Fludarabine and Cyclophosphamide With or Without Rituximab in Patients With Previously Untreated Chronic B-Cell Lymphocytic Leukemia

NCT ID: NCT00281918

Last Updated: 2013-09-19

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

817 participants

Study Classification

INTERVENTIONAL

Study Start Date

2003-07-31

Study Completion Date

2011-10-31

Brief Summary

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This randomized phase III trial is studying fludarabine, cyclophosphamide, and rituximab to see how well they work compared to fludarabine and cyclophosphamide in treating patients with B-cell chronic lymphocytic leukemia.

Detailed Description

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Conditions

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Leukemia

Keywords

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B-cell chronic lymphocytic leukemia stage I chronic lymphocytic leukemia stage II chronic lymphocytic leukemia stage III chronic lymphocytic leukemia stage IV chronic lymphocytic leukemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Fludarabine+Cyclophosphamide+Rituximab (FCR)

Group Type EXPERIMENTAL

Rituximab

Intervention Type DRUG

Intravenous repeating dose

Cyclophosphamide

Intervention Type DRUG

Intravenous repeating dose

Fludarabine Phosphate

Intervention Type DRUG

Intravenous repeating dose

Fludarabine+Cyclophosphamide (FC)

Group Type ACTIVE_COMPARATOR

Cyclophosphamide

Intervention Type DRUG

Intravenous repeating dose

Fludarabine Phosphate

Intervention Type DRUG

Intravenous repeating dose

Interventions

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Rituximab

Intravenous repeating dose

Intervention Type DRUG

Cyclophosphamide

Intravenous repeating dose

Intervention Type DRUG

Fludarabine Phosphate

Intravenous repeating dose

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

DISEASE CHARACTERISTICS:

* Diagnosed B-cell chronic lymphocytic leukemia (CLL) defined by the National Cancer Institute (NCI) Working Group criteria
* Meets 1 of the following criteria:

* Binet stage C disease
* Binet stage B disease AND ≥ 1 of the following signs or symptoms\*:

* B symptoms (night sweats, weight loss ≥ 10% within the previous 6 months, fevers \> 38°C or 100.4°F for ≥ 2 weeks without evidence of infection), or constitutional symptoms (fatigue)
* Continuous progression (doubling of peripheral lymphocyte count within the past 6 months and absolute lymphocyte count \> 50 G/I)
* Evidence of progressive marrow failure as manifested by the development/worsening of anemia and/or thrombocytopenia
* Massive, progressive or painful splenomegaly or hypersplenism
* Massive lymph nodes or lymph node clusters (\> 10 cm in longest diameter), danger of organ complications through large lymphoma (e.g., vascular compression or tracheal narrowing), or progressive lymphadenopathy
* Occurrence of symptomatic hyperviscosity problems at leukocyte counts \> 200 G/I (symptomatic leukostasis) NOTE: \* Marked hypogammaglobulinemia or the development of a monoclonal protein in the absence of any of the above criteria for active disease is not sufficient for eligibility
* No Binet stage A disease
* No transformation to an aggressive B-cell malignancy (e.g., diffuse large cell lymphoma, Richter's syndrome, or prolymphocytic leukemia)

PATIENT CHARACTERISTICS:

* Eastern Cooperative Oncology Group (ECOG) performance status 0-1
* Cumulative Illness Rating Scale (CIRS) score \> 6
* Life expectancy \> 6 months
* Bilirubin ≤ 2 times upper limit of normal (ULN)
* Alkaline phosphatase and transaminases ≤ 2 times ULN
* Creatinine clearance ≥ 70 mL/min
* Not pregnant or nursing
* Negative pregnancy test
* Fertile patients must use effective contraception during and for 2 months after study treatment
* No known hypersensitivity with anaphylactic reaction to humanized monoclonal antibodies or any of the study drugs
* No cerebral dysfunction that precludes chemotherapy
* No active bacterial, viral, or fungal infection
* No clinically significant autoimmune cytopenia or Coombs-positive hemolytic anemia
* No other active malignancy requiring concurrent treatment except basal cell carcinoma or tumors treated curatively by surgery
* No medical or psychological condition that would preclude study therapy
* No concurrent disease that requires prolonged (\> 1 month) therapy involving glucocorticoids

