Ofatumumab Added to Fludarabine-Cyclophosphamide vs Fludarabine-Cyclophosphamide Combination in Relapsed Subjects With Chronic Lymphocytic Leukemia

NCT ID: NCT00824265

Last Updated: 2020-06-18

Study Results

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

365 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-03-12

Study Completion Date

2017-10-25

Brief Summary

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The purpose of this study was to evaluate the safety and efficacy of ofatumumab added to fludarabine-cyclophosphamide in patients with relapsed Chronic Lymphocytic Leukemia (CLL).

Detailed Description

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Fludarabine is currently approved for treatment of relapsed Chronic Lymphocytic Leukemia. Studies have shown that drugs in combination with fludarabine have shown more effectiveness than fludarabine alone. The addition of ofatumumab to fludarabine-cyclophosphamide combination offers potentially a more effective therapy, without additional toxicity.

The objective of this study was to determine the effect of ofatumumab added to fludarabine and cyclophosphamide in patients with Chronic Lymphocytic Leukemia who have responded previously to therapy but later develop progressive disease and require additional therapy.

Conditions

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Leukaemia, Lymphocytic, Chronic

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Ofatumumab, Fludarabine, Cyclophosphamide

Ofatumumab Cycle 1-Day 1 300mg, Cycle 1-Day 8 1000mg, then Cycles 2-6 Day 1 1000mg every 28 days, Fludarabine 25mg/m2 Days 1-3 every 28 days for 6 cycles, Cyclophosphamide 250 mg/m2 Days 1-3 every 28 days for 6 cycles

Group Type EXPERIMENTAL

OFC Infusion

Intervention Type DRUG

Ofatumumab Cycle 1-Day 1 300mg, Cycle 1-Day 8 1000mg, then Cycles 2-6 Day 1 1000mg every 28 days, Fludarabine 25mg/m2 Days 1-3 every 28 days for 6 cycles, Cyclophosphamide 250 mg/m2 Days 1-3 every 28 days for 6 cycles

Fludarabine, Cyclophosphamide

Fludarabine 25mg/m2 Days 1-3 every 28 days for 6 cycles, Cyclophosphamide 250 mg/m2 Days 1-3 every 28 days for 6 cycles

Group Type ACTIVE_COMPARATOR

FC infusion

Intervention Type DRUG

Fludarabine 25mg/m2 Days 1-3 every 28 days for 6 cycles, Cyclophosphamide 250mg/m2 Days 1-3 every 28 days for 6 cycles

Interventions

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OFC Infusion

Ofatumumab Cycle 1-Day 1 300mg, Cycle 1-Day 8 1000mg, then Cycles 2-6 Day 1 1000mg every 28 days, Fludarabine 25mg/m2 Days 1-3 every 28 days for 6 cycles, Cyclophosphamide 250 mg/m2 Days 1-3 every 28 days for 6 cycles

Intervention Type DRUG

FC infusion

Fludarabine 25mg/m2 Days 1-3 every 28 days for 6 cycles, Cyclophosphamide 250mg/m2 Days 1-3 every 28 days for 6 cycles

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* confirmed and active CLL requiring treatment
* at least one previous treatment for CLL and having achieved a complete or partial remission/response but after a period of 6 or more months, shows evidence of disease progression
* fully active at a minimum or fully capable of selfcare and up and about more than 50% of waking hours
* age 18yrs or older
* signed written informed consent

Exclusion Criteria

* diagnosis of refractory CLL (failure to achieve a complete or partial remission/response or disease progression within 6 months of last anti-CLL treatment
* abnormal/inadequate blood values, liver and kidney function
* certain heart problems, serious significant diseases, AIHA, other current cancers or within the last 5 years
* active or chronic infections
* use of drugs to suppress allergic or inflammatory responses (glucocorticoids)
* CLL transformation
* CLL central nervous system involvement
* current participation in other clinical study
* inability to comply with the protocol activities
* lactating or pregnant women or female patients of child-bearing potential (or male patients with such partners) not willing to use adequate contraception
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Novartis Investigative Site

Rome, Lazio, Italy

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Rome, Lazio, Italy

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Genoa, Liguria, Italy

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Pavia, Lombardy, Italy

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Alessandria, Piedmont, Italy

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Novara, Piedmont, Italy

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Catania, Sicily, Italy

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Palermo, Sicily, Italy

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New Delhi, , India

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Boca Raton, Florida, United States

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Chicago, Illinois, United States

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Clinton, Maryland, United States

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Kansas City, Missouri, United States

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St Louis, Missouri, United States

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Memphis, Tennessee, United States

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Brasilia, Goiás, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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São Paulo, São Paulo, Brazil

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Porto Alegre, , Brazil

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Rio de Janeiro, , Brazil

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Rio de Janeiro, , Brazil

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Rio de Janeiro, , Brazil

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São Paulo, , Brazil

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Pleven, , Bulgaria

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Plovdiv, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Varna, , Bulgaria

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New Westminster, British Columbia, Canada

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Pune, , India

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Kitchener, Ontario, Canada

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Vadodara, , India

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Potenza, Basilicate, Italy

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Newmarket, Ontario, Canada

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Ottawa, Ontario, Canada

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Greenfield Park, Quebec, Canada

