Phase III Study of RAD001 Adjuvant Therapy in Poor Risk Patients With Diffuse Large B-Cell Lymphoma (DLBCL) of RAD001 Versus Matching Placebo After Patients Have Achieved Complete Response With First-line Rituximab-chemotherapy

NCT ID: NCT00790036

Last Updated: 2017-07-12

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

742 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-07-24

Study Completion Date

2016-06-15

Brief Summary

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Phase III study of RAD001 adjuvant therapy in poor risk patients with Diffuse Large B-Cell Lymphoma (DLBCL) of RAD001 versus matching placebo after patients had achieved complete response with first-line rituximab-chemotherapy

Detailed Description

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Conditions

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Diffuse Large B-cell Lymphoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

PREVENTION

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Everolimus

Participants who received Everolimus 10 mg (two 5 mg tablets), daily for 12 months

Group Type EXPERIMENTAL

Everolimus

Intervention Type DRUG

Everolimus was formulated as tablets of 5 mg strength, blister-packed under aluminum foil in units of 10 tablets.

Placebo

Participants who received Everolimus placebo 10 mg (two 5 mg tablets), daily for 12 months

Group Type PLACEBO_COMPARATOR

Everolimus Placebo

Intervention Type DRUG

Everolimus placebo was formulated as tablets of 5 mg strength, blister-packed under aluminum foil in units of 10 tablets.

Interventions

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Everolimus

Everolimus was formulated as tablets of 5 mg strength, blister-packed under aluminum foil in units of 10 tablets.

Intervention Type DRUG

Everolimus Placebo

Everolimus placebo was formulated as tablets of 5 mg strength, blister-packed under aluminum foil in units of 10 tablets.

Intervention Type DRUG

Other Intervention Names

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RAD001

Eligibility Criteria

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Inclusion Criteria

2. Patients defined as poor risk with IPI of 3, 4, or 5 at time of original diagnosis.
3. Patients age ≥ 18 years old.
4. Patients must have achieved complete remission (CR) based on the revised IWRC (Cheson et al 2007) following first line R-chemotherapy treatment. Radiation therapy (RT) during or after R-chemotherapy is acceptable provided: 1) it ends 4 weeks prior to start of study drug and, 2) in case of consolidation RT targeted at initial bulky tumor mass, administered after R-chemotherapy, patient is already in CR before initiating RT. Complete remission from R-chemotherapy must be confirmed by clinical and radiologic evaluation along with bone marrow confirmation (if bone marrow was involved by lymphoma before the R-chemotherapy treatment). Local pathology report on the bone marrow biopsy is acceptable. If bone marrow was not involved by lymphoma before R-chemotherapy treatment, then bone marrow confirmation after R-chemotherapy is not required.
5. Patients who received a minimum 5 cycles of R-chemotherapy treatment and maximum 8 cycles of R-chemotherapy treatment. Any variation of CHOP (R-CHOP-14, R-CHOP-21) is acceptable. Liposomal doxorubicin, epirubicin, or pirarubicin (also known as therarubicin) is acceptable. R-EPOCH is acceptable.
6. Patients' last treatment with R-chemotherapy must be 6 to 14 weeks prior to start of study drug.
7. Patients with ECOG performance status (PS) 0, 1, or 2.
8. Patients willing to provide a portion of his/her tumor tissue from original diagnosis or lymph node to confirm diagnosis.
9. The following laboratory values obtained ≤ 21 days prior to start of study drug:

* Absolute neutrophil count ≥ 1000/mm3 (or 1.0 GI/L, SI units)
* Platelet count ≥ 100,000/mm3 (or 100 GI/L, SI units)
* Hemoglobin ≥ 9 g/dL (can be achieved by transfusion)
* Total bilirubin ≤ 2 x ULN (if \>2 x ULN direct bilirubin is required and should be ≤1.5 x ULN)
* AST ≤ 3 x ULN
* Serum creatinine ≤ 2 x ULN
10. Women of childbearing potential must have had a negative serum pregnancy test 14 days prior to the start of study drug plus a negative local urine pregnancy test on Day 1, Cycle 1 prior to treatment and must be willing to use adequate methods of contraception during the study and for 8 weeks after study drug administration.
11. Patients who give a written informed consent obtained according to local guidelines.
12. Patients capable of swallowing intact study medication tablets and following directions regarding taking study drug, or have a daily caregiver who will be responsible for administering study drug.