PRIOR CONCURRENT THERAPY:

* No previous treatment of CLL by chemotherapy, radiotherapy, or immunotherapy
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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German CLL Study Group

OTHER

Sponsor Role collaborator

Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Michael Hallek, MD

Role: STUDY_CHAIR

Medizinische Universitaetsklinik I at the University of Cologne

Locations

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Gosford Hospital

Gosford, New South Wales, Australia

Site Status

Westmead Institute for Cancer Research at Westmead Hospital

Westmead - Wentworthville, New South Wales, Australia

Site Status

Royal Brisbane and Women's Hospital

Brisbane, Queensland, Australia

Site Status

Princess Alexandra Hospital

Brisbane, Queensland, Australia

Site Status

Peter MacCallum Cancer Centre

East Melbourne, Victoria, Australia

Site Status

Frankston Hospital

Frankston, Victoria, Australia

Site Status

Allg. Krankenhaus der Stadt Wien Universitaets-Kinderklinik

Vienna, , Austria

Site Status

Hanuschkrankenhaus

Vienna, , Austria

Site Status

Rudolfinerhaus

Vienna, , Austria

Site Status

AZ Sint-Jan

Bruges, , Belgium

Site Status

Institut Jules Bordet

Brussels, , Belgium

Site Status

Cliniques Universitaires Saint-Luc

Brussels, , Belgium

Site Status

Universitair Ziekenhuis Antwerpen

Edegem, , Belgium

Site Status

U.Z. Gasthuisberg

Leuven, , Belgium

Site Status

Clinique Universitaire De Mont-Godinne

Mont-Godinne Yvoir, , Belgium

Site Status

Masaryk University Hospital

Brno, , Czechia

Site Status

Fakultni Nemocnice Hradec Kralove

Hradec Králové, , Czechia

Site Status

University Hospital - Olomouc

Olomouc, , Czechia

Site Status

University Hospital in Pilsen - Lochotin

Pilsen-Lochotin, , Czechia

Site Status

First Medical Clinic of Charles University Hospital

Prague, , Czechia

Site Status

Copenhagen County Herlev University Hospital

Copenhagen, , Denmark

Site Status

Vejle Sygehus

Vejle, , Denmark

Site Status

Hopital Louis Pasteur

Colmar, , France

Site Status

Hopital Andre Mignot

Le Chesnay, , France

Site Status

Centre Leon Berard

Lyon, , France

Site Status

Marseille Institute of Cancer - Institut J. Paoli and I. Calmettes

Marseille, , France

Site Status

Centre Hospitalier Universitaire de Rennes

Rennes, , France

Site Status

Institut de Cancerologie de la Loire

Saint-Priest-en-Jarez, , France

Site Status

Praxis Fur Hamatologie und Onkologie Ahaus

Ahaus, , Germany

Site Status

Gemeinschaftspraxis Fuer Innere Medizin, Haematologie Und Internistische Onkologie

Ansbach, , Germany

Site Status

Hamatologische/Onkologische Gemeinschaftspraxis - Augsburg

Augsburg, , Germany

Site Status

Klinikum Augsburg

Augsburg, , Germany

Site Status

Humaine - Clinic

Bad Saarow, , Germany

Site Status

Internistische Praxis - Bayreuth

Bayreuth, , Germany

Site Status

Internistische Gemeinschaftspraxis - Berlin

Berlin, , Germany

Site Status

Charite - Universitaetsmedizin Berlin - Campus Benjamin Franklin

Berlin, , Germany

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Onkologische Schwerpunktpraxis Bielefeld

Bielefeld, , Germany

Site Status

Krankenhaus Bietigheim

Bietigheim, , Germany

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Augusta-Kranken-Anstalt gGmbH

Bochum, , Germany

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Marienhospital Bottrop gGmbH

