E7389 Versus Treatment of Physician's Choice in Patients With Locally Recurrent or Metastatic Breast Cancer

NCT ID: NCT00388726

Last Updated: 2020-01-07

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

762 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-11-30

Study Completion Date

2013-06-30

Brief Summary

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The purpose of this study is to compare Overall Survival (OS), Progression Free Survival (PFS), objective tumor response rate, duration of response, and safety in patients treated with E7389 versus the Treatment of Physician's Choice (TPC) in patients with locally recurrent or metastatic breast cancer.

Detailed Description

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Conditions

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Breast Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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1

Group Type EXPERIMENTAL

E7389

Intervention Type DRUG

1.4 mg/m\^2 intravenous (IV) infusion given over 2-5 minutes on Days 1 and 8 every 21 days.

2

Group Type ACTIVE_COMPARATOR

Physician's Choice

Intervention Type DRUG

Treatment of the Physician's Choice defined as any single agent chemotherapy, hormonal treatment or biological therapy approved for the treatment of cancer; or palliative treatment or radiotherapy, administered according to local practice, if applicable.

Interventions

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E7389

1.4 mg/m\^2 intravenous (IV) infusion given over 2-5 minutes on Days 1 and 8 every 21 days.

Intervention Type DRUG

Physician's Choice

Treatment of the Physician's Choice defined as any single agent chemotherapy, hormonal treatment or biological therapy approved for the treatment of cancer; or palliative treatment or radiotherapy, administered according to local practice, if applicable.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Female patients with histologically or cytologically confirmed carcinoma of the breast.

Every effort should be made to make paraffin embedded tissue or slides from the diagnostic biopsy or surgical specimen available for confirmation of diagnosis.
2. Patients with locally recurrent or metastatic disease who have received at least two (and not more than five) prior chemotherapeutic regimens for breast cancer, at least two of which were administered for treatment of locally recurrent and/or metastatic disease.

Prior therapy must be documented by the following criteria prior to entry onto study:
* Regimens must have included an anthracycline (e.g., doxorubicin, epirubicin) and a taxane (e.g., paclitaxel, docetaxel) in any combination or order. Treatment with any of these agents is not required if they are contraindicated for a certain patient.
* One or two of these regimens may have been administered as adjuvant and/or neoadjuvant therapy, but at least 2 must have been given for relapsed or metastatic disease.
* Patients must have proved refractory to the most recent chemotherapy, documented by progression on or within six (6) months of therapy.
* Patients with Human Epidermal Growth Factor 2 (HER2/neu) positive tumors may additionally have been treated with trastuzumab.
* Patients may have additionally been treated with anti-hormonal therapy.
3. Resolution of all chemotherapy or radiation-related toxicities to Grade 1 severity or lower, except for stable sensory neuropathy \<= Grade 2 and alopecia.
4. Age \>= 18 years.
5. Eastern Cooperative Oncology Group (ECOG) Performance Status of 0 to 2.
6. Life expectancy of \>= 3 months.
7. Adequate renal function as evidenced by serum creatinine \<= 2.0 mg/dL or calculated creatinine clearance \>= 40 mL/min per the Cockcroft and Gault formula.
8. Adequate bone marrow function as evidenced by absolute neutrophil count (ANC) \>= 1.5 x 10\^9/L, hemoglobin \>= 10.0 g/dL (a hemoglobin \<10.0 g/dL is acceptable if it is corrected by growth factor or transfusion), and platelet count \>= 100 x 10\^9/L.
9. Adequate liver function as evidenced by bilirubin \<= 1.5 times the upper limits of normal (ULN) and alkaline phosphatase, alanine aminotransferase (ALT), and aspartate aminotransferase (AST) \<= 3 x ULN (in the case of liver metastases \<= 5 x ULN), unless there are bone metastases, in which case liver specific alkaline phosphatase must be separated from the total and used to assess the liver function instead of the total alkaline phosphatase. In case alkaline phosphatase is \>3 x ULN (in absence of liver metastases) or \> 5 x ULN (in presence of liver metastases) AND patient is known to have bone metastases, the liver specific alkaline phosphatase must be separated from the total and used to assess the liver function instead of the total alkaline phosphatase.
10. Patients willing and able to comply with the study protocol for the duration of the study.
11. Written informed consent prior to any study-specific screening procedures with the understanding that the patient may withdraw consent at any time without prejudice.

