A Study to Evaluate the Safety, Tolerability, and Efficacy of BIIB017 (Peginterferon Beta-1a) in Pediatric Participants for the Treatment of Relapsing-Remitting Multiple Sclerosis

NCT ID: NCT03958877

Last Updated: 2025-09-11

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

152 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-10-18

Study Completion Date

2027-05-20

Brief Summary

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This study will evaluate the safety, tolerability, and descriptive efficacy of BIIB017 in pediatric participants with relapsing-remitting multiple sclerosis (RRMS) and to assess the pharmacokinetics (PK) of BIIB017 in pediatric participants with RRMS in Part 1. In Part 2, the study will evaluate the long-term safety of BIIB017 and further describe safety and the long-term multiple sclerosis (MS) outcomes after BIIB017 treatment in participants who completed the study treatment at Week 96 in Part 1 of the study.

Detailed Description

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Conditions

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Multiple Sclerosis, Relapsing-Remitting

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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BIIB017 (peginterferon beta-1a)

Participants will receive subcutaneous (SC) injection of BIIB017 (peginterferon beta-1a) 63 microgram (μg) on Day 1, followed by 94 μg at Week 2, followed by 125 μg at Week 4, and then 125 μg SC injection every 2 weeks up to Week 96 in Part 1 of the study. Eligible participants who enter optional Part 2 of the study will receive 125 μg SC injections of BIIB017 every 2 weeks for 96 Weeks.

Group Type EXPERIMENTAL

BIIB017 (peginterferon beta-1a)

Intervention Type DRUG

Administered as specified in the treatment arm

Avonex

Participants will receive Avonex (interferon beta type 1a) starting at a dose of 7.5 μg on Day 1, followed by an increase of 7.5 μg each week for 3 weeks, followed by 30 μg intramuscular (IM) injections every week up to Week 96 in Part 1 of the study. Eligible participants who enter optional Part 2 of the study will receive 125 μg SC injections of BIIB017 every 2 weeks for 96 Weeks.

Group Type ACTIVE_COMPARATOR

Interferon beta type 1a

Intervention Type DRUG

Administered as specified in the treatment arm

Interventions

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BIIB017 (peginterferon beta-1a)

Administered as specified in the treatment arm

Intervention Type DRUG

Interferon beta type 1a

Administered as specified in the treatment arm

Intervention Type DRUG

Other Intervention Names

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PLEGRIDY Avonex

Eligibility Criteria

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Inclusion Criteria

Part 1:

* Must have a diagnosis of RRMS as defined by the revised consensus definition for pediatric MS.
* Must have an EDSS score between 0.0 and 5.5.
* Must have experienced \>= 1 relapse in the 12 months prior to randomization (Day 1) or \>= 2 relapses in the 24 months prior to randomization (Day 1) or have evidence of asymptomatic disease activity (Gd-enhancing lesions) on brain MRI in the 6 months prior to randomization (Day 1).

Part 2:

• Participants who completed the study treatment in Part 1 (Week 96 Visit), as per protocol.

Exclusion Criteria

Part 1:

* Primary progressive, secondary progressive, or progressive relapsing MS. These conditions require the presence of continuous clinical disease worsening over a period of at least 3 months. Participants with these conditions may also have superimposed relapses but are distinguished from relapsing participants by the lack of clinically stable periods or clinical improvement.
* History of severe allergic or anaphylactic reactions or known drug hypersensitivity.
* Known allergy to any component of Avonex or BIIB017 formulation.
* Occurrence of an MS relapse that has occurred within 30 days prior to randomization (Day 1) and/or the participant has not stabilized from a previous relapse prior to randomization (Day 1).
* Any previous treatment with PEGylated human IFN β-1a.

Part 2:

* Any significant changes in medical history occurring after enrollment in Part 1, including laboratory test abnormalities or current clinically significant conditions that, in the opinion of the Investigator, would have excluded the participant's participation in Part 1. The Investigator must re-assess the participant's medical fitness for participation and consider any factors that would preclude treatment.
* The participant could not tolerate BIIB017 in Part 1.
Minimum Eligible Age

10 Years

Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Biogen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Biogen

Locations

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UC San Diego Health

La Jolla, California, United States

Site Status

UNC Hospitals

Chapel Hill, North Carolina, United States

Site Status

Meridian Clinical Research

Norfolk, Virginia, United States

Site Status

Hospital Italiano de Buenos Aires

Ciudad Autonoma Buenos Aires, Buenos Aires, Argentina

Site Status

Royal Children's Hospital

Parkville, Victoria, Australia

Site Status

Universitair Ziekenhuis Ghent

Ghent, East Flanders, Belgium

Site Status

Clinique CHC MontLégia

Liège, Wallonia, Belgium

Site Status

MHATNP 'Sv.Naum', EAD

Sofia, , Bulgaria

Site Status

University Hospital Centre Split

Split, Dalmatia, Croatia

Site Status

Children's Hospital Zagreb

Zagreb, , Croatia

Site Status

Clinical Hospital Center 'Sestre Milosrdnice'

