Efficacy and Safety in Subjects With Type 2 Diabetes Receiving Subcutaneous Basal Insulin and Prandial Inhalation of Technosphere/Insulin Versus Subcutaneous Premixed Insulin Therapy Over a 52-Week Treatment Period and a 4-Week Follow-up

NCT ID: NCT00309244

Last Updated: 2014-10-16

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

677 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-02-28

Study Completion Date

2008-09-30

Brief Summary

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The purpose of this 13 month study (12 month treatment period and 1 month follow-up period) is to determine whether inhaled insulin is safe and effective in the treatment of type 2 diabetes.

Detailed Description

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Conditions

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Diabetes Type 2

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

PREVENTION

Blinding Strategy

NONE

Study Groups

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TI + Insulin glargine

Technosphere® Insulin Inhalation Powder + insulin glargine

Group Type EXPERIMENTAL

Technosphere® Insulin Inhalation Powder

Intervention Type DRUG

Inhalation, 15U/30U

BPR 70/30

70% insulin aspart protamine suspension and 30% insulin aspart injection (rDNA origin)

Group Type ACTIVE_COMPARATOR

70% insulin aspart protamine suspension and 30% insulin aspart injection (rDNA origin)

Intervention Type DRUG

BPR 70/30, which is a premix of intermediate acting and rapid acting insulin given sc

Interventions

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Technosphere® Insulin Inhalation Powder

Inhalation, 15U/30U

Intervention Type DRUG

70% insulin aspart protamine suspension and 30% insulin aspart injection (rDNA origin)

BPR 70/30, which is a premix of intermediate acting and rapid acting insulin given sc

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Men or women ≥ 18 and ≤ 80 years old
* Clinical diagnosis of type 2 diabetes mellitus
* HbA1c \> 7.0% and ≤ 11.0%
* BMI ≤ 40 kg/m2
* Negative smoking status and urine cotinine test
* Written informed consent
* Receiving sc insulin 2-3 times daily administered as any of the following 3 regimens: self-mix regimen, pre-mix regimen, or long-acting analogue and regular or rapid-acting insulin analogue not to exceed 3 daily injections. Subjects may also have received oral antidiabetic agents including metformin or thiazolidinediones.
* No dose adjustments for insulin and oral antidiabetic agents within the preceding 6 weeks.
* FEV1 ≥ 70% of NHANES III predicted; TLC) ≥ 80% of predicted (Intermountain Thoracic Society); DLCO uncorrected ≥ 70% of predicted

