Phase 2 Trial of Prophylactic Rituximab Therapy for Prevention of CGVHD

NCT ID: NCT00186628

Last Updated: 2017-11-28

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

36 participants

Study Classification

INTERVENTIONAL

Study Start Date

2005-06-30

Study Completion Date

2010-12-31

Brief Summary

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To determine if rituximab administered after allogeneic transplantation decreases the incidence of chronic graft-vs-host disease (cGvHD)

Detailed Description

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To test if prophylactic anti-B-cell therapy (weekly rituximab) given within 60 to 90 days after allogeneic transplantation will decrease allogeneic donor B-cell immunity and possibly the incidence of chronic graft-vs-host disease (cGvHD).

Conditions

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Leukemia, Mast-Cell Mantle-cell Lymphoma

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Prophylactic Rituximab

Rituximab will be infused after a non-myeloablative transplantation regimen of total lymphoid irradiation (TLI) + anti-thymoglobulin (ATG), with the intention of reducing chronic graft-vs-host disease (cGvHD)

Group Type EXPERIMENTAL

Total lymphoid irradiation

Intervention Type PROCEDURE

Total lymphoid irradiation (TLI) administered at 80cGy for 10 days

Rituximab

Intervention Type DRUG

Rituximab 375 mg/m2 administered as an intravenous (IV) infusion once weekly for 4 doses.

Anti-thymoglobulin, rabbit (ATG, rabbit ATG)

Intervention Type DRUG

Rabbit anti-thymoglobulin (ATG) administered from Day -11 through Day -7 (5 doses) at 1.5 mg/kg/day, for a total dose of 7.5 mg/kg.

Cyclosporine

Intervention Type DRUG

Cyclosporine (CSP) administered orally at 6.25 mg/kg twice-a-day (BID) from Day -3 until through Day +56 post-peripheral blood progenitor cell (PBPC) infusion. Dose may be adjusted to maintain a therapeutic level of cyclosporine, or in response to renal insufficiency. If at Day +56, chimerism assessment demonstrates \> 40% donor cells in the CD3+ lineage, and the patient is without evidence of GvHD, then cyclosporine taper will begin (6% reduction per week).

Mycophenylate mofetil

Intervention Type DRUG

Mycophenylate mofetil (MMF) will be administered at 15 mg/kg po Day 0, at 5 to 10 hours after mobilized PBPC infusion is complete

Filgrastim

Intervention Type DRUG

Filgrastim provided as needed for neutrophil support

Granisetron

Intervention Type DRUG

Granisetron administered as an anti-nausea agent (anti-emetic) at 1 mg orally 30 to 60 minutes before TLI

Solumedrol

Intervention Type DRUG

Solumedrol, an anti-inflammatory glucocorticoid containing methylprednisolone sodium succinate, administered at 1 mg/kg as a premedication for anti-thymoglobulin (ATG)

Acetaminophen

Intervention Type DRUG

Acetaminophen administered orally at 650 mg 1 hour prior to infusion of PBPC

Diphenhydramine

Intervention Type DRUG

Diphenhydramine administered by intravenous infusion at 50 mg 1 hour prior to infusion of PBPC

Hydrocortisone

Intervention Type DRUG

Hydrocortisone administered by intravenous infusion at 100 mg 1 hour prior to infusion of PBPC

Interventions

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Total lymphoid irradiation

Total lymphoid irradiation (TLI) administered at 80cGy for 10 days

Intervention Type PROCEDURE

Rituximab

Rituximab 375 mg/m2 administered as an intravenous (IV) infusion once weekly for 4 doses.

Intervention Type DRUG

Anti-thymoglobulin, rabbit (ATG, rabbit ATG)

Rabbit anti-thymoglobulin (ATG) administered from Day -11 through Day -7 (5 doses) at 1.5 mg/kg/day, for a total dose of 7.5 mg/kg.

Intervention Type DRUG

Cyclosporine

Cyclosporine (CSP) administered orally at 6.25 mg/kg twice-a-day (BID) from Day -3 until through Day +56 post-peripheral blood progenitor cell (PBPC) infusion. Dose may be adjusted to maintain a therapeutic level of cyclosporine, or in response to renal insufficiency. If at Day +56, chimerism assessment demonstrates \> 40% donor cells in the CD3+ lineage, and the patient is without evidence of GvHD, then cyclosporine taper will begin (6% reduction per week).

Intervention Type DRUG

Mycophenylate mofetil

Mycophenylate mofetil (MMF) will be administered at 15 mg/kg po Day 0, at 5 to 10 hours after mobilized PBPC infusion is complete

Intervention Type DRUG

Filgrastim

Filgrastim provided as needed for neutrophil support

Intervention Type DRUG

Granisetron

Granisetron administered as an anti-nausea agent (anti-emetic) at 1 mg orally 30 to 60 minutes before TLI

Intervention Type DRUG

Solumedrol

Solumedrol, an anti-inflammatory glucocorticoid containing methylprednisolone sodium succinate, administered at 1 mg/kg as a premedication for anti-thymoglobulin (ATG)

Intervention Type DRUG

Acetaminophen

Acetaminophen administered orally at 650 mg 1 hour prior to infusion of PBPC

Intervention Type DRUG

Diphenhydramine

Diphenhydramine administered by intravenous infusion at 50 mg 1 hour prior to infusion of PBPC

Intervention Type DRUG

Hydrocortisone

Hydrocortisone administered by intravenous infusion at 100 mg 1 hour prior to infusion of PBPC

Intervention Type DRUG

Other Intervention Names

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TLI Rituxan CSP Sandimmune MMF CellCept G-CSF Granulocyte-colony stimulating factor Neupogen Sancuso Medrol Depo-Medrol A-Methapred Tylenol Benadryl Westcort

Eligibility Criteria

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Inclusion Criteria

* Between 18 and 76 years of age
* Chronic lymphocytic leukemia (CLL):

* Unmutated IgG VH gene status
* Mutated IgG VH genes (\> 2% nucleotide change compared to somatic sequence)
* Complete remission benefit most from allogeneic hematopoietic stem cell transplant (HSCT).