Bottrop, , Germany

Site Status

DIAKO Ev. Diakonie Krankenhaus gGmbH

Bremen, , Germany

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Krankenhaus Burglengenfeld

Burglengenfeld, , Germany

Site Status

Onkologische Schwerpunktpraxis at Facharzt fuer Innere Medizin

Coesfeld, , Germany

Site Status

Praxis Fuer Haematologie Internistische Onkologie

Cologne, , Germany

Site Status

Medizinische Universitaetsklinik I at the University of Cologne

Cologne, , Germany

Site Status

Onkologische Schwerpunktpraxis

Cottbus, , Germany

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Onkologische Gemeinschaftspraxis - Dresden

Dresden, , Germany

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Internistische Praxis - Dusseldorf

Düsseldorf, , Germany

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Florence-Nightingale-Krankenhause, Deaconess Kaiserswerth

Düsseldorf, , Germany

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Krankenhaus Benrath

Düsseldorf, , Germany

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Universitaetsklinikum Duesseldorf

Düsseldorf, , Germany

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St. Georg Klinikum Eisenach GmbH

Eisenach, , Germany

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Helios Klinikum Erfurt

Erfurt, , Germany

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Internistiche Praxis

Erfurt, , Germany

Site Status

Onkologische Schwerpunkt Praxis

Erlangen, , Germany

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St. Antonius Hospital

Eschweiler, , Germany

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Universitaetsklinikum Essen

Essen, , Germany

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Evangelisches Krankenhaus Essen Werden

Essen, , Germany

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Staedtische Kliniken Esslingen

Esslingen am Neckar, , Germany

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Internistische Gemeinschaftspraxis - Forchheim

Forchheim, , Germany

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Staedtische Kliniken Frankfurt am Main - Hoechst

Frankfurt, , Germany

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Klinikum Frankfurt (Oder) GmbH

Frankfurt (Oder), , Germany

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Gemeinschaftspraxis - Freiburg

Freiburg im Breisgau, , Germany

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Klinikum Garmisch - Partenkirchen GmbH

Garmisch-Partenkirchen, , Germany

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Internistische Praxis - Gerlingen

Gerlingen, , Germany

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Gemeinschaftspraxis Fuer Innere Medizin, Hematologie Und Onkologie

Giessen, , Germany

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Universitaetsklinikum Goettingen

Göttingen, , Germany

Site Status

Klinik Fuer Innere Medizin, Hematology/Oncology, Ernst Moritz Armdt Universitaet

Greifswald, , Germany

Site Status

St. Marien Hospital - Katholisches Krankenhaus Hagen gGmbH

Hagen, , Germany

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Internistische Praxis - Halle

Halle, , Germany

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Universitaetsklinikum Halle

Halle, , Germany

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Asklepios Klinik St. Georg

Hamburg, , Germany

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University Medical Center Hamburg - Eppendorf

Hamburg, , Germany

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St. Marien-Hospital Hamm - Klinik Knappenstrasse

Hamm, , Germany

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Evangelische Krankenhaus Hamm

Hamm, , Germany

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Krankenhaus Siloah - Medizinische Klinik II

Hanover, , Germany

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Universitatsklinikum Heidelberg

Heidelberg, , Germany

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Marienhospital at Ruhr University Bochum

Herne, , Germany

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Privatklinik Dr. R. Schindlbeck GmbH & Co. KG

Herrsching am Ammersee, , Germany

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Universitaetsklinikum des Saarlandes

Homburg, , Germany

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Clinic for Bone Marrow Transplantation and Hematology and Oncology

Idar-Oberstein, , Germany

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Gemeinschaftspraxis Innere Medizin

Jena, , Germany

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Staedtisches Klinikum Karlsruhe gGmbH

Karlsruhe, , Germany

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St. Vincentius-Kliniken

Karlsruhe, , Germany

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Internistische Gemeinschaftspraxis - Kassel

Kassel, , Germany

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Klinikum Kempten Oberallgaeu

Kempten, , Germany

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Internistische Praxis - Kiel

Kiel, , Germany

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University Hospital Schleswig-Holstein - Kiel Campus