Exclusion Criteria

* Total daily dose of insulin ≥1.4 IU/kg body weight
* Treatment with any sulfonylureas and/or meglitinides and/or alpha-glucosidase inhibitors within the preceding 8 weeks
* Treatment with pramlintide acetate (Symlin®), and/or any incretins (e.g., exenatide \[Byetta®\]) within the preceding 8 weeks
* Unstable diabetes mellitus control, defined as 2 or more episodes of severe hypoglycemia (requiring third party intervention) and/or any hospitalization or emergency room visit due to poor diabetic control or hyperglycemia requiring hospitalization within the preceding 6 months
* Exposure to an inhaled insulin at any time, treatment with an investigational drug within the preceding 3 months, and/or current participation in another clinical trial
* Allergy to insulin or to any drugs to be used as part of the clinical trial, or history of hypersensitivity to the investigational drug or to drugs of similar chemical structures
* History of active viral and/or cirrhotic hepatic disease and/or abnormal liver enzymes as evidenced by serum aspartate aminotransferase (AST)and/or alanine aminotransferase (ALT) ≥ 3 x Upper Limit of Normal (ULN)(Includes active hepatitis A, positive hepatitis B and/or hepatitis C serology)
* Serum creatinine \> 1.8 mg/dL in women and \> 2.0 mg/dL in men History of chronic obstructive pulmonary disease (COPD), asthma (any history of bronchospasm or asthma after the age of 14), and/or any other clinically important pulmonary disease confirmed by documented history, pulmonary function testing, or radiologic findings
* Congestive heart disease graded as class III or class IV according to New York Heart Association criteria and subjects currently being treated pharmacologically for ventricular dysrhythmias using amiodarone
* History of myocardial infarction, cardiac surgery, coronary angioplasty, and/or stroke within the preceding 3 months
* Symptomatic coronary artery disease, including crescendo angina, unstable angina, and/or unstable or symptomatic cardiac arrhythmias
* Poorly controlled arterial hypertension despite pharmacologic treatment, defined as systolic blood pressure (BP) \> 180 mm Hg and/or diastolic BP \> 110 mm Hg at screening
* History of malignancy within the preceding 5 years (other than excised basal cell carcinoma of the skin), any history of lung neoplasm, and/or subjects with current or previous chemotherapy or radiation therapy that may result in pulmonary toxicity
* History of acquired immunodeficiency syndrome (AIDS), AIDS-related complex (ARC), or positive human immunodeficiency virus (HIV) serology
* Prior diagnosis of systemic autoimmune or collagen vascular disease requiring previous or current treatment with systemic corticosteroids, cytotoxic drugs, or penicillamine
* Visit 1/Screening (Week -3), but prior to Visit 1 PFTs and before Visit 3/Baseline (Week 0), subject will be scheduled for PFTs after 30 days from resolution of respiratory infection. An additional hemoglobin and urine β-HCG (for women of childbearing potential age only) will be required
* Women who are pregnant, lactating or planning to become pregnant
* Women of childbearing potential (defined as pre-menopausal and not surgically sterilized or postmenopausal for less than 2 years) not practicing adequate birth control. Adequate birth control is defined as using oral, percutaneous and/or transdermal contraceptives; condoms and diaphragms with a spermicide, or intrauterine devices
* Current drug and/or alcohol abuse
* Subjects who in the opinion of the Investigator will be unable to comply with the requirements of the protocol
* Severe complications of diabetes mellitus, in the opinion of the Investigator, including: symptomatic autonomic neuropathy, disabling peripheral neuropathy, active proliferative retinopathy; nephropathy with renal failure, renal transplant and/or dialysis; history of foot ulcers; nontraumatic amputations due to gangrene;and/or vascular claudication
* Any other concurrent medical or major psychiatric condition which, in the opinion of the Investigator, makes the subject unsuitable for the clinical trial, or could limit the validity of the ICF and/or impair the subject's ability to participate in the trial
* Inability to perform PFT maneuvers meeting recommended American Thoracic Society (ATS) acceptability and repeatability criteria.
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Mannkind Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Coastal Clinical Research Inc

Mobile, Alabama, United States

Site Status

Quality of Life Medical & Research Center

Tucson, Arizona, United States

Site Status

Southern Arizona VA Healthcare System

Tucson, Arizona, United States

Site Status

Tucson Clinical Research

Tucson, Arizona, United States

Site Status

International Clinical Research Network

Chula Vista, California, United States

Site Status

Saad Hijazi MD Inc

Fresno, California, United States

Site Status

Valley Research

Fresno, California, United States

Site Status

Diabetes/Lipid Management and Research Center

Huntington Beach, California, United States

Site Status

South Bay Clinical Research

Inglewood, California, United States

Site Status

Southern California Endocrine Center

Pasadena, California, United States

Site Status

Coastal Biomedical Research Inc

Santa Monica, California, United States

Site Status

Diabetes Research Center

Tustin, California, United States

Site Status

University of Miami Diabetes Research Institute

Miami, Florida, United States

Site Status

International Research Associates LLC

Miami, Florida, United States

Site Status

Laureate Clinical Research Group

Atlanta, Georgia, United States

Site Status

Atlanta Pharmaceutical Research Center

Dunwoody, Georgia, United States

Site Status

North Atlanta Endocrinology & Diabetes PC

Lawrenceville, Georgia, United States

Site Status

Atlanta Center for Clinical Research

Roswell, Georgia, United States

Site Status

John H Stoger Jr Hospital of Cook County

Chicago, Illinois, United States

Site Status

Clintell Inc

Skokie, Illinois, United States

Site Status

Clintell Inc (Ellyin)