Exclusion Criteria

1. Patients who have received any of the following treatments within the specified period before E7389 or TPC treatment start:

* chemotherapy, radiation, trastuzumab or hormonal therapy within three weeks.
* any investigational drug within four weeks.
2. Radiation therapy encompassing \> 30% of marrow.
3. Prior treatment with mitomycin C or nitrosourea.
4. Pulmonary lymphangitic involvement that results in pulmonary dysfunction requiring active treatment, including the use of oxygen.
5. Patients with brain or subdural metastases are not eligible, unless they have completed local therapy and have discontinued the use of corticosteroids for this indication for at least 4 weeks before starting treatment in this study. Any signs (e.g., radiologic) and/or symptoms of brain metastases must be stable for at least 4 weeks before starting study treatment; radiographic stability should be determined by comparing a contrast-enhanced computed tomography or magnetic resonance imaging brain scan performed during screening to a prior scan performed at least 4 weeks earlier.
6. Patients with meningeal carcinomatosis.
7. Patients who are receiving anti-coagulant therapy with warfarin or related compounds, other than for line patency, and cannot be changed to heparin-based therapy if randomized to E7389 are not eligible. If a patient is to continue on mini-dose warfarin, then the prothrombin time (PT) or international normalized ratio (INR) must be closely monitored.
8. Women who are pregnant or breast-feeding; women of childbearing potential with either a positive pregnancy test at screening or no pregnancy test; women of childbearing potential unless (1) surgically sterile or (2) using adequate measures of contraception in the opinion of the Investigator. Perimenopausal women must be amenorrheic for at least 12 months to be considered of non-childbearing potential.
9. Severe/uncontrolled intercurrent illness/infection.
10. Significant cardiovascular impairment (history of congestive heart failure \> New York Heart Association grade II, unstable angina or myocardial infarction within the past six months, or serious cardiac arrhythmia).
11. Patients with organ allografts requiring immunosuppression.
12. Patients with known positive HIV status.
13. Patients who have had a prior malignancy, other than previous breast cancer, carcinoma in situ of the cervix, or non-melanoma skin cancer, unless the prior malignancy was diagnosed and definitively treated \>= 5 years previously with no subsequent evidence of recurrence.
14. Patients with pre-existing neuropathy \> Grade 2.
15. Patients with a hypersensitivity to halichondrin B and/or halichondrin B chemical derivative.
16. Patients who participated in a prior E7389 clinical trial whether or not E7389 was received.
17. Patients with other significant disease or disorders that, in the Investigator's opinion, would exclude the patient from the study.
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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Eisai Limited

INDUSTRY

Sponsor Role collaborator

Eisai Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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US Oncology St. Vincent's Hospital - Bruno Cancer Center

Birmingham, Alabama, United States

Site Status

Bellflower Satellite

Bellflower, California, United States

Site Status

Research Center

Gilroy, California, United States

Site Status

US Oncology

Denver, Colorado, United States

Site Status

Florida Cancer Research Institute

Davie, Florida, United States

Site Status

Innovative Medical Research of South Florida, Inc.

Miami, Florida, United States

Site Status

Peachtree Hematology/Oncology Consultants, PC

Atlanta, Georgia, United States

Site Status

US Oncology

Niles, Illinois, United States

Site Status

US Oncology

Indianapolis, Indiana, United States

Site Status

University of Iowa Hospital and Clinic

Iowa City, Iowa, United States

Site Status

Hematology Oncology Clinic

Baton Rouge, Louisiana, United States

Site Status

Oncology Care Associates, P.L.L.C.

Saint Joseph, Michigan, United States

Site Status

US Oncology

Columbia, Missouri, United States

Site Status

Montana Cancer Specialists

Missoula, Montana, United States

Site Status

US Oncology

Las Vegas, Nevada, United States

Site Status

US Oncology

Albany, New York, United States

Site Status

North Shore Hematology/Oncology Associates

East Setauket, New York, United States

Site Status

Weill Cornell Breast Cancer Center

New York, New York, United States

Site Status

Carolina Hematology Oncology Associates

Charlotte, North Carolina, United States

Site Status

US Oncology

Raleigh, North Carolina, United States

Site Status

US Oncology

Eugene, Oregon, United States

Site Status

St. Vincent Medical Center

Portland, Oregon, United States

Site Status

US Oncology

Bedford, Texas, United States

Site Status

US Oncology

Dallas, Texas, United States

Site Status

US Oncology

Houston, Texas, United States

Site Status

US Oncology

McAllen, Texas, United States

Site Status

US Oncology

Midland, Texas, United States

Site Status

US Oncology

Tyler, Texas, United States

Site Status

US Oncology

Spokane, Washington, United States

Site Status

Northwest Medical Specialists

Tacoma, Washington, United States

Site Status

US Oncology

Vancouver, Washington, United States

Site Status

US Oncology

Yakima, Washington, United States

Site Status

Instituto Oncologico "Las Heras"

