year when compared with placebo, is effective in reducing the total number of new or newly enlarging T2 hyperintense lesions on brain magnetic resonance imaging (MRI) scans, reducing the proportion of participants who relapse, and slowing the progression of disability.

Detailed Description

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This is a global multicenter, randomized, double-blind, parallel-group, placebo-controlled study. The treatment period is 96 weeks (2 years) in duration. Treatment Year 1 (Week 0 to Week 48) is referred to as the placebo-controlled treatment period of the study. At the beginning of Treatment Year 1, participants were randomized to receive placebo, peginterferon beta-1a 125 μg every 2 weeks, or peginterferon beta-1a 125 μg every 4 weeks. At the end of Treatment Year 1, participants in the placebo group were re-randomized to receive peginterferon beta-1a treatment so that during treatment Year 2 (Weeks 48 to Week 96) all participants received peginterferon beta-1a 125 μg every 2 or every 4 weeks. Per protocol, all primary and secondary endpoints pertain to Year 1 data.

Conditions

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Relapsing Multiple Sclerosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Placebo

Placebo every 2 weeks for 48 weeks followed by 125 µg peginterferon beta-1a subcutaneously every 2 or 4 weeks for 48 weeks.

Group Type PLACEBO_COMPARATOR

BIIB017 (peginterferon beta-1a)

Intervention Type DRUG

Supplied as a liquid in pre-filled syringes to deliver 0.5 mL of 0.25 mg/mL (125 µg dose), self-administered by subcutaneous injection.

Placebo

Intervention Type DRUG

Matched placebo provided in pre-filled syringes, to deliver 0.5 mL self-administered by subcutaneous injection.

Peginterferon Beta-1a Q2W

125 µg peginterferon beta-1a subcutaneously every 2 weeks (Q2W) for 96 weeks.

Group Type EXPERIMENTAL

BIIB017 (peginterferon beta-1a)

Intervention Type DRUG

Supplied as a liquid in pre-filled syringes to deliver 0.5 mL of 0.25 mg/mL (125 µg dose), self-administered by subcutaneous injection.

Peginterferon Beta-1a Q4W

125 µg peginterferon beta-1a subcutaneously every 4 weeks (Q4W) for 96 weeks. Participants received a placebo injection 2 weeks after each active injection (in order to maintain the blind with Q2W arm).

Group Type EXPERIMENTAL

BIIB017 (peginterferon beta-1a)

Intervention Type DRUG

Supplied as a liquid in pre-filled syringes to deliver 0.5 mL of 0.25 mg/mL (125 µg dose), self-administered by subcutaneous injection.

Placebo

Intervention Type DRUG

Matched placebo provided in pre-filled syringes, to deliver 0.5 mL self-administered by subcutaneous injection.

Interventions

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BIIB017 (peginterferon beta-1a)

Supplied as a liquid in pre-filled syringes to deliver 0.5 mL of 0.25 mg/mL (125 µg dose), self-administered by subcutaneous injection.

Intervention Type DRUG

Placebo

Matched placebo provided in pre-filled syringes, to deliver 0.5 mL self-administered by subcutaneous injection.

Intervention Type DRUG

Other Intervention Names

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PEG IFN ß-1a PEGylated interferon beta-1a Plegridy

Eligibility Criteria

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Inclusion Criteria

* Must have a confirmed diagnosis of relapsing multiple sclerosis (RMS), as defined by McDonald criteria 1 through 4 (Polman, 2005)
* Must have an EDSS score between 0.0 and 5.0.
* Must have experienced at least 2 relapses that have been medically documented within the last 3 years with at least one occurring in the last 12 months

Exclusion Criteria

* Other chronic disease of immune system, malignancies, urologic, pulmonary, gastrointestinal disease
* Pregnant or nursing women
* Prior treatment with interferon could not exceed 4 weeks and subjects must have discontinued interferon treatment 6 months prior to Baseline
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Biogen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Biogen

Locations

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Phoenix, Arizona, United States

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Ponte Vedra Beach, Florida, United States

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Atlanta, Georgia, United States

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Des Moines, Iowa, United States

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Lexington, Kentucky, United States

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Baltimore, Maryland, United States

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Teaneck, New Jersey, United States

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Raleigh, North Carolina, United States

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Akron, Ohio, United States

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Cleveland, Ohio, United States

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Franklin, Tennessee, United States

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Round Rock, Texas, United States

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Brussels, , Belgium

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Sint-Truiden, , Belgium

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Plovdiv, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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London, Ontario, Canada

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Montreal, Quebec, Canada

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Santiago, , Chile

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Barranquilla, Atlántico, Colombia

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Bogota, Cundinamarca, Colombia

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Bogotá, , Colombia

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Osijek, , Croatia

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Zagreb, , Croatia

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Brno, , Czechia

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Olomouc, , Czechia

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Ostrava, , Czechia

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Ostrava - Vitkovice, , Czechia