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Montreal, Quebec, Canada

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Sherbrooke, Quebec, Canada

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Saskatoon, Saskatchewan, Canada

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Karlsruhe, Baden-Wurttemberg, Germany

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Stuttgart, Baden-Wurttemberg, Germany

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Stuttgart, Baden-Wurttemberg, Germany

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Villingen-Schwenningen, Baden-Wurttemberg, Germany

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Munich, Bavaria, Germany

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Frankfurt am Main, Hesse, Germany

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Kassel, Hesse, Germany

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Hanover, Lower Saxony, Germany

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Lehrte, Lower Saxony, Germany

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Essen, North Rhine-Westphalia, Germany

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Moenchengladbach-Rheydt, North Rhine-Westphalia, Germany

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Münster, North Rhine-Westphalia, Germany

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Saarbrücken, Saarland, Germany

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Dresden, Saxony, Germany

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Hamburg, , Germany

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Lübeck, , Germany

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Athens, , Greece

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Athens, , Greece

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Thessaloniki, , Greece

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Bangalore, , India

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Mumbai, , India

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Mumbai, , India

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Ascoli Piceno, The Marches, Italy

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Guadalajara, Jalisco, Mexico

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Monterrey, Nuevo León, Mexico

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Monterrey, Nuevo León, Mexico

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Mexico City, , Mexico

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Amersfoort, , Netherlands

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Nijmegen, , Netherlands

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Rotterdam, , Netherlands

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The Hague, , Netherlands

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Chorzów, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Opole, , Poland

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Szczecin, , Poland

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Bucharest, , Romania

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Iași, , Romania

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Iași, , Romania

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Kazan', , Russia

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Moscow, , Russia

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Moscow, , Russia

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Novosibirsk, , Russia

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Saint Petersburg, , Russia

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St'Petersburg, , Russia

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Barcelona, , Spain

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Barcelona, , Spain

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Madrid, , Spain

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Salamanca, , Spain

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Seville, , Spain

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Taichung, , Taiwan

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Taipei, , Taiwan

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Bangkok, , Thailand

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Cherkasy, , Ukraine

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Dnipropetrovsk, , Ukraine

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Kharkiv, , Ukraine

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Khmelnytskyi, , Ukraine

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Kyiv, , Ukraine

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Lviv, , Ukraine

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Makiivka, , Ukraine

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Simferopil, , Ukraine

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Vinnitsa, , Ukraine

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Zhytomyr, , Ukraine

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Birmingham, , United Kingdom

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Bradford, , United Kingdom

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Burton-on-Trent, , United Kingdom

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Cottingham, , United Kingdom

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Dudley, , United Kingdom

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Glasgow, , United Kingdom

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Leicester, , United Kingdom

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London, , United Kingdom

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Manchester, , United Kingdom

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Sutton, , United Kingdom

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Swindon, , United Kingdom

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Truro, , United Kingdom

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Uxbridge, , United Kingdom

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Countries

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United States Brazil Bulgaria Canada Germany Greece India Italy Mexico Netherlands Poland Romania Russia Spain Taiwan Thailand Ukraine United Kingdom

References

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Robak T, Warzocha K, Govind Babu K, Kulyaba Y, Kuliczkowski K, Abdulkadyrov K, Loscertales J, Kryachok I, Kloczko J, Rekhtman G, Homenda W, Blonski JZ, McKeown A, Chang CN, Bal V, Lisby S, Gupta IV, Grosicki S. Health-related quality of life and patient-reported outcomes of ofatumumab plus fludarabine and cyclophosphamide versus fludarabine and cyclophosphamide in the COMPLEMENT 2 trial of patients with relapsed CLL. Leuk Lymphoma. 2017 Jul;58(7):1598-1606. doi: 10.1080/10428194.2016.1253837. Epub 2016 Nov 10.

Reference Type DERIVED
PMID: 27830957 (View on PubMed)

Robak T, Warzocha K, Govind Babu K, Kulyaba Y, Kuliczkowski K, Abdulkadyrov K, Loscertales J, Kryachok I, Kloczko J, Rekhtman G, Homenda W, Blonski JZ, McKeown A, Gorczyca MM, Carey JL, Chang CN, Lisby S, Gupta IV, Grosicki S. Ofatumumab plus fludarabine and cyclophosphamide in relapsed chronic lymphocytic leukemia: results from the COMPLEMENT 2 trial. Leuk Lymphoma. 2017 May;58(5):1084-1093. doi: 10.1080/10428194.2016.1233536. Epub 2016 Oct 12.

Reference Type DERIVED
PMID: 27731748 (View on PubMed)

Jewell RC, Laubscher K, Lewis E, Fang L, Gafoor Z, Carey J, McKeown A, West S, Wright O, Sedoti D, Dixon I, Hottenstein CS, Chan G. Assessment of the effect of ofatumumab on cardiac repolarization. J Clin Pharmacol. 2015 Jan;55(1):114-21. doi: 10.1002/jcph.376. Epub 2014 Aug 21.

Reference Type DERIVED
PMID: 25103870 (View on PubMed)

Other Identifiers

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110913

Identifier Type: -

Identifier Source: org_study_id

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