Skokie, Illinois, United States

Site Status

Medical Research of Louisiana

Metairie, Louisiana, United States

Site Status

Joslin Diabetes Center University of Maryland Medicine

Baltimore, Maryland, United States

Site Status

James A Dicke MDPA

Towson, Maryland, United States

Site Status

Wayne State University

Detroit, Michigan, United States

Site Status

Michigan Institute of Medicine

Livonia, Michigan, United States

Site Status

KMED Research

Saint Clair Shores, Michigan, United States

Site Status

Radiant Research Inc (Minneapolis)

Edina, Minnesota, United States

Site Status

International Diabetes Center

Minneapolis, Minnesota, United States

Site Status

Center for Urologic Clinical Trials University of Minnesota

Minneapolis, Minnesota, United States

Site Status

Amin Radparvar's Private Practice

City of Saint Peters, Missouri, United States

Site Status

MedEx Healthcare Research Inc

St Louis, Missouri, United States

Site Status

Billings Clinic Research Division

Billings, Montana, United States

Site Status

Montana Health Research Institute

Billings, Montana, United States

Site Status

Creighton Diabetes Center

Omaha, Nebraska, United States

Site Status

New Mexico Clinical Research & Osteoporosis Center

Albuquerque, New Mexico, United States

Site Status

University of New Mexico HCS

Albuquerque, New Mexico, United States

Site Status

Winthrop University Hospital

Mineola, New York, United States

Site Status

North Shore Diabetes and Endocrine Associates

New Hyde Park, New York, United States

Site Status

Univeristy of Physicians Group Endocrine Division

Staten Island, New York, United States

Site Status

Sensenbrenner Primary Care

Charlotte, North Carolina, United States

Site Status

East Carolina University (Tanenberg)

Greenville, North Carolina, United States

Site Status

Physician's East PA

Greenville, North Carolina, United States

Site Status

Valley Medical Primary Care

Centerville, Ohio, United States

Site Status

Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

Providence Health Partners - Center of Clinical Research

Dayton, Ohio, United States

Site Status

Cleveland Clinic Health System

East Cleveland, Ohio, United States

Site Status

Wells Institute for Health Awareness

Kettering, Ohio, United States

Site Status

Oregon Medical Group Clinical Resesarch

Eugene, Oregon, United States

Site Status

Lane Medical Research Group

Eugene, Oregon, United States

Site Status

Portland Diabetes & Endocrinology Center

Portland, Oregon, United States

Site Status

New Hope Research of Oregon

Portland, Oregon, United States

Site Status

Covance CRU Inc.

Portland, Oregon, United States

Site Status

Pennsylvania Research Institute

Bensalem, Pennsylvania, United States

Site Status

Thomas Jefferson University

Philadelphia, Pennsylvania, United States

Site Status

Upstate Pharmaceutical Research

Greenville, South Carolina, United States

Site Status

Southeastern Research Associates Inc

Taylors, South Carolina, United States

Site Status

AM Diabetes and Endocrinology Center

Bartlett, Tennessee, United States

Site Status

Memphis Internal Medicine PLLC

Memphis, Tennessee, United States

Site Status

The Endocrine Clinic

Memphis, Tennessee, United States

Site Status

Israel Hartman MD

Arlington, Texas, United States

Site Status

South Arlington Primary Care Assoc PA

Arlington, Texas, United States

Site Status

Dallas Diabetes & Endocrine Center

Dallas, Texas, United States

Site Status

North Texas Endocrine Center

Dallas, Texas, United States

Site Status

Radiant Research Dallas-North

Dallas, Texas, United States

Site Status

Baylor Endocrine Center

Dallas, Texas, United States

Site Status

Galenos Research

Dallas, Texas, United States

Site Status

Spuhler Medical Associates

Friendswood, Texas, United States

Site Status

Clinical Trial Network

Houston, Texas, United States

Site Status

Quality Assurance Research Center Inc

San Antonio, Texas, United States

Site Status

Covenant Clinic Research

San Antonio, Texas, United States

Site Status

Diabetes & Glandular Disease Research Assoc PA

San Antonio, Texas, United States

Site Status

SAM Clinical Research Center

San Antonio, Texas, United States

Site Status

Salt Lake Research

Salt Lake City, Utah, United States

Site Status

Sentara Medical Group

Norfolk, Virginia, United States

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Clinical Research Associates of Tidewater

Norfolk, Virginia, United States

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Larry D Stonesifer MD Inc PS