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Ostrava-Poruba, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Teplice, , Czechia

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Pärnu, , Estonia

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Tallinn, , Estonia

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Tartu, , Estonia

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Amiens, , France

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Clermont-Ferrand, , France

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Lyon, , France

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Marseille, , France

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Nice, , France

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Tbilisi, , Georgia

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Tbilisi, , Georgia

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Tbilisi, , Georgia

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Tbilisi, , Georgia

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Bayreuth, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Bochum, , Germany

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Cologne, , Germany

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Erbach im Odenwald, , Germany

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Erlangen, , Germany

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Hamburg, , Germany

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Hanover, , Germany

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Leipzig, , Germany

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Marburg, , Germany

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München, , Germany

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Münster, , Germany

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Prien am Chiemsee, , Germany

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Ulm, , Germany

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Westerstede, , Germany

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Athens, , Greece

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Athens, , Greece

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Thessaloniki, , Greece

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Ahmedabad, Gujarat, India

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Rajkot, Gujarat, India

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Bangalore, Karnataka, India

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Indore, Madhyr Pradesh, India

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Mumbai, Maharashtra, India

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Nagpur, Maharashtra, India

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Nashik, Maharashtra, India

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Pune, Maharashtra, India

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Pune, Maharashtra, India

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New Delhi, National Capital Territory of Delhi, India

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New Delhi, National Capital Territory of Delhi, India

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Saket, National Capital Territory of Delhi, India

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Amritsar, Punjab, India

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Jaipur, Rajasthan, India

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Chennai, Tamil Nadu, India

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Coimbatore, Tamil Nadu, India

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Kolkata, West Bengal, India

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Bangalore, , India

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Mangalore, , India

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Navi Mumbai, , India

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Nehru Nagar, , India

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Riga, , Latvia

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Aquas Calientes, , Mexico

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Chihuahua City, , Mexico

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Mexico City, , Mexico

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Mexico City, , Mexico

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Monterrey, Nuevo Leon, , Mexico

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Tijuana, Baja California, , Mexico

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Breda, , Netherlands

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Nieuwegein, , Netherlands

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Auckland, , New Zealand

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Christchurch, , New Zealand

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Dunedin, , New Zealand

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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San Isidro, , Peru

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Bialystok, , Poland

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Bialystok, , Poland

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Bydgoszcz, , Poland

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Gdansk, , Poland

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Gdansk, , Poland

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Gdansk, , Poland

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Gmina Końskie, , Poland

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Katowice, , Poland

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Katowice, , Poland

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Katowice, , Poland

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Krakow, , Poland

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Krakow, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Lublin, , Poland

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Lublin, , Poland

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Olsztyn, , Poland

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Plewiska, , Poland

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Poznan, , Poland

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Poznan, , Poland

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Szczecin, , Poland

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Szczecin, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Zabrze, , Poland

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Brasov, , Romania

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Bucharest, , Romania

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Campulung Muscel, , Romania

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Iași, , Romania

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Sibiu, , Romania

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Târgu Mureş, , Romania

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Chelyabinsk, , Russia

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Kaluga, , Russia

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Kazan', , Russia

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Krasnodar, , Russia

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Kursk, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Novosibirsk, , Russia

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Perm, , Russia

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Rostov-on-Don, , Russia

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Smolensk, , Russia

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Tomsk, , Russia

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Ufa, , Russia

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Belgrade, , Serbia

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Kragujevac, , Serbia

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Niš, , Serbia

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Córdoba, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Málaga, , Spain

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Seville, , Spain

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Chernivtsi, , Ukraine

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Dnipropetrovsk, , Ukraine

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Donetsk, , Ukraine

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Kharkiv, , Ukraine

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Kharkiv, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Odesa, , Ukraine

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Poltava, , Ukraine

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Simferopol, , Ukraine

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Ternopil, , Ukraine

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Vinnytsia, , Ukraine

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London, , United Kingdom

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Nottingham, , United Kingdom

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Salford, , United Kingdom

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Sheffield, , United Kingdom

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Countries

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United States Belgium Bulgaria Canada Chile Colombia Croatia Czechia Estonia France Georgia Germany Greece India Latvia Mexico Netherlands New Zealand Peru Poland Romania Russia Serbia Spain Ukraine United Kingdom

References

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Calabresi PA, Kieseier BC, Arnold DL, Balcer LJ, Boyko A, Pelletier J, Liu S, Zhu Y, Seddighzadeh A, Hung S, Deykin A; ADVANCE Study Investigators. Pegylated interferon beta-1a for relapsing-remitting multiple sclerosis (ADVANCE): a randomised, phase 3, double-blind study. Lancet Neurol. 2014 Jul;13(7):657-65. doi: 10.1016/S1474-4422(14)70068-7. Epub 2014 Apr 30.