Kiel, , Germany

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Praxis fuer Haematologie und Onkologie

Koblenz, , Germany

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Stiftungsklinikum Mittelrhein - Gesundheitszentrum Evangelisches Stift Sankt Martin Koblenz gGmbH

Koblez, , Germany

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Internistische Onkologische Praxis - Kronach

Kronach, , Germany

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Klinikum Landshut

Landshut, , Germany

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Onkologische Schwerpunktpraxis - Leer

Leer, , Germany

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Klinikum "St. Georg" Leipzig

Leipzig, , Germany

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Klinikum Lippe - Lemgo

Lemgo, , Germany

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Internistische Praxis - Loerrach

Loerrach, , Germany

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Gemeinschaftspraxis - Ludwigshafen

Ludwigshafen, , Germany

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Sana Kliniken Luebeck

Lübeck, , Germany

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Internistische Gemeinschaftspraxis - Magdeburg

Magdeburg, , Germany

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Staedtisches Klinikum Magdeburg - Altstadt

Magdeburg, , Germany

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Universitaetsklinkum Magdeburg der Otto-von-Guericke-Universitaet Magdeburg

Magdeburg, , Germany

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Universitatsklinik Mainz

Mainz, , Germany

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III Medizinische Klinik Mannheim

Mannheim, , Germany

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Krankenhaus Maria Hilf GmbH

Mönchengladbach, , Germany

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Klinikum der Universitaet Muenchen - Grosshadern Campus

Munich, , Germany

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Staedtisches Krankenhaus Muenchen - Harlaching

Munich, , Germany

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Klinikum Rechts Der Isar - Technische Universitaet Muenchen

Munich, , Germany

Site Status

Haematologische Schwerpunktpraxis

Munich, , Germany

Site Status

Hamatologie/Onkologie Praxisgemeinschaft - Muenchen

München, , Germany

Site Status

University of Muenster

Münster, , Germany

Site Status

Haematologisch - Onkologische Gemeinschaftspraxis

Münster, , Germany

Site Status

Onkologische Schwerpunktpraxis Dr. Schmidt

Neunkirchen, , Germany

Site Status

Praxis fuer Haematologie und Interne Onkologie

Norderstedt, , Germany

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Klinikum Nuernberg - Klinikum Nord

Nuremberg, , Germany

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Gemeinschaftspraxis - Oberhausen

Oberhausen, , Germany

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Internistische Gemeinschaftspraxis - Offenbach

Offenbach, , Germany

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Internistische Gemeinschaftspraxis - Oldenburg

Oldenburg, , Germany

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Klinikum Oldenburg

Oldenburg, , Germany

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Asklepios Klinik Pasewalk

Pasewalk, , Germany

Site Status

Municipal Hospital Complex

Pforzheim, , Germany

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Klinikum Ernst Von Bergmann

Potsdam, , Germany

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Elisabeth Krankenhaus

Recklinghausen, , Germany

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Krankenhaus Barmherzige Brueder Regensburg

