Evaluation of PROCHYMAL® Adult Human Stem Cells for Treatment-resistant Moderate-to-severe Crohn's Disease

NCT ID: NCT00482092

Last Updated: 2022-01-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

330 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-09-17

Study Completion Date

2014-09-15

Brief Summary

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Protocol 603 is enrolling subjects with moderate-to-severe Crohn's disease who are intolerant to, or have previously failed therapy with, at least one steroid and at least one immunosuppressant and a biologic monoclonal anti-body to tumor necrosis factor alpha. The protocol investigates the safety and efficacy of using PROCHYMAL® adult human stem cells to induce remission. PROCHYMAL is delivered through a vein in the arm four times over two weeks, for approximately an hour each time.

Detailed Description

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A significant number of individuals with Crohn's disease do not find relief with existing steroidal, immunosuppressive, or biologic therapies, and are forced to seek surgery or other drastic measures for treatment.

PROCHYMAL® adult human stem cells are manufactured from healthy, volunteer donors, extensively tested, and are stored to be available as needed. Human and animal studies have shown that the cells do not require any donor-recipient matching. The cells may have both immunosuppressive and healing benefits in Crohn's disease. The cells naturally migrate specifically to sites of inflammation, so their effects are believed to be local and self-limiting rather than systemic.

Protocol 603 is enrolling subjects to evaluate the ability of PROCHYMAL to induce remission in subjects with moderate-to-severe disease (Crohn's disease activity index -- CDAI -- of between 250 and 450, inclusive) who have failed or been intolerant of at least one drug in each of the steroid, immunosuppressant, and biologic classes.

Conditions

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Crohn's Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo

Participants will receive matching placebo administered as intravenous (IV) infusions.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Prochymal® Placebo-matching IV infusion

Prochymal® - Low dose

Participants will receive a total dose of Prochymal® 600 x 10\^6 cells, IV infusion, on four days, once daily.

Group Type ACTIVE_COMPARATOR

Prochymal®

Intervention Type DRUG

Prochymal® IV infusion

Prochymal® - High dose

Participants will receive a total dose of Prochymal® 1200 x 10\^6 cells, IV infusion, on four days, once daily.

Group Type ACTIVE_COMPARATOR

Prochymal®

Intervention Type DRUG

Prochymal® IV infusion

Interventions

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Prochymal®

Prochymal® IV infusion

Intervention Type DRUG

Placebo

Prochymal® Placebo-matching IV infusion

Intervention Type DRUG

Other Intervention Names

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Adult Human Mesenchymal Stem Cells

Eligibility Criteria

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Inclusion Criteria

* failed (within last 2 yr) or intolerant of at least one steroid AND at least one immunosuppressant AND at EXACTLY one biologic
* CDAI between 250 and 450, inclusive
* endoscopically or radiographically confirmed Crohn's disease of ileus or colon or both
* C-Reactive Protein Test (CRP) of at least 5 mg/l (0.5 mg/dl)\*OR\* CDAI of at least 300
* weight between 40 and 150 kg, inclusive
* adequate renal function
* negative tuberculosis skin (PPD) test (or evaluated low risk of TB activation)

Exclusion Criteria

* HIV or hepatitis infection active
* allergy to CT contrast agents, or to bovine or porcine products
* symptomatic fibrostenotic Crohn's disease
* permanent ostomy
* biologic therapy within past 90 d
* prednisone greater than 20 mg/d within past month
* short-bowel syndrome
* total parenteral nutrition
* abnormal liver function
* malignancy active within past 5 years (except completely resected basal or squamous cell carcinoma of skin)
* enteric pathogens, including C. difficile
* history of colonic mucosal dysplasia
* current or prior evidence of tuberculosis (TB) (unless risk of activation or re-activation deemed low)
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Mesoblast, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Mahboob Rahman, MD

Role: STUDY_DIRECTOR

Mesoblast, Inc.