Bahía Blanca, Buenos Aires, Argentina

Site Status

Hospital Britanico

C.a.b.a, Buenos Aires, Argentina

Site Status

Instituto FIDES especialidades Medicas

La Plata, Buenos Aires, Argentina

Site Status

Breast Clinica de la Mama

La Plata, Buenos Aires, Argentina

Site Status

CITEM

Quilmes, Buenos Aires, Argentina

Site Status

CER Instituto Medico

Quilmes Oeste, Buenos Aires, Argentina

Site Status

Instituto CAICI

Rosario, Pcia. Santa Fe, Argentina

Site Status

Centro Medico San Roque

San Miguel de Tucumán, San Miguel de Tucuman, Argentina

Site Status

Hosptial Interzonal General de Mar del Plata

Buenos Aires, , Argentina

Site Status

Clinica Universitaria Privada Reina Fabiola

Córdoba, , Argentina

Site Status

Sanatorio Frances

Córdoba, , Argentina

Site Status

Instituto de Oncologia y Especialidades Medicas

Rosario Santa Fe, , Argentina

Site Status

Clinica Especializada ISIS

Santa Fe, , Argentina

Site Status

The Queen Elizabeth Hospital

Southport, Queensland, Australia

Site Status

Servicio De Oncologia

Woodville South, South Australia, Australia

Site Status

Maroondah Breast Clinic

Melbourne, , Australia

Site Status

Mater Medical Centre

North Sydney, , Australia

Site Status

Mount Hospital

Perth, , Australia

Site Status

Royal Perth Hospital, Department of Medical Oncology

Perth, , Australia

Site Status

Medizinische Universitatsklinik Graz

Graz Steiermark, , Austria

Site Status

Salzburger Landeskliniken Universitatsklinik fur Innere medizin III

Salzburg, , Austria

Site Status

Institut Jules Bordet

Brussels, , Belgium

Site Status

Cliniques Universitaires Saint-Luc

Brussels, , Belgium

Site Status

Centre Hospitalier Notre-Dame - Reine Fabiola

Charleroi, , Belgium

Site Status

UZ Gent

Ghent, , Belgium

Site Status

AZ Groeninge, Campus Maria's Voorzienigheid

Kortrijk, , Belgium

Site Status

Centro Regional Integrado de Oncologia-CRIO

Fortaleza, Ceará, Brazil

Site Status

Centro de Pesquisas e Estudios do Centro Goiano

Giana, Goiás, Brazil

Site Status

Hospital Erasto Gaertner

Curitiba, Pará, Brazil

Site Status

Instituto Nacional do Cancer-Unidade III (INCA III)

Rio de Janiero, Rio de Janeiro, Brazil

Site Status

CPO-Centro de Pesquisas em Oncologia

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

CEPHO-Centro de Estudos e Pesquisa de Hematologia e oncologia

Santo André, São Paulo, Brazil

Site Status

Santo Andre Diagnosticos e Tratamentos

Santo André, São Paulo, Brazil

Site Status

Clinica de Oncologia Medica

São Paulo, São Paulo, Brazil

Site Status

Hospital Amaral Carvalho

Vila Assis, São Paulo, Brazil

Site Status

The Ottawa Hospital Regional Cancer Center

Ottawa, Ontario, Canada

Site Status

Sunnybrook Odette Cancer Centre

Toronto, Ontario, Canada

Site Status

McGill University Health Centre, Department of Oncology, Gerald Bronfman Center

Montreal, Quebec, Canada

Site Status

Clinical Hospital Osijek

Osijek, , Croatia

Site Status

University Hospital Center Zagreb

Zagreb, , Croatia

Site Status

University Hospital for Tumors Zagreb

Zagreb, , Croatia

Site Status

Masaryk Memorial Cancer Institute

Brno, , Czechia

Site Status

Hospital Jihlava

Jihlava, , Czechia

Site Status

Clinic of Radiotherapy and Oncology

Prague, , Czechia

Site Status

General Faculty Hospital Prague

Prague, , Czechia

Site Status

Fakultni Thomayerova Nemocnice

Prague, , Czechia

Site Status

Ustav radia ni onkologie 1. LF UK a FNB

Prague, , Czechia

Site Status

Centre Paul Papin

Agners Cedex 01, , France

Site Status

Hopital Jean Minjoz

Besançon, , France

Site Status

Polyclinique Boredaux Nord Aquitaine

Bordeaux, , France

Site Status

Centre Francois Baclesse Caen

Caen, , France

Site Status

Centre Jean Perrin - CRLC

Clermont-Ferrand, , France

Site Status

Centre Georges-Francois Lecierc

Dijon, , France

Site Status

Hopital Edourad Herriot

Lyon, , France

Site Status

Institut Curie

Paris, , France

Site Status

Clinique Armoricaine de Radiologie

Saint-Brieuc, , France

Site Status

Hopital Bretonneau

Tours, , France

Site Status

Semmelweis Medical University, III. Dep. of Internal Med.