Exclusion Criteria

1. Patients with evidence of disease according to the revised IWRC (Cheson et al 2007) after completion of the first-line R-chemotherapy treatment, prior to study entry.
2. Patients receiving ongoing radiation therapy or who received radiation therapy to the residual tumor masses \< 4 weeks from start of study drug.
3. Patients who have previously received systemic mTOR inhibitor (sirolimus, temsirolimus, everolimus, etc).
4. Patients with evidence of current central nervous system (CNS) involvement with lymphoma. Patients who have only had prophylactic intrathecal chemotherapy against CNS disease are eligible.
5. Patients with transformed follicular lymphoma.
6. Patients who received ibritumomab tiuxetan (Zevalin®), in order to avoid potential delayed kidney toxicities.
7. Patients who had myelosuppressive chemotherapy or biologic therapy \< 3 weeks from start of study drug.
8. Patients receiving chronic systemic immunosuppressive agents. Inhaled and topical steroids are acceptable. Patients may be receiving stable (not increased within the last month) chronic doses of corticosteroids with a maximum dose of 20 mg of prednisone or ≤5 mg of dexamethasone per day, if they are being given for disorders other than lymphoma such as rheumatoid arthritis, polymyalgia rheumatica, adrenal insufficiency or asthma.
9. Patients with active, bleeding diathesis.
10. Patients with a known history of HIV seropositivity.
11. Patients with known hypersensitivity to RAD001 (everolimus) or other rapamycins (sirolimus, temsirolimus) or to any of the excipients.
12. Patients who have any severe and/or uncontrolled medical conditions or other conditions that could affect their participation in the study such as:

* unstable angina pectoris, symptomatic congestive heart failure (NYHA II, III, IV), myocardial infarction ≤ 6 months prior to first study drug, serious uncontrolled cardiac arrhythmia, cerebrovascular accidents ≤ 6 months before study drug start
* severely impaired lung function as defined as spirometry and DLCO that is ≤ 50% of the normal predicted value and/or O2 saturation that is 88% or less at rest on room air
* poorly controlled diabetes as defined by fasting serum glucose \>2.0 x ULN
* any active (acute or chronic) or uncontrolled infection/disorders that impair the ability to evaluate the patient or for the patient to complete the study
* nonmalignant medical illnesses that are uncontrolled or whose control may be jeopardized by this study drug, such as severe hypertension that is not controlled with medical management and thyroid abnormalities whose thyroid function cannot be maintained in the normal range by medication
* liver disease such as cirrhosis or decompensated liver disease.
13. Patients who have a history of another primary malignancy ≤ 3 years, with the exception of non-melanoma skin cancer and carcinoma in situ of uterine cervix.
14. Female patients who are pregnant or breast feeding, or adults of reproductive potential who are not using effective birth control methods. If barrier contraceptives are being used, these must be continued throughout the trial by both sexes.
15. Patients who are using other investigational agents or who had received investigational drugs ≤ 4 weeks prior to study drug start.
16. Patients unwilling to or unable to comply with the protocol.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Ironwood Cancer and Research Centers SC

Chandler, Arizona, United States

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Highlands Oncology Group Dept of Highlands Oncology Grp

Fayetteville, Arkansas, United States

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University of California San Diego - Moores Cancer Center Dept of Moores Cancer Ctr (3)

La Jolla, California, United States

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USC/Kenneth Norris Comprehensive Cancer Center Dept.ofNorrisMedicalCenter(4)

Los Angeles, California, United States

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University of Colorado Health

Colorado Springs, Colorado, United States

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Denver Health & Hospital Authority CACZ885M2301

Denver, Colorado, United States

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Rocky Mountain Cancer Centers RMCC

Greenwood Village, Colorado, United States

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University Cancer Institute

Boynton Beach, Florida, United States

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University Cancer & Blood Center, LLC

Athens, Georgia, United States

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Columbus Regional

Columbus, Georgia, United States

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Rush University Medical Center Div. of Hematology & Oncology

Chicago, Illinois, United States

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Indiana University Hospital IU Cancer Center

Indianapolis, Indiana, United States

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Tulane University Health Sciences Center Office of Clinical Research

New Orleans, Louisiana, United States

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Lahey Clinic Dept of Lahey Clinic (3)

Burlington, Massachusetts, United States

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Mayo Clinic - Rochester Dept. of MayoClinic-Rochester

Rochester, Minnesota, United States

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Washington University School of Medicine Div. of Medical Oncology

St Louis, Missouri, United States

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Dartmouth Hitchcock Medical Center Dartmouth