Locations

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University of Southern California University Hospital

Los Angeles, California, United States

Site Status

University of California, San Francisco

San Francisco, California, United States

Site Status

Western States Clinical Research

Wheat Ridge, Colorado, United States

Site Status

Clinical Research of West Florida

Clearwater, Florida, United States

Site Status

Borland-Groover Clinic

Jacksonville, Florida, United States

Site Status

Shafran Gastroenterology Center

Winter Park, Florida, United States

Site Status

Atlanta Gastroenterology Associates

Atlanta, Georgia, United States

Site Status

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status

Carle Clinic Association

Urbana, Illinois, United States

Site Status

Indiana University Medical Center

Indianapolis, Indiana, United States

Site Status

Cotton-O'Neil Clinical Research Center

Topeka, Kansas, United States

Site Status

University of Kentucky Hospital

Lexington, Kentucky, United States

Site Status

University of Louisville Hospital

Louisville, Kentucky, United States

Site Status

Gulf Coast Research

Baton Rouge, Louisiana, United States

Site Status

University of Maryland, Baltimore

Baltimore, Maryland, United States

Site Status

National Institutes of Health

Bethesda, Maryland, United States

Site Status

Chevy Chase Clinical Research

Chevy Chase, Maryland, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Brigham and Womens Hospital

Boston, Massachusetts, United States

Site Status

Clinical Pharmacology Study Group

Worcester, Massachusetts, United States

Site Status

Center for Clinical Studies

Dearborn, Michigan, United States

Site Status

Center for Digestive Health

Troy, Michigan, United States

Site Status

University of Minnesota Hospital

Minneapolis, Minnesota, United States

Site Status

St Louis Center for Clinical Studies

St Louis, Missouri, United States

Site Status

Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status

Weill Cornell Medical College

New York, New York, United States

Site Status

Mount Sinai School of Medicine

New York, New York, United States

Site Status

Rochester Institute for Digestive Diseases

Rochester, New York, United States

Site Status

Rochester General Hospital

Rochester, New York, United States

Site Status

University Hospital and Medical Center

Stony Brook, New York, United States

Site Status

Charlotte Gastroenterology and Hepatology

Charlotte, North Carolina, United States

Site Status

Pinehurst Medical Clinic

Pinehurst, North Carolina, United States

Site Status

Wake Forest University

Winston-Salem, North Carolina, United States

Site Status

Gastroenterology United of Tulsa

Tulsa, Oklahoma, United States

Site Status

Options Health Research

Tulsa, Oklahoma, United States

Site Status

Allegheney Center for Digestive Health

Pittsburgh, Pennsylvania, United States

Site Status

University of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status

Gastroenterology Center of the Midsouth

Germantown, Tennessee, United States

Site Status

Nashville GI Specialists

Nashville, Tennessee, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Baylor University Medical Center

Dallas, Texas, United States

Site Status

University of Texas Medical Branch

Galveston, Texas, United States

Site Status

University of Texas Health Science Center

Houston, Texas, United States

Site Status

University of Vermont

Burlington, Vermont, United States

Site Status

Digestive and Liver Disease Specialists

Norfolk, Virginia, United States

Site Status

McGuire Research Institute

Richmond, Virginia, United States

Site Status

Seattle Gastroenterology Associates

Seattle, Washington, United States

Site Status

Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status

Royal Melbourne Hospital

Melbourne, Victoria, Australia

Site Status

University of Calgary

Calgary, Alberta, Canada

Site Status

University of Alberta Hospital

Edmonton, Alberta, Canada

Site Status

Health Science Centre

Winnipeg, Manitoba, Canada

Site Status

London Health Sciences Centre

London, Ontario, Canada

Site Status

Mount Sinai Hospital

Toronto, Ontario, Canada

Site Status

University of Otago

Christchurch, , New Zealand

Site Status

Waikato Hospital

Hamilton, , New Zealand

Site Status

Countries

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United States Australia Canada New Zealand

Other Identifiers

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CRD 603

Identifier Type: -

Identifier Source: org_study_id

NCT00609232

Identifier Type: -

Identifier Source: nct_alias

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