Zagreb, , Croatia

Site Status

University Hospital Centre Zagreb

Zagreb, , Croatia

Site Status

Fakultni nemocnice Hradec Kralove

Hradec Králové, , Czechia

Site Status

CHU Strasbourg - Hôpital Hautepierre

Strasbourg, Bas Rhin, France

Site Status

Hopital Purpan

Toulouse, Haute Garonne, France

Site Status

Hopital Gui de Chauliac

Montpellier, Herault, France

Site Status

Hopital Roger Salengro - CHU Lille

Lille, Nord, France

Site Status

Hôpital Bicêtre

Le Kremlin-Bicêtre, Val De Marne, France

Site Status

Universitaetsklinikum Freiburg

Freiburg im Breisgau, Baden-Wurttemberg, Germany

Site Status

Universitaetsmedizin Goettingen

Göttingen, Lower Saxony, Germany

Site Status

St. Josef-Hospital Universitaetsklinikum

Bochum, North Rhine-Westphalia, Germany

Site Status

Charité - Campus Virchow-Klinikum

Berlin, , Germany

Site Status

General Hospital of Larissa

Larissa, Thessaly, Greece

Site Status

General Hospital of Thessaloniki 'Hippokration'

Thessaloniki, , Greece

Site Status

Pecsi Tudomanyegyetem KK

Pécs, Baranya, Hungary

Site Status

Debreceni Egyetem

Debrecen, Hajdú-Bihar, Hungary

Site Status

Semmelweis Egyetem

Budapest, , Hungary

Site Status

Hadassah University Hospital - Ein Kerem

Jerusalem, Levant, Israel

Site Status

Schneider Children's Medical Center

Petach-Tikva, Tel Aviv, Israel

Site Status

Azienda Ospedaliero Universitaria Ospedale Pediatrico Meyer

Florence, , Italy

Site Status

Azienda Ospedaliera Universitaria 'Federico II'

Napoli, , Italy

Site Status

Azienda Ospedaliera Universitaria- Università degli Studi della Campania "Luigi Vanvitelli"

Napoli, , Italy

Site Status

Ibn Sina Hospital

Ash Shuwaykh, Shuwaikh, Kuwait

Site Status

Centro Hospitalar e Universitário Lisboa Norte E.P.E.

Lisbon, Lisbon District, Portugal

Site Status

Hospital Beatriz Ângelo

Loures, Lisbon District, Portugal

Site Status

Hospital de Braga

Braga, Minho, Portugal

Site Status

Centro Hospitalar e Universitário de Coimbra E.P.E. - Hospital Pediátrico

Coimbra, , Portugal

Site Status

Centro Hospitalar do Porto, E.P.E. - Hospital de Santo António

Porto, , Portugal

Site Status

SBEI HPE 'Bashkir State Medical University' of the MoH of the RF

Ufa, Bashkortostan Republic, Russia

Site Status

FSBI "Federal Siberian Scientific-Clinical Center of FMBA"

Krasnoyarsk, Krasnoyarsk Krai, Russia

Site Status

Nebbiolo LLC

Tomsk, Oblast, Russia

Site Status

LLC National center for socially significan disease

Saint Petersburg, Sankt-Peterburg, Russia

Site Status

SAIH 'Kemerovo Regional Clinical Hospital'

Kemerovo, Siberia, Russia

Site Status

RSBIH 'Belgorod Regional Clinical Hospital of Saint Ioasaf'

Belgorod, , Russia

Site Status

SBHI

Moscow, , Russia

Site Status

SBIH of Moscow region "Moscow Regional Scientific & Research

Moscow, , Russia

Site Status

SBEI HPE 'Rostov State Medical University' of the MoH of the RF

Rostov-on-Don, , Russia

Site Status

State Budgetary Institution of Healthcare of Yaroslavl region 'Clinical Hospital # 2'

Yaroslavl, , Russia

Site Status

King Faisal Specialist Hospital & Research Center

Jeddah, Mecca Region, Saudi Arabia

Site Status

King Saud University

Riyadh, , Saudi Arabia

Site Status

Clinic of Neurology and Psychiatry for Children and Youth

Belgrade, Balkans, Serbia

Site Status

University Children Hospital

Belgrade, Balkans, Serbia

Site Status

Mother and Child Health Care Institute of Serbia ,,Dr Vukan Cupic''

Belgrade, Balkans, Serbia

Site Status

Narodny ustav detskych chorob

Bratislava, , Slovakia

Site Status

Hospital Sant Joan de Deu

Esplugues de Llobregat, Barcelona, Spain

Site Status

Hospital Universitario Virgen de la Arrixaca

El Palmar, Murcia, Spain

Site Status

Hospital Universitario Reina Sofia

Córdoba, , Spain

Site Status

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status

Hopital Razi

Manouba, Mannouba, Tunisia

Site Status

Hôpital Fattouma Bourghiba

Monastir, , Tunisia

Site Status

Hôpital Habib Bourguiba

Sfax, , Tunisia

Site Status

Gazi University Medical Faculty Clinical Research Unit

Ankara, , Turkey (Türkiye)

Site Status

Akdeniz University Medical Faculty

Antalya, , Turkey (Türkiye)

Site Status

Izmir Dr. Behcet Uz Cocuk Hastaliklari ve Cerrahisi Egitim ve Arastirma Hastanesi

Izmir, , Turkey (Türkiye)

Site Status

Ondokuz Mayis Univ. Med. Fac.

Samsun, , Turkey (Türkiye)

Site Status

Countries

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United States Argentina Australia Belgium Bulgaria Croatia Czechia France Germany Greece Hungary Israel Italy Kuwait Portugal Russia Saudi Arabia Serbia Slovakia Spain Tunisia Turkey (Türkiye)

Other Identifiers

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2018-003008-38

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2023-505624-56

Identifier Type: OTHER

Identifier Source: secondary_id

105MS306

Identifier Type: -

Identifier Source: org_study_id

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