Federal Way, Washington, United States

Site Status

Rainier Clinical Research Center Inc

Renton, Washington, United States

Site Status

Cedar Research

Tacoma, Washington, United States

Site Status

Liberty Research Center

Tacoma, Washington, United States

Site Status

Hospital Interzonal de Agudos Pedro Fiorito

Avellaneda, Buenos Aires, Argentina

Site Status

CITDEEM - Centro de Investigacion y Tratamiento En Diabetes y Enfermedades Endocrino-Metabolicas

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status

FUNDAPRES/CIMel

Buenos Aires, , Argentina

Site Status

Centro Endocrinologic Tiempo

Buenos Aires, , Argentina

Site Status

Hospital Italiano de Buenos Aires

Buenos Aires, , Argentina

Site Status

Cons Asoc de Endocrinologia

Buenos Aires, , Argentina

Site Status

Centro Medico Dra De Salvo

Buenos Aires, , Argentina

Site Status

Hospital de Clinicas de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

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Hospital Sao Lucas da PUCRS

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

CPClin-Centro de Pesquisas Clinicas

São Paulo, São Paulo, Brazil

Site Status

Universidade Estabual de Maringa

Maringa Parana, , Brazil

Site Status

Nucleo de Medicina Integrada

Mogi das Cruzes, , Brazil

Site Status

Instituto Estadual De Diabetes e Endocrinologia Luis Capriglione

Rio de Janeiro, , Brazil

Site Status

Ccbr Brasil Centro de Analises e Pesquisas Clinicas Ltda

Rio de Janeiro, , Brazil

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Hospital Guilherme Alvaro

Santos, , Brazil

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Hospital do Rim e Hipertensao

São Paulo, , Brazil

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Instituto da Saude e Bem Estar da Mulher

São Paulo, , Brazil

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Blumenau Servicos Medicos S/C Ltda

São Paulo, , Brazil

Site Status

Centro de Pesquisa Clinica e Medicina Avancada

São Paulo, , Brazil

Site Status

Keele Medical Place

Downsview, Ontario, Canada

Site Status

Quest Clinical Trials

Markham, Ontario, Canada

Site Status

Lifestyle Metabolism Center

Oakville, Ontario, Canada

Site Status

Sarnia Institute of Clinical Research

Sarnia, Ontario, Canada

Site Status

Lifestyle Metabolism Center

Thornhill, Ontario, Canada

Site Status

Lifestyle Metabolism Center

Toronto, Ontario, Canada

Site Status

Hospital del Salvador

Santiago, Santiago Metropolitan, Chile

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Hospital Padre Alberto Hurtado

Santiago, Santiago Metropolitan, Chile

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Hospital Clinico Pontificia Universidad Catolica de Chile

Santiago, , Chile

Site Status

Hospital San Borja ArriaranUniversidad de Chile

Santiago, , Chile

Site Status

Instituto Mexicano de Investigacion

Mexico City, Durango, Mexico

Site Status

Hospital OCA

Monterrey, Nuevo Leon, MX, Mexico

Site Status

Hospital Universitario Dr Jose E Gonzalez

Monterrey, Nuevo León, Mexico

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Hospital Santa Engracia-CIMA

Garza García, , Mexico

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Centro de Estudios en Diabetes

Mexico City, , Mexico

Site Status

Cifbiotec

Mexico City, , Mexico

Site Status

Oddzial Chorob Wewnetrznych

Bialystock, POL, Poland

Site Status

NZOZ Specjalistyczny Osrodek Internistyczno - Diabetologiczny

Bialystok, POL, Poland

Site Status

Katedra I Klinika Chorob Metabolicznych Collegium Medicum Uniwersytety Jagiellonskiego

Krakow, POL, Poland

Site Status

Klliniczny nr 1 im Norberta Barlickiego Uniwersytetu Medycznego w Lodzi

Lodz, POL, Poland

Site Status

Instytut Centrum Zdrowia (009) Matki Polki

Lodz, POL, Poland

Site Status

Szpital Kolejowy im Dr w Roeflera(009) Oddzial Gastorenterologii

Pruszków, POL, Poland

Site Status

NZOZ Diabetologiczna Poradnia Specjalistyczna

Warsaw, , Poland

Site Status

NHI Kemerovo Regional Clinical Hospital

Kemerovo, RUS, Russia

Site Status

NI Principal Military Clinical Hospital n a academician N.N. Burdenko of the Ministry of Defense

