Safety and Efficacy of ProHema Modulated Umbilical Cord Blood Units in Subjects With Hematologic Malignancies.

NCT ID: NCT00890500

Last Updated: 2013-10-08

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

12 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-01-31

Study Completion Date

2013-10-31

Brief Summary

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The purpose of this research study is to determine the safety and efficacy of a reduced intensity conditioning regimen during a double umbilical cord blood unit transplant with one of the cord blood units modulated with ProHema.

Detailed Description

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The purpose of this research study is to determine the safety and efficacy of a reduced intensity conditioning regimen during a double umbilical cord blood unit transplant with one of the cord blood units modulated with ProHema.

-As part of this research study cord units will be modulated in the laboratory with ProHema before it is given to the participant. Two different treatment groups will be tested. Group 1: will have the second cord blood unit modulated with ProHema; Group 2: will have the first cord blood unit modulated with ProHema.

Conditions

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Hematologic Malignancies Allogeneic Stem Cell Transplantation

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

FACTORIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Group 1

2 umbilical cord units: Second cord blood unit modulated with ProHema

Group Type ACTIVE_COMPARATOR

Fludarabine

Intervention Type DRUG

30mg/m2/day IV x 6 days

Melphalan

Intervention Type DRUG

100 mg/m2/day IV x 1 day

Antithymocyte Globulin

Intervention Type DRUG

1mg/kg/day x 4 days

Sirolimus

Intervention Type DRUG

GVHD Prophylaxis: Target range 3-12 ng/ml

Tacrolimus

Intervention Type DRUG

GVHD Prophylaxis: Target range 5-10 ng/ml

Group 2

2 umbilical cord units: First cord blood unit modulated with ProHema

Group Type ACTIVE_COMPARATOR

Fludarabine

Intervention Type DRUG

30mg/m2/day IV x 6 days

Melphalan

Intervention Type DRUG

100 mg/m2/day IV x 1 day

Antithymocyte Globulin

Intervention Type DRUG

1mg/kg/day x 4 days

Sirolimus

Intervention Type DRUG

GVHD Prophylaxis: Target range 3-12 ng/ml

Tacrolimus

Intervention Type DRUG

GVHD Prophylaxis: Target range 5-10 ng/ml

Interventions

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Fludarabine

30mg/m2/day IV x 6 days

Intervention Type DRUG

Melphalan

100 mg/m2/day IV x 1 day

Intervention Type DRUG

Antithymocyte Globulin

1mg/kg/day x 4 days

Intervention Type DRUG

Sirolimus

GVHD Prophylaxis: Target range 3-12 ng/ml

Intervention Type DRUG

Tacrolimus

GVHD Prophylaxis: Target range 5-10 ng/ml

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Patients with hematologic malignancies for whom allogeneic stem cell transplantation is deemed clinically appropriate
* Patient must be ineligible for traditional myeloablative transplantation according to treating physician
* Lack of 6/6 or 5/6 HLA-matched related, 8/8 HLA-matched unrelated donor, or unrelated donor not available within a time frame necessary to perform a potentially curative stem cell transplant
* 18-65 years of age
* ECOG Performance Status 0-2

Exclusion Criteria

* The following hematologic malignancies are excluded:

* Myelofibrosis unless there has been exposure to cytotoxic chemotherapy for the treatment of progression to acute myeloid leukemia
* Chronic Myelogenous Leukemia, unless there has been exposure to cytotoxic chemotherapy for the treatment of blast phase, 3) Aplastic anemia, in the absence of transformation to Myelodysplastic disorder
* Cardiac disease: symptomatic congestive heart failure or evidence of left ventricular dysfunction as measured by gated radionucleotide ventriculogram or echocardiogram; active angina pectoris, or uncontrolled hypertension
* Pulmonary disease: symptomatic chronic obstructive lung disease, symptomatic restrictive lung disease, or corrected DLCO of \< 50% of predicted, corrected hemoglobin
* Renal disease: serum creatinine \> 2.0mg/dl
* Hepatic disease: serum bilirubin \> 2.0mg/dl (expect in the case of Gilbert's syndrome or ongoing hemolytic anemia), SGOT or SGPT \> 3 x upper limit of normal
* Neurologic disease: symptomatic leukoencephalopathy, active CNS malignancy or other neuropsychiatric abnormalities believed to preclude transplantation
* HIV antibody
* Uncontrolled infection
* Pregnancy or breast feeding mother
* Inability to comply with the requirements for care after allogeneic stem cell transplantation
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Dana-Farber Cancer Institute

OTHER

Sponsor Role collaborator

Fate Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Corey Cutler, MD, MPH, FRCP(C)

Role: PRINCIPAL_INVESTIGATOR

Dana-Farber Cancer Institute

Locations

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Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Countries

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United States

References

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Cutler C, Multani P, Robbins D, Kim HT, Le T, Hoggatt J, Pelus LM, Desponts C, Chen YB, Rezner B, Armand P, Koreth J, Glotzbecker B, Ho VT, Alyea E, Isom M, Kao G, Armant M, Silberstein L, Hu P, Soiffer RJ, Scadden DT, Ritz J, Goessling W, North TE, Mendlein J, Ballen K, Zon LI, Antin JH, Shoemaker DD. Prostaglandin-modulated umbilical cord blood hematopoietic stem cell transplantation. Blood. 2013 Oct 24;122(17):3074-81. doi: 10.1182/blood-2013-05-503177. Epub 2013 Aug 30.

Reference Type DERIVED
PMID: 23996087 (View on PubMed)

Other Identifiers

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FT1050-01

Identifier Type: -

Identifier Source: org_study_id