Muscle Response to Enzyme Replacement Therapy in Pompe Disease

NCT ID: NCT00713453

Last Updated: 2015-03-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Total Enrollment

16 participants

Study Classification

OBSERVATIONAL

Study Start Date

2007-01-31

Study Completion Date

2019-12-31

Brief Summary

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This study is to study the response of muscle cells from Pompe disease after enzyme replacement therapy

Detailed Description

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Conditions

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Pompe Disease

Study Design

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Observational Model Type

CASE_ONLY

Eligibility Criteria

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Inclusion Criteria

* patients with Pompe disease, prepare or on enzyme replacement therapy
* signed informed consent

Exclusion Criteria

\-
Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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National Taiwan University Hospital

OTHER

Sponsor Role lead

Responsible Party

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National Taiwan University Hospital

Yin-Hsiu Chien, M.D., PhD.

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Yin-Hsiu Chien, MD

Role: PRINCIPAL_INVESTIGATOR

National Taiwan University Hospital

Locations

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National Taiwan University Hospital

Taipei, , Taiwan

Site Status RECRUITING

Countries

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Taiwan

Central Contacts

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Yin-Hsiu Chien, MD

Role: CONTACT

886-2-23123456 ext. 71937

Facility Contacts

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Yin-Hsiu Chien, MD

Role: primary

886-2-23123456 ext. 71937

Other Identifiers

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200704066R

Identifier Type: -

Identifier Source: org_study_id

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