Safety, Tolerability and PK/PD Study in Young Adult Patients With Childhood Onset Growth Hormone Deficiency (GHD).

NCT ID: NCT00778518

Last Updated: 2009-10-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

36 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-07-31

Study Completion Date

2009-10-31

Brief Summary

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Study to find the optimal dose of Growth Hormone Replacement in young adult patients suffering from childhood onset growth hormone deficiency (GHD).

Detailed Description

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The primary objective of this study is to evaluate the safety, tolerability and pharmacodynamic response of three different ARX201 doses (PEG-ahGH) when administered repeatedly to young adult patients with childhood onset growth hormone deficiency (GHD).

Conditions

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Growth Hormone Deficiency

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

SINGLE

Participants

Study Groups

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1

low dose

Group Type ACTIVE_COMPARATOR

ARX201

Intervention Type DRUG

Reconstituted lyophilized drug product at 2.5 mg/wk; 3 periods over six months.

2

Medium dose

Group Type ACTIVE_COMPARATOR

ARX201

Intervention Type DRUG

Reconstituted lyophilized drug product at 5.0 mg/wk; 3 periods over six months.

3

High Dose

Group Type ACTIVE_COMPARATOR

ARX201

Intervention Type DRUG

Reconstituted lyophilized drug product at 10.0 mg/wk; 3 periods over six months.

Interventions

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ARX201

Reconstituted lyophilized drug product at 2.5 mg/wk; 3 periods over six months.

Intervention Type DRUG

ARX201

Reconstituted lyophilized drug product at 5.0 mg/wk; 3 periods over six months.

Intervention Type DRUG

ARX201

Reconstituted lyophilized drug product at 10.0 mg/wk; 3 periods over six months.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* 18-30 years old
* GHD of childhood onset
* completed growth
* IGF-1 \<=2SDS
* rhGH treatment naive
* hGH levels below cut-off

Exclusion Criteria

* History of malignancy or intracranial tumors
* ECG abnormality
* ICH
* hepatic dysfunction
* renal impairment
* major medical conditions
* inadequate T4
* positive for HBV, HCV, or HIV
* alcohol or drug abuse
Minimum Eligible Age

18 Years

Maximum Eligible Age

30 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Merck Serono International SA

INDUSTRY

Sponsor Role collaborator

Ambrx, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Clinical Research and Development, Ambrx, Inc.

Principal Investigators

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Mihaly Juhasz, MD

Role: STUDY_DIRECTOR

Accelsiors CRO & Consultancy Services

Locations

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Accelsiors CRO and Consultancy Services

Budapest, , Hungary

Site Status

Countries

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Hungary

Other Identifiers

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EudraCT: 2007-001746-40

Identifier Type: -

Identifier Source: secondary_id

PRO-ARX201-701

Identifier Type: -

Identifier Source: org_study_id

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