Regensburg, , Germany

Site Status

Klinik und Poliklinik fuer Innere Medizin - Universitaet Rostock

Rostock, , Germany

Site Status

Caritasklinik St. Theresia

Saarbrücken, , Germany

Site Status

Nordwestkrankenhaus Sanderbusch

Sanderbusch, , Germany

Site Status

St. Marien - Krankenhaus Siegen GMBH

Siegen, , Germany

Site Status

Internistische Gemeinschaftspraxis - Stuttgart

Stuttgart, , Germany

Site Status

Haematologische Praxis

Stuttgart, , Germany

Site Status

Klinik fuer Onkologie - Katharinenhospital Stuttgart

Stuttgart, , Germany

Site Status

Diakonie Klinikum Stuttgart

Stuttgart, , Germany

Site Status

Marienhospital Stuttgart

Stuttgart, , Germany

Site Status

KKH Torgau

Torgau, , Germany

Site Status

Onkologische Gemeinschaftspraxis - Trier

Trier, , Germany

Site Status

Krankenanstalt Mutterhaus der Borromaerinnen

Trier, , Germany

Site Status

Praxis Fuer Internistische Haematologie / Onkologie

Troisdorf, , Germany

Site Status

Universitaetsklinikum Tuebingen

Tübingen, , Germany

Site Status

Comprehensive Cancer Center Ulm at Universitaetsklinikum Ulm

Ulm, , Germany

Site Status

Municipal Hospital Complex

Villingen-Schwenningen, , Germany

Site Status

Praxis fur Innere Medizin - Wanzleben

Wanzleben, , Germany

Site Status

Haematologische Praxis

Weiden, , Germany

Site Status

Schwerpunktpraxis Hamatologie/Onkologie - Wesel

Wesel, , Germany

Site Status

Dr. Horst-Schmidt-Kliniken

Wiesbaden, , Germany

Site Status

Kliniken St. Antonius

Wuppertal, , Germany

Site Status

Hamatologisch - Onkologische Praxis Wurzburg

Würzburg, , Germany

Site Status

Medizinische Klinik und Poliklinik II - Universitaetsklinikum Wuerzburg

Würzburg, , Germany

Site Status

Soroka University Medical Center

Beersheba, , Israel

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BNAI Zion Medical Center

Haifa, , Israel

Site Status

Rambam Medical Center

Haifa, , Israel

Site Status

Hadassah University Hospital

Jerusalem, , Israel

Site Status

Riverview Cancer Care Medical Associates, PC

Kfar Saba, , Israel

Site Status

Kaplan Hospital

Rehovot, , Israel

Site Status

Ospedale Oncologico A. Businco

Cagliari, , Italy

Site Status

Fondazione Centro San Raffaele Del Monte Tabor

Milan, , Italy

Site Status

Perugia Regional Cancer Center

Perugia, , Italy

Site Status

Ospedale Sant' Eugenio

Rome, , Italy

Site Status

Policlinico A. Gemelli - Universita Cattolica del Sacro Cuore

Rome, , Italy

Site Status

Auckland City Hospital

Auckland, , New Zealand

Site Status

Canterbury Health Laboratories

Christchurch, , New Zealand

Site Status

Palmerston North Hospital

Palmerston North, , New Zealand

Site Status

Hospital General Universitario Morales Meseguer

Murcia, , Spain

Site Status

Hospital Virgen Del La Salud

Toledo, , Spain

Site Status

Countries

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Australia Austria Belgium Czechia Denmark France Germany Israel Italy New Zealand Spain

References

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Langerbeins P, Giza A, Robrecht S, Cramer P, von Tresckow J, Al-Sawaf O, Fink AM, Furstenau M, Kutsch N, Simon F, Goede V, Hoechstetter M, Niemann CU, da Cunha-Bang C, Kater A, Dubois J, Gregor M, Staber PB, Tausch E, Schneider C, Stilgenbauer S, Eichhorst B, Fischer K, Hallek M. Reassessing the chronic lymphocytic leukemia International Prognostic Index in the era of targeted therapies. Blood. 2024 Jun 20;143(25):2588-2598. doi: 10.1182/blood.2023022564.

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Bloehdorn J, Krzykalla J, Holzmann K, Gerhardinger A, Jebaraj BMC, Bahlo J, Humphrey K, Tausch E, Robrecht S, Mertens D, Schneider C, Fischer K, Hallek M, Dohner H, Benner A, Stilgenbauer S. Integrative prognostic models predict long-term survival after immunochemotherapy in chronic lymphocytic leukemia patients. Haematologica. 2022 Mar 1;107(3):615-624. doi: 10.3324/haematol.2020.251561.

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Dimier N, Delmar P, Ward C, Morariu-Zamfir R, Fingerle-Rowson G, Bahlo J, Fischer K, Eichhorst B, Goede V, van Dongen JJM, Ritgen M, Bottcher S, Langerak AW, Kneba M, Hallek M. A model for predicting effect of treatment on progression-free survival using MRD as a surrogate end point in CLL. Blood. 2018 Mar 1;131(9):955-962. doi: 10.1182/blood-2017-06-792333. Epub 2017 Dec 18.