Lebanon, New Hampshire, United States

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Levine Cancer Institute Oncology

Charlotte, North Carolina, United States

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Wake Forest University Baptist Medical Center Dept. of WFUHS

Winston-Salem, North Carolina, United States

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University of Pittsburgh Medical Center SC-3

Pittsburgh, Pennsylvania, United States

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Medical University of South Carolina -Hollings Cancer Center MUSC/HCC (2)

Charleston, South Carolina, United States

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Cancer Centers of the Carolinas Cancer Centers of Carolinas (3

Greenville, South Carolina, United States

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University of Tennessee Cancer Institute SC-2

Memphis, Tennessee, United States

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The West Clinic

Memphis, Tennessee, United States

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The Center for Cancer and Blood Disorders Dept. of The Ctr for C & BD

Fort Worth, Texas, United States

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University of Texas/MD Anderson Cancer Center Dept of MD Anderson (18)

Houston, Texas, United States

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Baylor College of Medicine Dept.of Baylor College of Med.

Houston, Texas, United States

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South Texas Oncology and Hematology, PA South Texas Oncology (2)

San Antonio, Texas, United States

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Texas A&M HealthSciencesCtr-Scott & White Memorial Hospital CenterForCancerPrevention&Care

Temple, Texas, United States

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University of Vermont Office of Clinical Trials Res.

Burlington, Vermont, United States

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University of Virginia Health Systems SC-2

Charlottesville, Virginia, United States

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Blue Ridge Research Center at Roanoke Neurological Center SC

Roanoke, Virginia, United States

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Dean Health System

Madison, Wisconsin, United States

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Waukesha Memorial Hospital Cancer Center Dept.ofWaukeshaMemorialHosp.

Waukesha, Wisconsin, United States

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Novartis Investigative Site

La Plata, Buenos Aires, Argentina

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Buenos Aires, , Argentina

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Córdoba, , Argentina

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Douglas, Queensland, Australia

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Greenslopes, Queensland, Australia

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Clayton, Victoria, Australia

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Geelong, Victoria, Australia

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Innsbruck, Tyrol, Austria

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Leoben, , Austria

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Linz, , Austria

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Vienna, , Austria

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Vienna, , Austria

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Curitiba, Paraná, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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Campinas, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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Brampton, Ontario, Canada

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Cambridge, Ontario, Canada

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Mississauga, Ontario, Canada

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Ottawa, Ontario, Canada

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Toronto, Ontario, Canada

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Toronto, Ontario, Canada

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Greenfield Park, Quebec, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Chengdu, Sichuan, China

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Hangzhou, Zhejiang, China

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Beijing, , China

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Beijing, , China

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Guangzhou, , China

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Shanghai, , China

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Bogotá, Cundinamarca, Colombia

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Bucaramanga, , Colombia

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Medellín, , Colombia

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Brno - Bohunice, Czech Republic, Czechia

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Hradec Králové, CZE, Czechia

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Olomouc, CZE, Czechia

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Prague, , Czechia

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Al Mansurah, , Egypt

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Alexandria, , Egypt

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Cairo, , Egypt

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Cairo, , Egypt

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Cairo, , Egypt

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Amiens Cedex1, , France

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Brest, , France

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La Roche-sur-Yon, , France

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Limoges, , France

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Pessac, , France

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Saint-Priest-en-Jarez, , France

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Aachen, , Germany

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Bad Saarow, , Germany

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Bamberg, , Germany

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Cologne, , Germany

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Dresden, , Germany

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Freiburg im Breisgau, , Germany

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Hamburg, , Germany

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München, , Germany

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Heraklion Crete, Greece, Greece

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Athens, GR, Greece

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Ioannina, GR, Greece

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Athens, , Greece

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Hong Kong, , Hong Kong

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Budapest, , Hungary

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Győr, , Hungary

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Kaposvár, , Hungary

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Pécs, , Hungary

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Szeged, , Hungary

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Haifa, , Israel

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Jerusalem, , Israel

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Petah Tikva, , Israel

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Ramat Gan, , Israel

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Tel Aviv, , Israel

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Brindisi, BR, Italy

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Catania, CT, Italy

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San Giovanni Rotondo, FG, Italy

