Extended Evaluation of PROCHYMAL® Adult Human Stem Cells for Treatment-Resistant Moderate-to-Severe Crohn's Disease

NCT ID: NCT00543374

Last Updated: 2021-12-28

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

98 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-09-17

Study Completion Date

2011-04-28

Brief Summary

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Protocol 610 is enrolling subjects who successfully achieved clinical benefit (reduction in Crohn's Disease Activity Index (CDAI) of at least 100 points) in Protocol 603. Protocol 610 is evaluating the length of initial effect of PROCHYMAL® adult human mesenchymal stem cells and the ability of these cells to successfully re-induce clinical benefit.

Detailed Description

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A significant number of individuals with Crohn's disease do not find relief with existing steroidal, immunosuppressive, or biologic therapies, and are forced to seek surgery or other drastic measures for treatment.

PROCHYMAL® adult human stem cells are manufactured from healthy, volunteer donors, extensively tested, and are stored to be available as needed. Human and animal studies have shown that the cells do not require any donor-recipient matching. The cells may have both immunosuppressive and healing benefits in Crohn's disease. The cells naturally migrate specifically to sites of inflammation, so their effects are believed to be local and self-limiting rather than systemic.

Protocol 610 is an extension study offered only to those subjects who successfully achieved clinical benefit (reduction of CDAI of at least 100 points) in Protocol 603.

Conditions

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Crohn's Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo

PROCHYMAL Low dose

Low dose (total of 600 million cells)

Group Type ACTIVE_COMPARATOR

PROCHYMAL adult human mesenchymal stem cells

Intervention Type DRUG

intravenous infusion four times over two weeks; possibly repeated once

PROCHYMAL High dose

High dose (total of 1200 cells)

Group Type ACTIVE_COMPARATOR

PROCHYMAL adult human mesenchymal stem cells

Intervention Type DRUG

intravenous infusion four times over two weeks; possibly repeated once

Interventions

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Placebo

Placebo

Intervention Type DRUG

PROCHYMAL adult human mesenchymal stem cells

intravenous infusion four times over two weeks; possibly repeated once

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Participation in Osiris Protocol 603, with drop of at least 100 points in CDAI at Day 28

Exclusion Criteria

* Substance abuse
* Failure to receive full dose of all interventions in Protocol 603
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Mesoblast, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Mahboob Rahman, MD

Role: STUDY_DIRECTOR

Mesoblast, Inc.

Locations

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Advanced Clinical Research Institute

Anaheim, California, United States

Site Status

Veteran's Administration Medical Center (does not require vet status)

Long Beach, California, United States

Site Status

University of Southern California University Hospital

Los Angeles, California, United States

Site Status

University of California, San Francisco

San Francisco, California, United States

Site Status

Western States Clinical Research

Wheat Ridge, Colorado, United States

Site Status

Gastroenterology Center of Connecticut

Hamden, Connecticut, United States

Site Status

Clinical Research of West Florida

Clearwater, Florida, United States

Site Status

Borland-Groover Clinic

Jacksonville, Florida, United States

Site Status

Venture Research Institute

Miami, Florida, United States

Site Status

Shafran Gastroenterology Center

Winter Park, Florida, United States

Site Status

Atlanta Gastroenterology Associates

Atlanta, Georgia, United States

Site Status

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status

Carle Clinic Association

Urbana, Illinois, United States

Site Status

Indiana University Medical Center

Indianapolis, Indiana, United States

Site Status

Cotton-O'Neil Clinical Research Center

Topeka, Kansas, United States

Site Status

University of Kentucky Hospital

Lexington, Kentucky, United States

Site Status

University of Louisville Hospital

Louisville, Kentucky, United States

Site Status

Gulf Coast Research

Baton Rouge, Louisiana, United States

Site Status

National Institutes of Health

Bethesda, Maryland, United States

Site Status

Metropolitan Gastroenterology Group

Chevy Chase, Maryland, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Brigham and Womens Hospital

Boston, Massachusetts, United States

Site Status

Clinical Pharmacology Study Group

Worcester, Massachusetts, United States

Site Status

Center for Clinical Studies

Dearborn, Michigan, United States

Site Status

Center for Digestive Health

Troy, Michigan, United States

Site Status

University of Minnesota Hospital

Minneapolis, Minnesota, United States

Site Status

St Louis Center for Clinical Studies

St Louis, Missouri, United States

Site Status

Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status

Gastroenterology Research Associates

Cedar Knolls, New Jersey, United States

Site Status

Holy Name Hospital

Teaneck, New Jersey, United States

Site Status

Weill Cornell Medical College

New York, New York, United States

Site Status

Mount Sinai School of Medicine

New York, New York, United States

Site Status

Rochester Institute for Digestive Diseases

Rochester, New York, United States

Site Status

Rochester General Hospital

Rochester, New York, United States

Site Status

University Hospital and Medical Center

Stony Brook, New York, United States

Site Status

Charlotte Gastroenterology and Hepatology

Charlotte, North Carolina, United States

Site Status

Pinehurst Medical Clinic

Pinehurst, North Carolina, United States

Site Status

Wake Forest University

Winston-Salem, North Carolina, United States

Site Status

Dayton Science Institute

Dayton, Ohio, United States

Site Status

Gastroenterology United of Tulsa

Tulsa, Oklahoma, United States

Site Status

Options Health Research

Tulsa, Oklahoma, United States

Site Status

Allegheney Center for Digestive Health

Pittsburgh, Pennsylvania, United States

Site Status

University of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status

Gastroenterology Center of the Midsouth

Germantown, Tennessee, United States

Site Status

Nashville GI Specialists

Nashville, Tennessee, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Baylor University Medical Center

Dallas, Texas, United States

Site Status

University of Texas Medical Branch

Galveston, Texas, United States

Site Status

Memorial Hermann Hospital

Houston, Texas, United States

Site Status

University of Vermont

Burlington, Vermont, United States

Site Status

Digestive and Liver Disease Specialists

Norfolk, Virginia, United States

Site Status

McGuire Research Institute

Richmond, Virginia, United States

Site Status

Seattle Gastroenterology Associates

Seattle, Washington, United States

Site Status

University of Calgary

Calgary, Alberta, Canada

Site Status

University of Alberta Hospital

Edmonton, Alberta, Canada

Site Status

Health Sciences Centre

Winnipeg, Manitoba, Canada

Site Status

London Health Sciences Centre

London, Ontario, Canada

Site Status

Mount Sinai Hospital

Toronto, Ontario, Canada

Site Status

Countries

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United States Canada

Other Identifiers

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CRD 610

Identifier Type: -

Identifier Source: org_study_id