Muscle Response to Enzyme Replacement Therapy in Pompe Disease
NCT ID: NCT00713453
Last Updated: 2015-03-24
Study Results
The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.
Basic Information
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UNKNOWN
16 participants
OBSERVATIONAL
2007-01-31
2019-12-31
Brief Summary
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Detailed Description
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Conditions
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Study Design
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CASE_ONLY
Eligibility Criteria
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Inclusion Criteria
* signed informed consent
Exclusion Criteria
ALL
Yes
Sponsors
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National Taiwan University Hospital
OTHER
Responsible Party
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National Taiwan University Hospital
Yin-Hsiu Chien, M.D., PhD.
Principal Investigators
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Yin-Hsiu Chien, MD
Role: PRINCIPAL_INVESTIGATOR
National Taiwan University Hospital
Locations
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National Taiwan University Hospital
Taipei, , Taiwan
Countries
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Central Contacts
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Facility Contacts
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Other Identifiers
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200704066R
Identifier Type: -
Identifier Source: org_study_id
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