Multicentric Study Comparison Between Erythropoietin and Erythropoietin Associated to Differentiating Therapy With Acid 13-cis-retinoic and Dihydroxyvitamin D3 in Myelodysplastic Syndromes Without Excess of Blasts

NCT ID: NCT00804050

Last Updated: 2011-06-28

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

184 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-03-31

Study Completion Date

2010-03-31

Brief Summary

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This is a prospective, randomized multicenter phase III clinical trial designed to evaluate the safety and activity of comparison between Erythropoietin and Erythropoietin Associated to Differentiating Therapy With Acid 13-Cis-Retinoic and Dihydroxyvitamin D3 in Myelodysplastic Syndromes Without Excess of Blasts

Detailed Description

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Conditions

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Myelodysplastic Syndromes

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Infusion A: rEPO

rEPO for 4 mounths consequently

Group Type EXPERIMENTAL

infusion A: rEPO

Intervention Type DRUG

rEPO 40.000 unit/week for 4 mounths, then patients who have obtained an erythroid response, will continue for another 4 months with therapy rEPO. Patients who have not obtained an erythroid response, will increase the dose rEPO to 80,000 units per week for an additional 4 months.

Infusion B combined r-EPO

rEPO in association with acid 13-cis-retinoic acid and Dihydroxyvitamin D3 for 4 mounths consequently

Group Type EXPERIMENTAL

B Infusion rEPO combined with vitamins pills

Intervention Type DRUG

rEPO 40.000 unit/week plus acid 13 cis-retinoic (20 mg/die) plus Dihydroxyvitamin D3 (1 μg os/die), for 4 mounths. Patients who have obtained an erythroid response will continue for another 4 months with the same therapy. Patients who have not obtained an erythroid will increase the dose of rEPO to 80,000 units per week for additional 4 months.Patients also will continue with the same doses of acid 13-cis-retinoic acid and Dihydroxyvitamin D3

Interventions

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infusion A: rEPO

rEPO 40.000 unit/week for 4 mounths, then patients who have obtained an erythroid response, will continue for another 4 months with therapy rEPO. Patients who have not obtained an erythroid response, will increase the dose rEPO to 80,000 units per week for an additional 4 months.

Intervention Type DRUG

B Infusion rEPO combined with vitamins pills

rEPO 40.000 unit/week plus acid 13 cis-retinoic (20 mg/die) plus Dihydroxyvitamin D3 (1 μg os/die), for 4 mounths. Patients who have obtained an erythroid response will continue for another 4 months with the same therapy. Patients who have not obtained an erythroid will increase the dose of rEPO to 80,000 units per week for additional 4 months.Patients also will continue with the same doses of acid 13-cis-retinoic acid and Dihydroxyvitamin D3

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Age higher than 18;
2. Confirmed diagnosis by osseous biopsy and bone marrow cyto-morphologic counts of blast cells, of Myelodysplastic syndrome without excess of blasts: "refractary anemia", "refractary anemia with rings sideroblasts", "refractary citopenya with multilineage dysplasia", " refractary citopenya with multilineage dysplasia and rings sideroblasts" or "5q-syndrome" without excess of blasts based on WHO classification (appendix).
3. Low or intermediate-1 IPSS (appendix).
4. Hb \< 11g/dl.
5. rEPO serum level \< 500mU/L.
6. Women in menopause from at least one year.
7. Informed consent

Exclusion Criteria

1. Myelodisplastic syndrome with excess of blasts (RAEB).
2. IPSS score intermediate-2 or high (appendix).
3. Forecasted allogeneic bone marrow transplant within 1 year after diagnosis(patients younger than 60 years, transfusion dependents or with serious leuko/thrombocytopenia and HLA compatible family donor).Considering the time needed to perform this procedure, the indication of a transplant from non-consanguineous donor has no contraindication to the inclusion in this protocol of the response to rEPO therapy ± differentiating therapy.
4. Renal failure with creatininemia value greater than 3 times the normal limit.
5. Chronic hepatophaty with bilirubinemia value greater than 3 times the normal limit and/or AST or ALT or ALP values greater than 5 times the normal limit.
6. Presence of second tumor or other serious pathology with life expectancy lower than one year.
7. Presence of neurologic or psychiatric pathologies that make the patient unreliable in the acquisition of drugs.
8. Allergy/intolerance known to use drugs.
9. Pregnant women.
10. Women of childbearing age or in menopause from less than one year.
11. Age \< 18 years old.
12. HIV positive.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Centro di Riferimento per l'Epidemiologia e la Prev. Oncologica Piemonte

OTHER

Sponsor Role collaborator

Fondazione Italiana Sindromi Mielodisplastiche-ETS

OTHER

Sponsor Role lead

Responsible Party

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University of Torino - Ospedale S Giovanni Battista

Principal Investigators

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Dario Ferrero, MD

Role: STUDY_DIRECTOR

University of Torino - Ospedale San Giovanni Battista

Alessandro Levis, MD

Role: STUDY_DIRECTOR

Ospedale SS. Antonio, Biagio e Cesare Arrigo

Locations

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Ospedale SS. Antonio, Biagio e Cesare Arrigo

Alessandria, , Italy

Site Status

Ospedale degli Infermi

Biella, , Italy

Site Status

Spedali civili

Brescia, , Italy

Site Status

Ospedale Santo Spirito

Casale (AL), , Italy

Site Status

Ospedale Maggiore

Chieri (TO), , Italy

Site Status

Policlinico dell'Annunziata

Cosenza, , Italy

Site Status

Ospedale Santa Croce e Carle

Cuneo, , Italy

Site Status

Ospedale Santa Croce

Fano (PU), , Italy

Site Status

Ospedale San Martino

Genova, , Italy

Site Status

Ospedale civile

Ivrea (TO), , Italy

Site Status

Ospedale San Gerardo

Monza (MI), , Italy

Site Status

Ospedale Maggiore della Carità

Novara, , Italy

Site Status

Ospedale Civile

Ovada (AL), , Italy

Site Status

Istituto clinico Humanitas

Rozzano (MI), , Italy

Site Status

Ospedale San Giovanni Battista Molinette

Torino, , Italy

Site Status

Ospedale Cardinale Panico

Tricase (LE), , Italy

Site Status

Ospedale Sant'Andrea

Vercelli, , Italy

Site Status

Ospedale San Bortolo

Vicenza, , Italy

Site Status

Countries

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Italy

Other Identifiers

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2006-006482-16

Identifier Type: -

Identifier Source: secondary_id

EPO2006-AISSM04

Identifier Type: -

Identifier Source: org_study_id

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