Ursodiol, Combination Chemotherapy, and Bevacizumab in Treating Patients With Stage IV Colorectal Cancer

NCT ID: NCT00873275

Last Updated: 2025-06-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

11 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-03-11

Study Completion Date

2025-02-26

Brief Summary

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RATIONALE: Drugs used in chemotherapy, such as ursodiol, oxaliplatin, leucovorin, and fluorouracil, work in different ways to stop the growth of tumor cells, either by killing the cells or by stopping them from dividing. Monoclonal antibodies, such as bevacizumab, can block tumor growth in different ways. Some block the ability of tumor cells to grow and spread. Others find tumor cells and help kill them or carry tumor-killing substances to them. Bevacizumab may also stop the growth of colorectal cancer by blocking blood flow to the tumor. Giving ursodiol together with leucovorin calcium, fluorouracil, oxaliplatin, and bevacizumab may be an effective treatment for colorectal cancer.

PURPOSE: This phase I trial is studying the side effects and best dose of ursodiol when given together with combination chemotherapy and bevacizumab in treating patients with stage IV colorectal cancer.

Detailed Description

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OBJECTIVES:

Primary

* To determine the active dose and/or maximum tolerated dose of ursodiol when given in combination with fluorouracil, leucovorin calcium, oxaliplatin (FOLFOX regimen), and bevacizumab in patients with metastatic colorectal cancer.
* To determine the pharmacokinetics of ursodiol when given with this regimen.

Secondary

* To determine the systemic metabolic effects of ursodiol activation of nuclear receptor farnesoid X receptor (FXR) in glucose and lipid metabolism.
* To develop assays to detect ursodiol activation of FXR.
* To identify and evaluate potential serum biomarkers of FXR activation.
* To determine genes regulated by activation of FXR at target tissues.

OUTLINE: This is a dose-escalation study of ursodiol.

Patients receive oral ursodiol twice daily on days 1-28 (days -6 to 28 of course 1), leucovorin calcium intravenously (IV) over 2 hours on days 1 and 15, fluorouracil IV over 46 hours on days 1-2 and 15-16, and oxaliplatin IV over 2 hours and bevacizumab IV over 30-90 minutes on days 1 and 15. Courses repeat every 4 weeks in the absence of disease progression or unacceptable toxicity.

Blood sample is collected periodically for pharmacokinetic studies. Samples are also analyzed for the role of nuclear receptor farnesoid X receptor (FXR) in glucose uptake and metabolism using PET scan imaging, an oral glucose tolerance test, and HbA1c levels; the effects of FXR activation on lipid metabolism; and a marker for response to FXR activation via western blot. Available formalin-fixed paraffin-embedded tumor tissue blocks are analyzed for FXR expressing via IHC; expression of known FXR target genes via RNA analysis and real-time PCR; and expression of genes involved in glucose metabolism.

Conditions

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Colorectal Cancer

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Treatment (ursodiol, combination chemotherapy, bevacizumab)

Patients receive oral ursodiol twice daily on days 1-28 (days -6 to 28 of course 1), leucovorin calcium IV over 2 hours on days 1 and 15, fluorouracil IV over 46 hours on days 1-2 and 15-16, and oxaliplatin IV over 2 hours and bevacizumab IV over 30-90 minutes on days 1 and 15. Courses repeat every 4 weeks in the absence of disease progression or unacceptable toxicity.

Group Type EXPERIMENTAL

bevacizumab

Intervention Type BIOLOGICAL

5mg/kg IV day 1 and 15 of each 28 day course of treatment

FOLFOX regimen

Intervention Type DRUG

Leucovorin, 5-FU and Oxaliplatin

fluorouracil

Intervention Type DRUG

400 mg/m2 IV bolus immediately following leucovorin on days 1 and 15 of a 28 day course of treatment. Then 2.4 gm/m2 IV continuous infusion over 46 hours immediately following bolus dose on days 1 and 2 and 15 and 16 of a 28 day course of treatment

leucovorin calcium

Intervention Type DRUG

400 mg/m2 IV infusion over 2 hours on days 1 and 15 of a 28 day course of treatment.

oxaliplatin

Intervention Type DRUG

85 mg/m2 IV infusion over 2 hours on days 1 and 15 of a 28 day course of treatment.

ursodiol

Intervention Type DRUG

Dose escalation in cohorts (3 patients/cohort) from an initial dose of 125 mg PO BID through 625 mgs PO BID beginning on Day -6 from infusion of bevacizumab and FOLFOX continuing for the duration of the treatment.