(Physicians will be encouraged to provide aggressive chemotherapy prior to nonmyeloablative transplantation.)

* Mantle cell lymphoma (MCL): Transplant physicians believe subject would benefit from allogeneic HSCT.
* Adequate renal (Cr \< 2.4 mg/dL) and hepatic (Bilirubin \< 3.0 mg/dL, Aspartate aminotransferase (AST) \< 100 IU) function.
* Men and women of reproductive potential must agree to use an acceptable method of birth control during treatment and for six months after completion of treatment.
* All subjects must provide written informed consent


* Genotypically or phenotypically human leukocyte antigen (HLA)-identical.
* Age \< 76 unless cleared by institutional PI
* Capable of giving written, informed consent.
* Must consent to peripheral blood stem cell (PBSC) mobilization with G-CSF and apheresis

Exclusion Criteria

* Recipient has a 9 of 10 or 10 of 10 HLA identical donor (high resolution molecular genotyping at HLA A, B, C and DrB1, and DQ)
* Pregnancy
* Lactating
* Serious uncontrolled infection
* HIV seropositivity
* Hepatitis B or C seropositivity
* Cardiac function: ejection fraction \< 40% or uncontrolled cardiac failure
* Pulmonary: Diffusing capacity - carbon monoxide (DLCO) \< 50% predicted
* Liver function abnormalities: elevation of bilirubin to ≥ 3 mg/dL and/or AST \> 100
* Renal: creatinine \> 2.4
* Karnofsky performance score ≤ 60%
* Patients with poorly controlled hypertension (systolic blood pressure \> 150 or diastolic blood pressure \> 90 repeatedly).
* Known life-threatening hypersensitivity to rituximab or other anti-B cell antibodies.
* Inability to comply with the allogeneic transplant treatment.
* Uncontrolled central nervous system (CNS) involvement with disease


* Identical twin to subject
* Contra-indication to subcutaneous G-CSF at a dose of 16 mg/kg/d for 5 consecutive days
* Serious medical or psychological illness
* Prior malignancy within the preceding five years, with the exception of non-melanoma skin cancers.
* HIV seropositivity
Minimum Eligible Age

18 Years

Maximum Eligible Age

76 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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The Leukemia and Lymphoma Society

OTHER

Sponsor Role collaborator

National Cancer Institute (NCI)

NIH

Sponsor Role collaborator

Stanford University

OTHER

Sponsor Role lead

Responsible Party

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David Miklos

Assistant Professor of Medicine

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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David Miklos

Role: PRINCIPAL_INVESTIGATOR

Stanford University

Locations

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Stanford University School of Medicine

Stanford, California, United States

Site Status

Countries

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United States

References

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Filipovich AH, Weisdorf D, Pavletic S, Socie G, Wingard JR, Lee SJ, Martin P, Chien J, Przepiorka D, Couriel D, Cowen EW, Dinndorf P, Farrell A, Hartzman R, Henslee-Downey J, Jacobsohn D, McDonald G, Mittleman B, Rizzo JD, Robinson M, Schubert M, Schultz K, Shulman H, Turner M, Vogelsang G, Flowers ME. National Institutes of Health consensus development project on criteria for clinical trials in chronic graft-versus-host disease: I. Diagnosis and staging working group report. Biol Blood Marrow Transplant. 2005 Dec;11(12):945-56. doi: 10.1016/j.bbmt.2005.09.004.

Reference Type BACKGROUND
PMID: 16338616 (View on PubMed)

Arai S, Sahaf B, Narasimhan B, Chen GL, Jones CD, Lowsky R, Shizuru JA, Johnston LJ, Laport GG, Weng WK, Benjamin JE, Schaenman J, Brown J, Ramirez J, Zehnder JL, Negrin RS, Miklos DB. Prophylactic rituximab after allogeneic transplantation decreases B-cell alloimmunity with low chronic GVHD incidence. Blood. 2012 Jun 21;119(25):6145-54. doi: 10.1182/blood-2011-12-395970. Epub 2012 May 4.

Reference Type RESULT
PMID: 22563089 (View on PubMed)

Other Identifiers

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IRB-02372

Identifier Type: -

Identifier Source: org_study_id

96160

Identifier Type: OTHER

Identifier Source: secondary_id

BMT172

Identifier Type: OTHER

Identifier Source: secondary_id

SPO

Identifier Type: OTHER

Identifier Source: secondary_id

P01CA049605

Identifier Type: NIH

Identifier Source: secondary_id

View Link

NCT00234013

Identifier Type: -

Identifier Source: nct_alias