Reference Type RESULT
PMID: 24794721 (View on PubMed)

Loomis SJ, Sadhu N, Fisher E, Gafson AR, Huang Y, Yang C, Hughes EE, Marshall E, Herman A, John S, Runz H, Jia X, Bhangale T, Bronson PG. Genome-wide study of longitudinal brain imaging measures of multiple sclerosis progression across six clinical trials. Sci Rep. 2023 Aug 31;13(1):14313. doi: 10.1038/s41598-023-41099-0.

Reference Type DERIVED
PMID: 37652990 (View on PubMed)

Calabresi PA, Arnold DL, Sangurdekar D, Singh CM, Altincatal A, de Moor C, Engle B, Goyal J, Deykin A, Szak S, Kieseier BC, Rudick RA, Plavina T. Temporal profile of serum neurofilament light in multiple sclerosis: Implications for patient monitoring. Mult Scler. 2021 Sep;27(10):1497-1505. doi: 10.1177/1352458520972573. Epub 2020 Dec 14.

Reference Type DERIVED
PMID: 33307998 (View on PubMed)

Cleanthous S, Cano S, Kinter E, Marquis P, Petrillo J, You X, Wakeford C, Sabatella G. Measuring the impact of multiple sclerosis: Enhancing the measurement performance of the Multiple Sclerosis Impact Scale (MSIS-29) using Rasch Measurement Theory (RMT). Mult Scler J Exp Transl Clin. 2017 Aug 15;3(3):2055217317725917. doi: 10.1177/2055217317725917. eCollection 2017 Jul-Sep.

Reference Type DERIVED
PMID: 29104758 (View on PubMed)

Scott TF, Kieseier BC, Newsome SD, Arnold DL, You X, Hung S, Sperling B. Improvement in relapse recovery with peginterferon beta-1a in patients with multiple sclerosis. Mult Scler J Exp Transl Clin. 2016 Nov 15;2:2055217316676644. doi: 10.1177/2055217316676644. eCollection 2016 Jan-Dec.

Reference Type DERIVED
PMID: 28607743 (View on PubMed)

Newsome SD, Kieseier BC, Liu S, You X, Kinter E, Hung S, Sperling B. Peginterferon beta-1a reduces disability worsening in relapsing-remitting multiple sclerosis: 2-year results from ADVANCE. Ther Adv Neurol Disord. 2017 Jan;10(1):41-50. doi: 10.1177/1756285616676065. Epub 2016 Nov 16.

Reference Type DERIVED
PMID: 28450894 (View on PubMed)

Arnold DL, Calabresi PA, Kieseier BC, Liu S, You X, Fiore D, Hung S. Peginterferon beta-1a improves MRI measures and increases the proportion of patients with no evidence of disease activity in relapsing-remitting multiple sclerosis: 2-year results from the ADVANCE randomized controlled trial. BMC Neurol. 2017 Feb 10;17(1):29. doi: 10.1186/s12883-017-0799-0.

Reference Type DERIVED
PMID: 28183276 (View on PubMed)

Newsome SD, Guo S, Altincatal A, Proskorovsky I, Kinter E, Phillips G, You X, Sabatella G. Impact of peginterferon beta-1a and disease factors on quality of life in multiple sclerosis. Mult Scler Relat Disord. 2015 Jul;4(4):350-7. doi: 10.1016/j.msard.2015.06.004. Epub 2015 Jun 14.

Reference Type DERIVED
PMID: 26195056 (View on PubMed)

Arnold DL, Calabresi PA, Kieseier BC, Sheikh SI, Deykin A, Zhu Y, Liu S, You X, Sperling B, Hung S. Effect of peginterferon beta-1a on MRI measures and achieving no evidence of disease activity: results from a randomized controlled trial in relapsing-remitting multiple sclerosis. BMC Neurol. 2014 Dec 31;14:240. doi: 10.1186/s12883-014-0240-x.

Reference Type DERIVED
PMID: 25551571 (View on PubMed)

Kieseier BC, Arnold DL, Balcer LJ, Boyko AA, Pelletier J, Liu S, Zhu Y, Seddighzadeh A, Hung S, Deykin A, Sheikh SI, Calabresi PA. Peginterferon beta-1a in multiple sclerosis: 2-year results from ADVANCE. Mult Scler. 2015 Jul;21(8):1025-35. doi: 10.1177/1352458514557986. Epub 2014 Nov 28.

Reference Type DERIVED
PMID: 25432952 (View on PubMed)

Hu X, Cui Y, White J, Zhu Y, Deykin A, Nestorov I, Hung S. Pharmacokinetics and pharmacodynamics of peginterferon beta-1a in patients with relapsing-remitting multiple sclerosis in the randomized ADVANCE study. Br J Clin Pharmacol. 2015 Mar;79(3):514-22. doi: 10.1111/bcp.12521.

Reference Type DERIVED
PMID: 25265472 (View on PubMed)

Other Identifiers

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2008-006333-27

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

105MS301

Identifier Type: -

Identifier Source: org_study_id

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