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Weisser M, Yeh RF, Duchateau-Nguyen G, Palermo G, Nguyen TQ, Shi X, Stinson SY, Yu N, Dufour A, Robak T, Salogub GN, Dmoszynska A, Solal-Celigny P, Warzocha K, Loscertales J, Catalano J, Larratt L, Rossiev VA, Bence-Bruckler I, Geisler CH, Montillo M, Fischer K, Fink AM, Hallek M, Bloehdorn J, Busch R, Benner A, Dohner H, Valente N, Wenger MK, Stilgenbauer S, Dornan D. PTK2 expression and immunochemotherapy outcome in chronic lymphocytic leukemia. Blood. 2014 Jul 17;124(3):420-5. doi: 10.1182/blood-2013-12-538975. Epub 2014 Jun 10.

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Pflug N, Bahlo J, Shanafelt TD, Eichhorst BF, Bergmann MA, Elter T, Bauer K, Malchau G, Rabe KG, Stilgenbauer S, Dohner H, Jager U, Eckart MJ, Hopfinger G, Busch R, Fink AM, Wendtner CM, Fischer K, Kay NE, Hallek M. Development of a comprehensive prognostic index for patients with chronic lymphocytic leukemia. Blood. 2014 Jul 3;124(1):49-62. doi: 10.1182/blood-2014-02-556399. Epub 2014 May 5.

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Stilgenbauer S, Schnaiter A, Paschka P, Zenz T, Rossi M, Dohner K, Buhler A, Bottcher S, Ritgen M, Kneba M, Winkler D, Tausch E, Hoth P, Edelmann J, Mertens D, Bullinger L, Bergmann M, Kless S, Mack S, Jager U, Patten N, Wu L, Wenger MK, Fingerle-Rowson G, Lichter P, Cazzola M, Wendtner CM, Fink AM, Fischer K, Busch R, Hallek M, Dohner H. Gene mutations and treatment outcome in chronic lymphocytic leukemia: results from the CLL8 trial. Blood. 2014 May 22;123(21):3247-54. doi: 10.1182/blood-2014-01-546150. Epub 2014 Mar 20.

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Eichhorst BF, Fischer K, Fink AM, Elter T, Wendtner CM, Goede V, Bergmann M, Stilgenbauer S, Hopfinger G, Ritgen M, Bahlo J, Busch R, Hallek M; German CLL Study Group (GCLLSG). Limited clinical relevance of imaging techniques in the follow-up of patients with advanced chronic lymphocytic leukemia: results of a meta-analysis. Blood. 2011 Feb 10;117(6):1817-21. doi: 10.1182/blood-2010-04-282228. Epub 2010 Dec 7.

Reference Type DERIVED
PMID: 21139079 (View on PubMed)

Hallek M, Fischer K, Fingerle-Rowson G, Fink AM, Busch R, Mayer J, Hensel M, Hopfinger G, Hess G, von Grunhagen U, Bergmann M, Catalano J, Zinzani PL, Caligaris-Cappio F, Seymour JF, Berrebi A, Jager U, Cazin B, Trneny M, Westermann A, Wendtner CM, Eichhorst BF, Staib P, Buhler A, Winkler D, Zenz T, Bottcher S, Ritgen M, Mendila M, Kneba M, Dohner H, Stilgenbauer S; International Group of Investigators; German Chronic Lymphocytic Leukaemia Study Group. Addition of rituximab to fludarabine and cyclophosphamide in patients with chronic lymphocytic leukaemia: a randomised, open-label, phase 3 trial. Lancet. 2010 Oct 2;376(9747):1164-74. doi: 10.1016/S0140-6736(10)61381-5.

Reference Type DERIVED
PMID: 20888994 (View on PubMed)

Other Identifiers

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GCLLSG-CLL-8

Identifier Type: -

Identifier Source: secondary_id

EU-20560

Identifier Type: -

Identifier Source: secondary_id

ML17102

Identifier Type: -

Identifier Source: secondary_id

CDR0000454560

Identifier Type: -

Identifier Source: org_study_id