Moscow, RUS, Russia

Site Status

NEI HPE Moscow State University of Medicine and Dentistry of FAHSD City Clinical Hospital #70

Moscow, RUS, Russia

Site Status

Moscow City Clinical Hospital # 13

Moscow, RUS, Russia

Site Status

SEI HPE Moscow Medical Academy IM Sechenov of Roszdrav Clinic of Endocrinology

Moscow, RUS, Russia

Site Status

SI Internal Affairs of Moscow- Clinical Hospital

Moscow, RUS, Russia

Site Status

RAAMS Endocrinology and Diabetology Department

Moscow, RUS, Russia

Site Status

St Petersburg NHI City Polytclinic #77 City Diabetological Center #4

Saint Petersburg, RUS, Russia

Site Status

Central Medical Sanitary Unit #122

Saint Petersburg, RUS, Russia

Site Status

Pavlov State Medical Univ of St Petersburg

Saint Petersburg, RUS, Russia

Site Status

NEI HPE Smolensk State Medical Academy of FAHSD RNHI Smolensk Regional Clinical Hospital

Smolensk, RUS, Russia

Site Status

MHI Clinical Hospital for Emergency Care na NV Soloviev

Yaroslavl, RUS, Russia

Site Status

MCHI Medical Sanitary Unit of Novo-Yaroslavsky Oil Refining Plant

Yaroslavl, RUS, Russia

Site Status

NHI Yaroslavl Regional Clinical Hospital

Yaroslavl, RUS, Russia

Site Status

NI Central Clinical Hospital of RAS

Moscow, , Russia

Site Status

City Clinical Hospital # 61

Moscow, , Russia

Site Status

Complejo Hospitalario Nuestra Senora de Valme

Seville, Andalusia, Spain

Site Status

Hospital de Mataro

Mataró, Barcelona, Spain

Site Status

Hospital del Mar (Cano)

Barcelona, , Spain

Site Status

Centro Médico Teknon

Barcelona, , Spain

Site Status

Hospital Universitario de la Princessa

Madrid, , Spain

Site Status

Hospital Ramon y Cajal

Madrid, , Spain

Site Status

Corporacion Sanitaria Parc Tauli Unidad de Endocrinologia

Sabadell, , Spain

Site Status

Complejo Hospitalario Virgen del Rocio

Seville, , Spain

Site Status

Hospital Virgen Macarena (policlinico) 2ª planta Servicio de Endocrinologia y Nutricion

Seville, , Spain

Site Status

Birchwood Surgery

Letchworth Garden City, Herts, United Kingdom

Site Status

Lister Hospital

Stevenage, Herts, United Kingdom

Site Status

Guy's & St Thomas Hospital

London, , United Kingdom

Site Status

Yaxley Group Practice

Peterborough, , United Kingdom

Site Status

Countries

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United States Argentina Brazil Canada Chile Mexico Poland Russia Spain United Kingdom

References

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Peyrot M, Rubin RR. Patient-reported outcomes in adults with type 2 diabetes using mealtime inhaled technosphere insulin and basal insulin versus premixed insulin. Diabetes Technol Ther. 2011 Dec;13(12):1201-6. doi: 10.1089/dia.2011.0037. Epub 2011 Oct 14.

Reference Type DERIVED
PMID: 21999640 (View on PubMed)

Rosenstock J, Lorber DL, Gnudi L, Howard CP, Bilheimer DW, Chang PC, Petrucci RE, Boss AH, Richardson PC. Prandial inhaled insulin plus basal insulin glargine versus twice daily biaspart insulin for type 2 diabetes: a multicentre randomised trial. Lancet. 2010 Jun 26;375(9733):2244-53. doi: 10.1016/S0140-6736(10)60632-0.

Reference Type DERIVED
PMID: 20609970 (View on PubMed)

Other Identifiers

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MKC-TI-102

Identifier Type: -

Identifier Source: org_study_id

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