Budapest, , Hungary

Site Status

Debrecen Medical University, Department of Oncology

Debrecen, , Hungary

Site Status

University of Pecs

Pécs, , Hungary

Site Status

Markusovszky Teaching Hospital, Dept. of Oncoradiology, Sec. Med. Oncology

Szombathely, , Hungary

Site Status

Azienda Ospedaliera Careggi

Firenze (FI), , Italy

Site Status

Ospedale San Martino

Genova, , Italy

Site Status

Ospedale "Vito Fazzi" - Lecce

Lecce (LE), , Italy

Site Status

Istituto Scientifico San Raffaele

Milan, , Italy

Site Status

Ospedale San Filippo Neri

Roma, , Italy

Site Status

Istituto Clinico Humanitas

Rozzano, , Italy

Site Status

UO di Oncologia

Sora, , Italy

Site Status

Akademickie Centrum Kliniczne Szpital Akademii Medycznej w

Gdansk, , Poland

Site Status

Szpital Morski im PCK w Gdyni Gdynskie Centrum Onkologii

Gdynia, , Poland

Site Status

Centrum Onkologii Instytut M. Sklodowskiej Curie w Warszawie Oddzial Gilwice

Gilwice, , Poland

Site Status

Centrum Onkologii Instytut M Sklodowskiej Curie, Oddzial w Krakowie

Krakow, , Poland

Site Status

Szpital Kiniczny Przemienienia Panskiego Uniwersyteu Medycznego im Karola Marcinkowskiego w Poznaniu

Poznan, , Poland

Site Status

Zachodniopomorski e Centrum

Szczecin, , Poland

Site Status

Centrum Onkologii Instytut im M. Sklodowskiej Curie w Warszawie

Warsaw, , Poland

Site Status

Republic Clinical Oncology Dispensary

Izhervsk Udmurtia, , Russia

Site Status

Kazan State Medical University

Kazan', , Russia

Site Status

Krasnodar Territory Clinical Oncology Center

Krasnodar, , Russia

Site Status

Burdenko Main Military Hospital

Moscow, , Russia

Site Status

Nizhniy Novgorod City Oncology Center

Nizhny Novgorod, , Russia

Site Status

City Clinical Hospital #1

Novosibirisk, , Russia

Site Status

Republican Oncology Center

Petrozavodsk, , Russia

Site Status

State Institution of Healthcare Stavropol Region clinical Oncology dispensary

Pyatigorsk, , Russia

Site Status

Pavlov Medical University

Saint Petersburg, , Russia

Site Status

St Petersburg City Oncology Center

Saint Petersburg, , Russia

Site Status

NN Petrov Research Institute of Oncology

Saint Petersburg, , Russia

Site Status

Tomsk Regional Oncology Dispensary

Tomsk, , Russia

Site Status

GUZ YO Regional Clinical Oncology Hospital

Yaroslavl, , Russia

Site Status

Panorama Medical Centre

Panorama, Cape Town, South Africa

Site Status

Eastern Cape Oncology Centre, GVI, St Georges Hospital

Port Elizabeth, Eastern Cape, South Africa

Site Status

Sandton Oncology Centre

Johannesburg, , South Africa

Site Status

Pretoria Academic Hospital

Pretoria, , South Africa

Site Status

Hospital Vall d Hebron

Barcelona, , Spain

Site Status

Hospital Mutua de Terrassa

Barcelona, , Spain

Site Status

Hospital Universitario de Girona Dr. Josep Trueta

Girona, , Spain

Site Status

Complejo Hospitalario de Jaen

Jaén, , Spain

Site Status

Hospital Unversitatio de Salamanca

Salamanca, , Spain

Site Status

Hospital Universitario de Canarias

Santa Cruz de Tenerife, , Spain

Site Status

Hospital General Virgen del Rocio

Seville, , Spain

Site Status

Hospital Clinico de Zaragoza

Zanagoza, , Spain

Site Status

Kantonsspital Aarau

Aarau, , Switzerland

Site Status

Inselspital Bern

Bern Bern, , Switzerland

Site Status

Kantonsspital Oncology Haematology

Sankt Gallen, , Switzerland

Site Status

Spital Thun-Simmental AG

Thun, , Switzerland

Site Status

Kantonsspital Winterhur

Winterhur, , Switzerland

Site Status

Countries

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United States Argentina Australia Austria Belgium Brazil Canada Croatia Czechia France Hungary Italy Poland Russia South Africa Spain Switzerland