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Florence, FI, Italy

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Genova, GE, Italy

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Lecce, LE, Italy

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Milan, MI, Italy

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Rozzano, MI, Italy

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Modena, MO, Italy

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Palermo, PA, Italy

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Piacenza, PC, Italy

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Pescara, PE, Italy

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Pisa, PI, Italy

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Potenza, PZ, Italy

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Reggio Calabria, RC, Italy

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Reggio Emilia, RE, Italy

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Siena, SI, Italy

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Venezia, VE, Italy

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Nagoya, Aichi-ken, Japan

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Kashiwa, Chiba, Japan

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Matsuyama, Ehime, Japan

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Kure, Hiroshima, Japan

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Kanazawa, Ishikawa-ken, Japan

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Shinjuku-ku, Japan, Japan

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Kyoto, Kyoto, Japan

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Sendai, Miyagi, Japan

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Osaka, Osaka, Japan

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Suita, Osaka, Japan

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Sunto-gun, Shizuoka, Japan

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Chuo-ku, Tokyo, Japan

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Koto, Tokyo, Japan

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Fukuoka, , Japan

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Beirut, , Lebanon

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Beirut, , Lebanon

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Beirut, , Lebanon

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Beirut, , Lebanon

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Saida, , Lebanon

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Mexico City, Mexico City, Mexico

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Monterrey, Nuevo León, Mexico

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Grafton, Auckland, New Zealand

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Wellington, , New Zealand

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Oslo, , Norway

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Jesus Maria, Lima region, Peru

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San Isidro, Lima region, Peru

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Lublin, Lublin Voivodeship, Poland

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Bydgoszcz, , Poland

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Lodz, , Poland

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Warsaw, , Poland

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Moscow, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Nizhny Novgorod, , Russia

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Petrozavodsk, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Dammam, , Saudi Arabia

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Jeddah, , Saudi Arabia

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Riyadh, , Saudi Arabia

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Singapore, , Singapore

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Singapore, , Singapore

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Singapore, , Singapore

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Bratislava, , Slovakia

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Gyeonggi-do, Korea, South Korea

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Seoul, Korea, South Korea

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Seoul, Korea, South Korea

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Seoul, Korea, South Korea

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Cadiz, Andalusia, Spain

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Seville, Andalusia, Spain

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Sabadell, Barcelona, Spain

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Donostia / San Sebastian, Basque Country, Spain

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Santander, Cantabria, Spain

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Badalona, Catalonia, Spain

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Barcelona, Catalonia, Spain

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Barcelona, Catalonia, Spain

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Barcelona, Catalonia, Spain

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Majadahonda, Madrid, Spain

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Pozuelo de Alarcón, Madrid, Spain

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Pamplona, Navarre, Spain

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Valencia, Valencia, Spain

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Madrid, , Spain

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Zurich, CH, Switzerland

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Bellinzona, , Switzerland

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Bangkok, , Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Songkhla, , Thailand

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Ankara, , Turkey (Türkiye)

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Ankara, , Turkey (Türkiye)

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Antalya, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Talas / Kayseri, , Turkey (Türkiye)

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Caracas, Distrito Federal, Venezuela

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Caracas, Distrito Federal, Venezuela

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Countries

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United States Argentina Australia Austria Brazil Canada China Colombia Czechia Egypt France Germany Greece Hong Kong Hungary Israel Italy Japan Lebanon Mexico New Zealand Norway Peru Poland Russia Saudi Arabia Singapore Slovakia South Korea Spain Switzerland Thailand Turkey (Türkiye) Venezuela

References

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Witzig TE, Tobinai K, Rigacci L, Ikeda T, Vanazzi A, Hino M, Shi Y, Mayer J, Costa LJ, Bermudez Silva CD, Zhu J, Belada D, Bouabdallah K, Kattan JG, Kuruvilla J, Kim WS, Larouche JF, Ogura M, Ozcan M, Fayad L, Wu C, Fan J, Louveau AL, Voi M, Cavalli F. Adjuvant everolimus in high-risk diffuse large B-cell lymphoma: final results from the PILLAR-2 randomized phase III trial. Ann Oncol. 2018 Mar 1;29(3):707-714. doi: 10.1093/annonc/mdx764.

Reference Type DERIVED
PMID: 29253068 (View on PubMed)

Related Links

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http://www.novartisclinicaltrials.com/webapp/etrials/searchTrial.do?t=i&trialID=755&keywords=crad001n2301

Visit NovartisClinicalTrials.com: Pre-qualify for a trial, and view a list of trials and participating study centers.

Other Identifiers

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2008-000498-40

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CRAD001N2301

Identifier Type: -

Identifier Source: org_study_id

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