RNA analysis

Intervention Type GENETIC

Analysis on discard tissues

gene expression analysis

Intervention Type GENETIC

Determined in normal and malignant tissues in patients who undergo surgical resection after treatment on this trial

polymerase chain reaction

Intervention Type GENETIC

Analysis on discard tissues

western blotting

Intervention Type GENETIC

Determined on blood collected at Day -6, Day 0 and Day 7 (1 week after the first cycle of chemotherapy) from treatment and at the end of treatment

immunohistochemistry staining method

Intervention Type OTHER

Performed on tumor blocks from the primary and the metastases from the patients on study

laboratory biomarker analysis

Intervention Type OTHER

Performed on blood collected at Day -6, Day 0 and Day 7 (1 week after the first cycle of chemotherapy) from treatment and at the end of treatment

pharmacological study

Intervention Type OTHER

Day 0, day 7 before treatment, 1/2 hour after the start of treatment, 1, 2, 3, 4, and 8 hours after the start of treatment.

positron emission tomography (PET)

Intervention Type PROCEDURE

Patients will undergo PET scan imaging as part of their original staging or at baseline. If the PET scan was more than 2 weeks prior to Day 0 from study treatment, there will be a PET scan at Day 0. In any case there will be a PET scan when the patient completes treatment.

Interventions

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bevacizumab

5mg/kg IV day 1 and 15 of each 28 day course of treatment

Intervention Type BIOLOGICAL

FOLFOX regimen

Leucovorin, 5-FU and Oxaliplatin

Intervention Type DRUG

fluorouracil

400 mg/m2 IV bolus immediately following leucovorin on days 1 and 15 of a 28 day course of treatment. Then 2.4 gm/m2 IV continuous infusion over 46 hours immediately following bolus dose on days 1 and 2 and 15 and 16 of a 28 day course of treatment

Intervention Type DRUG

leucovorin calcium

400 mg/m2 IV infusion over 2 hours on days 1 and 15 of a 28 day course of treatment.

Intervention Type DRUG

oxaliplatin

85 mg/m2 IV infusion over 2 hours on days 1 and 15 of a 28 day course of treatment.

Intervention Type DRUG

ursodiol

Dose escalation in cohorts (3 patients/cohort) from an initial dose of 125 mg PO BID through 625 mgs PO BID beginning on Day -6 from infusion of bevacizumab and FOLFOX continuing for the duration of the treatment.

Intervention Type DRUG

RNA analysis

Analysis on discard tissues

Intervention Type GENETIC

gene expression analysis

Determined in normal and malignant tissues in patients who undergo surgical resection after treatment on this trial

Intervention Type GENETIC

polymerase chain reaction

Analysis on discard tissues

Intervention Type GENETIC

western blotting

Determined on blood collected at Day -6, Day 0 and Day 7 (1 week after the first cycle of chemotherapy) from treatment and at the end of treatment

Intervention Type GENETIC

immunohistochemistry staining method

Performed on tumor blocks from the primary and the metastases from the patients on study

Intervention Type OTHER

laboratory biomarker analysis

Performed on blood collected at Day -6, Day 0 and Day 7 (1 week after the first cycle of chemotherapy) from treatment and at the end of treatment

Intervention Type OTHER

pharmacological study

Day 0, day 7 before treatment, 1/2 hour after the start of treatment, 1, 2, 3, 4, and 8 hours after the start of treatment.

Intervention Type OTHER

positron emission tomography (PET)

Patients will undergo PET scan imaging as part of their original staging or at baseline. If the PET scan was more than 2 weeks prior to Day 0 from study treatment, there will be a PET scan at Day 0. In any case there will be a PET scan when the patient completes treatment.

Intervention Type PROCEDURE

Eligibility Criteria

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Inclusion Criteria

* Patients with advanced, biopsy proven metastatic colorectal cancer
* Karnofsky Performance Status \>= 80
* Prior therapy completed at least 3 weeks before protocol treatment initiation with recovery from any side-effects
* Serum albumin and prealbumin within normal limits
* Alanine aminotransferase (ALT) within 3 x upper limit of normal
* Alkaline phosphatase within 3 x upper limit of normal
* Serum bilirubin within normal limits
* Absolute neutrophil count \>= 1500/ul
* Serum creatinine within 1.5 x upper limit of normal
* Ability to understand and sign an institutional review board (IRB) approved informed consent
* Ability to use appropriate contraception and no evidence of pregnancy in female patients of reproductive potential

Exclusion Criteria

* Significant medical or psychiatric condition that would make treatment unsafe
* Use of systemic steroids use within 7 days from start of trial
* Nursing women
* Patients unable to comply with protocol related studies and follow up
* Weight loss of greater than 10% in the last 6 months
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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National Cancer Institute (NCI)

NIH

Sponsor Role collaborator

City of Hope Medical Center

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Lily L. Lai, MD

Role: PRINCIPAL_INVESTIGATOR

City of Hope Medical Center

Locations

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City of Hope Medical Center

Duarte, California, United States

Site Status

Countries

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United States

Other Identifiers

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P30CA033572

Identifier Type: NIH

Identifier Source: secondary_id

View Link

CHNMC-08005

Identifier Type: -

Identifier Source: secondary_id

CDR0000637521

Identifier Type: REGISTRY

Identifier Source: secondary_id

NCI-2010-00926

Identifier Type: REGISTRY

Identifier Source: secondary_id

08005

Identifier Type: -

Identifier Source: org_study_id

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