References

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Hoon SN, Lau PK, White AM, Bulsara MK, Banks PD, Redfern AD. Capecitabine for hormone receptor-positive versus hormone receptor-negative breast cancer. Cochrane Database Syst Rev. 2021 May 26;5(5):CD011220. doi: 10.1002/14651858.CD011220.pub2.

Reference Type DERIVED
PMID: 34037241 (View on PubMed)

Miyoshi Y, Yoshimura Y, Saito K, Muramoto K, Sugawara M, Alexis K, Nomoto K, Nakamura S, Saeki T, Watanabe J, Perez-Garcia JM, Cortes J. High absolute lymphocyte counts are associated with longer overall survival in patients with metastatic breast cancer treated with eribulin-but not with treatment of physician's choice-in the EMBRACE study. Breast Cancer. 2020 Jul;27(4):706-715. doi: 10.1007/s12282-020-01067-2. Epub 2020 Mar 5.

Reference Type DERIVED
PMID: 32133606 (View on PubMed)

Wedam SB, Beaver JA, Amiri-Kordestani L, Bloomquist E, Tang S, Goldberg KB, Sridhara R, Ibrahim A, Kim G, Kluetz P, McKee A, Pazdur R. US Food and Drug Administration Pooled Analysis to Assess the Impact of Bone-Only Metastatic Breast Cancer on Clinical Trial Outcomes and Radiographic Assessments. J Clin Oncol. 2018 Apr 20;36(12):1225-1231. doi: 10.1200/JCO.2017.74.6917. Epub 2018 Mar 9.

Reference Type DERIVED
PMID: 29522361 (View on PubMed)

Twelves C, Cortes J, Kaufman PA, Yelle L, Awada A, Binder TA, Olivo M, Song J, O'Shaughnessy JA, Jove M, Perez EA. "New" metastases are associated with a poorer prognosis than growth of pre-existing metastases in patients with metastatic breast cancer treated with chemotherapy. Breast Cancer Res. 2015 Dec 9;17(1):150. doi: 10.1186/s13058-015-0657-1.

Reference Type DERIVED
PMID: 27391598 (View on PubMed)

Muss H, Cortes J, Vahdat LT, Cardoso F, Twelves C, Wanders J, Dutcus CE, Yang J, Seegobin S, O'Shaughnessy J. Eribulin monotherapy in patients aged 70 years and older with metastatic breast cancer. Oncologist. 2014 Apr;19(4):318-27. doi: 10.1634/theoncologist.2013-0282. Epub 2014 Mar 28.

Reference Type DERIVED
PMID: 24682463 (View on PubMed)

Cortes J, O'Shaughnessy J, Loesch D, Blum JL, Vahdat LT, Petrakova K, Chollet P, Manikas A, Dieras V, Delozier T, Vladimirov V, Cardoso F, Koh H, Bougnoux P, Dutcus CE, Seegobin S, Mir D, Meneses N, Wanders J, Twelves C; EMBRACE (Eisai Metastatic Breast Cancer Study Assessing Physician's Choice Versus E7389) investigators. Eribulin monotherapy versus treatment of physician's choice in patients with metastatic breast cancer (EMBRACE): a phase 3 open-label randomised study. Lancet. 2011 Mar 12;377(9769):914-23. doi: 10.1016/S0140-6736(11)60070-6. Epub 2011 Mar 2.

Reference Type DERIVED
PMID: 21376385 (View on PubMed)

Twelves C, Cortes J, Vahdat LT, Wanders J, Akerele C, Kaufman PA. Phase III trials of eribulin mesylate (E7389) in extensively pretreated patients with locally recurrent or metastatic breast cancer. Clin Breast Cancer. 2010 Apr;10(2):160-3. doi: 10.3816/CBC.2010.n.023.

Reference Type DERIVED
PMID: 20299316 (View on PubMed)

Other Identifiers

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2006-001949-34

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

E7389-G000-305

Identifier Type: -

Identifier Source: org_study_id

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